{"id":2564,"date":"2025-01-23T22:26:59","date_gmt":"2025-01-23T19:26:59","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2564"},"modified":"2025-03-07T14:53:34","modified_gmt":"2025-03-07T11:53:34","slug":"belief-biomed-announces-ind-clearance-by-fda-for-duchenne-muscular-dystrophy-gene-therapy-candidate-bbm-d101","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/pt\/belief-biomed-announces-ind-clearance-by-fda-for-duchenne-muscular-dystrophy-gene-therapy-candidate-bbm-d101\/","title":{"rendered":"Belief BioMed anuncia autoriza\u00e7\u00e3o de IND por FDA para o candidato \u00e0 terapia gen\u00e9tica para distrofia muscular de Duchenne BBM-D101"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Belief BioMed relata libera\u00e7\u00e3o do FDA IND para o candidato \u00e0 terapia gen\u00e9tica BBM-D101 para distrofia muscular de Duchenne.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">A Food and Drug Administration (FDA) dos EUA aprovou um pedido de Novo Medicamento Investigacional (IND) para o candidato \u00e0 terapia gen\u00e9tica para Distrofia Muscular de Duchenne (DMD) da Belief BioMed (BBM), BBM-D101. A BBM \u00e9 uma empresa de biotecnologia com vis\u00e3o de futuro que se concentra na cria\u00e7\u00e3o de terapias gen\u00e9ticas inovadoras.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">O objetivo desta pesquisa cl\u00ednica aberta de dose \u00fanica foi avaliar a seguran\u00e7a e a efic\u00e1cia de uma \u00fanica infus\u00e3o intravenosa em pacientes com DMD entre 4 e 9 anos. Devido ao seu caps\u00eddeo modificado, o BBM-D101 \u00e9 mais eficaz na transdu\u00e7\u00e3o de tecido muscular. Como resultado, prev\u00ea-se que o BBM-D101 tenha boa seguran\u00e7a e a dosagem cl\u00ednica sugerida \u00e9 menor do que os produtos de terapia gen\u00e9tica de v\u00edrus adenoassociado (AAV) compar\u00e1veis autorizados.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Saber mais:<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/pt\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Poss\u00edveis novas terapias gen\u00e9ticas futuras para a distrofia muscular de Duchenne<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>Belief BioMed Reports FDA IND Clearance for Gene Therapy Candidate BBM-D101 for Duchenne Muscular Dystrophy. The U.S. Food and Drug Administration (FDA) has approved an Investigational New Drug (IND) application for Belief BioMed&#8217;s (BBM) Duchenne Muscular Dystrophy (DMD) gene therapy candidate, BBM-D101. BBM is a forward-thinking biotechnology company that focuses on creating innovative gene therapies. [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2565,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[199,197,123,66,61,198],"class_list":["post-2564","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-bbm-d101","tag-belief-biomed","tag-china","tag-duchenne-muscular-dystrophy","tag-gene-therapy","tag-shanghai"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/2564","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/comments?post=2564"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/2564\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media\/2565"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media?parent=2564"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/categories?post=2564"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/tags?post=2564"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}