{"id":8642,"date":"2026-09-02T12:51:17","date_gmt":"2026-09-02T09:51:17","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8642"},"modified":"2026-09-02T13:28:12","modified_gmt":"2026-09-02T10:28:12","slug":"newbiologix-synastra-dmd-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/newbiologix-synastra-dmd-gene-therapy\/","title":{"rendered":"NewBiologix ve Synastra, DMD Gen Terapisi \u00dcretimini Geli\u015ftirmek \u0130\u00e7in Ortakl\u0131k Kurdu"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>Yeni bir uluslararas\u0131 i\u015f birli\u011fi, Duchenne kas distrofisi (DMD) i\u00e7in potansiyel bir gen terapisi geli\u015ftirilmesini desteklemek amac\u0131yla \u0130svi\u00e7re ve T\u00fcrkiye&#039;den biyoteknoloji uzmanl\u0131\u011f\u0131n\u0131 bir araya getiriyor.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0130svi\u00e7re merkezli biyoteknoloji \u015firketi NewBiologix SA, T\u00fcrkiye merkezli gen terapisi \u015firketi Synastra Biotechnology Inc. ile Synastra&#039;nin ara\u015ft\u0131rma a\u015famas\u0131ndaki DMD gen terapisi program\u0131 i\u00e7in istikrarl\u0131 bir \u00fcretici h\u00fccre hatt\u0131 geli\u015ftirmek \u00fczere bir anla\u015fma imzalad\u0131.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Bu ortakl\u0131k, gen terapisindeki en \u00f6nemli zorluklardan birine odaklan\u0131yor: tedavi i\u00e7in gereken b\u00fcy\u00fck miktarda viral vekt\u00f6r\u00fcn tutarl\u0131, \u00f6l\u00e7eklenebilir ve potansiyel olarak daha uygun maliyetli bir \u015fekilde \u00fcretilmesi.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0130\u00e7indekiler<\/h2><nav><ul><li><a href=\"#a-partnership-focused-on-dmd-gene-therapy-manufacturing\">DMD Gen Terapisi \u00dcretimine Odaklanan Bir Ortakl\u0131k<\/a><\/li><li><a href=\"#a-dmd-gene-therapy-program-emerging-from-turkiye\">T\u00fcrkiye&#039;den Yeni Bir DMD Gen Terapisi Program\u0131 Ortaya \u00c7\u0131k\u0131yor<\/a><\/li><li><a href=\"#connecting-turkish-innovation-with-global-manufacturing\">T\u00fcrk \u0130novasyonunu K\u00fcresel \u00dcretimle Ba\u011flamak<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 id=\"a-partnership-focused-on-dmd-gene-therapy-manufacturing\" class=\"wp-block-heading\">DMD Gen Terapisi \u00dcretimine Odaklanan Bir Ortakl\u0131k<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Anla\u015fma uyar\u0131nca, NewBiologix, Synastra&#039;nin DMD program\u0131 i\u00e7in istikrarl\u0131 bir Ara\u015ft\u0131rma H\u00fccre Bankas\u0131 geli\u015ftirmek ve karakterize etmek amac\u0131yla Xcell\u2122 Stabil \u00dcretim Platformunu kullanacakt\u0131r.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Platform, tekrarlanan ge\u00e7ici transkripsiyon s\u00fcre\u00e7lerini genetik olarak tasarlanm\u0131\u015f, kararl\u0131 \u00fcretici h\u00fccre hatlar\u0131yla de\u011fi\u015ftirmek \u00fczere tasarlanm\u0131\u015ft\u0131r. \u015eirketlere g\u00f6re, bu yakla\u015f\u0131m rekombinant adeno-ili\u015fkili vir\u00fcs (rAAV) \u00fcretimini daha tekrarlanabilir ve \u00f6l\u00e7eklenebilir hale getirmeye yard\u0131mc\u0131 olabilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Bu durum, \u00f6zellikle DMD gen terapisi i\u00e7in \u00f6nemlidir \u00e7\u00fcnk\u00fc sistemik tedavi \u00e7ok y\u00fcksek dozlarda rAAV vekt\u00f6rleri gerektirebilir. Bu nedenle \u00fcretim kapasitesi, tutarl\u0131l\u0131k, \u00f6l\u00e7eklenebilirlik ve maliyet, bu terapilerin gelecekteki geli\u015ftirilmesi ve eri\u015filebilirli\u011finde \u00f6nemli fakt\u00f6rler haline gelebilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Anla\u015fma ayr\u0131ca, program\u0131n ticari bir lisansa d\u00f6n\u00fc\u015ft\u00fcr\u00fclmesi se\u00e7ene\u011fini de i\u00e7eriyor ve bu da gelecekteki klinik ve ticari \u00fcretim faaliyetlerini destekleyebilir.<\/p>\n\n\n\n<h2 id=\"a-dmd-gene-therapy-program-emerging-from-turkiye\" class=\"wp-block-heading\">T\u00fcrkiye&#039;den Yeni Bir DMD Gen Terapisi Program\u0131 Ortaya \u00c7\u0131k\u0131yor<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Bu i\u015f birli\u011finin en dikkat \u00e7ekici y\u00f6nlerinden biri, Synastra&#039;nin T\u00fcrkiye men\u015feli olmas\u0131d\u0131r.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Synastra Biyoteknoloji, \u00dcsk\u00fcdar \u00dcniversitesi ve Unifon-Biotech GSYF Giri\u015fim Sermayesi Yat\u0131r\u0131m Fonu aras\u0131ndaki i\u015f birli\u011fiyle kurulmu\u015ftur. <strong>\u015eirketin ba\u015f\u0131nda molek\u00fcler biyolog ve genetik m\u00fchendis Dr. Cihan Ta\u015ftan bulunmakta olup, kendisi Y\u00f6netim Kurulu Ba\u015fkan Yard\u0131mc\u0131s\u0131 ve Genel M\u00fcd\u00fcr olarak g\u00f6rev yapmaktad\u0131r.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Synastra&#039;nin \u00f6nc\u00fc program\u0131, DMD i\u00e7in ara\u015ft\u0131rma a\u015famas\u0131nda olan AAV tabanl\u0131 bir mikro-distrofin gen terapisi aday\u0131d\u0131r.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u015eirket, program\u0131n\u0131 ilerletmek i\u00e7in genom m\u00fchendisli\u011fi, sentetik biyoloji, AAV vekt\u00f6r tasar\u0131m\u0131, analitik ve CMC stratejisi, preklinik geli\u015ftirme ve klinik uygulamaya y\u00f6nelik \u00e7al\u0131\u015fmalar\u0131 bir araya getiriyor.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Bu \u00e7al\u0131\u015fman\u0131n bilimsel altyap\u0131s\u0131n\u0131n bir k\u0131sm\u0131, \u00dcsk\u00fcdar \u00dcniversitesi ile olan i\u015f birli\u011fi ve Transgenik H\u00fccre Teknolojileri Uygulama ve Ara\u015ft\u0131rma Merkezi (TRGENMER) arac\u0131l\u0131\u011f\u0131yla sa\u011flanmaktad\u0131r.<\/p>\n\n\n\n<h2 id=\"connecting-turkish-innovation-with-global-manufacturing\" class=\"wp-block-heading\">T\u00fcrk \u0130novasyonunu K\u00fcresel \u00dcretimle Ba\u011flamak<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">NewBiologix ile yap\u0131lan ortakl\u0131k, T\u00fcrkiye&#039;de ortaya \u00e7\u0131kan bir gen terapisi program\u0131n\u0131 uluslararas\u0131 bir \u00fcretim teknolojisi platformuyla birle\u015ftirme yolunda \u00f6nemli bir ad\u0131m\u0131 temsil etmektedir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Synastra, potansiyel bir tedavinin yaln\u0131zca bilimsel tasar\u0131m\u0131na odaklanmak yerine, bilimsel, \u00fcretim ve uygulama s\u00fcre\u00e7lerini en ba\u015f\u0131ndan itibaren in\u015fa etti\u011fini belirtiyor.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Ama\u00e7, uluslararas\u0131 \u00fcretim, kalite ve d\u00fczenleyici standartlara do\u011fru ilerleyebilecek bir DMD gen terapisi program\u0131 geli\u015ftirmektir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">DMD toplulu\u011fu i\u00e7in bu i\u015fbirli\u011fi, halihaz\u0131rda bir tedavi y\u00f6nteminin mevcut oldu\u011fu anlam\u0131na gelmesinden ziyade, Duchenne kas distrofisinin alt\u0131nda yatan genetik nedeni ele almak i\u00e7in geli\u015ftirilen bir ba\u015fka deneysel yakla\u015f\u0131m\u0131 temsil etmesi a\u00e7\u0131s\u0131ndan \u00f6nemlidir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Ba\u015far\u0131l\u0131 olmas\u0131 durumunda, devam eden geli\u015ftirme \u00e7al\u0131\u015fmalar\u0131, T\u00fcrkiye k\u00f6kenli bu program\u0131n klinik uygulamaya daha da yakla\u015fmas\u0131na ve nihayetinde yeni tedavi se\u00e7eneklerine acilen ihtiya\u00e7 duyan hastalara ve ailelere ula\u015fma olas\u0131l\u0131\u011f\u0131na yard\u0131mc\u0131 olabilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Daha Fazlas\u0131n\u0131 Ke\u015ffedin<\/strong>:&nbsp;<a href=\"https:\/\/dmdwarrior.com\/tr\/clinical-trials\/\" target=\"_blank\" rel=\"noopener\">Duchenne Klinik Ara\u015ft\u0131rmalar\u0131n\u0131 Ke\u015ffedin<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>A new international collaboration is bringing together biotechnology expertise from Switzerland and Turkiye to support the development of a potential gene therapy for Duchenne muscular dystrophy (DMD). Swiss biotechnology company NewBiologix S.A. has entered into an agreement with Synastra Biotechnology Inc., a Turkiye-based gene therapy company, to develop a stable producer cell line for Synastra\u2019s [&hellip;]<\/p>\n","protected":false},"author":8,"featured_media":8643,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[892,887,891,818,66,61,888,889,890,80,81],"class_list":["post-8642","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-aav-gene-therapy","tag-cihan-tastan","tag-dmd-gene-therapy","tag-dmd-research","tag-duchenne-muscular-dystrophy","tag-gene-therapy","tag-micro-dystrophin","tag-newbiologix","tag-synastra-biotechnology","tag-turkey","tag-turkiye"],"subtitle":"Yeni bir ortakl\u0131k, Duchenne gen terapisi geli\u015ftirme \u00e7al\u0131\u015fmalar\u0131n\u0131 g\u00fc\u00e7lendirebilir. T\u00fcrkiye merkezli Synastra, ara\u015ft\u0131rma a\u015famas\u0131ndaki mikro-distrofin terapisini ilerletmek i\u00e7in \u0130svi\u00e7reli biyoteknoloji \u015firketi NewBiologix ile i\u015f birli\u011fi yap\u0131yor. Bu i\u015f birli\u011fi, T\u00fcrk inovasyonunu k\u00fcresel \u00fcretim uzmanl\u0131\u011f\u0131yla birle\u015ftiriyor.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/8642","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/8"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=8642"}],"version-history":[{"count":2,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/8642\/revisions"}],"predecessor-version":[{"id":8645,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/8642\/revisions\/8645"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/8643"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=8642"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=8642"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=8642"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}