{"id":2570,"date":"2025-01-24T11:20:01","date_gmt":"2025-01-24T08:20:01","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2570"},"modified":"2025-03-07T13:21:44","modified_gmt":"2025-03-07T10:21:44","slug":"will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/pt\/will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies\/","title":{"rendered":"A parceria entre a Genethon e a Eukar\u00ffs reduzir\u00e1 o custo das terapias gen\u00e9ticas?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">A \u00fanica terapia gen\u00e9tica aprovada pelo FDA para distrofia muscular de Duchenne est\u00e1 custando muito caro para as fam\u00edlias. As fam\u00edlias simplesmente n\u00e3o podem pagar esse pre\u00e7o proibitivo. Os fabricantes devem reconsiderar o pre\u00e7o das terapias gen\u00e9ticas para DMD. De acordo com um an\u00fancio da Genethon em 23 de janeiro, a colabora\u00e7\u00e3o com a Eukar\u00ffs pode reduzir o pre\u00e7o das terapias gen\u00e9ticas para DMD a um n\u00edvel razo\u00e1vel.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Hoje, a Eukar\u00ffs, uma empresa de biotecnologia que cria uma tecnologia revolucion\u00e1ria que aumenta drasticamente os rendimentos da biofabrica\u00e7\u00e3o, e a Genethon, uma pioneira e l\u00edder na pesquisa e desenvolvimento de tratamentos gen\u00e9ticos para doen\u00e7as raras, anunciaram a forma\u00e7\u00e3o de um acordo estrat\u00e9gico. A colabora\u00e7\u00e3o usa a tecnologia C3P3 exclusiva da Eukar\u00ffs, um novo m\u00e9todo de express\u00e3o de RNA mensageiro (mRNA) em c\u00e9lulas de mam\u00edferos, para reduzir o custo de produ\u00e7\u00e3o de medicamentos de terapia gen\u00e9tica.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Saber mais:<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/pt\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Poss\u00edveis novas terapias gen\u00e9ticas futuras para a distrofia muscular de Duchenne<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Leia mais:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/pt\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\">Perguntas frequentes sobre Elevidys<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA-approved only gene therapy for Duchenne muscular dystrophy is costing far too much for families to afford. Families simply cannot afford this prohibitive price. Manufacturers should reconsider the price of DMD gene therapies. According to an announcement by Genethon on January 23, the collaboration with Eukar\u00ffs could bring the price of DMD gene therapies [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2572,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[201,66,200,72,61,105,202],"class_list":["post-2570","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-c3p3-technology","tag-duchenne-muscular-dystrophy","tag-eukarys","tag-gene-editing","tag-gene-therapy","tag-genethon","tag-mrna"],"subtitle":"O pre\u00e7o de 2,9 milh\u00f5es de d\u00f3lares da terapia gen\u00e9tica ELEVIDYS, desenvolvida para Distrofia Muscular de Duchenne e aprovada pelo FDA, preocupa as fam\u00edlias. De acordo com o an\u00fancio feito pela Genethon, sua parceria com a Eukar\u00ffs reduzir\u00e1 o custo das terapias gen\u00e9ticas.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/2570","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/comments?post=2570"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/2570\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media\/2572"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media?parent=2570"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/categories?post=2570"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/tags?post=2570"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}