{"id":8567,"date":"2026-08-24T13:49:06","date_gmt":"2026-08-24T10:49:06","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8567"},"modified":"2026-08-24T16:14:23","modified_gmt":"2026-08-24T13:14:23","slug":"pbgene-dmd-first-patient-dosed-gene-editing-study","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/pbgene-dmd-first-patient-dosed-gene-editing-study\/","title":{"rendered":"PBGENE-DMD \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u092a\u094d\u0930\u0935\u0947\u0936: \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u091c\u0940\u0928-\u0938\u0902\u092a\u093e\u0926\u0928 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u092a\u0939\u0932\u0947 \u0930\u094b\u0917\u0940 \u0915\u094b \u0916\u0941\u0930\u093e\u0915 \u0926\u0940 \u0917\u0908"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Precision BioSciences \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u091c\u0940\u0928 \u090f\u0921\u093f\u091f\u093f\u0902\u0917 \u092e\u0947\u0902 \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0909\u092a\u0932\u092c\u094d\u0927\u093f \u0939\u093e\u0938\u093f\u0932 \u0915\u0940 \u0939\u0948\u0964. <strong>\u0915\u0902\u092a\u0928\u0940 \u0928\u0947 24 \u0905\u0917\u0938\u094d\u0924, 2026 \u0915\u094b \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0907\u0928 \u0935\u093f\u0935\u094b \u091c\u0940\u0928-\u090f\u0921\u093f\u091f\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940, PBGENE-DMD \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u091a\u0930\u0923 1\/2 FUNCTION-DMD \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u092a\u0939\u0932\u0947 \u0930\u094b\u0917\u0940 \u0915\u094b \u0916\u0941\u0930\u093e\u0915 \u0926\u0940 \u0917\u0908 \u0939\u0948\u0964.<\/strong> \u092a\u0939\u0932\u0940 \u0916\u0941\u0930\u093e\u0915 \u0905\u0930\u094d\u0915\u093e\u0902\u0938\u0938 \u091a\u093f\u0932\u094d\u0921\u094d\u0930\u0928\u094d\u0938 \u0939\u0949\u0938\u094d\u092a\u093f\u091f\u0932 \u092e\u0947\u0902 \u0926\u0940 \u0917\u0908, \u091c\u094b \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u0935\u093f\u0936\u0947\u0937 \u0926\u0947\u0916\u092d\u093e\u0932 \u0915\u0947\u0902\u0926\u094d\u0930 \u0939\u0948\u0964.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#what-is-pbgene-dmd\">PBGENE-DMD \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#why-exons-45-55-matter-in-duchenne\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u092e\u0947\u0902 \u090f\u0915\u094d\u0938\u0949\u0928 45-55 \u0915\u093e \u092e\u0939\u0924\u094d\u0935 \u0915\u094d\u092f\u094b\u0902 \u0939\u0948?<\/a><\/li><li><a href=\"#function-dmd-phase-1-2-trial-begins\">FUNCTION-DMD \u0915\u0947 \u091a\u0930\u0923 1\/2 \u0915\u093e \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0939\u0941\u0906<\/a><\/li><li><a href=\"#how-pbgene-dmd-differs-from-microdystrophin\">PBGENE-DMD \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0938\u0947 \u0915\u093f\u0938 \u092a\u094d\u0930\u0915\u093e\u0930 \u092d\u093f\u0928\u094d\u0928 \u0939\u0948?<\/a><\/li><li><a href=\"#what-should-dmd-families-watch-next\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0906\u0917\u0947 \u0915\u094d\u092f\u093e \u0926\u0947\u0916\u0928\u093e \u091a\u093e\u0939\u093f\u090f?<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 id=\"what-is-pbgene-dmd\" class=\"wp-block-heading\">PBGENE-DMD \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">PBGENE-DMD \u0915\u094b \u0915\u0947\u0935\u0932 \u090f\u0915 \u091b\u094b\u091f\u093e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0926\u0947\u0928\u0947 \u0915\u0947 \u092c\u091c\u093e\u092f \u0905\u0902\u0924\u0930\u094d\u0928\u093f\u0939\u093f\u0924 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0926\u094b\u0937 \u0915\u094b \u0926\u0942\u0930 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948\u0964 \u0907\u0938 \u0909\u092a\u091a\u093e\u0930 \u092e\u0947\u0902 \u0926\u094b \u092a\u0942\u0930\u0915 ARCUS \u0928\u094d\u092f\u0942\u0915\u094d\u0932\u093f\u090f\u091c\u093c \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u091c\u093f\u0928\u094d\u0939\u0947\u0902 \u090f\u0915 \u0939\u0940 AAV \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 DMD \u091c\u0940\u0928 \u0938\u0947 \u090f\u0915\u094d\u0938\u0949\u0928 45-55 \u0915\u094b \u0939\u091f\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092a\u0939\u0941\u0902\u091a\u093e\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964 \u0907\u0938\u0915\u093e \u0932\u0915\u094d\u0937\u094d\u092f \u0930\u0940\u0921\u093f\u0902\u0917 \u092b\u094d\u0930\u0947\u092e \u0915\u094b \u092c\u0939\u093e\u0932 \u0915\u0930\u0928\u093e \u0914\u0930 \u0932\u0917\u092d\u0917 \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0938\u0902\u092d\u0935 \u092c\u0928\u093e\u0928\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0930\u0923\u0928\u0940\u0924\u093f \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0926\u0943\u0937\u094d\u091f\u093f \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u091c\u0940\u0928 \u0938\u0902\u092a\u093e\u0926\u0928 \u0915\u094b \u092a\u0939\u0932\u0947 \u092d\u0940 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u0947 \u0935\u093f\u0918\u091f\u0928\u0915\u093e\u0930\u0940 \u0915\u094d\u0937\u0947\u0924\u094d\u0930\u094b\u0902 \u0915\u094b \u0939\u091f\u093e\u0928\u0947 \u0914\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0915\u094b \u092c\u0939\u093e\u0932 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0924\u0930\u0940\u0915\u0947 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u091c\u093e\u0902\u091a\u093e \u0917\u092f\u093e \u0939\u0948\u0964 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u0928\u0947 \u0921\u0940\u090f\u092e\u0921\u0940 \u092e\u0949\u0921\u0932 \u092e\u0947\u0902 \u090f\u0915\u094d\u0938\u0949\u0928 45-55 \u0915\u0947 \u0935\u093f\u0932\u094b\u092a\u0928 \u0914\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0915\u0940 \u092c\u0939\u093e\u0932\u0940 \u0915\u094b \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u093f\u092f\u093e \u0939\u0948\u0964 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/precision-biosciences-pbgene-dmd-restores-production-of-nearly-full-length-dystrophin-protein\/\" target=\"_blank\" data-type=\"post\" data-id=\"3860\" rel=\"noreferrer noopener\">1\u091f\u0940\u092a\u094029\u091f\u0940<\/a><\/p>\n\n\n\n<h2 id=\"why-exons-45-55-matter-in-duchenne\" class=\"wp-block-heading\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u092e\u0947\u0902 \u090f\u0915\u094d\u0938\u0949\u0928 45-55 \u0915\u093e \u092e\u0939\u0924\u094d\u0935 \u0915\u094d\u092f\u094b\u0902 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0915\u094d\u0938\u0949\u0928 45-55 \u0915\u094d\u0937\u0947\u0924\u094d\u0930 \u0921\u0940\u090f\u092e\u0921\u0940 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u093e \u090f\u0915 \u092a\u094d\u0930\u092e\u0941\u0916 \u0939\u0949\u091f\u0938\u094d\u092a\u0949\u091f \u0939\u0948\u0964. <strong>Precision BioSciences \u0915\u093e \u0905\u0928\u0941\u092e\u093e\u0928 \u0939\u0948 \u0915\u093f \u0907\u0938 \u0915\u094d\u0937\u0947\u0924\u094d\u0930 \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u0947 \u0915\u093e\u0930\u0923 DMD \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u0917\u092d\u0917 60 \u092a\u094d\u0930\u0924\u093f\u0936\u0924 \u0932\u0921\u093c\u0915\u094b\u0902 \u0915\u094b PBGENE-DMD \u0926\u094d\u0935\u093e\u0930\u093e \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u0920\u0940\u0915 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u092f\u094b\u0917\u094d\u092f\u0924\u093e \u0915\u094b \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u0947 \u0938\u093e\u0925 \u092d\u094d\u0930\u092e\u093f\u0924 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u091c\u093e\u0928\u093e \u091a\u093e\u0939\u093f\u090f\u0964 \u0915\u093f\u0938\u0940 \u0930\u094b\u0917\u0940 \u092e\u0947\u0902 \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u094d\u0937\u0947\u0924\u094d\u0930 \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948 \u0914\u0930 \u092b\u093f\u0930 \u092d\u0940 \u092f\u0939 \u0928\u093f\u0930\u094d\u0927\u093e\u0930\u093f\u0924 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948 \u0915\u093f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092f\u093e \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0909\u092a\u092f\u0941\u0915\u094d\u0924 \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902\u0964.<\/p>\n\n\n\n<h2 id=\"function-dmd-phase-1-2-trial-begins\" class=\"wp-block-heading\">FUNCTION-DMD \u0915\u0947 \u091a\u0930\u0923 1\/2 \u0915\u093e \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0939\u0941\u0906<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>FUNCTION-DMD \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0935\u0930\u094d\u0924\u092e\u093e\u0928 \u092e\u0947\u0902 2-7 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0906\u092f\u0941 \u0915\u0947 \u0910\u0938\u0947 DMD \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0936\u093e\u092e\u093f\u0932 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948 \u091c\u094b \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u0948\u0902 \u0914\u0930 \u091c\u093f\u0928\u0915\u0947 \u090f\u0915\u094d\u0938\u0949\u0928 45 \u0914\u0930 55 \u0915\u0947 \u092c\u0940\u091a \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u092a\u093e\u090f \u0917\u090f \u0939\u0948\u0902\u0964.<\/strong> \u0905\u092e\u0947\u0930\u093f\u0915\u093e \u092e\u0947\u0902 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0932\u093f\u090f \u0915\u0908 \u0935\u093f\u0936\u0947\u0937\u0940\u0915\u0943\u0924 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0915\u0947\u0902\u0926\u094d\u0930 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902, \u0914\u0930 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0921\u0947\u091f\u093e 2026 \u0915\u0947 \u0905\u0902\u0924 \u0924\u0915 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b\u0928\u0947 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948\u0964 \u0905\u092d\u0940 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/duchenne-exon-deletion-tool\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u091a\u0947\u0928 \u090f\u0915\u094d\u0938\u0949\u0928 \u0935\u093f\u0932\u094b\u092a\u0928 \u0909\u092a\u0915\u0930\u0923<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u094b \u0924\u0924\u094d\u0915\u093e\u0932 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915\u0924\u093e \u0926\u0940 \u091c\u093e\u0928\u0940 \u091a\u093e\u0939\u093f\u090f\u0964 \u091a\u0942\u0902\u0915\u093f PBGENE-DMD \u0921\u0940\u090f\u0928\u090f \u0915\u094b \u0938\u094d\u0925\u093e\u092f\u0940 \u0930\u0942\u092a \u0938\u0947 \u0938\u0902\u0936\u094b\u0927\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948, \u0907\u0938\u0932\u093f\u090f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0915\u094b \u0928 \u0915\u0947\u0935\u0932 \u092f\u0939 \u0938\u094d\u0925\u093e\u092a\u093f\u0924 \u0915\u0930\u0928\u093e \u0939\u094b\u0917\u093e \u0915\u093f \u0938\u0902\u092a\u093e\u0926\u0928 \u0939\u094b\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902, \u092c\u0932\u094d\u0915\u093f \u092f\u0939 \u092d\u0940 \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u090f\u0915 \u0938\u094d\u0935\u0940\u0915\u093e\u0930\u094d\u092f \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932 \u0914\u0930 \u0938\u093e\u0930\u094d\u0925\u0915 \u091c\u0948\u0935\u093f\u0915 \u0914\u0930 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u094d\u0930\u092d\u093e\u0935 \u0909\u0924\u094d\u092a\u0928\u094d\u0928 \u0915\u0930\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0905\u0902\u0924\u0930 \u0905\u0924\u094d\u092f\u0902\u0924 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0964 \u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0938\u092b\u0932\u0924\u093e \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0915\u094b \u0938\u094d\u0925\u093e\u092a\u093f\u0924 \u0928\u0939\u0940\u0902 \u0915\u0930\u0924\u0940\u0964 \u0921\u0940\u090f\u092e\u0921\u0940 \u0926\u0935\u093e \u0935\u093f\u0915\u093e\u0938 \u0915\u0947 \u0932\u093f\u090f 1\u091f\u0940\u092a\u0940169\u091f\u0940 \u0926\u093f\u0936\u093e\u0928\u093f\u0930\u094d\u0926\u0947\u0936 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0938\u093e\u0930\u094d\u0925\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u0947 \u092e\u0939\u0924\u094d\u0935 \u092a\u0930 \u091c\u094b\u0930 \u0926\u0947\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u091c\u0939\u093e\u0902 \u0938\u0902\u092d\u0935 \u0939\u094b, \u0915\u0902\u0915\u093e\u0932, \u0936\u094d\u0935\u0938\u0928 \u0914\u0930 \u0939\u0943\u0926\u092f \u0938\u0902\u092c\u0902\u0927\u0940 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u0906\u0915\u0932\u0928 \u0915\u094b \u092a\u094d\u0930\u094b\u0924\u094d\u0938\u093e\u0939\u093f\u0924 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/clinical-trials\/pbgene-dmd-phase-1-2a-clinical-trial-for-duchenne-function-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">PBGENE-DMD \u091a\u0930\u0923 1\/2a \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u200b\u200b\u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>\n\n\n\n<h2 id=\"how-pbgene-dmd-differs-from-microdystrophin\" class=\"wp-block-heading\">PBGENE-DMD \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0938\u0947 \u0915\u093f\u0938 \u092a\u094d\u0930\u0915\u093e\u0930 \u092d\u093f\u0928\u094d\u0928 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u092e\u0941\u0916 \u0905\u0902\u0924\u0930\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0947 \u0932\u0915\u094d\u0937\u093f\u0924 \u0938\u094d\u0930\u094b\u0924 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0939\u0948\u0964 PBGENE-DMD \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0930\u094b\u0917\u0940 \u0915\u0947 \u0938\u094d\u0935\u092f\u0902 \u0915\u0947 DMD \u091c\u0940\u0928 \u0915\u094b \u0938\u0902\u092a\u093e\u0926\u093f\u0924 \u0915\u0930\u0928\u093e \u0939\u0948, \u091c\u093f\u0938\u0938\u0947 \u0938\u0902\u092d\u0935\u0924\u0903 \u0932\u0917\u092d\u0917 \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0915\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u0905\u0902\u0924\u0930\u094d\u091c\u093e\u0924 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0938\u0902\u092d\u0935 \u0939\u094b \u0938\u0915\u0947\u0964 \u092f\u0939 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0935\u093f\u0927\u093f\u092f\u094b\u0902 \u0938\u0947 \u092d\u093f\u0928\u094d\u0928 \u0939\u0948, \u091c\u093f\u0928\u092e\u0947\u0902 \u090f\u0915 \u091b\u094b\u091f\u093e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0938\u0902\u0918\u091f\u0915 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Precision BioSciences \u0928\u0947 \u0909\u0924\u094d\u0938\u093e\u0939\u091c\u0928\u0915 \u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u093f\u090f \u0939\u0948\u0902, \u091c\u093f\u0928\u092e\u0947\u0902 \u092a\u0936\u0941 \u092e\u0949\u0921\u0932\u094b\u0902 \u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u092c\u0939\u093e\u0932\u0940 \u0914\u0930 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0938\u0941\u0927\u093e\u0930 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902\u0964 \u092f\u0947 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u0905\u092d\u0940 \u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0939\u0948\u0902 \u0914\u0930 \u0907\u0938\u0932\u093f\u090f \u092f\u0939 \u0938\u094d\u0925\u093e\u092a\u093f\u0924 \u0928\u0939\u0940\u0902 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0915\u093f \u092e\u0928\u0941\u0937\u094d\u092f\u094b\u0902 \u092e\u0947\u0902 \u092d\u0940 \u0907\u0938\u0940 \u092a\u094d\u0930\u0915\u093e\u0930 \u0915\u0947 \u0932\u093e\u092d \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b\u0902\u0917\u0947 \u092f\u093e \u0928\u0939\u0940\u0902\u0964.<\/p>\n\n\n\n<h2 id=\"what-should-dmd-families-watch-next\" class=\"wp-block-heading\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0906\u0917\u0947 \u0915\u094d\u092f\u093e \u0926\u0947\u0916\u0928\u093e \u091a\u093e\u0939\u093f\u090f?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0909\u092a\u0932\u092c\u094d\u0927\u093f\u092f\u093e\u0901 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0921\u0947\u091f\u093e, \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u092c\u0939\u093e\u0932\u0940, \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0914\u0930 \u0938\u094d\u0925\u093e\u092f\u093f\u0924\u094d\u0935 \u0939\u094b\u0902\u0917\u0940\u0964 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0915\u0902\u092a\u0928\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0915\u093f\u090f \u0917\u090f \u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0914\u0930 \u0938\u0939\u0915\u0930\u094d\u092e\u0940-\u0938\u092e\u0940\u0915\u094d\u0937\u093f\u0924 \u092e\u093e\u0928\u0935 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0938\u093e\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0915\u0947 \u092c\u0940\u091a \u0938\u093e\u0935\u0927\u093e\u0928\u0940\u092a\u0942\u0930\u094d\u0935\u0915 \u0905\u0902\u0924\u0930 \u0915\u0930\u0928\u093e \u091a\u093e\u0939\u093f\u090f\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u0940\u090f\u092e\u0921\u0940 \u090f\u0915 \u092c\u0939\u0941-\u092a\u094d\u0930\u0923\u093e\u0932\u0940\u0917\u0924 \u0930\u094b\u0917 \u0939\u0948 \u091c\u093f\u0938\u092e\u0947\u0902 \u0915\u0902\u0915\u093e\u0932, \u0939\u0943\u0926\u092f \u0914\u0930 \u0936\u094d\u0935\u0938\u0928 \u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u093e\u0902 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0924\u0940 \u0939\u0948\u0902, \u0907\u0938\u0932\u093f\u090f \u0935\u094d\u092f\u093e\u092a\u0915 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0932\u093f\u090f, \u092a\u0939\u0932\u0947 \u092e\u0930\u0940\u091c\u093c \u0915\u094b \u0926\u0940 \u0917\u0908 \u0916\u0941\u0930\u093e\u0915 \u090f\u0915 \u0936\u0941\u0930\u0941\u0906\u0924 \u0939\u0948, \u0905\u0902\u0924 \u0928\u0939\u0940\u0902\u0964 PBGENE-DMD \u0905\u092c \u092a\u094d\u0930\u092f\u094b\u0917\u0936\u093e\u0932\u093e \u0935\u093f\u0915\u093e\u0938 \u0938\u0947 \u0928\u093f\u0915\u0932\u0915\u0930 \u092e\u093e\u0928\u0935 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u091a\u0930\u0923 \u092e\u0947\u0902 \u092a\u0939\u0941\u0901\u091a \u0917\u092f\u093e \u0939\u0948\u0964 \u0905\u0917\u0932\u093e \u0938\u0935\u093e\u0932 \u092f\u0939 \u0939\u0948 \u0915\u093f \u0915\u094d\u092f\u093e \u091c\u0940\u0928-\u0938\u0902\u092a\u093e\u0926\u0928 \u0915\u0940 \u092f\u0939 \u0930\u0923\u0928\u0940\u0924\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0938\u094d\u0925\u093e\u092f\u0940 \u0914\u0930 \u0938\u093e\u0930\u094d\u0925\u0915 \u0932\u093e\u092d\u094b\u0902 \u092e\u0947\u0902 \u0905\u092a\u0928\u0947 \u091c\u0948\u0935\u093f\u0915 \u0935\u093e\u0926\u0947 \u0915\u094b \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u093f\u0924 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0922\u0942\u0902\u0922\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/clinical-trials\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u091c\u093e\u0928\u0947\u0902 <\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>Precision BioSciences has reached an important milestone in Duchenne muscular dystrophy (DMD) gene editing. The company announced on August 24, 2026, that the first patient has been dosed in the Phase 1\/2 FUNCTION-DMD clinical trial evaluating PBGENE-DMD, an investigational in vivo gene-editing therapy for Duchenne. The first dose was administered at Arkansas Children\u2019s Hospital, a [&hellip;]<\/p>\n","protected":false},"author":5,"featured_media":8568,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[726,242,359,72,725,314,724,313],"class_list":["post-8567","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-arcus-gene-editing","tag-clinical-trials","tag-full-length-dystrophin","tag-gene-editing","tag-gene-editing-therapy","tag-pbgene-dmd","tag-pbgene-dmd-therapy","tag-precision-biosciences"],"subtitle":"\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u092e\u0947\u0902 PBGENE-DMD \u0928\u0947 \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0909\u092a\u0932\u092c\u094d\u0927\u093f \u0939\u093e\u0938\u093f\u0932 \u0915\u0940 \u0939\u0948\u0964 FUNCTION-DMD \u0915\u0947 \u092a\u0939\u0932\u0947\/\u0926\u0942\u0938\u0930\u0947 \u091a\u0930\u0923 \u0915\u0947 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u092a\u0939\u0932\u0947 \u092e\u0930\u0940\u091c \u0915\u094b \u0926\u0935\u093e \u0926\u0940 \u091c\u093e \u091a\u0941\u0915\u0940 \u0939\u0948\u0964 \u0915\u094d\u092f\u093e \u091c\u0940\u0928 \u090f\u0921\u093f\u091f\u093f\u0902\u0917 \u0938\u0947 DMD \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u092e\u0947\u0902 \u090f\u0915 \u0928\u092f\u093e \u092f\u0941\u0917 \u0936\u0941\u0930\u0942 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948?","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8567","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/5"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=8567"}],"version-history":[{"count":5,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8567\/revisions"}],"predecessor-version":[{"id":8574,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8567\/revisions\/8574"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/8568"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=8567"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=8567"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=8567"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}