{"id":2455,"date":"2025-01-16T11:50:08","date_gmt":"2025-01-16T08:50:08","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2455"},"modified":"2025-01-16T13:21:23","modified_gmt":"2025-01-16T10:21:23","slug":"solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy\/","title":{"rendered":"Solid Biosciences, SGT-003 Gen Terapisi i\u00e7in Klinik Deneme Hakk\u0131nda Bilgi Yay\u0131mlad\u0131"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Solid Biosciences, SGT-003 gen terapisi klinik denemesinde d\u00f6rt hastaya doz uyguland\u0131\u011f\u0131n\u0131, t\u00fcm hastalarda iyi tolere edildi\u011fini ve herhangi bir yan etki g\u00f6zlenmedi\u011fini; ilk \u00fc\u00e7 hastadan elde edilen verilerin 2025&#039;in ilk \u00e7eyre\u011finde mevcut olabilece\u011fini payla\u015ft\u0131.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Duchenne Musk\u00fcler Distrofi (DMD) i\u00e7in SGT-003 Gen Terapisi<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>Devam eden INSPIRE DUCHENNE klinik \u00e7al\u0131\u015fmas\u0131nda doz uygulanan ilk d\u00f6rt hastada SGT-003&#039;\u00fcn iyi tolere edilmeye devam etti\u011fi g\u00f6r\u00fcld\u00fc.<\/li>\n\n\n\n<li>Geni\u015fletilmi\u015f INSPIRE DUCHENNE protokol\u00fc kapsam\u0131nda hasta kayd\u0131 ve dozlama devam ediyor.<\/li>\n\n\n\n<li>Kuzey Amerika&#039;da alt\u0131 klinik merkez faaliyete ge\u00e7irildi (be\u015fi ABD&#039;de, biri Kanada&#039;da).<\/li>\n\n\n\n<li>\u0130ngiltere \u0130la\u00e7 ve Sa\u011fl\u0131k \u00dcr\u00fcnleri D\u00fczenleme Kurumu (MHRA), INSPIRE DUCHENNE klinik ara\u015ft\u0131rma ba\u015fvurusunu (CTA) onaylad\u0131 ve ilk saha aktivasyonunun 2025&#039;in 2. yar\u0131s\u0131nda ger\u00e7ekle\u015fmesi bekleniyor.<\/li>\n\n\n\n<li>Solid&#039;in 2025&#039;in ilk \u00e7eyre\u011finde doz verilen ilk \u00fc\u00e7 hastaya ait verileri bildirmesi bekleniyor.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Daha fazla bilgi edin:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/tr\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\">Duchenne Musk\u00fcler Distrofisi \u0130\u00e7in Umut Veren Yeni Gen Terapileri<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Solid Biosciences shared that four patients have been dosed in the SGT-003 gene therapy clinical trial; it was well tolerated in all patients with no side effects observed; and data from the first three patients could be available in Q1 2025. SGT-003 Gene Therapy for Duchenne Muscular Dystrophy (DMD) Learn More: Potential Upcoming New Gene [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2458,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[171,72,61,110,170,109,79],"class_list":["post-2455","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-canada","tag-gene-editing","tag-gene-therapy","tag-sgt-003","tag-sgt-003-gene-therapy","tag-solid-biosciences","tag-usa"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2455","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=2455"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2455\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/2458"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=2455"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=2455"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=2455"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}