{"id":2570,"date":"2025-01-24T11:20:01","date_gmt":"2025-01-24T08:20:01","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2570"},"modified":"2025-03-07T13:21:44","modified_gmt":"2025-03-07T10:21:44","slug":"will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies\/","title":{"rendered":"Genethon ve Eukar\u00ffs Ortakl\u0131\u011f\u0131 Gen Terapilerinin Maliyetini D\u00fc\u015f\u00fcrecek mi?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Duchenne kas distrofisi i\u00e7in FDA onayl\u0131 tek gen terapisi, ailelerin kar\u015f\u0131layabilece\u011finden \u00e7ok daha pahal\u0131. Aileler bu fahi\u015f fiyat\u0131 kar\u015f\u0131layamaz. \u00dcreticiler DMD gen terapilerinin fiyat\u0131n\u0131 yeniden g\u00f6zden ge\u00e7irmeli. Genethon&#039;un 23 Ocak&#039;taki duyurusuna g\u00f6re, Eukar\u00ffs ile yap\u0131lan i\u015f birli\u011fi DMD gen terapilerinin fiyat\u0131n\u0131 makul bir seviyeye d\u00fc\u015f\u00fcrebilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Bug\u00fcn, biyo\u00fcretim verimini \u00f6nemli \u00f6l\u00e7\u00fcde art\u0131ran oyun de\u011fi\u015ftirici bir teknoloji yaratan biyoteknoloji firmas\u0131 Eukar\u00ffs ve nadir hastal\u0131klar i\u00e7in gen tedavilerinin ara\u015ft\u0131rma ve geli\u015ftirmesinde \u00f6nc\u00fc ve lider olan Genethon, stratejik bir anla\u015fman\u0131n olu\u015fturuldu\u011funu duyurdu. \u0130\u015f birli\u011fi, gen terapisi ila\u00e7lar\u0131n\u0131n \u00fcretim maliyetini d\u00fc\u015f\u00fcrmek i\u00e7in memeli h\u00fccrelerinde yeni bir haberci RNA (mRNA) ifade y\u00f6ntemi olan Eukar\u00ffs&#039;in benzersiz C3P3 teknolojisini kullan\u0131yor.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Daha fazla bilgi edin:<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/tr\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Duchenne Musk\u00fcler Distrofisi \u0130\u00e7in Umut Veren Yeni Gen Terapileri<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Devam\u0131n\u0131 oku:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/tr\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\">Elevidys Hakk\u0131nda S\u0131k\u00e7a Sorulan Sorular<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA-approved only gene therapy for Duchenne muscular dystrophy is costing far too much for families to afford. Families simply cannot afford this prohibitive price. Manufacturers should reconsider the price of DMD gene therapies. According to an announcement by Genethon on January 23, the collaboration with Eukar\u00ffs could bring the price of DMD gene therapies [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2572,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[201,66,200,72,61,105,202],"class_list":["post-2570","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-c3p3-technology","tag-duchenne-muscular-dystrophy","tag-eukarys","tag-gene-editing","tag-gene-therapy","tag-genethon","tag-mrna"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2570","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=2570"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2570\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/2572"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=2570"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=2570"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=2570"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}