{"id":2543,"date":"2025-01-23T11:09:58","date_gmt":"2025-01-23T08:09:58","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2543"},"modified":"2025-01-23T11:10:00","modified_gmt":"2025-01-23T08:10:00","slug":"personalized-miniorgans-could-speed-up-treatment-of-duchenne","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/personalized-miniorgans-could-speed-up-treatment-of-duchenne\/","title":{"rendered":"Ki\u015fiselle\u015ftirilmi\u015f Miniorganlar Duchenne Tedavisini H\u0131zland\u0131rabilir"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Ki\u015fiselle\u015ftirilmi\u015f antisens oligon\u00fckleotidler (ASO&#039;lar), Duchenne kas distrofisi (DMD) tedavisine y\u00f6nelik \u00e7al\u0131\u015fmalar\u0131 h\u0131zland\u0131rabilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Her y\u0131l on binlerce bebek, hen\u00fcz hi\u00e7bir tedavi denenmemi\u015f kadar nadir g\u00f6r\u00fclen genetik anormalliklerin yol a\u00e7t\u0131\u011f\u0131 gizemli hastal\u0131klarla do\u011fuyor. Ara\u015ft\u0131rmac\u0131lar, hastalar\u0131n kan h\u00fccrelerinden \u00fcretilen k\u00fc\u00e7\u00fck doku par\u00e7alar\u0131n\u0131 kullanarak, bu hasta \u00e7ocuklardan baz\u0131lar\u0131n\u0131n \u00f6zelle\u015ftirilmi\u015f ila\u00e7lar\u0131n\u0131 test etmek i\u00e7in gereken laboratuvar \u00e7al\u0131\u015fmalar\u0131n\u0131 h\u0131zland\u0131rmak i\u00e7in bir y\u00f6ntem ke\u015ffettiler.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Nadir g\u00f6r\u00fclen genetik hastal\u0131klar\u0131 tedavi etmek i\u00e7in kullan\u0131ld\u0131\u011f\u0131nda, ki\u015fiselle\u015ftirilmi\u015f antisens oligon\u00fckleotidler (ASO&#039;lar) \u00fcmit verici sonu\u00e7lar g\u00f6stermi\u015ftir. Bu terap\u00f6tik yakla\u015f\u0131ma duyarl\u0131 patojenik genetik varyasyonlara sahip nadir hastal\u0131klar\u0131 olan ki\u015fileri belirleme kapasitesinin, klinik dizileme teknolojisi ilerlemeye devam ettik\u00e7e artmas\u0131 muhtemeldir.<\/p>","protected":false},"excerpt":{"rendered":"<p>Personalized antisense oligonucleotides (ASOs) may accelerate studies on treating Duchenne muscular dystrophy (DMD). Every year, tens of thousands of babies are born with enigmatic illnesses brought on by genetic abnormalities that are so uncommon that no treatment has yet been attempted. Researchers have now discovered a method to expedite the laboratory work required to test [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2545,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[191,66,190,189],"class_list":["post-2543","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-aso","tag-duchenne-muscular-dystrophy","tag-miniorgans","tag-organoids"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2543","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=2543"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2543\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/2545"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=2543"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=2543"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=2543"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}