{"id":8153,"date":"2026-06-24T15:04:11","date_gmt":"2026-06-24T12:04:11","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8153"},"modified":"2026-06-24T15:51:29","modified_gmt":"2026-06-24T12:51:29","slug":"regenxbio-completes-rgx-202-confirmatory-study-for-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/regenxbio-completes-rgx-202-confirmatory-study-for-duchenne-muscular-dystrophy\/","title":{"rendered":"REGENXBIO \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f RGX-202 \u0915\u0940 \u092a\u0941\u0937\u094d\u091f\u093f \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u093e \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0942\u0930\u093e \u0915\u093f\u092f\u093e"},"content":{"rendered":"<p class=\"wp-block-paragraph\">REGENXBIO \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (DMD) \u0915\u0947 \u0932\u093f\u090f \u0905\u092a\u0928\u0940 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 RGX-202 \u0915\u0947 \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0926\u0935\u093e \u0915\u0940 \u0916\u0941\u0930\u093e\u0915 \u0926\u0947\u0928\u0947 \u0915\u093e \u0915\u093e\u0930\u094d\u092f \u092a\u0942\u0930\u093e \u0939\u094b\u0928\u0947 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0939\u0948\u0964 \u092f\u0939 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0909\u092a\u0932\u092c\u094d\u0927\u093f \u0915\u0902\u092a\u0928\u0940 \u0915\u0947 \u092a\u0902\u091c\u0940\u0915\u0930\u0923 \u0935\u093f\u0915\u093e\u0938 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0915\u0947 \u092a\u0942\u0930\u093e \u0939\u094b\u0928\u0947 \u0915\u093e \u092a\u094d\u0930\u0924\u0940\u0915 \u0939\u0948 \u0914\u0930 2026 \u0915\u0940 \u0924\u0940\u0938\u0930\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0916\u093e\u0926\u094d\u092f \u090f\u0935\u0902 \u0914\u0937\u0927\u093f \u092a\u094d\u0930\u0936\u093e\u0938\u0928 (FDA) \u0915\u094b \u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0906\u0935\u0947\u0926\u0928 (BLA) \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0902\u092a\u0928\u0940 \u0915\u094b \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948 \u0915\u093f \u0905\u0917\u0930 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b RGX-202 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b\u0928\u0947 \u0935\u093e\u0932\u0940 \u0905\u0917\u0932\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u092c\u0928 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0906\u0930\u091c\u0940\u090f\u0915\u094d\u0938-202 \u0935\u093f\u0915\u093e\u0938 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0928\u093f\u0930\u094d\u0927\u093e\u0930\u093f\u0924 \u0938\u092e\u092f \u0938\u0947 \u092a\u0939\u0932\u0947 \u092a\u0942\u0930\u093e \u0939\u094b \u0917\u092f\u093e\u0964<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">REGENXBIO \u0915\u0947 \u0905\u0928\u0941\u0938\u093e\u0930, \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0914\u0930 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u091c\u093e\u0902\u091a\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0926\u094b\u0928\u094b\u0902 \u0915\u0940 \u0913\u0930 \u0938\u0947 \u092a\u094d\u0930\u092c\u0932 \u0930\u0941\u091a\u093f \u0915\u0947 \u0915\u093e\u0930\u0923 \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0928\u093e\u092e\u093e\u0902\u0915\u0928 \u0914\u0930 \u0916\u0941\u0930\u093e\u0915 \u0926\u0947\u0928\u0947 \u0915\u093e \u0915\u093e\u0930\u094d\u092f \u0905\u092a\u0947\u0915\u094d\u0937\u093e \u0938\u0947 \u092a\u0939\u0932\u0947 \u0939\u0940 \u092a\u0942\u0930\u093e \u0939\u094b \u0917\u092f\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092a\u0942\u0930\u093e \u0939\u094b\u0928\u0947 \u0938\u0947 \u0915\u0902\u092a\u0928\u0940 \u0915\u094b FDA \u0915\u0947 \u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092e\u093e\u0930\u094d\u0917 \u0915\u0947 \u0924\u0939\u0924 \u0905\u092a\u0928\u0940 \u0928\u093f\u092f\u094b\u091c\u093f\u0924 BLA \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924\u093f \u0915\u0947 \u0938\u093e\u0925 \u0906\u0917\u0947 \u092c\u0922\u093c\u0928\u0947 \u0915\u0940 \u0905\u0928\u0941\u092e\u0924\u093f \u092e\u093f\u0932 \u0917\u0908 \u0939\u0948\u0964 \u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/biologics-license-application-bla\/\" target=\"_blank\" data-type=\"post\" data-id=\"5027\" rel=\"noreferrer noopener\">FDA \u0926\u0935\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092e\u0947\u0902 BLA \u0915\u093e \u0915\u094d\u092f\u093e \u0905\u0930\u094d\u0925 \u0939\u0948?<\/a><\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u094d\u092f\u093e \u0939\u0948?<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0917\u0902\u092d\u0940\u0930 \u092c\u0940\u092e\u093e\u0930\u093f\u092f\u094b\u0902 \u0915\u0947 \u0906\u0936\u093e\u091c\u0928\u0915 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u094b \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0924\u0915 \u0905\u0927\u093f\u0915 \u0924\u0947\u091c\u093c\u0940 \u0938\u0947 \u092a\u0939\u0941\u0901\u091a\u093e\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092c\u0928\u093e\u0908 \u0917\u0908 \u0939\u0948\u0964 \u0907\u0938 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u0947 \u0924\u0939\u0924, \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u094b \u0910\u0938\u0947 \u0935\u0948\u0915\u0932\u094d\u092a\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 (\u091c\u0948\u0938\u0947 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930) \u0915\u0947 \u0906\u0927\u093e\u0930 \u092a\u0930 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948 \u091c\u094b \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0932\u093e\u092d \u0915\u093e \u0905\u0928\u0941\u092e\u093e\u0928 \u0932\u0917\u093e\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u094b\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">REGENXBIO \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f RGX-202 \u0905\u092a\u0928\u0947 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0921\u0947\u091f\u093e, \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0914\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932 \u0915\u0947 \u0906\u0927\u093e\u0930 \u092a\u0930 \u0907\u0928 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e\u0913\u0902 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">FDA \u0915\u094b 2026 \u0915\u0940 \u0924\u0940\u0938\u0930\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u0939\u0948\u0964<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">REGENXBIO \u0928\u0947 2026 \u0915\u0940 \u0924\u0940\u0938\u0930\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u0905\u092a\u0928\u093e BLA \u0906\u0935\u0947\u0926\u0928 \u091c\u092e\u093e \u0915\u0930\u0928\u093e \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u092c\u0928\u093e\u0908 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0906\u0935\u0947\u0926\u0928 \u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0928\u0947 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u090f\u092b\u093f\u0928\u093f\u091f\u0940 \u0921\u094d\u092f\u0942\u0936\u0947\u0928\u00ae \u0915\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0914\u0930 \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u092e\u0947\u0902 \u0928\u093e\u092e\u093e\u0902\u0915\u093f\u0924 63 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0921\u0947\u091f\u093e\u0964.<\/li>\n\n\n\n<li>\u092e\u0941\u0916\u094d\u092f \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 30 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0921\u0947\u091f\u093e\u0964.<\/li>\n\n\n\n<li>\u092e\u0941\u0916\u094d\u092f \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u0915\u092e \u0938\u0947 \u0915\u092e \u0906\u0927\u0947 \u0915\u0947 \u0932\u093f\u090f \u092c\u093e\u0930\u0939 \u092e\u0939\u0940\u0928\u0947 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e\u0964.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f FDA \u0915\u0940 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0905\u092a\u0947\u0915\u094d\u0937\u093e \u0915\u0947 \u0905\u0928\u0941\u0930\u0942\u092a \u0906\u0917\u0947 \u092c\u0922\u093c\u0924\u0940 \u0939\u0948, \u0924\u094b \u0915\u0902\u092a\u0928\u0940 \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f RGX-202 \u0915\u094b \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 2027 \u0915\u0940 \u0926\u0942\u0938\u0930\u0940 \u091b\u092e\u093e\u0939\u0940 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0906\u0930\u091c\u0940\u090f\u0915\u094d\u0938-202 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u092a\u0930\u093f\u0923\u093e\u092e<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u092a\u094d\u0930\u0915\u093e\u0936\u093f\u0924 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0906\u0902\u0915\u0921\u093c\u094b\u0902 \u092e\u0947\u0902 RGX-202 \u0915\u0947 \u0932\u093f\u090f \u0909\u0924\u094d\u0938\u093e\u0939\u091c\u0928\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0938\u093e\u092e\u0928\u0947 \u0906\u090f \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0932\u0915\u094d\u0937\u094d\u092f \u0938\u092b\u0932\u0924\u093e\u092a\u0942\u0930\u094d\u0935\u0915 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930 \u0932\u093f\u092f\u093e \u0917\u092f\u093e\u0964<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">RGX-202 \u0928\u0947 \u0905\u092a\u0928\u0947 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0932\u0915\u094d\u0937\u094d\u092f \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u093f\u092f\u093e, \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 12\u0935\u0947\u0902 \u0938\u092a\u094d\u0924\u093e\u0939 \u0915\u0947 \u092c\u093e\u0926 93 \u092a\u094d\u0930\u0924\u093f\u0936\u0924 \u0938\u0947 \u0905\u0927\u093f\u0915 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0915\u092e \u0938\u0947 \u0915\u092e 10 \u092a\u094d\u0930\u0924\u093f\u0936\u0924 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0926\u0947\u0916\u0940 \u0917\u0908\u0964 \u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/rgx-202-phase-3-affinity-duchenne-results-released-by-regenxbio\/\" target=\"_blank\" rel=\"noreferrer noopener\">RGX-202 \u0938\u0947 NSAA \u092e\u0947\u0902 \u0935\u0943\u0926\u094d\u0927\u093f \u0926\u0947\u0916\u0940 \u0917\u0908 \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 \u092a\u094d\u0930\u092e\u0941\u0916 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930 \u0921\u0947\u091f\u093e \u0905\u0928\u0941\u092a\u0932\u092c\u094d\u0927 \u0939\u0948\u0964<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928, \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u0938\u0902\u0915\u094d\u0937\u093f\u092a\u094d\u0924 \u0930\u0942\u092a \u0939\u0948 \u091c\u093f\u0938\u0947 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u0928\u094d\u0928 \u0915\u0930\u0928\u0947 \u0915\u093e \u0932\u0915\u094d\u0937\u094d\u092f \u0930\u0916\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u0915\u092e\u0940 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u093e \u092e\u0942\u0932 \u0915\u093e\u0930\u0923 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u093f\u0928 \u092e\u0930\u0940\u091c\u094b\u0902 \u0928\u0947 12 \u092e\u0939\u0940\u0928\u0947 \u0915\u0947 \u092b\u0949\u0932\u094b-\u0905\u092a \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u093f\u092f\u093e, \u0909\u0928\u092e\u0947\u0902 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0928\u0947 \u0915\u0908 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092e\u093e\u092a\u0926\u0902\u0921\u094b\u0902 \u092e\u0947\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0938\u0941\u0927\u093e\u0930 \u0926\u0947\u0916\u0947\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0928\u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0936\u093e\u092e\u093f\u0932 \u0925\u0947:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0938\u092e\u092f\u092c\u0926\u094d\u0927 \u092b\u093c\u0902\u0915\u094d\u0936\u0928 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/li>\n\n\n\n<li><a href=\"https:\/\/dmdwarrior.com\/hi\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" data-type=\"post\" data-id=\"4959\" rel=\"noreferrer noopener\">\u0928\u0949\u0930\u094d\u0925 \u0938\u094d\u091f\u093e\u0930 \u090f\u092e\u094d\u092c\u0941\u0932\u0947\u091f\u0930\u0940 \u0905\u0938\u0947\u0938\u092e\u0947\u0902\u091f (\u090f\u0928\u090f\u0938\u090f\u090f) \u0938\u094d\u0915\u094b\u0930<\/a><\/li>\n\n\n\n<li>\u0938\u092e\u0917\u094d\u0930 \u0936\u093e\u0930\u0940\u0930\u093f\u0915 \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 \u0938\u0902\u0915\u0947\u0924\u0915<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0902\u092a\u0928\u0940 \u0928\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u092e\u093e\u092a\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0915\u0940 \u090f\u0915 \u092e\u091c\u092c\u0942\u0924 \u092e\u093e\u0924\u094d\u0930\u093e \u0915\u0940 \u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0926\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0914\u0930 \u0915\u093e\u0930\u094d\u092f\u092a\u094d\u0930\u0923\u093e\u0932\u0940 \u0915\u0947 \u092c\u0940\u091a \u092e\u091c\u092c\u0942\u0924 \u0938\u0939\u0938\u0902\u092c\u0902\u0927<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">REGENXBIO \u0928\u0947 \u0938\u092a\u094d\u0924\u093e\u0939 12 \u092e\u0947\u0902 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0914\u0930 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u090f\u0915 \u0935\u0930\u094d\u0937 \u092c\u093e\u0926 \u0926\u0947\u0916\u0947 \u0917\u090f \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0938\u0941\u0927\u093e\u0930\u094b\u0902 \u0915\u0947 \u092c\u0940\u091a \u090f\u0915 \u092e\u091c\u092c\u0942\u0924 \u0938\u0902\u092c\u0902\u0927 \u0915\u0940 \u092d\u0940 \u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0915\u0940\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u094b \u090f\u0915 \u0935\u0948\u0915\u0932\u094d\u092a\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0928\u0947 \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0924\u093e \u0939\u0948 \u091c\u094b \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0932\u093e\u092d \u0915\u0940 \u092d\u0935\u093f\u0937\u094d\u092f\u0935\u093e\u0923\u0940 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0939\u093e\u092f\u0915 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0906\u0930\u091c\u0940\u090f\u0915\u094d\u0938-202 \u0915\u0940 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0902\u092a\u0928\u0940 \u0928\u0947 \u092c\u0924\u093e\u092f\u093e \u0915\u093f \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u0906\u0930\u091c\u0940\u090f\u0915\u094d\u0938-202 \u0915\u094b \u0906\u092e \u0924\u094c\u0930 \u092a\u0930 \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u0938\u0939\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0928\u0947 \u090f\u0915 \u0905\u0928\u0941\u0915\u0942\u0932 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932 \u0915\u0940 \u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0915\u0940 \u0939\u0948, \u091c\u093f\u0938\u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 REGENXBIO \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u092f\u0939 RGX-202 \u0915\u094b \u0935\u0930\u094d\u0924\u092e\u093e\u0928 \u092e\u0947\u0902 \u0935\u093f\u0915\u093e\u0938 \u0915\u0947 \u0905\u0927\u0940\u0928 \u0905\u0928\u094d\u092f \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0909\u092a\u091a\u093e\u0930 \u0935\u093f\u0915\u0932\u094d\u092a\u094b\u0902 \u0938\u0947 \u0905\u0932\u0917 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0928\u093f\u0930\u0902\u0924\u0930 \u0928\u093f\u0917\u0930\u093e\u0928\u0940 \u0938\u0947 \u092e\u0930\u0940\u091c\u094b\u0902 \u0915\u0940 \u0928\u093f\u0917\u0930\u093e\u0928\u0940 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b\u0917\u0940\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">REGENXBIO \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0935\u093e\u0923\u093f\u091c\u094d\u092f\u093f\u0915 \u0932\u0949\u0928\u094d\u091a \u0915\u0940 \u0924\u0948\u092f\u093e\u0930\u0940 \u0915\u0930 \u0930\u0939\u093e \u0939\u0948<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">FDA \u0915\u0940 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u092e\u0947\u0902, REGENXBIO \u0928\u0947 \u092a\u0939\u0932\u0947 \u0939\u0940 \u0905\u092a\u0928\u0947 \u0935\u093f\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0914\u0930 \u0935\u093e\u0923\u093f\u091c\u094d\u092f\u093f\u0915 \u092c\u0941\u0928\u093f\u092f\u093e\u0926\u0940 \u0922\u093e\u0902\u091a\u0947 \u0915\u094b \u0924\u0948\u092f\u093e\u0930 \u0915\u0930\u0928\u093e \u0936\u0941\u0930\u0942 \u0915\u0930 \u0926\u093f\u092f\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0902\u092a\u0928\u0940 \u092e\u0948\u0930\u0940\u0932\u0948\u0902\u0921 \u0915\u0947 \u0930\u0949\u0915\u0935\u093f\u0932 \u092e\u0947\u0902 \u0938\u094d\u0925\u093f\u0924 \u0905\u092a\u0928\u0947 \u0935\u093f\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0928\u0935\u093e\u091a\u093e\u0930 \u0915\u0947\u0902\u0926\u094d\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930 \u0930\u0939\u0940 \u0939\u0948, \u091c\u0939\u093e\u0902 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0935\u093e\u0923\u093f\u091c\u094d\u092f\u093f\u0915 \u0906\u092a\u0942\u0930\u094d\u0924\u093f \u0915\u0947 \u0932\u093f\u090f \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u092a\u093f\u091b\u0932\u0947 \u0935\u0930\u094d\u0937 \u0936\u0941\u0930\u0942 \u0939\u0941\u0906 \u0925\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f RGX-202 \u0915\u094b \u0928\u093f\u092f\u093e\u092e\u0915\u0940\u092f \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b \u092f\u0939 \u0935\u093f\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0924\u0924\u094d\u092a\u0930\u0924\u093e \u0935\u094d\u092f\u093e\u092a\u0915 \u0930\u094b\u0917\u0940 \u092a\u0939\u0941\u0902\u091a \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0939\u093e\u092f\u0915 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0907\u0938\u0915\u093e \u0915\u094d\u092f\u093e \u0905\u0930\u094d\u0925 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u093e \u092a\u0942\u0930\u093e \u0939\u094b\u0928\u093e RGX-202 \u0914\u0930 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0915\u0926\u092e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">2026 \u0915\u0940 \u0924\u0940\u0938\u0930\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 FDA \u0906\u0935\u0947\u0926\u0928 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u0914\u0930 2027 \u0915\u0940 \u0926\u0942\u0938\u0930\u0940 \u091b\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0928\u093f\u0930\u094d\u0923\u092f \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0915\u0947 \u0938\u093e\u0925, \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092a\u0930\u093f\u0935\u093e\u0930 \u0906\u0917\u093e\u092e\u0940 \u0928\u093f\u092f\u093e\u092e\u0915 \u0918\u091f\u0928\u093e\u0915\u094d\u0930\u092e\u094b\u0902 \u092a\u0930 \u092c\u093e\u0930\u0940\u0915\u0940 \u0938\u0947 \u0928\u091c\u0930 \u0930\u0916\u0947\u0902\u0917\u0947\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b RGX-202 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0935\u093f\u0915\u0932\u094d\u092a \u092c\u0928 \u0938\u0915\u0924\u093e \u0939\u0948, \u091c\u093f\u0938\u0938\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0935\u093f\u0915\u0932\u094d\u092a \u092c\u0922\u093c\u0947\u0902\u0917\u0947 \u0914\u0930 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0939\u094b\u0917\u093e\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0905\u0915\u094d\u0938\u0930 \u092a\u0942\u091b\u0947 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u0936\u094d\u0928 (FAQ)<\/h2>\n\n\n<div id=\"rank-math-faq\" class=\"rank-math-block\">\n<div class=\"rank-math-list\">\n<div id=\"faq-question-1782302007464\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">RGX-202 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0906\u0930\u091c\u0940\u090f\u0915\u094d\u0938-202 \u090f\u0915 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0939\u0948 \u091c\u093f\u0938\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u0930\u0940\u091c\u0947\u0928\u090f\u0915\u094d\u0938\u092c\u093e\u092f\u094b \u0926\u094d\u0935\u093e\u0930\u093e \u0935\u093f\u0915\u0938\u093f\u0924 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302015108\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">REGENXBIO RGX-202 \u0915\u094b FDA \u092e\u0947\u0902 \u0915\u092c \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0930\u0947\u0917\u093e?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0915\u0902\u092a\u0928\u0940 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e 2026 \u0915\u0940 \u0924\u0940\u0938\u0930\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0905\u092a\u0928\u0947 \u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u090f\u092a\u094d\u0932\u0940\u0915\u0947\u0936\u0928 (\u092c\u0940\u090f\u0932\u090f) \u091c\u092e\u093e \u0915\u0930\u0928\u0947 \u0915\u0940 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302022653\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092e\u0941\u0916\u094d\u092f \u092a\u0930\u093f\u0923\u093e\u092e \u0915\u094d\u092f\u093e \u0925\u0947?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>12\u0935\u0947\u0902 \u0938\u092a\u094d\u0924\u093e\u0939 \u0924\u0915 93 \u092a\u094d\u0930\u0924\u093f\u0936\u0924 \u0938\u0947 \u0905\u0927\u093f\u0915 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0915\u092e \u0938\u0947 \u0915\u092e 10 \u092a\u094d\u0930\u0924\u093f\u0936\u0924 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0941\u0908, \u0914\u0930 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0906\u0902\u0915\u0921\u093c\u094b\u0902 \u0928\u0947 \u090f\u0915 \u0935\u0930\u094d\u0937 \u0915\u0947 \u092c\u093e\u0926 \u0938\u093e\u0930\u094d\u0925\u0915 \u0938\u0941\u0927\u093e\u0930 \u0926\u093f\u0916\u093e\u092f\u093e\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302027017\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0906\u0930\u091c\u0940\u090f\u0915\u094d\u0938-202 \u0915\u094b \u0915\u092c \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u092f\u0926\u093f FDA \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0905\u092a\u0947\u0915\u094d\u0937\u093e \u0915\u0947 \u0905\u0928\u0941\u0930\u0942\u092a \u0906\u0917\u0947 \u092c\u0922\u093c\u0924\u0940 \u0939\u0948, \u0924\u094b REGENXBIO \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f RGX-202 \u0915\u094b \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 2027 \u0915\u0947 \u0909\u0924\u094d\u0924\u0930\u093e\u0930\u094d\u0927 \u092e\u0947\u0902 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1782302033436\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u092c\u0940\u090f\u0932\u090f \u092a\u0948\u0915\u0947\u091c \u092e\u0947\u0902 \u0915\u093f\u0924\u0928\u0947 \u092e\u0930\u0940\u091c\u093c \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u092a\u094d\u0930\u0938\u094d\u0924\u093e\u0935\u093f\u0924 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924\u093f \u092e\u0947\u0902 \u092e\u0941\u0916\u094d\u092f \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 63 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0938\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0921\u0947\u091f\u093e \u0914\u0930 30 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0938\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0921\u0947\u091f\u093e \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0928\u0947 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>REGENXBIO has announced the completion of patient dosing in the confirmatory study of RGX-202, its investigational gene therapy for Duchenne Muscular Dystrophy (DMD). This important milestone marks the completion of the company&#8217;s registrational development program and supports a planned Biologics License Application (BLA) submission to the U.S. Food and Drug Administration (FDA) in the third [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":8158,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[525,88,652,61,107,108],"class_list":["post-8153","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-affinity-duchenne","tag-fda","tag-fda-drug-approval","tag-gene-therapy","tag-regenxbio","tag-rgx-202"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8153","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=8153"}],"version-history":[{"count":3,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8153\/revisions"}],"predecessor-version":[{"id":8157,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8153\/revisions\/8157"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/8158"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=8153"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=8153"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=8153"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}