{"id":2190,"date":"2025-01-02T01:50:35","date_gmt":"2025-01-01T22:50:35","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2190"},"modified":"2025-01-02T02:00:28","modified_gmt":"2025-01-01T23:00:28","slug":"is-duchenne-gene-therapy-a-suitable-treatment-despite-its-immunogenic-class-effect","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/tr\/is-duchenne-gene-therapy-a-suitable-treatment-despite-its-immunogenic-class-effect\/","title":{"rendered":"Duchenne Gen Terapisi \u0130mm\u00fcnojenik S\u0131n\u0131f Etkisine Ra\u011fmen Uygun Bir Tedavi midir?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Kardiyomiyopati veya solunum komplikasyonlar\u0131 sonucu ilerleyen kas g\u00fc\u00e7s\u00fczl\u00fc\u011f\u00fc ve nihai \u00f6l\u00fcm, \u015fiddetli bir X ba\u011flant\u0131l\u0131 bozukluk olan Duchenne kas distrofisi (DMD)&#039;nin ay\u0131rt edici \u00f6zellikleridir. \u015eu anda DMD i\u00e7in bir tedavi yoktur ve standart tedavilerin birincil odak noktas\u0131 semptom y\u00f6netimidir. Gen terapileri, imm\u00fcnos\u00fcpresif \u00f6nlemler ve optimize edilmi\u015f vekt\u00f6r tasar\u0131mlar\u0131 kullanarak hastal\u0131\u011f\u0131n genetik nedenini daha etkili bir \u015fekilde ele alabilir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Duchenne kas distrofisi (DMD) hastal\u0131\u011f\u0131nda gen terapisi tedavilerinin etkileri nelerdir, gen terapileri i\u015fe yar\u0131yor mu? \u0130\u015fte kapsaml\u0131 bir analiz.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/www.tandfonline.com\/eprint\/BFZQKYN3YY3AHAVX9S27\/full?target=10.1080\/14740338.2024.2447072\" target=\"_blank\" rel=\"noreferrer noopener\">Devam\u0131n\u0131 oku<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/x.com\/ToshifumiYokota\" target=\"_blank\" rel=\"noreferrer noopener\">Prof. Toshi Yokota&#039;y\u0131 takip edin<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Progressive muscle weakness and eventual mortality as a result of cardiomyopathy or respiratory complications are the hallmarks of Duchenne muscular dystrophy (DMD), a severe X-linked disorder. At present, there is no cure for DMD, and the primary focus of standard treatments is on symptom management. Gene therapies can more effectively address the genetic cause of [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2192,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[66,33,72,61],"class_list":["post-2190","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-duchenne-muscular-dystrophy","tag-elevidys","tag-gene-editing","tag-gene-therapy"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2190","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/comments?post=2190"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/posts\/2190\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media\/2192"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/media?parent=2190"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/categories?post=2190"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/tr\/wp-json\/wp\/v2\/tags?post=2190"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}