{"id":5112,"date":"2025-11-04T18:55:24","date_gmt":"2025-11-04T15:55:24","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5112"},"modified":"2025-11-04T18:55:26","modified_gmt":"2025-11-04T15:55:26","slug":"ppmd-funding-to-myogene-bio-for-myodys-gene-editing-platform","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/ru\/ppmd-funding-to-myogene-bio-for-myodys-gene-editing-platform\/","title":{"rendered":"PPMD \u043f\u0440\u0435\u0434\u043e\u0441\u0442\u0430\u0432\u043b\u044f\u0435\u0442 $400 000 \u043d\u0430 \u0444\u0438\u043d\u0430\u043d\u0441\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u0435 MyoGene Bio \u0434\u043b\u044f \u043f\u043b\u0430\u0442\u0444\u043e\u0440\u043c\u044b \u0440\u0435\u0434\u0430\u043a\u0442\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u044f \u0433\u0435\u043d\u043e\u0432 MyoDys"},"content":{"rendered":"<p class=\"wp-block-paragraph\">PPMD \u043f\u0440\u0435\u0434\u043e\u0441\u0442\u0430\u0432\u0438\u043b\u0430 \u0444\u0438\u043d\u0430\u043d\u0441\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u0435 \u0432 \u0440\u0430\u0437\u043c\u0435\u0440\u0435 $400\u00a0000 \u0434\u043b\u044f MyoGene \u0447\u0435\u0440\u0435\u0437 PPMD Venture Pathways, \u0432\u0435\u043d\u0447\u0443\u0440\u043d\u043e-\u0444\u0438\u043b\u0430\u043d\u0442\u0440\u043e\u043f\u0438\u0447\u0435\u0441\u043a\u0443\u044e \u0438\u043d\u0438\u0446\u0438\u0430\u0442\u0438\u0432\u0443 \u043e\u0440\u0433\u0430\u043d\u0438\u0437\u0430\u0446\u0438\u0438, \u043a\u043e\u0442\u043e\u0440\u0430\u044f \u043f\u0440\u0435\u0434\u043e\u0441\u0442\u0430\u0432\u043b\u044f\u0435\u0442 \u043e\u0442\u0440\u0430\u0441\u043b\u0435\u0432\u043e\u0435 \u0444\u0438\u043d\u0430\u043d\u0441\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u0435 \u0434\u043b\u044f \u0443\u0441\u043a\u043e\u0440\u0435\u043d\u0438\u044f \u0440\u0430\u0437\u0440\u0430\u0431\u043e\u0442\u043a\u0438 \u0442\u0435\u0440\u0430\u043f\u0435\u0432\u0442\u0438\u0447\u0435\u0441\u043a\u0438\u0445 \u0441\u0440\u0435\u0434\u0441\u0442\u0432 \u0434\u043b\u044f \u043b\u0435\u0447\u0435\u043d\u0438\u044f \u043c\u044b\u0448\u0435\u0447\u043d\u043e\u0439 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u0438 \u0414\u044e\u0448\u0435\u043d\u043d\u0430 \u0438 \u0411\u0435\u043a\u043a\u0435\u0440\u0430.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0427\u0442\u043e \u0442\u0430\u043a\u043e\u0435 MyoDys?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0421\u0442\u0440\u0430\u0442\u0435\u0433\u0438\u044f MyoGene, \u0438\u0437\u0432\u0435\u0441\u0442\u043d\u0430\u044f \u043a\u0430\u043a MyoDys 45-55, \u0438\u0441\u043f\u043e\u043b\u044c\u0437\u0443\u0435\u0442 \u0442\u0435\u0445\u043d\u043e\u043b\u043e\u0433\u0438\u044e \u0440\u0435\u0434\u0430\u043a\u0442\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u044f \u0433\u0435\u043d\u043e\u0432 \u0434\u043b\u044f \u0440\u0435\u0434\u0430\u043a\u0442\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u044f \u0433\u0435\u043d\u0430 \u041c\u0414\u0414 \u0443 \u0447\u0435\u043b\u043e\u0432\u0435\u043a\u0430.<\/strong> \u041e\u043d\u0438 \u043d\u0430\u0446\u0435\u043b\u0435\u043d\u044b \u043d\u0430 \u043e\u0431\u0448\u0438\u0440\u043d\u0443\u044e \u0434\u0435\u043b\u0435\u0446\u0438\u044e \u044d\u043a\u0437\u043e\u043d\u043e\u0432 45\u201355, \u043e\u0445\u0432\u0430\u0442\u044b\u0432\u0430\u044e\u0449\u0443\u044e \u043e\u0447\u0430\u0433 \u0431\u043e\u043b\u0435\u0437\u043d\u0435\u0442\u0432\u043e\u0440\u043d\u044b\u0445 \u0432\u0430\u0440\u0438\u0430\u043d\u0442\u043e\u0432 \u0438 \u0441\u043e\u0437\u0434\u0430\u044e\u0449\u0443\u044e \u0432\u043d\u0443\u0442\u0440\u0438\u0440\u0430\u043c\u043e\u0447\u043d\u0443\u044e \u0434\u0435\u043b\u0435\u0446\u0438\u044e, \u043a\u043e\u0442\u043e\u0440\u0430\u044f \u0432\u043e\u0441\u0441\u0442\u0430\u043d\u0430\u0432\u043b\u0438\u0432\u0430\u0435\u0442 \u0432\u044b\u0440\u0430\u0431\u043e\u0442\u043a\u0443 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u043d\u0430. \u041f\u043e\u0434\u0445\u043e\u0434 MyoGene \u0438\u043c\u0438\u0442\u0438\u0440\u0443\u0435\u0442 \u0434\u0435\u043b\u0435\u0446\u0438\u044e, \u043d\u0430\u0431\u043b\u044e\u0434\u0430\u0435\u043c\u0443\u044e \u043f\u0440\u0438 \u043b\u0451\u0433\u043a\u043e\u0439 \u043c\u044b\u0448\u0435\u0447\u043d\u043e\u0439 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u0438 \u0411\u0435\u043a\u043a\u0435\u0440\u0430, \u0441\u0432\u044f\u0437\u0430\u043d\u043d\u0443\u044e \u0441 \u0432\u044b\u0440\u0430\u0431\u043e\u0442\u043a\u043e\u0439 \u0432\u044b\u0441\u043e\u043a\u043e\u0444\u0443\u043d\u043a\u0446\u0438\u043e\u043d\u0430\u043b\u044c\u043d\u043e\u0433\u043e \u0431\u0435\u043b\u043a\u0430 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u043d\u0430. \u041f\u043e\u0434\u043e\u0431\u043d\u0430\u044f \u0434\u0435\u043b\u0435\u0446\u0438\u044f \u0438 \u0440\u0435\u0444\u0440\u0435\u0439\u043c\u0438\u043d\u0433 \u0433\u0435\u043d\u0430 DMD \u043c\u043e\u0433\u0443\u0442 \u0431\u044b\u0442\u044c \u0432\u044b\u043f\u043e\u043b\u043d\u0435\u043d\u044b \u043f\u0440\u0438\u043c\u0435\u0440\u043d\u043e \u0443 50% \u043f\u0430\u0446\u0438\u0435\u043d\u0442\u043e\u0432 \u0441 \u043c\u044b\u0448\u0435\u0447\u043d\u043e\u0439 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u0435\u0439 \u0414\u044e\u0448\u0435\u043d\u043d\u0430. <strong>\u0412 \u043e\u0442\u043b\u0438\u0447\u0438\u0435 \u043e\u0442 \u0433\u0435\u043d\u043d\u043e\u0439 \u0442\u0435\u0440\u0430\u043f\u0438\u0438, \u043a\u043e\u0442\u043e\u0440\u0430\u044f \u043f\u0440\u0435\u0434\u043f\u043e\u043b\u0430\u0433\u0430\u0435\u0442 \u0432\u0432\u0435\u0434\u0435\u043d\u0438\u0435 \u0442\u0440\u0430\u043d\u0441\u0433\u0435\u043d\u0430 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u043d\u0430, \u0434\u043e\u043b\u0433\u043e\u0432\u0435\u0447\u043d\u043e\u0441\u0442\u044c \u043a\u043e\u0442\u043e\u0440\u043e\u0433\u043e \u043d\u0435\u0438\u0437\u0432\u0435\u0441\u0442\u043d\u0430, \u0440\u0435\u0434\u0430\u043a\u0442\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u0435 \u0414\u041d\u041a \u043f\u0440\u0435\u0434\u0441\u0442\u0430\u0432\u043b\u044f\u0435\u0442 \u0441\u043e\u0431\u043e\u0439 \u043f\u043e\u0441\u0442\u043e\u044f\u043d\u043d\u043e\u0435 \u0438\u0437\u043c\u0435\u043d\u0435\u043d\u0438\u0435.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u041f\u043e\u0434\u0434\u0435\u0440\u0436\u043a\u0430 PPMD \u043f\u043e\u0437\u0432\u043e\u043b\u0438\u0442 MyoGene \u043f\u0440\u043e\u0432\u0435\u0441\u0442\u0438 \u043a\u043b\u044e\u0447\u0435\u0432\u044b\u0435 \u0438\u0441\u0441\u043b\u0435\u0434\u043e\u0432\u0430\u043d\u0438\u044f \u0434\u043b\u044f \u043f\u0440\u043e\u0434\u0432\u0438\u0436\u0435\u043d\u0438\u044f \u043a \u043a\u043b\u0438\u043d\u0438\u0447\u0435\u0441\u043a\u043e\u0439 \u0440\u0435\u0430\u043b\u0438\u0437\u0430\u0446\u0438\u0438. MyoGene \u0441\u043e\u0431\u0435\u0440\u0435\u0442 \u0434\u0430\u043d\u043d\u044b\u0435, \u0441\u0440\u0430\u0432\u043d\u0438\u0432\u0430\u044e\u0449\u0438\u0435 \u0444\u0443\u043d\u043a\u0446\u0438\u043e\u043d\u0430\u043b\u044c\u043d\u043e\u0441\u0442\u044c \u0438\u0441\u043f\u0440\u0430\u0432\u043b\u0435\u043d\u043d\u043e\u0433\u043e \u0431\u0435\u043b\u043a\u0430 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u043d\u0430 \u0441 \u0434\u0435\u043b\u0435\u0446\u0438\u0435\u0439 45-55 \u0441 \u0434\u0440\u0443\u0433\u0438\u043c\u0438 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u043d\u0430\u043c\u0438, \u0430 \u0442\u0430\u043a\u0436\u0435 \u043f\u0440\u043e\u0434\u043e\u043b\u0436\u0438\u0442 \u0440\u0430\u0431\u043e\u0442\u0443 \u043f\u043e \u0445\u0430\u0440\u0430\u043a\u0442\u0435\u0440\u0438\u0441\u0442\u0438\u043a\u0435 \u0431\u0435\u0437\u043e\u043f\u0430\u0441\u043d\u043e\u0441\u0442\u0438 \u044d\u0442\u043e\u0433\u043e \u043f\u043e\u0434\u0445\u043e\u0434\u0430.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u041f\u043e\u0434\u043f\u0438\u0441\u0430\u0442\u044c\u0441\u044f \u043d\u0430 \u044d\u0442\u0443 \u0441\u0442\u0440\u0430\u043d\u0438\u0446\u0443<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/ru\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0412\u0441\u0435 \u043a\u043b\u0438\u043d\u0438\u0447\u0435\u0441\u043a\u0438\u0435 \u0438\u0441\u043f\u044b\u0442\u0430\u043d\u0438\u044f \u043f\u043e \u043c\u044b\u0448\u0435\u0447\u043d\u043e\u0439 \u0434\u0438\u0441\u0442\u0440\u043e\u0444\u0438\u0438 \u0414\u044e\u0448\u0435\u043d\u043d\u0430<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>PPMD has provided $400,000 in funding to MyoGene through PPMD Venture Pathways, the organization&#8217;s venture-philanthropy initiative that provides industry funding to accelerate therapeutic development for Duchenne and Becker. What is MyoDys? MyoGene&#8217;s strategy, known as MyoDys 45-55, utilizes gene editing technology to edit an individual&#8217;s DMD gene. They target a large deletion of exons 45-55, [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":5113,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[451,450,452],"class_list":["post-5112","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-myodys","tag-myogene-bio","tag-ppmd"],"subtitle":"PPMD \u043f\u0440\u0435\u0434\u043e\u0441\u0442\u0430\u0432\u043b\u044f\u0435\u0442 $400 000 \u043d\u0430 \u0444\u0438\u043d\u0430\u043d\u0441\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u0435 MyoGene Bio \u0447\u0435\u0440\u0435\u0437 \u043f\u0440\u043e\u0433\u0440\u0430\u043c\u043c\u0443 PPMD Venture Pathways \u0434\u043b\u044f \u043f\u043e\u0434\u0434\u0435\u0440\u0436\u043a\u0438 \u0440\u0430\u0437\u0440\u0430\u0431\u043e\u0442\u043a\u0438 \u043f\u043b\u0430\u0442\u0444\u043e\u0440\u043c\u044b \u0440\u0435\u0434\u0430\u043a\u0442\u0438\u0440\u043e\u0432\u0430\u043d\u0438\u044f \u0433\u0435\u043d\u043e\u0432.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/posts\/5112","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/comments?post=5112"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/posts\/5112\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/media\/5113"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/media?parent=5112"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/categories?post=5112"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/ru\/wp-json\/wp\/v2\/tags?post=5112"}],"curies":[{"name":"WP","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}