{"id":4847,"date":"2025-10-22T12:36:26","date_gmt":"2025-10-22T09:36:26","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4847"},"modified":"2025-11-03T19:59:05","modified_gmt":"2025-11-03T16:59:05","slug":"aji-bio-pharma-gene-tools-llc-collaboration-for-duchenne-muscular-dystrophy-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/aji-bio-pharma-gene-tools-llc-collaboration-for-duchenne-muscular-dystrophy-dmd\/","title":{"rendered":"Aji Bio-Pharma ve Gene Tools LLC, Duchenne Musk\u00fcler Distrofisi (DMD) i\u00e7in \u0130\u015f Birli\u011fi Yapacaklar\u0131n\u0131 Duyurdu"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Biyofarmas\u00f6tik s\u00f6zle\u015fmeli geli\u015ftirme ve \u00fcretim hizmetleri alan\u0131nda lider bir sa\u011flay\u0131c\u0131 olan Aji Bio-Pharma ve Gene Tools LLC, Duchenne kas distrofisi (DMD) gibi \u00e7ok \u00e7e\u015fitli genetik hastal\u0131klar\u0131n tedavisinde \u00f6nemli potansiyele sahip benzersiz bir oligon\u00fckleotid terap\u00f6tik s\u0131n\u0131f\u0131 olan fosforodiamidat morfolino oligomerlerine (PMO&#039;lar) eri\u015fimi geni\u015fletmek i\u00e7in resmi bir i\u015f birli\u011fi duyurdu. Bu ortakl\u0131k, erken ara\u015ft\u0131rma a\u015famalar\u0131nda safla\u015ft\u0131r\u0131lm\u0131\u015f PMO \u00fcretimini m\u00fcmk\u00fcn k\u0131larak ve \u0130yi Laboratuvar Uygulamalar\u0131 (GLP) ve \u0130yi \u00dcretim Uygulamalar\u0131 (GMP) \u00fcretimine sorunsuz bir \u015fekilde ge\u00e7i\u015f sa\u011flayarak geli\u015ftirme s\u00fcrecindeki kritik bir bo\u015flu\u011fu gideriyor.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">PMO&#039;lar, \u00f6zel \u00fcretim kabiliyetleri gerektiren yap\u0131sal olarak farkl\u0131 oligon\u00fckleotidlerdir. Aji Bio-Pharma, b\u00fcy\u00fck \u00f6l\u00e7ekli GLP ve GMP \u00fcretimi i\u00e7in optimize edilmi\u015f AJIPHASE s\u0131v\u0131 faz teknolojisi sayesinde PMO \u00fcretiminde derin bir uzmanl\u0131k olu\u015fturmu\u015ftur. Ancak, erken a\u015fama ara\u015ft\u0131rmalar daha k\u00fc\u00e7\u00fck ve \u00e7e\u015fitli PMO gruplar\u0131 gerektirir. Aji Bio-Pharma, d\u00fcnya \u00e7ap\u0131ndaki ara\u015ft\u0131rmac\u0131lara kat\u0131 fazda k\u00fc\u00e7\u00fck \u00f6l\u00e7ekli PMO sentezi sa\u011flamada lider olan Gene Tools LLC ile i\u015f birli\u011fi yaparak bu ihtiyac\u0131 kar\u015f\u0131lamaktad\u0131r.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Anla\u015fma kapsam\u0131nda, Gene Tools LLC \u00f6nceden safla\u015ft\u0131r\u0131lm\u0131\u015f PMO sentezini sa\u011flayacak, Aji Bio-Pharma ise safla\u015ft\u0131rma ve kalite kontrol\u00fcn\u00fc ger\u00e7ekle\u015ftirecek. Bu birliktelik, m\u00fc\u015fterilerin erken analiz d\u00fczeyindeki ara\u015ft\u0131rmalardan toksikoloji ve GLP \u00e7al\u0131\u015fmalar\u0131na h\u0131zla ge\u00e7melerini sa\u011flayarak klinik geli\u015ftirmeye giden sorunsuz bir yol a\u00e7acak.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Devam\u0131n\u0131 oku<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/tr\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">Duchenne \u0130\u00e7in Klinik Ara\u015ft\u0131rmalar (T\u00fcm Ara\u015ft\u0131rmalar\u0131n Listesi)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Aji Bio-Pharma a leading provider of biopharmaceutical contract development and manufacturing services, and Gene Tools LLC announced a formal collaboration to broaden access to phosphorodiamidate morpholino oligomers (PMOs), a unique class of oligonucleotide therapeutics with significant potential for treating a broad range of genetic diseases, such as Duchenne muscular dystrophy (DMD). This partnership addresses a [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4848,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[441,443,442],"class_list":["post-4847","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-aji-bio-pharma","tag-ajiphase","tag-gene-tools-llc"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/4847","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=4847"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/4847\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/4848"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=4847"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=4847"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=4847"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}