{"id":4074,"date":"2025-07-11T11:35:06","date_gmt":"2025-07-11T08:35:06","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4074"},"modified":"2025-07-11T13:23:35","modified_gmt":"2025-07-11T10:23:35","slug":"belief-biomed-bbm-d101-gene-therapy-phase-1-2-clinical-trial-nct07058662","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/pt\/belief-biomed-bbm-d101-gene-therapy-phase-1-2-clinical-trial-nct07058662\/","title":{"rendered":"In\u00edcio do ensaio cl\u00ednico de fase 1\/2 da terapia gen\u00e9tica BBM-D101"},"content":{"rendered":"<p class=\"wp-block-paragraph\">A Belief BioMed (BBM), com sede na China, \u00e9 uma empresa global de biotecnologia inovadora que integra o desenvolvimento, a fabrica\u00e7\u00e3o e a aplica\u00e7\u00e3o cl\u00ednica de produtos de terapia g\u00eanica. Foi anunciado na p\u00e1gina publicada no ClinicalTrials.gov com o ID NCT07058662 que os ensaios de fase 1\/2 da terapia g\u00eanica BBM-D101, desenvolvida para a Distrofia Muscular de Duchenne, ser\u00e3o iniciados.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u00cdndice<\/h2><nav><ul><li><a href=\"#bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">Ensaio cl\u00ednico de fase 1\/2 da terapia gen\u00e9tica BBM-D101<\/a><\/li><li><a href=\"#bbm-d-101-clinical-trial-nct-07058662\">Ensaio Cl\u00ednico BBM-D101 \u2013 NCT07058662<\/a><\/li><li><a href=\"#bbm-d-101-phase-1-2-participation-criteria\">Crit\u00e9rios de participa\u00e7\u00e3o da fase 1\/2 do BBM-D101<\/a><\/li><li><a href=\"#how-can-i-contact-with-belief-bio-med\">Como posso entrar em contato com Belief BioMed?<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">Ensaio cl\u00ednico de fase 1\/2 da terapia gen\u00e9tica BBM-D101<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">O objetivo do estudo \u00e9 avaliar a seguran\u00e7a, tolerabilidade e efic\u00e1cia do BBM-D101 no tratamento de participantes com Distrofia Muscular de Duchenne.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">O BBM-D101 \u00e9 uma terapia de adi\u00e7\u00e3o gen\u00e9tica baseada em um cassete gen\u00e9tico de prote\u00edna terap\u00eautica de administra\u00e7\u00e3o de AAV no m\u00fasculo para o tratamento de DMD. A prote\u00edna terap\u00eautica pode mediar o complexo proteico associado \u00e0 distrofina para prevenir a distrofia muscular e resgatar a fun\u00e7\u00e3o muscular.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-clinical-trial-nct-07058662\">Ensaio Cl\u00ednico BBM-D101 \u2013 NCT07058662<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>In\u00edcio do estudo (estimado)<\/strong>: 2025-06-30<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Conclus\u00e3o prim\u00e1ria (estimada)<\/strong>: 2027-06-30<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Conclus\u00e3o do estudo (estimada)<\/strong>: 2031-06-30<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>N\u00famero de participantes (estimado)<\/strong>: 9 (Masculino)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Locais<\/strong>: China<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Idades eleg\u00edveis para estudo<\/strong>: 4 anos a 9 anos (crian\u00e7a)<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-phase-1-2-participation-criteria\">Crit\u00e9rios de participa\u00e7\u00e3o da fase 1\/2 do BBM-D101<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">As pessoas devem cumprir os requisitos de inclus\u00e3o para serem eleg\u00edveis. Se uma pessoa tiver outra doen\u00e7a ou estiver em tratamento que a impe\u00e7a de receber terapia gen\u00e9tica, ela poder\u00e1 n\u00e3o participar. O conjunto completo de crit\u00e9rios de inclus\u00e3o e exclus\u00e3o pode ser encontrado clicando no link deste estudo \u2013 <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT07058662\" target=\"_blank\" rel=\"noreferrer noopener\">NCT07058662<\/a> \u2013.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"how-can-i-contact-with-belief-bio-med\">Como posso entrar em contato com Belief BioMed?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Nome<\/strong>: Hanyang Hu<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>N\u00famero de telefone<\/strong>: +86-021-33588288<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>E-mail<\/strong>: huhanyang@beliefbiomed.com<\/p>","protected":false},"excerpt":{"rendered":"<p>Belief BioMed (BBM), headquartered in China, is a global innovative biotechnology company integrating the development, manufacturing and clinical application of gene therapy products. It was announced on the page published on ClinicalTrials.gov with the ID NCT07058662 that the phase 1\/2 trials of BBM-D101 gene therapy developed for Duchenne Muscular Dystrophy will be initiated. BBM-D101 Gene [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4082,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[199,197,123,137,61,389],"class_list":["post-4074","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-bbm-d101","tag-belief-biomed","tag-china","tag-clinical-trial","tag-gene-therapy","tag-nct07058662"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/4074","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/comments?post=4074"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/4074\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media\/4082"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media?parent=4074"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/categories?post=4074"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/tags?post=4074"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}