{"id":2190,"date":"2025-01-02T01:50:35","date_gmt":"2025-01-01T22:50:35","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2190"},"modified":"2025-01-02T02:00:28","modified_gmt":"2025-01-01T23:00:28","slug":"is-duchenne-gene-therapy-a-suitable-treatment-despite-its-immunogenic-class-effect","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/pt\/is-duchenne-gene-therapy-a-suitable-treatment-despite-its-immunogenic-class-effect\/","title":{"rendered":"A terapia gen\u00e9tica de Duchenne \u00e9 um tratamento adequado apesar de seu efeito de classe imunog\u00eanica?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Fraqueza muscular progressiva e mortalidade eventual como resultado de cardiomiopatia ou complica\u00e7\u00f5es respirat\u00f3rias s\u00e3o as marcas registradas da distrofia muscular de Duchenne (DMD), um dist\u00farbio grave ligado ao X. Atualmente, n\u00e3o h\u00e1 cura para a DMD, e o foco principal dos tratamentos padr\u00e3o \u00e9 o gerenciamento dos sintomas. As terapias gen\u00e9ticas podem abordar de forma mais eficaz a causa gen\u00e9tica da doen\u00e7a empregando medidas imunossupressoras e designs de vetores otimizados.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Quais s\u00e3o os efeitos dos tratamentos de terapia gen\u00e9tica na doen\u00e7a da distrofia muscular de Duchenne (DMD), as terapias gen\u00e9ticas funcionam? Aqui est\u00e1 uma an\u00e1lise abrangente.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/www.tandfonline.com\/eprint\/BFZQKYN3YY3AHAVX9S27\/full?target=10.1080\/14740338.2024.2447072\" target=\"_blank\" rel=\"noreferrer noopener\">Ler mais<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/x.com\/ToshifumiYokota\" target=\"_blank\" rel=\"noreferrer noopener\">Siga o Prof. Toshi Yokota<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Progressive muscle weakness and eventual mortality as a result of cardiomyopathy or respiratory complications are the hallmarks of Duchenne muscular dystrophy (DMD), a severe X-linked disorder. At present, there is no cure for DMD, and the primary focus of standard treatments is on symptom management. Gene therapies can more effectively address the genetic cause of [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2192,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[66,33,72,61],"class_list":["post-2190","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-duchenne-muscular-dystrophy","tag-elevidys","tag-gene-editing","tag-gene-therapy"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/2190","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/comments?post=2190"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/posts\/2190\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media\/2192"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/media?parent=2190"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/categories?post=2190"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/pt\/wp-json\/wp\/v2\/tags?post=2190"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}