{"id":6701,"date":"2026-03-09T18:17:40","date_gmt":"2026-03-09T15:17:40","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6701"},"modified":"2026-03-09T18:34:31","modified_gmt":"2026-03-09T15:34:31","slug":"vamorolone-agamree-in-dmd-real-world-experience","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/vamorolone-agamree-in-dmd-real-world-experience\/","title":{"rendered":"DMD&#039;de Vamorolone (Agamree): Ger\u00e7ek D\u00fcnya Deneyimi"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Santhera Pharmaceuticals, AGAMREE (vamorolone) ilac\u0131n\u0131n devam eden GUARDIAN \u00e7al\u0131\u015fmas\u0131n\u0131n ba\u015flang\u0131\u00e7 verileri de dahil olmak \u00fczere, uzun vadeli ger\u00e7ek d\u00fcnya kar\u015f\u0131la\u015ft\u0131rmal\u0131 analizlerinin tam sonu\u00e7lar\u0131n\u0131n, Orlando, Florida&#039;da d\u00fczenlenen Kas Distrofisi Derne\u011fi (MDA) Klinik ve Bilimsel Konferans\u0131 2026&#039;da sunuldu\u011funu duyurdu. Daha Fazla Bilgi Edinin: <a href=\"https:\/\/dmdwarrior.com\/tr\/what-is-agamree-vamorolone-what-is-agamree-used-for\/\" data-type=\"post\" data-id=\"2333\">Agamree (Vamorolone) Nedir?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Veri seti, Duchenne kas distrofisi (DMD) olan erkek \u00e7ocuklarda sekiz y\u0131la kadar (ortanca yakla\u015f\u0131k be\u015f y\u0131l) AGAMREE maruziyetini i\u00e7ermektedir. Analizler, \u00e7e\u015fitli eri\u015fim programlar\u0131 arac\u0131l\u0131\u011f\u0131yla tedaviye devam eden klinik \u00e7al\u0131\u015fmalara kat\u0131lanlar\u0131n yan\u0131 s\u0131ra Faz 4 GUARDIAN \u00e7al\u0131\u015fmas\u0131ndan (NCT06713135) elde edilen verileri de i\u00e7ermektedir. GUARDIAN&#039;dan elde edilen temel sonu\u00e7lar da dahil olmak \u00fczere uzun vadeli veriler, deflazakort veya prednizon ile tedavi edilen e\u011filim e\u015fle\u015ftirilmi\u015f tarihsel bir kontrol kohortu ile kar\u015f\u0131la\u015ft\u0131r\u0131lm\u0131\u015ft\u0131r.<a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06713135\" target=\"_blank\" rel=\"noreferrer noopener\">NCT06713135<\/a>)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Veriler, vamorolonun geleneksel kortikosteroidlere k\u0131yasla uzun vadeli etkinli\u011fini korudu\u011funu, ayn\u0131 zamanda tolerans\u0131n\u0131 iyile\u015ftirdi\u011fini ve s\u0131kl\u0131kla doz azalt\u0131m\u0131na veya tedavinin kesilmesine yol a\u00e7an ve uzun vadeli hasta sonu\u00e7lar\u0131n\u0131 etkileyen steroidle ili\u015fkili \u00f6nemli yan etkileri anlaml\u0131 \u015fekilde azaltt\u0131\u011f\u0131n\u0131 g\u00f6stermektedir. Daha fazla bilgi i\u00e7in: <a href=\"https:\/\/dmdwarrior.com\/tr\/pros-and-cons-of-steroids-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" data-type=\"post\" data-id=\"6244\" rel=\"noreferrer noopener\">Duchenne Kas Distrofisi \u0130\u00e7in Steroidlerin (Kortizon) Avantajlar\u0131 ve Dezavantajlar\u0131 Nelerdir?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Bu Sayfay\u0131 Takip Edin<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/tr\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">Duchenne i\u00e7in T\u00fcm Klinik Ara\u015ft\u0131rmalar<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Santhera Pharmaceuticals announced that full results from long-term real-world comparative analyses, including baseline data from the ongoing GUARDIAN study of AGAMREE (vamorolone), were presented at the Muscular Dystrophy Association (MDA) Clinical &amp; Scientific Conference 2026 in Orlando, Florida. Learn More: What is Agamree (Vamorolone)? The dataset includes up to eight years of AGAMREE exposure (median [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6703,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[42,41,43],"class_list":["post-6701","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-agamree","tag-santhera","tag-vamorolone"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/6701","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=6701"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/6701\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/6703"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=6701"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=6701"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=6701"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}