{"id":4142,"date":"2025-07-17T12:11:19","date_gmt":"2025-07-17T09:11:19","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4142"},"modified":"2025-11-03T20:21:36","modified_gmt":"2025-11-03T17:21:36","slug":"insmed-ins1201-gene-therapy-phase-1-clinical-trial-nct06817382","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/insmed-ins1201-gene-therapy-phase-1-clinical-trial-nct06817382\/","title":{"rendered":"INS1201 Gen Terapisi Faz 1 Klinik \u00c7al\u0131\u015fmas\u0131 Ba\u015fl\u0131yor"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Insmed, ClinicalTrials.gov&#039;de NCT06817382 ID numaras\u0131yla yay\u0131nlanan sayfada, Duchenne Musk\u00fcler Distrofi i\u00e7in geli\u015ftirilen INS1201 gen tedavisinin faz 1 denemelerine ba\u015flanaca\u011f\u0131n\u0131 duyurdu.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0130\u00e7indekiler<\/h2><nav><ul><li><a href=\"#bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">INS1201 Gen Terapisi Faz 1 Klinik \u00c7al\u0131\u015fmas\u0131<\/a><\/li><li><a href=\"#what-is-insmed-ins-1201-gene-therapy\">Insmed INS1201 Gen Terapisi Nedir?<\/a><\/li><li><a href=\"#bbm-d-101-clinical-trial-nct-07058662\">INS1201 Klinik Ara\u015ft\u0131rmas\u0131 \u2013 NCT06817382<\/a><\/li><li><a href=\"#bbm-d-101-phase-1-2-participation-criteria\">INS1201 Faz 1 Kat\u0131l\u0131m Kriterleri<\/a><\/li><li><a href=\"#how-can-i-contact-with-belief-bio-med\">Insmed ile Nas\u0131l \u0130leti\u015fime Ge\u00e7ebilirim?<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">INS1201 Gen Terapisi Faz 1 Klinik \u00c7al\u0131\u015fmas\u0131<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Bu \u00e7al\u0131\u015fman\u0131n temel amac\u0131, ayakta tedavi g\u00f6ren DMD&#039;li erkek kat\u0131l\u0131mc\u0131larda IT uygulamas\u0131 yoluyla tek doz INS1201&#039;in g\u00fcvenli\u011fini ve tolere edilebilirli\u011fini de\u011ferlendirmektir.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-insmed-ins-1201-gene-therapy\">Insmed INS1201 Gen Terapisi Nedir?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">INS1201, sistemik intraven\u00f6z enjeksiyon gerektiren Elevidys&#039;nin aksine, merkezi sinir sistemini do\u011frudan hedef al\u0131r ve intratekal olarak uygulan\u0131r. Sistemik gen tedavilerindeki g\u00fcvenlik ve etkinlik sorunlar\u0131n\u0131n bu odaklanm\u0131\u015f uygulama stratejisiyle ele al\u0131nmas\u0131 ama\u00e7lanmaktad\u0131r.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0130ntratekal uygulama, gerekli dozu on ila elli kata kadar \u00f6nemli \u00f6l\u00e7\u00fcde d\u00fc\u015f\u00fcr\u00fcr, ilac\u0131 ihtiya\u00e7 duyulan yere yo\u011funla\u015ft\u0131rarak sistemik toksisiteyi ve hedef d\u0131\u015f\u0131 etkileri \u00f6nler. Omurilik yaralanmas\u0131, sinir hasar\u0131 ve enfeksiyon riski gibi engellere ra\u011fmen, bu hastalara daha g\u00fcvenli ve muhtemelen daha ba\u015far\u0131l\u0131 bir se\u00e7enek sa\u011flayabilir, \u00f6zellikle de intraven\u00f6z tedavide kullan\u0131lan b\u00fcy\u00fck viral vekt\u00f6r dozajlar\u0131yla ili\u015fkili g\u00fcvenlik sorunlar\u0131 \u0131\u015f\u0131\u011f\u0131nda.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-clinical-trial-nct-07058662\">INS1201 Klinik Ara\u015ft\u0131rmas\u0131 \u2013 NCT06817382<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u00c7al\u0131\u015fma Ba\u015flang\u0131c\u0131 (Tahmini)<\/strong>: 2025-05-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Birincil Tamamlanma (Tahmini)<\/strong>: 2028-01-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u00c7al\u0131\u015fman\u0131n Tamamlanmas\u0131 (Tahmini)<\/strong>: 2028-03-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Kat\u0131l\u0131mc\u0131 Say\u0131s\u0131 (Tahmini)<\/strong>: 12 (Erkek)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Konumlar<\/strong>: ABD<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u00c7al\u0131\u015fmaya Uygun Ya\u015flar<\/strong>: 2 Ya\u015f\u0131ndan 4 Ya\u015f\u0131na Kadar (\u00c7ocuk)<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-phase-1-2-participation-criteria\">INS1201 Faz 1 Kat\u0131l\u0131m Kriterleri<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Uygun olabilmek i\u00e7in ki\u015filerin dahil olma gerekliliklerini yerine getirmeleri gerekir. Bir ki\u015finin ba\u015fka bir rahats\u0131zl\u0131\u011f\u0131 varsa veya gen terapisi almas\u0131n\u0131 engelleyebilecek bir tedavi g\u00f6r\u00fcyorsa, kat\u0131l\u0131m g\u00f6steremeyebilir. Dahil olma ve hari\u00e7 tutma kriterlerinin tamam\u0131na bu \u00e7al\u0131\u015fma ba\u011flant\u0131s\u0131na t\u0131klayarak ula\u015f\u0131labilir \u2013 <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06817382\" target=\"_blank\" rel=\"noreferrer noopener\">NCT06817382<\/a> \u2013.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"how-can-i-contact-with-belief-bio-med\">Insmed ile Nas\u0131l \u0130leti\u015fime Ge\u00e7ebilirim?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0130sim<\/strong>: Insmed T\u0131bbi Bilgiler<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Telefon Numaras\u0131<\/strong>: 18444467633<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>E-posta<\/strong>: medicalinformation@insmed.com<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Devam\u0131n\u0131 oku<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/tr\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">Duchenne \u0130\u00e7in Klinik Ara\u015ft\u0131rmalar (T\u00fcm Ara\u015ft\u0131rmalar\u0131n Listesi)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Insmed was announced on the page published on ClinicalTrials.gov with the ID NCT06817382 that the phase 1 trials of INS1201 gene therapy developed for Duchenne Muscular Dystrophy will be initiated. INS1201 Gene Therapy Phase 1 Clinical Trial The primary objective of this study is to evaluate the safety and tolerability of a single dose of [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4148,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,61,173,174,172],"class_list":["post-4142","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-gene-therapy","tag-ins1201","tag-ins1201-gene-therapy","tag-insmed"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/4142","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=4142"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/4142\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/4148"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=4142"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=4142"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=4142"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}