{"id":3823,"date":"2025-05-07T15:43:13","date_gmt":"2025-05-07T12:43:13","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3823"},"modified":"2025-05-07T15:43:14","modified_gmt":"2025-05-07T12:43:14","slug":"sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/pt\/sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells\/","title":{"rendered":"O m\u00e9todo de administra\u00e7\u00e3o mediado por ultrassom SonoThera pode fornecer distrofina de comprimento total \u00e0s c\u00e9lulas"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Os resultados do estudo, que est\u00e3o sendo desenvolvidos atualmente para o tratamento da distrofia muscular de Duchenne (DMD) do SonoThera, demonstram a capacidade da tecnologia de administra\u00e7\u00e3o mediada por ultrassom de administrar medicamentos gen\u00e9ticos. <strong>Essa tecnologia permite a express\u00e3o total da prote\u00edna distrofina nos m\u00fasculos esquel\u00e9ticos, card\u00edacos e diafragma em modelos de camundongos e primatas n\u00e3o humanos (NHP).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">A SonoThera, uma empresa de biotecnologia dedicada a tratar a causa raiz de doen\u00e7as humanas por meio do desenvolvimento da pr\u00f3xima gera\u00e7\u00e3o de medicamentos gen\u00e9ticos, anunciou hoje que apresentar\u00e1 novos dados na 28\u00aa reuni\u00e3o anual da Sociedade Americana de Terapia Gen\u00e9tica e Celular (ASGCT), que ser\u00e1 realizada de 13 a 17 de maio em Nova Orleans, Louisiana.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201cTemos o prazer de apresentar novos dados na ASGCT destacando o potencial da administra\u00e7\u00e3o mediada por ultrassom na solu\u00e7\u00e3o dos principais desafios da medicina gen\u00e9tica\u201d, disse Kenneth Greenberg, PhD, CEO da SonoThera. <strong>\u201cEsses dados continuam a demonstrar nossas capacidades \u00fanicas, incluindo a express\u00e3o direcionada de distrofina humana de comprimento total no m\u00fasculo e o fornecimento de cargas gen\u00e9ticas superdimensionadas de maneira dur\u00e1vel, segura, redox e n\u00e3o invasiva.<\/strong> Estamos ansiosos para compartilhar nossos dados mais recentes na reuni\u00e3o anual deste ano.\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Saber mais: <a href=\"https:\/\/dmdwarrior.com\/pt\/sonothera-presents-new-data-of-genetic-medicine-using-targeted-ultrasound-mediated-delivery-umd-in-treating-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Transmiss\u00e3o Mediada por Ultrassom (UMD)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The findings of the study, which are currently being developed for SonoThera&#8217;s Duchenne Muscular Dystrophy (DMD) treatment, demonstrate the capability of Ultrasound-Mediated Delivery technology to deliver genetic drugs. This technology enables full-length dystrophin protein expression in skeletal, cardiac, and diaphragm muscles in mouse and non-human primate (NHP) models. SonoThera, a biotechnology company dedicated to treating [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3824,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[366,359,367,285,286],"class_list":["post-3823","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-asgct-2025","tag-full-length-dystrophin","tag-kenneth-greenberg","tag-sonothera","tag-ultrasound-mediated-delivery"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/3823","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/comments?post=3823"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/3823\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media\/3824"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media?parent=3823"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/categories?post=3823"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/tags?post=3823"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}