{"id":2226,"date":"2025-01-02T23:09:53","date_gmt":"2025-01-02T20:09:53","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2226"},"modified":"2025-11-03T19:23:00","modified_gmt":"2025-11-03T16:23:00","slug":"what-is-deramiocel","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/what-is-deramiocel\/","title":{"rendered":"Deramiocel nedir? CAP-1002 ne i\u015fe yarar?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Nadir hastal\u0131klar\u0131n tedavisi i\u00e7in d\u00f6n\u00fc\u015ft\u00fcr\u00fcc\u00fc h\u00fccre ve ekzosom bazl\u0131 tedaviler geli\u015ftiren bir biyoteknoloji \u015firketi olan Capricor Therapeutics, bug\u00fcn Duchenne kas distrofisi (DMD) kardiyomiyopatisi te\u015fhisi konan hastalar\u0131n tedavisinde kullan\u0131lmak \u00fczere ara\u015ft\u0131rma a\u015famas\u0131ndaki bir h\u00fccre tedavisi olan deramiocel i\u00e7in tam onay almak amac\u0131yla ABD G\u0131da ve \u0130la\u00e7 Dairesi&#039;ne (FDA) Biyolojik Lisans Ba\u015fvurusu&#039;nun (BLA) sunulmas\u0131n\u0131n tamamland\u0131\u011f\u0131n\u0131 duyurdu. <strong>Peki Deramiocel nedir ve ne i\u015fe yarar?<\/strong><\/p>\n\n\n\n<h2 class=\"wp-block-heading\"><strong>Deramiocel Nedir?<\/strong><\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Capricor Therapeutics taraf\u0131ndan geli\u015ftirilen Deramiocel (CAP-1002), kas dejenerasyonu ve g\u00fc\u00e7s\u00fczl\u00fc\u011f\u00fc ile karakterize \u015fiddetli ve ilerleyici bir genetik bozukluk olan Duchenne Musk\u00fcler Distrofi (DMD) i\u00e7in ara\u015ft\u0131r\u0131lan umut verici bir tedavi y\u00f6ntemidir.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">Etki Mekanizmas\u0131<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">Deramiocel, kardiyak kaynakl\u0131 mezenkimal k\u00f6k h\u00fccrelerden (MSC) t\u00fcretilen h\u00fccre bazl\u0131 bir terapidir. Bu k\u00f6k h\u00fccreler, kas onar\u0131m\u0131n\u0131 ve rejenerasyonunu destekleyen fakt\u00f6rleri salg\u0131lama yetene\u011fine sahiptir. Deramiocel&#039;in amac\u0131, bu k\u00f6k h\u00fccrelerin rejeneratif \u00f6zelliklerini kullanarak iltihab\u0131 azaltmak, doku onar\u0131m\u0131n\u0131 te\u015fvik etmek ve DMD&#039;den muzdarip bireylerde hasarl\u0131 kas dokusunu potansiyel olarak yenilemektir.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">Deramiocel&#039;in DMD&#039;de Potansiyel Kullan\u0131m\u0131n\u0131n Temel Noktalar\u0131:<\/h3>\n\n\n\n<ol class=\"wp-block-list\">\n<li><strong>H\u00fccre Bazl\u0131 Terapi<\/strong>: Deramiocel, kalp dokusundan izole edilen ve daha sonra i\u015flenip hastalara verilen k\u00f6k h\u00fccreleri kullan\u0131r. Mezenkimal k\u00f6k h\u00fccrelerin, iltihab\u0131 azaltan ve kas rejenerasyonunu uyaran proteinler ve sitokinler salg\u0131layarak iyile\u015fmeyi destekledi\u011fi d\u00fc\u015f\u00fcn\u00fclmektedir.<\/li>\n\n\n\n<li><strong>Kas Yenilenmesini Hedefleme<\/strong>: DMD, iskelet kaslar\u0131nda ilerleyici hasara ve zay\u0131fl\u0131\u011fa yol a\u00e7ar. Deramiocel, v\u00fccudun do\u011fal iyile\u015fme s\u00fcre\u00e7lerini uyararak ve kas h\u00fccrelerinin hayatta kalmas\u0131n\u0131 ve b\u00fcy\u00fcmesini te\u015fvik eden bir ortam yaratarak kas dokusunun yenilenmesine yard\u0131mc\u0131 olabilir.<\/li>\n\n\n\n<li><strong>Hastal\u0131\u011f\u0131n \u0130lerleyi\u015fini Yava\u015flatma Potansiyeli<\/strong>: Deramiocel, iltihab\u0131 gidererek ve kas dokusunun onar\u0131m\u0131n\u0131 destekleyerek, DMD&#039;deki kas dejenerasyonunun ilerlemesini yava\u015flatmaya yard\u0131mc\u0131 olabilir ve bu da hastalar\u0131n hareket kabiliyetini ve ya\u015fam kalitesini art\u0131rabilir.<\/li>\n\n\n\n<li><strong>Nas\u0131l Uygulan\u0131r<\/strong>:H\u00fccreler genellikle enjeksiyon yoluyla uygulan\u0131r ve bu sayede hasarl\u0131 kas dokular\u0131na ula\u015farak onar\u0131c\u0131 fakt\u00f6rlerin sal\u0131nmas\u0131 sa\u011flan\u0131r.<\/li>\n<\/ol>\n\n\n\n<h3 class=\"wp-block-heading\">Capricor Therapeutics, Duchenne Musk\u00fcler Distrofi Tedavisi \u0130\u00e7in Deramiocel \u0130\u00e7in ABD FDA&#039;ye Biyolojik Lisans Ba\u015fvurusunu Tamamlad\u0131<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">Son g\u00fcncellemelere g\u00f6re, Capricor Therapeutics, Deramiocel&#039;in DMD i\u00e7in g\u00fcvenli\u011fini ve etkinli\u011fini de\u011ferlendirmek \u00fczere klinik deneyler y\u00fcr\u00fct\u00fcyor. Bu deneylerden elde edilen sonu\u00e7lar, bu tedavinin Duchenne Musk\u00fcler Distrofisi olan bireyler i\u00e7in uygulanabilir bir tedavi se\u00e7ene\u011fi olup olmayaca\u011f\u0131n\u0131 belirleyecek.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Etkili oldu\u011fu kan\u0131tlan\u0131rsa Deramiocel, DMD tedavisinde \u00f6nemli bir ilerleme sa\u011flayabilir ve bu zorlu durumdan etkilenen hastalara ve ailelerine yeni bir umut sunabilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Daha fazla bilgi edin:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/tr\/capricor-therapeutics-publishes-peer-reviewed-study-about-cell-therapy-deramiocel\/\">Capricor Therapeutics, Deramiocel H\u00fccre Terapisi Hakk\u0131nda Hakemli Bir \u00c7al\u0131\u015fma Yay\u0131nlad\u0131<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Capricor Therapeutics, a biotechnology company developing transformative cell and exosome-based therapeutics for the treatment of rare diseases, today announced the completion of the submission of its Biologics License Application (BLA) to the U.S. Food and Drug Administration (FDA) seeking full approval for deramiocel, an investigational cell therapy, to treat patients diagnosed with Duchenne muscular dystrophy [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2228,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[90,86,87,89,85,88],"class_list":["post-2226","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-cap-1002","tag-capricor","tag-capricor-therapeutics","tag-cardiomyopathy","tag-deramiocel","tag-fda"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2226","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=2226"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2226\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/2228"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=2226"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=2226"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=2226"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}