{"id":3846,"date":"2025-05-13T17:38:41","date_gmt":"2025-05-13T14:38:41","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3846"},"modified":"2025-05-13T17:47:11","modified_gmt":"2025-05-13T14:47:11","slug":"elevidys-gene-therapy-approved-in-japan","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/pt\/elevidys-gene-therapy-approved-in-japan\/","title":{"rendered":"Sarepta Therapeutics anuncia aprova\u00e7\u00e3o no Jap\u00e3o de ELEVIDYS, uma terapia gen\u00e9tica para tratar distrofia muscular de Duchenne"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Pessoas de 3 a menos de 8 anos que n\u00e3o apresentem dele\u00e7\u00f5es nos \u00e9xons 8 e\/ou 9 do gene DMD e que apresentem resultado negativo para anticorpos anti-AAVrh74 s\u00e3o eleg\u00edveis para usar ELEVIDYS. Esta \u00e9 a primeira aprova\u00e7\u00e3o mundial que abrange pessoas com menos de quatro anos.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Saber mais:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/pt\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Perguntas frequentes sobre Elevidys usado para distrofia muscular de Duchenne<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Terapia gen\u00e9tica ELEVIDYS aprovada no Jap\u00e3o<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">A Sarepta Therapeutics, l\u00edder em medicina gen\u00e9tica de precis\u00e3o para doen\u00e7as raras, anunciou hoje que o Minist\u00e9rio da Sa\u00fade, Trabalho e Bem-Estar do Jap\u00e3o (MHLW) aprovou o ELEVIDYS (delandistrogene moxeparvovec) para o tratamento da distrofia muscular de Duchenne (DMD) sob o caminho de aprova\u00e7\u00e3o condicional e por tempo limitado no Jap\u00e3o.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Leia mais:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/pt\/will-elevidys-receive-approval-from-the-european-medicines-agency-ema\/\">O Elevidys receber\u00e1 aprova\u00e7\u00e3o da Ag\u00eancia Europeia de Medicamentos (EMA)?<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>People aged 3 to under 8 who do not have deletions in exons 8 and\/or 9 of the DMD gene and who test negative for anti-AAVrh74 antibodies are eligible to use ELEVIDYS. This is the first worldwide approval that covers people under the age of four. Learn More: Frequently Asked Questions About Elevidys Used for [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3847,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[33,61,142],"class_list":["post-3846","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-elevidys","tag-gene-therapy","tag-japan"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/3846","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/comments?post=3846"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/3846\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media\/3847"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media?parent=3846"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/categories?post=3846"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/tags?post=3846"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}