{"id":8116,"date":"2026-06-12T19:47:11","date_gmt":"2026-06-12T16:47:11","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=8116"},"modified":"2026-06-12T20:04:35","modified_gmt":"2026-06-12T17:04:35","slug":"if-elevidys-works-why-is-sarepta-stock-falling","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/if-elevidys-works-why-is-sarepta-stock-falling\/","title":{"rendered":"\u0905\u0917\u0930 Elevidys \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0915\u093e\u0930\u0917\u0930 \u0939\u0948, \u0924\u094b \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930\u094b\u0902 \u092e\u0947\u0902 \u0917\u093f\u0930\u093e\u0935\u091f \u0915\u094d\u092f\u094b\u0902 \u0906 \u0930\u0939\u0940 \u0939\u0948? \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0941\u0928\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0915\u094d\u092f\u093e \u091c\u093e\u0928\u0928\u093e \u091a\u093e\u0939\u093f\u090f?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0915\u0947 \u0915\u0941\u091b \u0939\u0940 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0928\u0947 1\u091f\u0940\u092a\u0940114\u091f\u0940 (\u0921\u0947\u0932\u093e\u0902\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u091c\u0940\u0928 \u092e\u094b\u0915\u094d\u0938\u0947\u092a\u093e\u0930\u0935\u094b\u0935\u0947\u0915) \u091c\u093f\u0924\u0928\u093e \u0909\u0924\u094d\u0938\u093e\u0939, \u0935\u093f\u0935\u093e\u0926 \u0914\u0930 \u092c\u0939\u0938 \u092a\u0948\u0926\u093e \u0915\u0940 \u0939\u0948, \u091c\u094b 1\u091f\u0940\u092a\u094019\u091f\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u0935\u093f\u0915\u0938\u093f\u0924 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f, Elevidys \u0906\u0936\u093e \u0915\u0940 \u0915\u093f\u0930\u0923 \u0939\u0948\u0964 \u092f\u0939 \u092a\u0939\u0932\u0940 \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0939\u0948 \u091c\u093f\u0938\u0947 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u092e\u0947\u0902 \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u092a\u0939\u0941\u0901\u091a\u093e\u0915\u0930 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0905\u0902\u0924\u0930\u094d\u0928\u093f\u0939\u093f\u0924 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0915\u093e\u0930\u0923 \u0915\u094b \u0926\u0942\u0930 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948\u0964 \u0907\u0938 \u0909\u092a\u091a\u093e\u0930 \u0915\u094b 2023 \u092e\u0947\u0902 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0916\u093e\u0926\u094d\u092f \u090f\u0935\u0902 \u0914\u0937\u0927\u093f \u092a\u094d\u0930\u0936\u093e\u0938\u0928 (FDA) \u0938\u0947 \u0924\u094d\u0935\u0930\u093f\u0924 \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f \u092e\u093f\u0932\u0940 \u0914\u0930 \u092c\u093e\u0926 \u092e\u0947\u0902 2024 \u092e\u0947\u0902 \u0907\u0938\u0915\u093e \u0935\u093f\u0938\u094d\u0924\u093e\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0941\u0906\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0932\u0947\u0915\u093f\u0928 \u0938\u093e\u0925 \u0939\u0940 \u0938\u093e\u0925, \u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930\u094b\u0902 \u092e\u0947\u0902 \u092d\u093e\u0930\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u0906\u0908 \u0939\u0948, \u0928\u093f\u092f\u093e\u092e\u0915 \u0935\u093f\u0935\u093e\u0926 \u0938\u093e\u092e\u0928\u0947 \u0906\u090f \u0939\u0948\u0902, \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u091a\u093f\u0902\u0924\u093e\u090f\u0902 \u0924\u0947\u091c \u0939\u094b \u0917\u0908 \u0939\u0948\u0902, \u0914\u0930 \u0915\u0908 \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0932\u093e\u092d \u0915\u0940 \u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915 \u092e\u093e\u0924\u094d\u0930\u093e \u092a\u0930 \u092c\u0939\u0938 \u0915\u0930\u0928\u093e \u091c\u093e\u0930\u0940 \u0930\u0916\u0947 \u0939\u0941\u090f \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0938\u094d\u0925\u093f\u0924\u093f \u0915\u0920\u093f\u0928 \u0932\u0947\u0915\u093f\u0928 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092a\u094d\u0930\u0936\u094d\u0928 \u0909\u0920\u093e\u0924\u0940 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0905\u0917\u0930 Elevidys \u0915\u093e\u0930\u0917\u0930 \u0939\u0948, \u0924\u094b \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930\u094b\u0902 \u092e\u0947\u0902 \u0907\u0924\u0928\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u0915\u094d\u092f\u094b\u0902 \u0906\u0908 \u0939\u0948?<\/li>\n\n\n\n<li>\u0915\u094d\u092f\u093e \u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u092f\u0939 \u0909\u092a\u091a\u093e\u0930 \u0905\u092a\u094d\u0930\u092d\u093e\u0935\u0940 \u0939\u0948?<\/li>\n\n\n\n<li>\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0941\u091b \u092a\u094d\u0930\u092e\u0941\u0916 \u0932\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0935\u093f\u092b\u0932 \u0915\u094d\u092f\u094b\u0902 \u0930\u0939\u0947?<\/li>\n\n\n\n<li>Elevidys \u0915\u094b FDA \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u094d\u092f\u094b\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 \u092f\u0942\u0930\u094b\u092a\u0940\u092f \u0914\u0937\u0927\u093f \u090f\u091c\u0947\u0902\u0938\u0940 (EMA) \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u094d\u092f\u094b\u0902 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948?<\/li>\n\n\n\n<li>\u0909\u092a\u091a\u093e\u0930 \u0915\u0930\u093e\u0928\u0947 \u0915\u093e \u0928\u093f\u0930\u094d\u0923\u092f \u0932\u0947\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0915\u094d\u092f\u093e-\u0915\u094d\u092f\u093e \u0938\u092e\u091d\u0928\u093e \u091a\u093e\u0939\u093f\u090f?<\/li>\n\n\n\n<li>\u0915\u094d\u092f\u093e \u0906\u091c Elevidys \u0938\u094d\u0935\u0940\u0915\u093e\u0930 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u092e\u093f\u0932\u0928\u0947 \u0935\u093e\u0932\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e\u0913\u0902 \u0915\u0947 \u0932\u093f\u090f \u092a\u093e\u0924\u094d\u0930\u0924\u093e \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948?<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0928 \u0938\u0935\u093e\u0932\u094b\u0902 \u0915\u0947 \u091c\u0935\u093e\u092c \u092d\u093e\u0935\u0928\u093e\u0924\u094d\u092e\u0915 \u0938\u094b\u0936\u0932 \u092e\u0940\u0921\u093f\u092f\u093e \u092c\u0939\u0938\u094b\u0902 \u0915\u0947 \u092c\u091c\u093e\u092f \u0938\u093e\u0915\u094d\u0937\u094d\u092f-\u0906\u0927\u093e\u0930\u093f\u0924 \u0939\u094b\u0928\u0947 \u091a\u093e\u0939\u093f\u090f\u0964.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#understanding-what-elevidys-actually-does\">Elevidys \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u0915\u094d\u092f\u093e \u0915\u0930\u0924\u093e \u0939\u0948, \u0907\u0938\u0947 \u0938\u092e\u091d\u0928\u093e<\/a><ul><\/ul><\/li><li><a href=\"#if-elevidys-works-why-has-sareptas-stock-fallen-so-dramatically\">\u0905\u0917\u0930 Elevidys \u0915\u093e\u0930\u0917\u0930 \u0939\u0948, \u0924\u094b \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930\u094b\u0902 \u092e\u0947\u0902 \u0907\u0924\u0928\u0940 \u092d\u093e\u0930\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u0915\u094d\u092f\u094b\u0902 \u0906\u0908 \u0939\u0948?<\/a><ul><\/ul><\/li><li><a href=\"#why-viral-videos-should-not-be-used-as-scientific-evidence\">\u0935\u093e\u092f\u0930\u0932 \u0935\u0940\u0921\u093f\u092f\u094b \u0915\u094b \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u092a\u094d\u0930\u092e\u093e\u0923 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0915\u094d\u092f\u094b\u0902 \u0928\u0939\u0940\u0902 \u0907\u0938\u094d\u0924\u0947\u092e\u093e\u0932 \u0915\u093f\u092f\u093e \u091c\u093e\u0928\u093e \u091a\u093e\u0939\u093f\u090f<\/a><ul><\/ul><\/li><li><a href=\"#are-nsaa-scores-enough-to-measure-success\">\u0915\u094d\u092f\u093e \u090f\u0928\u090f\u0938\u090f\u090f \u0915\u0947 \u0905\u0902\u0915 \u0938\u092b\u0932\u0924\u093e \u092e\u093e\u092a\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092a\u0930\u094d\u092f\u093e\u092a\u094d\u0924 \u0939\u0948\u0902?<\/a><ul><\/ul><\/li><li><a href=\"#how-many-extra-years-could-elevidys-add\">Elevidys \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u092e\u0947\u0930\u093e \u092c\u0947\u091f\u093e \u0915\u093f\u0924\u0928\u0947 \u0914\u0930 \u0938\u093e\u0932 \u091c\u0940\u0935\u093f\u0924 \u0930\u0939\u0947\u0917\u093e?<\/a><ul><\/ul><\/li><li><a href=\"#is-elevidys-worth-3-2-million\">\u0915\u094d\u092f\u093e Elevidys \u0915\u0940 \u0915\u0940\u092e\u0924 3.2 \u092e\u093f\u0932\u093f\u092f\u0928 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0939\u0948?<\/a><ul><\/ul><\/li><li><a href=\"#why-is-elevidys-approved-by-the-fda-but-not-by-the-ema\">Elevidys \u0915\u094b FDA \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u094d\u092f\u094b\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 EMA \u0926\u094d\u0935\u093e\u0930\u093e \u0928\u0939\u0940\u0902?<\/a><ul><\/ul><\/li><li><a href=\"#could-receiving-elevidys-limit-future-treatment-options\">\u0915\u094d\u092f\u093e Elevidys \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0935\u093f\u0915\u0932\u094d\u092a \u0938\u0940\u092e\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902?<\/a><ul><\/ul><\/li><li><a href=\"#what-new-duchenne-therapies-are-coming\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0932\u093f\u090f \u0915\u094c\u0928-\u0915\u094c\u0928 \u0938\u0940 \u0928\u0908 \u0909\u092a\u091a\u093e\u0930 \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0902 \u0906 \u0930\u0939\u0940 \u0939\u0948\u0902?<\/a><ul><\/ul><\/li><li><a href=\"#why-families-continue-campaigning-for-elevidys\">\u092a\u0930\u093f\u0935\u093e\u0930 Elevidys \u0915\u0947 \u0932\u093f\u090f \u0905\u092d\u093f\u092f\u093e\u0928 \u0915\u094d\u092f\u094b\u0902 \u091c\u093e\u0930\u0940 \u0930\u0916\u0947 \u0939\u0941\u090f \u0939\u0948\u0902?<\/a><\/li><li><a href=\"#questions-every-family-should-ask-before-choosing-elevidys\">Elevidys \u091a\u0941\u0928\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0939\u0930 \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u094b \u092f\u0947 \u0938\u0935\u093e\u0932 \u092a\u0942\u091b\u0928\u0947 \u091a\u093e\u0939\u093f\u090f<\/a><\/li><li><a href=\"#conclusion\">\u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"understanding-what-elevidys-actually-does\" class=\"wp-block-heading\">Elevidys \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u0915\u094d\u092f\u093e \u0915\u0930\u0924\u093e \u0939\u0948, \u0907\u0938\u0947 \u0938\u092e\u091d\u0928\u093e<\/h2>\n\n\n\n<h3 id=\"elevidys-is-not-a-full-dystrophin-replacement\" class=\"wp-block-heading\">Elevidys \u090f\u0915 \u092a\u0942\u0930\u094d\u0923 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u0924\u093f\u0938\u094d\u0925\u093e\u092a\u0928 \u0928\u0939\u0940\u0902 \u0939\u0948\u0964<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0924\u092c \u0939\u094b\u0924\u0940 \u0939\u0948 \u091c\u092c \u0921\u0940\u090f\u092e\u0921\u0940 \u091c\u0940\u0928 \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0947 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u094b \u0930\u094b\u0915\u0924\u0947 \u0939\u0948\u0902, \u091c\u094b \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0939\u0948 \u091c\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0930\u0947\u0936\u094b\u0902 \u0915\u094b \u0915\u094d\u0937\u0924\u093f \u0938\u0947 \u092c\u091a\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u0938\u0902\u092a\u0942\u0930\u094d\u0923 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u094b \u092a\u0941\u0928\u0930\u094d\u0938\u094d\u0925\u093e\u092a\u093f\u0924 \u0928\u0939\u0940\u0902 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0915\u0947 \u092c\u091c\u093e\u092f, \u092f\u0939 \u090f\u0921\u0947\u0928\u094b-\u090f\u0938\u094b\u0938\u093f\u090f\u091f\u0947\u0921 \u0935\u093e\u092f\u0930\u0938 (AAV) \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0915\u0947 \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0928\u093e\u092e\u0915 \u090f\u0915 \u0938\u0902\u0915\u094d\u0937\u093f\u092a\u094d\u0924 \u0938\u0902\u0938\u094d\u0915\u0930\u0923 \u0935\u093f\u0924\u0930\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948\u0964 \u0907\u0938 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094b \u0907\u0938\u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092a\u0942\u0930\u094d\u0923 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0907\u0924\u0928\u093e \u092c\u0921\u093c\u093e \u0939\u0948 \u0915\u093f \u0935\u0930\u094d\u0924\u092e\u093e\u0928 AAV \u0935\u093f\u0924\u0930\u0923 \u092a\u094d\u0930\u0923\u093e\u0932\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0938\u092e\u093e\u0939\u093f\u0924 \u0928\u0939\u0940\u0902 \u0939\u094b \u092a\u093e\u0924\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0905\u0902\u0924\u0930 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u090f\u0915 \u091b\u094b\u091f\u093e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928-\u091c\u0948\u0938\u093e \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u092c\u0928\u093e\u0928\u093e \u0939\u0948 \u091c\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u0915\u094b \u0906\u0902\u0936\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 \u092f\u0939 \u0938\u094d\u0935\u0938\u094d\u0925 \u0935\u094d\u092f\u0915\u094d\u0924\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u092a\u093e\u090f \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u0938\u0902\u092a\u0942\u0930\u094d\u0923 \u092a\u094d\u0930\u093e\u0915\u0943\u0924\u093f\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u094b \u092a\u0941\u0928\u0903 \u0909\u0924\u094d\u092a\u0928\u094d\u0928 \u0928\u0939\u0940\u0902 \u0915\u0930\u0924\u093e \u0939\u0948\u0964 \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u093e \u0939\u0948 \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092c\u093e\u0926 \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0928\u093f\u0930\u0902\u0924\u0930 \u092c\u0928\u0940 \u0930\u0939\u0924\u0940 \u0939\u0948, \u091c\u094b FDA \u0915\u0940 \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f \u0915\u093e \u090f\u0915 \u092a\u094d\u0930\u092e\u0941\u0916 \u0906\u0927\u093e\u0930 \u092c\u0928\u093e\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"if-elevidys-works-why-has-sareptas-stock-fallen-so-dramatically\" class=\"wp-block-heading\">\u0905\u0917\u0930 Elevidys \u0915\u093e\u0930\u0917\u0930 \u0939\u0948, \u0924\u094b \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930\u094b\u0902 \u092e\u0947\u0902 \u0907\u0924\u0928\u0940 \u092d\u093e\u0930\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u0915\u094d\u092f\u094b\u0902 \u0906\u0908 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u092a\u0930\u093f\u0935\u093e\u0930 \u092f\u0939 \u092e\u093e\u0928 \u0932\u0947\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u0936\u0947\u092f\u0930 \u0915\u0940 \u0915\u0940\u092e\u0924 \u092e\u0947\u0902 \u0917\u093f\u0930\u093e\u0935\u091f \u0915\u093e \u092e\u0924\u0932\u092c \u092f\u0939 \u0939\u0948 \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u0915\u093e\u0930\u0917\u0930 \u0928\u0939\u0940\u0902 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u0948\u0935 \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u0940 \u0915\u0947 \u0915\u094d\u0937\u0947\u0924\u094d\u0930 \u092e\u0947\u0902, \u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915\u0924\u093e \u0915\u0939\u0940\u0902 \u0905\u0927\u093f\u0915 \u091c\u091f\u093f\u0932 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 id=\"investor-concerns-extend-beyond-clinical-results\" class=\"wp-block-heading\">\u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u0940 \u091a\u093f\u0902\u0924\u093e\u090f\u0902 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0938\u0947 \u092a\u0930\u0947 \u0939\u0948\u0902\u0964<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0928\u093f\u0935\u0947\u0936\u0915 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0938\u0941\u0930\u0915\u094d\u0937\u093e \u091c\u094b\u0916\u093f\u092e<\/li>\n\n\n\n<li>\u0928\u093f\u092f\u093e\u092e\u0915 \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e<\/li>\n\n\n\n<li>\u0935\u093e\u0923\u093f\u091c\u094d\u092f\u093f\u0915 \u0917\u094b\u0926 \u0932\u0947\u0928\u093e<\/li>\n\n\n\n<li>\u092c\u0940\u092e\u093e \u092a\u094d\u0930\u0924\u093f\u092a\u0942\u0930\u094d\u0924\u093f<\/li>\n\n\n\n<li>\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u092a\u094d\u0930\u0924\u093f\u092f\u094b\u0917\u093f\u0924\u093e<\/li>\n\n\n\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u0915\u0941\u091b \u0932\u093e\u092d \u0939\u094b\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902, \u092f\u0939 \u092a\u0942\u091b\u0928\u0947 \u0915\u0947 \u092c\u091c\u093e\u092f\u0964.<\/p>\n\n\n\n<h3 id=\"safety-concerns-have-had-major-impact\" class=\"wp-block-heading\">\u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u091a\u093f\u0902\u0924\u093e\u0913\u0902 \u0915\u093e \u092c\u0921\u093c\u093e \u092a\u094d\u0930\u092d\u093e\u0935 \u092a\u0921\u093c\u093e \u0939\u0948<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">2025 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928, \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e\u094b\u0902 \u0938\u0947 \u091c\u0941\u0921\u093c\u0947 \u0924\u0940\u0935\u094d\u0930 \u092f\u0915\u0943\u0924 \u0935\u093f\u092b\u0932\u0924\u093e \u0915\u0947 \u092e\u093e\u092e\u0932\u094b\u0902 \u0914\u0930 \u0930\u094b\u0917\u0940 \u0915\u0940 \u092e\u094c\u0924\u094b\u0902 \u0928\u0947 \u0928\u093f\u092f\u093e\u092e\u0915\u094b\u0902 \u0914\u0930 \u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u0940 \u0913\u0930 \u0938\u0947 \u0917\u0939\u0928 \u091c\u093e\u0902\u091a \u0915\u094b \u092c\u0922\u093c\u093e\u0935\u093e \u0926\u093f\u092f\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092c\u093e\u0926 \u092e\u0947\u0902 FDA \u0928\u0947 Elevidys \u0915\u0940 \u092a\u094d\u0930\u093f\u0938\u094d\u0915\u094d\u0930\u093f\u092a\u094d\u0936\u0928 \u0938\u0902\u092c\u0902\u0927\u0940 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0915\u094b \u0905\u092a\u0921\u0947\u091f \u0915\u093f\u092f\u093e \u0914\u0930 \u0917\u0902\u092d\u0940\u0930 \u0924\u0940\u0935\u094d\u0930 \u092f\u0915\u0943\u0924 \u0915\u094d\u0937\u0924\u093f \u0914\u0930 \u0924\u0940\u0935\u094d\u0930 \u092f\u0915\u0943\u0924 \u0935\u093f\u092b\u0932\u0924\u093e \u0915\u0947 \u0938\u0902\u092c\u0902\u0927 \u092e\u0947\u0902 \u0905\u0927\u093f\u0915 \u092e\u091c\u092c\u0942\u0924 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u091a\u0947\u0924\u093e\u0935\u0928\u093f\u092f\u093e\u0901 \u091c\u094b\u0921\u093c\u0940\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f \u092f\u0947 \u0918\u091f\u0928\u093e\u090f\u0902 \u092e\u0941\u0916\u094d\u092f \u0930\u0942\u092a \u0938\u0947 \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0905\u0938\u092e\u0930\u094d\u0925 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u092c\u0940\u091a \u0939\u0941\u0908\u0902, \u0932\u0947\u0915\u093f\u0928 \u0907\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u0947 \u0935\u093f\u0936\u094d\u0935\u093e\u0938 \u0915\u094b \u0915\u093e\u092b\u0940 \u0939\u0926 \u0924\u0915 \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0915\u093f\u092f\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u094b \u0928 \u0915\u0947\u0935\u0932 \u0907\u0938 \u092c\u093e\u0924 \u0915\u0940 \u091a\u093f\u0902\u0924\u093e \u0939\u094b\u0924\u0940 \u0939\u0948 \u0915\u093f \u0915\u094b\u0908 \u0909\u092a\u091a\u093e\u0930 \u0915\u093e\u0930\u0917\u0930 \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902, \u092c\u0932\u094d\u0915\u093f \u0907\u0938 \u092c\u093e\u0924 \u0915\u0940 \u092d\u0940 \u091a\u093f\u0902\u0924\u093e \u0939\u094b\u0924\u0940 \u0939\u0948 \u0915\u093f \u0915\u094d\u092f\u093e \u0928\u093f\u092f\u093e\u092e\u0915 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0907\u0938\u0915\u0947 \u0909\u092a\u092f\u094b\u0917 \u0915\u094b \u092a\u094d\u0930\u0924\u093f\u092c\u0902\u0927\u093f\u0924 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<h3 id=\"clinical-trial-results-have-been-interpreted-differently\" class=\"wp-block-heading\">\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u0940 \u0905\u0932\u0917-\u0905\u0932\u0917 \u0935\u094d\u092f\u093e\u0916\u094d\u092f\u093e \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0935\u093f\u0935\u093e\u0926 \u0915\u093e \u090f\u0915 \u092a\u094d\u0930\u092e\u0941\u0916 \u0915\u093e\u0930\u0923 \u090f\u092e\u094d\u092c\u093e\u0930\u094d\u0915 \u092b\u0947\u091c 3 \u0905\u0927\u094d\u092f\u092f\u0928 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092e\u0942\u0932 \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u090f\u092e\u094d\u092c\u093e\u0930\u094d\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923, \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u0928\u0949\u0930\u094d\u0925 \u0938\u094d\u091f\u093e\u0930 \u090f\u092e\u094d\u092c\u0941\u0932\u0947\u091f\u0930\u0940 \u0905\u0938\u0947\u0938\u092e\u0947\u0902\u091f (\u090f\u0928\u090f\u0938\u090f\u090f) \u0938\u094d\u0915\u094b\u0930 \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0905\u092a\u0928\u0947 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0932\u0915\u094d\u0937\u094d\u092f \u0915\u094b \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0935\u093f\u092b\u0932 \u0930\u0939\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u0915\u0908 \u092e\u093e\u0927\u094d\u092f\u092e\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u092e\u0947\u0902 Elevidys \u0915\u0947 \u092a\u0915\u094d\u0937 \u092e\u0947\u0902 \u0930\u0941\u091d\u093e\u0928 \u0926\u093f\u0916\u0947, \u0914\u0930 \u092c\u093e\u0926 \u0915\u0947 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923\u094b\u0902 \u0938\u0947 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u092e\u0947\u0902 \u0915\u092e\u0940 \u0915\u093e \u0938\u0902\u0915\u0947\u0924 \u092e\u093f\u0932\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u092e\u0930\u094d\u0925\u0915\u094b\u0902 \u0915\u093e \u0924\u0930\u094d\u0915 \u0939\u0948 \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0927\u0940\u092e\u0940 \u0939\u094b\u0924\u0940 \u0939\u0948 \u0914\u0930 \u0915\u092e \u0938\u092e\u092f \u0905\u0935\u0927\u093f \u092e\u0947\u0902 \u0907\u0938\u0947 \u092e\u093e\u092a\u0928\u093e \u092e\u0941\u0936\u094d\u0915\u093f\u0932 \u0939\u094b\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0906\u0932\u094b\u091a\u0915\u094b\u0902 \u0915\u093e \u0924\u0930\u094d\u0915 \u0939\u0948 \u0915\u093f \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0932\u0915\u094d\u0937\u094d\u092f \u0915\u093e \u0928 \u092e\u093f\u0932 \u092a\u093e\u0928\u093e \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0938\u0935\u093e\u0932 \u0916\u0921\u093c\u0947 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0915\u093e \u092a\u0930\u093f\u0923\u093e\u092e \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0938\u0939\u092e\u0924\u093f \u0915\u0947 \u092c\u091c\u093e\u092f \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0905\u0938\u0939\u092e\u0924\u093f \u0939\u0948\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"why-viral-videos-should-not-be-used-as-scientific-evidence\" class=\"wp-block-heading\">\u0935\u093e\u092f\u0930\u0932 \u0935\u0940\u0921\u093f\u092f\u094b \u0915\u094b \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u092a\u094d\u0930\u092e\u093e\u0923 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0915\u094d\u092f\u094b\u0902 \u0928\u0939\u0940\u0902 \u0907\u0938\u094d\u0924\u0947\u092e\u093e\u0932 \u0915\u093f\u092f\u093e \u091c\u093e\u0928\u093e \u091a\u093e\u0939\u093f\u090f<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0905\u0915\u094d\u0938\u0930 \u0938\u094b\u0936\u0932 \u092e\u0940\u0921\u093f\u092f\u093e \u092a\u0930 \u0910\u0938\u0947 \u0928\u093e\u091f\u0915\u0940\u092f \u0935\u0940\u0921\u093f\u092f\u094b \u0926\u0947\u0916\u0928\u0947 \u0915\u094b \u092e\u093f\u0932\u0924\u0947 \u0939\u0948\u0902 \u091c\u093f\u0928\u092e\u0947\u0902 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0947 \u0907\u0932\u093e\u091c \u0938\u0947 \u092a\u0939\u0932\u0947 \u0914\u0930 \u092c\u093e\u0926 \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u0926\u093f\u0916\u093e\u0908 \u0926\u0947\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0947 \u0935\u0940\u0921\u093f\u092f\u094b \u092d\u093e\u0935\u0928\u093e\u0924\u094d\u092e\u0915 \u0930\u0942\u092a \u0938\u0947 \u092c\u0939\u0941\u0924 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u093e\u0932\u0940 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u092f\u0947 \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u092a\u094d\u0930\u092e\u093e\u0923 \u0928\u0939\u0940\u0902 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<h3 id=\"the-problem-with-anecdotal-evidence\" class=\"wp-block-heading\">\u0915\u093f\u0938\u094d\u0938\u0947-\u0915\u0939\u093e\u0928\u093f\u092f\u094b\u0902 \u092a\u0930 \u0906\u0927\u093e\u0930\u093f\u0924 \u0938\u093e\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0915\u0940 \u0938\u092e\u0938\u094d\u092f\u093e<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0915 \u092c\u091a\u094d\u091a\u093e \u0909\u092a\u0938\u094d\u0925\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092e\u091c\u092c\u0942\u0924<\/li>\n\n\n\n<li>\u0914\u0930 \u0924\u0947\u091c<\/li>\n\n\n\n<li>\u0905\u0927\u093f\u0915 \u090a\u0930\u094d\u091c\u093e\u0935\u093e\u0928<\/li>\n\n\n\n<li>\u0914\u0930 \u0905\u0927\u093f\u0915 \u0938\u094d\u0925\u093f\u0930<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u0910\u0938\u0947 \u0915\u093e\u0930\u0923\u094b\u0902 \u0938\u0947 \u091c\u093f\u0928\u0915\u093e \u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u0915\u094b\u0908 \u0938\u0902\u092c\u0902\u0927 \u0928\u0939\u0940\u0902 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0928 \u0915\u093e\u0930\u0915\u094b\u0902 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0935\u093f\u0915\u093e\u0938<\/li>\n\n\n\n<li>\u092d\u094c\u0924\u093f\u0915 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e<\/li>\n\n\n\n<li>\u0915\u0949\u0930\u094d\u091f\u093f\u0915\u094b\u0938\u094d\u091f\u0947\u0930\u0949\u0907\u0921 \u0915\u093e \u0909\u092a\u092f\u094b\u0917<\/li>\n\n\n\n<li>\u092a\u094d\u0930\u0947\u0930\u0923\u093e<\/li>\n\n\n\n<li>\u092a\u094d\u0930\u093e\u0915\u0943\u0924\u093f\u0915 \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928\u0936\u0940\u0932\u0924\u093e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0915 \u091b\u094b\u091f\u0940 \u0935\u0940\u0921\u093f\u092f\u094b \u0915\u094d\u0932\u093f\u092a \u0938\u0947 \u092f\u0939 \u0928\u093f\u0930\u094d\u0927\u093e\u0930\u093f\u0924 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u092e\u0947\u0902 \u0915\u094b\u0908 \u092c\u0926\u0932\u093e\u0935 \u0906\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902\u0964.<\/p>\n\n\n\n<h3 id=\"objective-biomarkers-matter-more\" class=\"wp-block-heading\">\u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f\u092a\u0942\u0930\u094d\u0923 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930 \u0905\u0927\u093f\u0915 \u092e\u093e\u092f\u0928\u0947 \u0930\u0916\u0924\u0947 \u0939\u0948\u0902<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u0940 \u092a\u093e\u0930\u0926\u0930\u094d\u0936\u0940 \u0930\u093f\u092a\u094b\u0930\u094d\u091f\u093f\u0902\u0917 \u0915\u093e \u0905\u0928\u0941\u0930\u094b\u0927 \u0915\u0930\u0928\u093e \u091a\u093e\u0939\u093f\u090f:<\/p>\n\n\n\n<h4 id=\"ck-creatine-kinase\" class=\"wp-block-heading\">\u0938\u0940\u0915\u0947 (\u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c)<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u092e\u0947\u0902 \u0938\u0940\u0915\u0947 \u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u092c \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u0915\u094b\u0936\u093f\u0915\u093e\u090f\u0902 \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u0939\u094b \u091c\u093e\u0924\u0940 \u0939\u0948\u0902, \u0924\u094b \u0938\u0940\u0915\u0947 \u0930\u0915\u094d\u0924\u092a\u094d\u0930\u0935\u093e\u0939 \u092e\u0947\u0902 \u0930\u093f\u0938 \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092c\u093e\u0926 \u0938\u0940\u0915\u0947 \u0915\u093e \u0938\u094d\u0924\u0930 \u0915\u092e \u0939\u094b\u0928\u093e \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0915\u094d\u0937\u0924\u093f \u092e\u0947\u0902 \u0915\u092e\u0940 \u0915\u093e \u0938\u0902\u0915\u0947\u0924 \u0926\u0947 \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h4 id=\"ast-and-alt\" class=\"wp-block-heading\">\u090f\u090f\u0938\u091f\u0940 \u0914\u0930 \u090f\u090f\u0932\u091f\u0940<\/h4>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u090f\u0938\u091f\u0940 \u0914\u0930 \u090f\u090f\u0932\u091f\u0940 \u0915\u094b \u0905\u0915\u094d\u0938\u0930 \u0932\u093f\u0935\u0930 \u090f\u0902\u091c\u093e\u0907\u092e \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0926\u0947\u0916\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u092e\u0947\u0902, \u092c\u0922\u093c\u0947 \u0939\u0941\u090f \u090f\u090f\u0938\u091f\u0940 \u0914\u0930 \u090f\u090f\u0932\u091f\u0940 \u0915\u093e \u0915\u093e\u0930\u0923 \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u090a\u0924\u0915 \u092d\u0940 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0925 \u0907\u0928 \u0938\u0902\u0915\u0947\u0924\u0915\u094b\u0902 \u092a\u0930 \u0928\u091c\u093c\u0930 \u0930\u0916\u0928\u0947 \u0938\u0947 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0938\u094d\u0935\u093e\u0938\u094d\u0925\u094d\u092f \u0914\u0930 \u0909\u092a\u091a\u093e\u0930 \u0915\u0940 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0926\u094b\u0928\u094b\u0902 \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f Elevidys \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u092b\u093e\u0907\u092c\u0930 \u0915\u0940 \u0930\u0915\u094d\u0937\u093e \u0915\u0930\u0924\u093e \u0939\u0948, \u0924\u094b \u0915\u0908 \u0935\u093f\u0936\u0947\u0937\u091c\u094d\u091e \u0924\u0930\u094d\u0915 \u0926\u0947\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u0947 \u0938\u093e\u0925-\u0938\u093e\u0925 CK \u0930\u0941\u091d\u093e\u0928\u094b\u0902 \u092a\u0930 \u092d\u0940 \u0909\u0924\u0928\u093e \u0939\u0940 \u0927\u094d\u092f\u093e\u0928 \u0926\u093f\u092f\u093e \u091c\u093e\u0928\u093e \u091a\u093e\u0939\u093f\u090f\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/ck-levels-after-duchenne-gene-therapy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092e\u0947\u0902 \u0935\u0940\u0921\u093f\u092f\u094b \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 CK, AST \u0914\u0930 ALT \u0921\u0947\u091f\u093e \u0915\u094d\u092f\u094b\u0902 \u0905\u0927\u093f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0902?<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"are-nsaa-scores-enough-to-measure-success\" class=\"wp-block-heading\">\u0915\u094d\u092f\u093e \u090f\u0928\u090f\u0938\u090f\u090f \u0915\u0947 \u0905\u0902\u0915 \u0938\u092b\u0932\u0924\u093e \u092e\u093e\u092a\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092a\u0930\u094d\u092f\u093e\u092a\u094d\u0924 \u0939\u0948\u0902?<\/h2>\n\n\n\n<h3 id=\"what-is-nsaa\" class=\"wp-block-heading\">\u090f\u0928\u090f\u0938\u090f\u090f \u0915\u094d\u092f\u093e \u0939\u0948?<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0928\u0949\u0930\u094d\u0925 \u0938\u094d\u091f\u093e\u0930 \u090f\u092e\u094d\u092c\u0941\u0932\u0947\u091f\u0930\u0940 \u0905\u0938\u0947\u0938\u092e\u0947\u0902\u091f \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0935\u094d\u092f\u093e\u092a\u0915 \u0930\u0942\u092a \u0938\u0947 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0917\u0924\u093f\u0935\u093f\u0927\u093f\u092f\u094b\u0902 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0924\u093e \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0916\u0921\u093c\u0947<\/li>\n\n\n\n<li>\u091a\u0932\u0928\u093e<\/li>\n\n\n\n<li>\u0906\u0930\u094b\u0939\u0923<\/li>\n\n\n\n<li>\u0915\u0942\u0926<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0909\u091a\u094d\u091a \u0938\u094d\u0915\u094b\u0930 \u092c\u0947\u0939\u0924\u0930 \u092e\u094b\u091f\u0930 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0937\u092e\u0924\u093e \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0924\u093e \u0939\u0948\u0964 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" target=\"_blank\" data-type=\"post\" data-id=\"4959\" rel=\"noreferrer noopener\">\u090f\u0928\u090f\u0938\u090f\u090f \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/p>\n\n\n\n<h3 id=\"the-limitations-of-nsaa\" class=\"wp-block-heading\">\u090f\u0928\u090f\u0938\u090f\u090f \u0915\u0940 \u0938\u0940\u092e\u093e\u090f\u0901<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0928\u090f\u0938\u090f\u090f \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u093e\u0930\u0915\u094b\u0902 \u0938\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0906\u092f\u0941<\/li>\n\n\n\n<li>\u092a\u094d\u0930\u0947\u0930\u0923\u093e<\/li>\n\n\n\n<li>\u0925\u0915\u093e\u0928<\/li>\n\n\n\n<li>\u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928\u0915\u0930\u094d\u0924\u093e \u0915\u0947 \u0905\u0902\u0924\u0930<\/li>\n\n\n\n<li>\u0938\u0940\u0916\u0928\u0947 \u0915\u0947 \u092a\u094d\u0930\u092d\u093e\u0935<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u093f\u0938\u0940 \u092c\u091a\u094d\u091a\u0947 \u092e\u0947\u0902 \u0936\u093e\u0930\u0940\u0930\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0915\u094b\u0908 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0938\u0941\u0927\u093e\u0930 \u0939\u0941\u090f \u092c\u093f\u0928\u093e \u092d\u0940 \u0909\u0938\u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u092e\u0947\u0902 \u0905\u0938\u094d\u0925\u093e\u092f\u0940 \u0930\u0942\u092a \u0938\u0947 \u0938\u0941\u0927\u093e\u0930 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0940 \u0915\u093e\u0930\u0923\u0935\u0936, \u0915\u0908 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u090f\u0928\u090f\u0938\u090f\u090f \u0915\u0940 \u0935\u094d\u092f\u093e\u0916\u094d\u092f\u093e \u091c\u0948\u0935\u093f\u0915 \u092e\u093e\u0930\u094d\u0915\u0930\u094b\u0902 \u0915\u0947 \u0938\u093e\u0925-\u0938\u093e\u0925 \u0915\u0940 \u091c\u093e\u0928\u0940 \u091a\u093e\u0939\u093f\u090f\u0964.<\/p>\n\n\n\n<h3 id=\"why-dystrophin-production-matters\" class=\"wp-block-heading\">\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0905\u0902\u0924\u0924\u0903, \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u0915\u092e\u0940 \u0915\u0947 \u0915\u093e\u0930\u0923 \u0939\u094b\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u094b \u092a\u094d\u0930\u0924\u093f\u0938\u094d\u0925\u093e\u092a\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u0940 \u0917\u0908 \u0925\u0947\u0930\u0947\u092a\u0940 \u092e\u0947\u0902 \u0906\u0926\u0930\u094d\u0936 \u0930\u0942\u092a \u0938\u0947 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0935\u093f\u0936\u0947\u0937\u0924\u093e\u090f\u0902 \u0939\u094b\u0928\u0940 \u091a\u093e\u0939\u093f\u090f:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092e\u091c\u092c\u0942\u0924 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0909\u0924\u094d\u092a\u093e\u0926\u0928<\/li>\n\n\n\n<li>\u0928\u093f\u0930\u0902\u0924\u0930 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f<\/li>\n\n\n\n<li>\u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u093e \u0938\u0902\u0930\u0915\u094d\u0937\u0923<\/li>\n\n\n\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0932\u093e\u092d<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u090f\u0915 \u092a\u094d\u0930\u092e\u0941\u0916 \u0915\u093e\u0930\u0923 \u0925\u093e \u091c\u093f\u0938\u0915\u0947 \u091a\u0932\u0924\u0947 FDA \u0915\u0947 \u0938\u092e\u0940\u0915\u094d\u0937\u0915\u094b\u0902 \u0928\u0947 Elevidys \u0915\u094b \u091c\u0948\u0935\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0938\u0915\u094d\u0930\u093f\u092f \u092e\u093e\u0928\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0907\u0938 \u092c\u093e\u0924 \u092a\u0930 \u092c\u0939\u0938 \u091c\u093e\u0930\u0940 \u0930\u0916\u0947 \u0939\u0941\u090f \u0939\u0948\u0902 \u0915\u093f \u0938\u093e\u0930\u094d\u0925\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0932\u093e\u092d \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u0915\u093f\u0924\u0928\u0940 \u092e\u093e\u0924\u094d\u0930\u093e \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/biomarkers-in-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0915\u0947\u0935\u0932 \u090f\u0928\u090f\u0938\u090f\u090f \u0939\u0940 \u092a\u0930\u094d\u092f\u093e\u092a\u094d\u0924 \u0928\u0939\u0940\u0902 \u0939\u0948<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"how-many-extra-years-could-elevidys-add\" class=\"wp-block-heading\">Elevidys \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u092e\u0947\u0930\u093e \u092c\u0947\u091f\u093e \u0915\u093f\u0924\u0928\u0947 \u0914\u0930 \u0938\u093e\u0932 \u091c\u0940\u0935\u093f\u0924 \u0930\u0939\u0947\u0917\u093e?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0936\u093e\u092f\u0926 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0926\u094d\u0935\u093e\u0930\u093e \u092a\u0942\u091b\u093e \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u093e \u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092a\u094d\u0930\u0936\u094d\u0928 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0926\u0941\u0930\u094d\u092d\u093e\u0917\u094d\u092f\u0935\u0936, \u0915\u093f\u0938\u0940 \u0915\u094b \u0928\u0939\u0940\u0902 \u092a\u0924\u093e\u0964.<\/p>\n\n\n\n<h3 id=\"no-survival-benefit-has-yet-been-proven\" class=\"wp-block-heading\">\u0905\u092d\u0940 \u0924\u0915 \u0907\u0938\u0938\u0947 \u091c\u0940\u0935\u0928 \u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0915\u094b\u0908 \u0932\u093e\u092d \u0938\u093f\u0926\u094d\u0927 \u0928\u0939\u0940\u0902 \u0939\u0941\u0906 \u0939\u0948\u0964<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u0915\u0947 \u0905\u0938\u094d\u0924\u093f\u0924\u094d\u0935 \u092e\u0947\u0902 \u0906\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0905\u092d\u0940 \u0924\u0915 \u092f\u0939 \u0938\u093e\u092c\u093f\u0924 \u0928\u0939\u0940\u0902 \u0939\u094b \u092a\u093e\u092f\u093e \u0939\u0948 \u0915\u093f \u092f\u0939 \u091c\u0940\u0935\u0928 \u092a\u094d\u0930\u0924\u094d\u092f\u093e\u0936\u093e \u0915\u094b \u092c\u0922\u093c\u093e\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>2 \u0938\u093e\u0932<\/li>\n\n\n\n<li>5 \u0938\u093e\u0932<\/li>\n\n\n\n<li>10 \u0935\u0930\u094d\u0937<\/li>\n\n\n\n<li>20 \u0938\u093e\u0932<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u091c\u0940\u0935\u0928 \u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0905\u0927\u094d\u092f\u092f\u0928 \u0905\u092d\u0940 \u0924\u0915 \u092e\u094c\u091c\u0942\u0926 \u0939\u0940 \u0928\u0939\u0940\u0902 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u0940\u0935\u0928\u0915\u093e\u0932 \u092e\u0947\u0902 \u0938\u091f\u0940\u0915 \u0935\u0943\u0926\u094d\u0927\u093f \u0915\u0947 \u0938\u0902\u092c\u0902\u0927 \u092e\u0947\u0902 \u0915\u094b\u0908 \u092d\u0940 \u0926\u093e\u0935\u093e \u092b\u093f\u0932\u0939\u093e\u0932 \u0905\u091f\u0915\u0932\u092c\u093e\u091c\u0940 \u0939\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 id=\"what-clinical-trials-suggest\" class=\"wp-block-heading\">\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0938\u0947 \u0915\u094d\u092f\u093e \u092a\u0924\u093e \u091a\u0932\u0924\u093e \u0939\u0948<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093f\u092f\u093e \u0905\u0928\u0941\u0935\u0930\u094d\u0924\u0940 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923\u094b\u0902 \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u0924\u093e \u0939\u0948 \u0915\u093f Elevidys \u092a\u094d\u0930\u093e\u0915\u0943\u0924\u093f\u0915 \u0907\u0924\u093f\u0939\u093e\u0938 \u0938\u092e\u0942\u0939\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f \u0932\u0902\u092c\u0947 \u0938\u092e\u092f \u0924\u0915 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0927\u0940\u092e\u0940 \u0939\u094b\u0928\u0947 \u0915\u0940 \u092a\u0941\u0937\u094d\u091f\u093f \u0939\u094b \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b \u0938\u0948\u0926\u094d\u0927\u093e\u0902\u0924\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0907\u0938\u0938\u0947 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u092e\u0947\u0902 \u0926\u0947\u0930\u0940 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u0915\u093e \u0928\u0941\u0915\u0938\u093e\u0928<\/li>\n\n\n\n<li>\u0936\u094d\u0935\u0938\u0928 \u0938\u0902\u092c\u0902\u0927\u0940 \u0917\u093f\u0930\u093e\u0935\u091f<\/li>\n\n\n\n<li>\u0939\u0943\u0926\u092f \u0938\u0902\u092c\u0902\u0927\u0940 \u091c\u091f\u093f\u0932\u0924\u093e\u090f\u0901<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u091c\u0940\u0935\u0928\u0915\u093e\u0932 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0915\u094b \u0938\u093e\u092c\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0915\u0908 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0935\u0930\u094d\u0937\u094b\u0902 \u0915\u0947 \u0905\u0935\u0932\u094b\u0915\u0928 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u094b\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u092f\u0939 \u0938\u092e\u091d\u0928\u093e \u091a\u093e\u0939\u093f\u090f \u0915\u093f \u0935\u0930\u094d\u0924\u092e\u093e\u0928 \u0938\u093e\u0915\u094d\u0937\u094d\u092f \u091c\u0948\u0935\u093f\u0915 \u0917\u0924\u093f\u0935\u093f\u0927\u093f \u0914\u0930 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0932\u093e\u092d \u0915\u094b \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 - \u0928 \u0915\u093f \u091c\u0940\u0935\u0928 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0915\u0947 \u0938\u093f\u0926\u094d\u0927 \u092a\u094d\u0930\u092e\u093e\u0923 \u0915\u094b\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/elevidys-gene-therapy-efficacy-in-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0938\u0947 \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u092e\u0947\u0902 \u0915\u093f\u0924\u0928\u093e \u0938\u0941\u0927\u093e\u0930 \u0939\u094b\u0924\u093e \u0939\u0948?<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"is-elevidys-worth-3-2-million\" class=\"wp-block-heading\">\u0915\u094d\u092f\u093e Elevidys \u0915\u0940 \u0915\u0940\u092e\u0924 3.2 \u092e\u093f\u0932\u093f\u092f\u0928 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0915\u0947 \u0905\u0928\u0941\u0938\u093e\u0930, Elevidys \u0915\u0947 \u090f\u0915 \u0909\u092a\u091a\u093e\u0930 \u0915\u0940 \u0932\u093e\u0917\u0924 \u0932\u0917\u092d\u0917 32 \u0932\u093e\u0916 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0940 \u0935\u091c\u0939 \u0938\u0947 \u092f\u0939 \u0907\u0924\u093f\u0939\u093e\u0938 \u0915\u0940 \u0938\u092c\u0938\u0947 \u092e\u0939\u0902\u0917\u0940 \u0926\u0935\u093e\u0913\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 id=\"the-economic-question\" class=\"wp-block-heading\">\u0906\u0930\u094d\u0925\u093f\u0915 \u092a\u094d\u0930\u0936\u094d\u0928<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092e\u0942\u0932\u094d\u092f \u0907\u0928 \u092c\u093e\u0924\u094b\u0902 \u092a\u0930 \u0928\u093f\u0930\u094d\u092d\u0930 \u0915\u0930\u0924\u093e \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0932\u093e\u092d \u0915\u0940 \u092e\u093e\u0924\u094d\u0930\u093e<\/li>\n\n\n\n<li>\u0932\u093e\u092d \u0915\u0940 \u0905\u0935\u0927\u093f<\/li>\n\n\n\n<li>\u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932<\/li>\n\n\n\n<li>\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0935\u093f\u0915\u0932\u094d\u092a<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f \u0915\u094b\u0908 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f \u0938\u094d\u0935\u0938\u094d\u0925 \u091c\u0940\u0935\u0928 \u092e\u0947\u0902 \u0915\u0908 \u0926\u0936\u0915 \u091c\u094b\u0921\u093c \u0926\u0947\u0924\u0940 \u0939\u0948, \u0924\u094b \u092c\u0939\u0941\u0924 \u0938\u0947 \u0932\u094b\u0917 \u0924\u0930\u094d\u0915 \u0926\u0947\u0902\u0917\u0947 \u0915\u093f \u092f\u0939 \u0938\u093e\u0930\u094d\u0925\u0915 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f \u0932\u093e\u092d \u092e\u093e\u092e\u0942\u0932\u0940 \u0938\u093e\u092c\u093f\u0924 \u0939\u094b\u0924\u093e \u0939\u0948, \u0924\u094b \u092e\u0942\u0932\u094d\u092f \u092a\u094d\u0930\u0938\u094d\u0924\u093e\u0935 \u0905\u0927\u093f\u0915 \u0935\u093f\u0935\u093e\u0926\u093e\u0938\u094d\u092a\u0926 \u0939\u094b \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092b\u093f\u0932\u0939\u093e\u0932, \u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u092e\u0942\u0932\u094d\u092f \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u092c\u0928\u093e \u0939\u0941\u0906 \u0939\u0948 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0905\u092d\u0940 \u092d\u0940 \u0905\u091c\u094d\u091e\u093e\u0924 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"why-is-elevidys-approved-by-the-fda-but-not-by-the-ema\" class=\"wp-block-heading\">Elevidys \u0915\u094b FDA \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u094d\u092f\u094b\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 EMA \u0926\u094d\u0935\u093e\u0930\u093e \u0928\u0939\u0940\u0902?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u092a\u0930\u093f\u0935\u093e\u0930 \u092f\u0939 \u092e\u093e\u0928 \u0932\u0947\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u090f\u0915 \u0928\u093f\u092f\u093e\u092e\u0915 \u0926\u094d\u0935\u093e\u0930\u093e \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932\u0928\u0947 \u0938\u0947 \u0905\u0928\u094d\u092f \u091c\u0917\u0939\u094b\u0902 \u092a\u0930 \u092d\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0939\u092e\u0947\u0936\u093e \u0938\u0939\u0940 \u0928\u0939\u0940\u0902 \u0939\u094b\u0924\u093e\u0964.<\/p>\n\n\n\n<h3 id=\"different-regulatory-standards\" class=\"wp-block-heading\">\u0935\u093f\u092d\u093f\u0928\u094d\u0928 \u0928\u093f\u092f\u093e\u092e\u0915 \u092e\u093e\u0928\u0915<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">FDA \u0914\u0930 EMA \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u091c\u094b\u0916\u093f\u092e \u0938\u0939\u0928\u0936\u0940\u0932\u0924\u093e<\/li>\n\n\n\n<li>\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e<\/li>\n\n\n\n<li>\u0938\u093e\u0902\u0916\u094d\u092f\u093f\u0915\u0940\u092f \u092a\u094d\u0930\u092e\u093e\u0923<\/li>\n\n\n\n<li>\u0905\u0927\u0942\u0930\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0905\u0932\u0917-\u0905\u0932\u0917 \u0924\u0930\u0940\u0915\u0947 \u0938\u0947\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">FDA \u0928\u0947 \u0910\u0924\u093f\u0939\u093e\u0938\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0909\u0928 \u0917\u0902\u092d\u0940\u0930 \u092c\u0940\u092e\u093e\u0930\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e\u0913\u0902 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0907\u091a\u094d\u091b\u093e \u0926\u093f\u0916\u093e\u0908 \u0939\u0948 \u091c\u093f\u0928\u0915\u0947 \u0932\u093f\u090f \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0935\u093f\u0915\u0932\u094d\u092a \u0909\u092a\u0932\u092c\u094d\u0927 \u0928\u0939\u0940\u0902 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0942\u0930\u094b\u092a\u0940\u092f \u0928\u093f\u092f\u093e\u092e\u0915 \u0915\u092d\u0940-\u0915\u092d\u0940 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0905\u0927\u093f\u0915 \u092e\u091c\u092c\u0942\u0924 \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u0938\u093e\u0915\u094d\u0937\u094d\u092f \u0915\u0940 \u092e\u093e\u0902\u0917 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0915\u093e \u092f\u0939 \u092e\u0924\u0932\u092c \u0928\u0939\u0940\u0902 \u0939\u0948 \u0915\u093f \u090f\u0915 \u090f\u091c\u0947\u0902\u0938\u0940 \u0938\u0939\u0940 \u0939\u0948 \u0914\u0930 \u0926\u0942\u0938\u0930\u0940 \u0917\u0932\u0924\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0909\u092a\u0932\u092c\u094d\u0927 \u0938\u093e\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0915\u0940 \u0935\u093f\u092d\u093f\u0928\u094d\u0928 \u0935\u094d\u092f\u093e\u0916\u094d\u092f\u093e\u0913\u0902 \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/why-elevidys-was-not-approved-by-the-european-medicines-agency-ema\/\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys \u0915\u094b \u092f\u0942\u0930\u094b\u092a\u0940\u092f \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u090f\u091c\u0947\u0902\u0938\u0940 (EMA) \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u094d\u092f\u094b\u0902 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e?<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"could-receiving-elevidys-limit-future-treatment-options\" class=\"wp-block-heading\">\u0915\u094d\u092f\u093e Elevidys \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0935\u093f\u0915\u0932\u094d\u092a \u0938\u0940\u092e\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u092a\u094d\u0930\u0936\u094d\u0928 \u092a\u0930 \u091c\u093f\u0924\u0928\u0940 \u091a\u0930\u094d\u091a\u093e \u0939\u094b\u0928\u0940 \u091a\u093e\u0939\u093f\u090f, \u0909\u0924\u0928\u0940 \u0905\u0915\u094d\u0938\u0930 \u0928\u0939\u0940\u0902 \u0939\u094b\u0924\u0940\u0964.<\/p>\n\n\n\n<h3 id=\"the-aav-antibody-problem\" class=\"wp-block-heading\">\u090f\u090f\u0935\u0940 \u090f\u0902\u091f\u0940\u092c\u0949\u0921\u0940 \u0938\u092e\u0938\u094d\u092f\u093e<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u092e\u0947\u0902 AAV \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092c\u093e\u0926, \u092a\u094d\u0930\u0924\u093f\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u0923\u093e\u0932\u0940 \u0909\u0938 \u0915\u093e\u0930\u0915 \u0915\u0947 \u0916\u093f\u0932\u093e\u092b \u090f\u0902\u091f\u0940\u092c\u0949\u0921\u0940 \u0935\u093f\u0915\u0938\u093f\u0924 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0938\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0926\u094b\u092c\u093e\u0930\u093e \u0916\u0941\u0930\u093e\u0915 \u0926\u0947\u0928\u0947 \u092e\u0947\u0902 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0902 \u0909\u0924\u094d\u092a\u0928\u094d\u0928 \u0939\u094b\u0924\u0940 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<h3 id=\"potential-impact-on-future-gene-therapies\" class=\"wp-block-heading\">\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u0930 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092a\u094d\u0930\u092d\u093e\u0935<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940 \u0915\u0940 \u0915\u0908 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092d\u0940 \u090f\u090f\u0935\u0940 \u0924\u0915\u0928\u0940\u0915\u094b\u0902 \u092a\u0930 \u0928\u093f\u0930\u094d\u092d\u0930 \u0915\u0930\u0924\u0940 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u092a\u0942\u091b\u0928\u093e \u091a\u093e\u0939\u093f\u090f:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0915\u094d\u092f\u093e \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0947 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u092e\u0947\u0902 \u092d\u0940 \u0907\u0938\u0940 \u0924\u0930\u0939 \u0915\u0947 \u0935\u0948\u0915\u094d\u091f\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u092f\u093e \u091c\u093e\u090f\u0917\u093e?<\/li>\n\n\n\n<li>\u0915\u094d\u092f\u093e \u092e\u0948\u0902 \u0905\u092c \u092d\u0940 \u092a\u093e\u0924\u094d\u0930 \u0930\u0939\u0942\u0902\u0917\u093e?<\/li>\n\n\n\n<li>\u0915\u094d\u092f\u093e \u0916\u0941\u0930\u093e\u0915 \u0915\u094b \u0926\u094b\u092c\u093e\u0930\u093e \u0928\u093f\u0930\u094d\u0927\u093e\u0930\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0930\u0923\u0928\u0940\u0924\u093f\u092f\u093e\u0901 \u0935\u093f\u0915\u0938\u093f\u0924 \u0915\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948\u0902?<\/li>\n\n\n\n<li>\u0915\u094c\u0928-\u0915\u094c\u0928 \u0938\u0947 \u0935\u093f\u0915\u0932\u094d\u092a \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902?<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0947 \u091a\u0930\u094d\u091a\u093e\u090f\u0902 \u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0939\u094b\u0928\u0940 \u091a\u093e\u0939\u093f\u090f, \u092c\u093e\u0926 \u092e\u0947\u0902 \u0928\u0939\u0940\u0902\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"what-new-duchenne-therapies-are-coming\" class=\"wp-block-heading\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0932\u093f\u090f \u0915\u094c\u0928-\u0915\u094c\u0928 \u0938\u0940 \u0928\u0908 \u0909\u092a\u091a\u093e\u0930 \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0902 \u0906 \u0930\u0939\u0940 \u0939\u0948\u0902?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092a\u093e\u0907\u092a\u0932\u093e\u0907\u0928 \u0924\u0947\u091c\u0940 \u0938\u0947 \u0935\u093f\u0915\u0938\u093f\u0924 \u0939\u094b \u0930\u0939\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 id=\"next-generation-gene-therapies\" class=\"wp-block-heading\">\u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940 \u0915\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u0915\u0902\u092a\u0928\u093f\u092f\u093e\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u092c\u0922\u093c\u093e\u0928\u0947 \u092f\u093e \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0938\u0947 \u0909\u0928\u094d\u0928\u0924 \u0924\u0930\u0940\u0915\u0947 \u0935\u093f\u0915\u0938\u093f\u0924 \u0915\u0930 \u0930\u0939\u0940 \u0939\u0948\u0902\u0964 \u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0932\u093f\u090f \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0906\u0917\u093e\u092e\u0940 \u0928\u0908 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940<\/a><\/p>\n\n\n\n<h3 id=\"cell-therapies\" class=\"wp-block-heading\">\u0938\u0947\u0932 \u0925\u0947\u0930\u0947\u092a\u0940<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e \u0910\u0938\u0940 \u0915\u094b\u0936\u093f\u0915\u093e-\u0906\u0927\u093e\u0930\u093f\u0924 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0915\u0940 \u0916\u094b\u091c \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902 \u091c\u094b \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u090a\u0924\u0915\u094b\u0902 \u0915\u094b \u092a\u0941\u0928\u0930\u094d\u091c\u0940\u0935\u093f\u0924 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<h3 id=\"m-rna-therapies\" class=\"wp-block-heading\">mRNA \u0925\u0947\u0930\u0947\u092a\u0940<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0909\u092d\u0930\u0924\u0947 \u0939\u0941\u090f mRNA \u0926\u0943\u0937\u094d\u091f\u093f\u0915\u094b\u0923\u094b\u0902 \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0947 \u092c\u091c\u093e\u092f \u092a\u0942\u0930\u094d\u0923-\u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0938\u0902\u092d\u0935 \u092c\u0928\u093e\u0928\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0930\u0923\u0928\u0940\u0924\u093f \u0928\u0947 \u0915\u093e\u092b\u0940 \u0927\u094d\u092f\u093e\u0928 \u0906\u0915\u0930\u094d\u0937\u093f\u0924 \u0915\u093f\u092f\u093e \u0939\u0948 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092f\u0939 \u090f\u090f\u0935\u0940 \u0935\u0948\u0915\u094d\u091f\u0930 \u0938\u0947 \u091c\u0941\u0921\u093c\u0940 \u0906\u0915\u093e\u0930 \u0938\u0902\u092c\u0902\u0927\u0940 \u0938\u0940\u092e\u093e\u0913\u0902 \u0915\u094b \u0926\u0942\u0930 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 id=\"gene-editing\" class=\"wp-block-heading\">\u091c\u0940\u0928 \u0938\u0902\u092a\u093e\u0926\u0928<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">CRISPR \u092a\u0930 \u0906\u0927\u093e\u0930\u093f\u0924 \u0926\u0943\u0937\u094d\u091f\u093f\u0915\u094b\u0923 \u0905\u092d\u0940 \u092d\u0940 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0939\u0948\u0902, \u0932\u0947\u0915\u093f\u0928 \u0938\u094d\u0925\u093e\u092f\u0940 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0938\u0941\u0927\u093e\u0930 \u0915\u0940 \u0938\u0902\u092d\u093e\u0935\u0928\u093e \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<h3 id=\"full-length-dystrophin-strategies\" class=\"wp-block-heading\">\u092a\u0942\u0930\u094d\u0923-\u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0940 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0930\u0923\u0928\u0940\u0924\u093f\u092f\u093e\u0901<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u092c\u0939\u093e\u0932\u0940 \u0915\u094b \u0905\u0902\u0924\u093f\u092e \u0932\u0915\u094d\u0937\u094d\u092f \u092e\u093e\u0928\u0924\u0947 \u0939\u0948\u0902 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092f\u0939 \u092a\u094d\u0930\u093e\u0915\u0943\u0924\u093f\u0915 \u091c\u0940\u0935 \u0935\u093f\u091c\u094d\u091e\u093e\u0928 \u0938\u0947 \u0938\u092c\u0938\u0947 \u0905\u0927\u093f\u0915 \u092e\u093f\u0932\u0924\u093e \u091c\u0941\u0932\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0935\u093f\u0915\u0938\u093f\u0924 \u0939\u094b\u0928\u0947 \u0935\u093e\u0932\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0902 \u0907\u0938 \u0932\u0915\u094d\u0937\u094d\u092f \u0915\u094b \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930 \u092a\u093e\u090f\u0902\u0917\u0940 \u092f\u093e \u0928\u0939\u0940\u0902, \u092f\u0939 \u0905\u092d\u0940 \u0924\u0915 \u0905\u091c\u094d\u091e\u093e\u0924 \u0939\u0948\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"why-families-continue-campaigning-for-elevidys\" class=\"wp-block-heading\">\u092a\u0930\u093f\u0935\u093e\u0930 Elevidys \u0915\u0947 \u0932\u093f\u090f \u0905\u092d\u093f\u092f\u093e\u0928 \u0915\u094d\u092f\u094b\u0902 \u091c\u093e\u0930\u0940 \u0930\u0916\u0947 \u0939\u0941\u090f \u0939\u0948\u0902?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0906\u0932\u094b\u091a\u0915 \u0915\u092d\u0940-\u0915\u092d\u0940 \u092f\u0939 \u092e\u093e\u0928 \u0932\u0947\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u092a\u0930\u093f\u0935\u093e\u0930 \u0907\u0938 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0905\u0928\u092d\u093f\u091c\u094d\u091e \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0927\u093e\u0930\u0923\u093e \u0905\u0915\u094d\u0938\u0930 \u0905\u0928\u0941\u091a\u093f\u0924 \u0939\u094b\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0905\u0927\u093f\u0915\u093e\u0902\u0936 \u092a\u0930\u093f\u0935\u093e\u0930 \u092f\u0939 \u0938\u092e\u091d\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0928\u093f\u0930\u0902\u0924\u0930 \u092a\u094d\u0930\u0917\u0924\u093f\u0936\u0940\u0932 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u0930 \u0938\u093e\u0932 \u092e\u093e\u092f\u0928\u0947 \u0930\u0916\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u0930 \u092e\u0939\u0940\u0928\u093e \u092e\u093e\u092f\u0928\u0947 \u0930\u0916\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092e\u093e\u0924\u093e-\u092a\u093f\u0924\u093e \u0905\u0915\u094d\u0938\u0930 \u0907\u0932\u093e\u091c \u0915\u093e \u0935\u093f\u0915\u0932\u094d\u092a \u0907\u0938\u0932\u093f\u090f \u091a\u0941\u0928\u0924\u0947 \u0939\u0948\u0902 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0909\u0928\u094d\u0939\u0947\u0902 \u0921\u0930 \u0939\u094b\u0924\u093e \u0939\u0948 \u0915\u093f \u0935\u0947 \u090f\u0915 \u0910\u0938\u0947 \u0905\u0935\u0938\u0930 \u0915\u094b \u0916\u094b \u0926\u0947\u0902\u0917\u0947 \u091c\u094b \u0936\u093e\u092f\u0926 \u0915\u092d\u0940 \u0935\u093e\u092a\u0938 \u0928 \u0906\u090f\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u092e\u0930\u094d\u0925\u0915\u094b\u0902 \u0915\u093e \u0924\u0930\u094d\u0915 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092a\u094d\u0930\u0924\u0940\u0915\u094d\u0937\u093e \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u091c\u094b\u0916\u093f\u092e \u0939\u094b\u0924\u0947 \u0939\u0948\u0902<\/li>\n\n\n\n<li>\u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u091c\u093e\u0930\u0940 \u0939\u0948<\/li>\n\n\n\n<li>\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901 \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u0939\u0948\u0902\u0964<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u0902\u0936\u092f\u0935\u093e\u0926\u093f\u092f\u094b\u0902 \u0915\u093e \u0924\u0930\u094d\u0915 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0938\u092c\u0942\u0924 \u0905\u092d\u0940 \u092d\u0940 \u0905\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0902<\/li>\n\n\n\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0932\u093e\u092d \u0905\u091c\u094d\u091e\u093e\u0924 \u0939\u0948<\/li>\n\n\n\n<li>\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901 \u0905\u0927\u093f\u0915 \u0932\u093e\u092d \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0902\u0964<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0926\u094b\u0928\u094b\u0902 \u0939\u0940 \u0926\u0943\u0937\u094d\u091f\u093f\u0915\u094b\u0923 \u0938\u092e\u091d\u0928\u0947 \u092f\u094b\u0917\u094d\u092f \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"questions-every-family-should-ask-before-choosing-elevidys\" class=\"wp-block-heading\">Elevidys \u091a\u0941\u0928\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0939\u0930 \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u094b \u092f\u0947 \u0938\u0935\u093e\u0932 \u092a\u0942\u091b\u0928\u0947 \u091a\u093e\u0939\u093f\u090f<\/h2>\n\n\n\n<ol class=\"wp-block-list\">\n<li>\u091c\u0948\u0935\u093f\u0915 \u0932\u093e\u092d \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u092e\u093e\u0923 \u0915\u094d\u092f\u093e \u0939\u0948\u0902?<\/li>\n\n\n\n<li>\u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0932\u093e\u092d \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u0938\u093e\u0915\u094d\u0937\u094d\u092f \u0915\u094d\u092f\u093e \u0939\u0948\u0902?<\/li>\n\n\n\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0915\u094c\u0928-\u0915\u094c\u0928 \u0938\u0947 \u0906\u0902\u0915\u0921\u093c\u0947 \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u0948\u0902?<\/li>\n\n\n\n<li>\u092f\u0926\u093f \u092c\u0947\u0939\u0924\u0930 \u0909\u092a\u091a\u093e\u0930 \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b \u091c\u093e\u090f\u0902 \u0924\u094b \u0915\u094d\u092f\u093e \u0939\u094b\u0917\u093e?<\/li>\n\n\n\n<li>\u0915\u094d\u092f\u093e \u0907\u0938\u0938\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u092a\u093e\u0924\u094d\u0930\u0924\u093e \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948?<\/li>\n\n\n\n<li>\u092e\u0947\u0930\u0947 \u092c\u091a\u094d\u091a\u0947 \u092e\u0947\u0902 \u0907\u0938 \u0938\u092e\u092f \u092c\u0940\u092e\u093e\u0930\u0940 \u0915\u0947 \u0915\u094d\u092f\u093e \u0932\u0915\u094d\u0937\u0923 \u0939\u0948\u0902?<\/li>\n\n\n\n<li>\u091c\u094b\u0916\u093f\u092e-\u0932\u093e\u092d \u0915\u093e \u092f\u0939 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923 \u092e\u0947\u0930\u0947 \u092c\u091a\u094d\u091a\u0947 \u0915\u0947 \u092e\u093e\u092e\u0932\u0947 \u092e\u0947\u0902 \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u0915\u0948\u0938\u0947 \u0932\u093e\u0917\u0942 \u0939\u094b\u0924\u093e \u0939\u0948?<\/li>\n<\/ol>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u094b\u0908 \u092d\u0940 \u0938\u094b\u0936\u0932 \u092e\u0940\u0921\u093f\u092f\u093e \u0935\u0940\u0921\u093f\u092f\u094b \u0907\u0928 \u0938\u0935\u093e\u0932\u094b\u0902 \u0915\u093e \u091c\u0935\u093e\u092c \u0928\u0939\u0940\u0902 \u0926\u0947 \u0938\u0915\u0924\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0947\u0935\u0932 \u0938\u093e\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0915\u0940 \u0938\u093e\u0935\u0927\u093e\u0928\u0940\u092a\u0942\u0930\u094d\u0935\u0915 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0914\u0930 \u0905\u0928\u0941\u092d\u0935\u0940 \u0928\u094d\u092f\u0942\u0930\u094b\u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0935\u093f\u0936\u0947\u0937\u091c\u094d\u091e\u094b\u0902 \u0938\u0947 \u092a\u0930\u093e\u092e\u0930\u094d\u0936 \u0939\u0940 \u0907\u0938\u0915\u093e \u0938\u092e\u093e\u0927\u093e\u0928 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0905\u0915\u094d\u0938\u0930 \u092a\u0942\u091b\u0947 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u0936\u094d\u0928<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 id=\"conclusion\" class=\"wp-block-heading\">\u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u0915\u094b \u0932\u0947\u0915\u0930 \u091a\u0932 \u0930\u0939\u0940 \u092c\u0939\u0938 \u0906\u0927\u0941\u0928\u093f\u0915 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0915\u0940 \u0938\u092c\u0938\u0947 \u0915\u0920\u093f\u0928 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0924\u0940 \u0939\u0948: \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u092e\u0947\u0902 \u091c\u0940\u0935\u0928 \u092c\u0926\u0932\u0928\u0947 \u0935\u093e\u0932\u0947 \u0928\u093f\u0930\u094d\u0923\u092f \u0932\u0947\u0928\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u092e\u0947\u0902 \u0915\u094b\u0908 \u0938\u0902\u0926\u0947\u0939 \u0928\u0939\u0940\u0902 \u0939\u0948 \u0915\u093f Elevidys \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u0930\u0924\u093e \u0939\u0948 \u0914\u0930 \u091c\u0948\u0935\u093f\u0915 \u0938\u0915\u094d\u0930\u093f\u092f\u0924\u093e \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948\u0964 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u092b\u0949\u0932\u094b-\u0905\u092a \u0921\u0947\u091f\u093e \u0938\u0947 \u092f\u0939 \u092d\u0940 \u092a\u0924\u093e \u091a\u0932\u0924\u093e \u0939\u0948 \u0915\u093f \u0915\u092e \u0938\u0947 \u0915\u092e \u0915\u0941\u091b \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0927\u0940\u092e\u0940 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948\u0964 \u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u0909\u092a\u091a\u093e\u0930 \u0915\u0940 \u0938\u094d\u0925\u093e\u092f\u093f\u0924\u094d\u0935\u0924\u093e, \u0938\u0941\u0930\u0915\u094d\u0937\u093e, \u091c\u0940\u0935\u0928 \u0930\u0915\u094d\u0937\u093e \u0932\u093e\u092d, \u0932\u093e\u0917\u0924-\u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0914\u0930 \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0947 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u0940\u092f \u0935\u093f\u0915\u0932\u094d\u092a\u094b\u0902 \u092a\u0930 \u0907\u0938\u0915\u0947 \u092a\u094d\u0930\u092d\u093e\u0935 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092a\u094d\u0930\u0936\u094d\u0928 \u0905\u092d\u0940 \u092d\u0940 \u092c\u0928\u0947 \u0939\u0941\u090f \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u0915\u0947 \u0938\u092e\u0930\u094d\u0925\u0915 \u0905\u0915\u094d\u0938\u0930 FDA \u0915\u0940 \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f \u0914\u0930 \u0906\u0936\u093e\u091c\u0928\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937\u094b\u0902 \u0915\u093e \u0939\u0935\u093e\u0932\u093e \u0926\u0947\u0924\u0947 \u0939\u0948\u0902\u0964 \u0935\u0939\u0940\u0902, \u0906\u0932\u094b\u091a\u0915\u094b\u0902 \u0915\u093e \u0924\u0930\u094d\u0915 \u0939\u0948 \u0915\u093f CK, AST, ALT \u091c\u0948\u0938\u0947 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930\u094b\u0902, \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0914\u0930 \u091c\u0940\u0935\u0928 \u092a\u094d\u0930\u0924\u094d\u092f\u093e\u0936\u093e \u0915\u0947 \u0938\u0902\u092c\u0902\u0927 \u092e\u0947\u0902 \u0905\u0927\u093f\u0915 \u092a\u093e\u0930\u0926\u0930\u094d\u0936\u093f\u0924\u093e \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u0948\u0964 \u092f\u0947 \u0905\u0928\u0938\u0941\u0932\u091d\u0947 \u092a\u094d\u0930\u0936\u094d\u0928 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u092d\u0940\u0924\u0930 \u092c\u0939\u0938 \u0915\u094b \u0939\u0935\u093e \u0926\u0947\u0924\u0947 \u0930\u0939\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930 \u0915\u0940 \u0915\u0940\u092e\u0924 \u092e\u0947\u0902 \u092d\u093e\u0930\u0940 \u0917\u093f\u0930\u093e\u0935\u091f\u2014\u0932\u0917\u092d\u0917 15 \u092e\u0939\u0940\u0928\u094b\u0902 \u092e\u0947\u0902 122 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0938\u0947 \u0918\u091f\u0915\u0930 15 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0924\u0915\u2014\u0915\u093f\u0938\u0940 \u092d\u0940 \u091c\u0948\u0935 \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u0940 \u0915\u0902\u092a\u0928\u0940 \u0915\u0947 \u0932\u093f\u090f \u0938\u093e\u092e\u093e\u0928\u094d\u092f \u0909\u0924\u093e\u0930-\u091a\u0922\u093c\u093e\u0935 \u0928\u0939\u0940\u0902 \u0939\u0948\u0964 \u0939\u093e\u0932\u093e\u0902\u0915\u093f \u0915\u0947\u0935\u0932 \u0936\u0947\u092f\u0930 \u0915\u0947 \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 \u0938\u0947 \u092f\u0939 \u0928\u093f\u0930\u094d\u0927\u093e\u0930\u093f\u0924 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0915\u093f \u0915\u094b\u0908 \u0909\u092a\u091a\u093e\u0930 \u0915\u093e\u0930\u0917\u0930 \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902, \u0932\u0947\u0915\u093f\u0928 \u092c\u093e\u091c\u093e\u0930 \u092e\u0942\u0932\u094d\u092f \u092e\u0947\u0902 \u0907\u0924\u0928\u0940 \u092c\u0921\u093c\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u0924\u093e \u0939\u0948 \u0915\u093f \u0915\u0908 \u0928\u093f\u0935\u0947\u0936\u0915 \u0909\u092a\u0932\u092c\u094d\u0927 \u0906\u0902\u0915\u0921\u093c\u094b\u0902, \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0935\u093f\u0915\u093e\u0938, \u0928\u093f\u092f\u093e\u092e\u0915 \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e, \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u092a\u094d\u0930\u0924\u093f\u0938\u094d\u092a\u0930\u094d\u0927\u093e \u0914\u0930 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0938\u092e\u0917\u094d\u0930 \u091c\u094b\u0916\u093f\u092e-\u0932\u093e\u092d \u0905\u0928\u0941\u092a\u093e\u0924 \u0915\u094b \u0932\u0947\u0915\u0930 \u091a\u093f\u0902\u0924\u093f\u0924 \u0939\u094b \u0917\u090f \u0939\u0948\u0902\u0964 \u092f\u0947 \u091a\u093f\u0902\u0924\u093e\u090f\u0902 \u0905\u0902\u0924\u0924\u0903 \u0938\u0939\u0940 \u0938\u093e\u092c\u093f\u0924 \u0939\u094b\u0924\u0940 \u0939\u0948\u0902 \u092f\u093e \u0928\u0939\u0940\u0902, \u092f\u0939 \u0924\u094b \u0906\u0928\u0947 \u0935\u093e\u0932\u0947 \u0938\u092e\u092f \u092e\u0947\u0902 \u0939\u0940 \u092a\u0924\u093e \u091a\u0932\u0947\u0917\u093e, \u0932\u0947\u0915\u093f\u0928 \u092f\u0939 \u0917\u093f\u0930\u093e\u0935\u091f \u0938\u094d\u092a\u0937\u094d\u091f \u0930\u0942\u092a \u0938\u0947 \u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u0947 \u0935\u093f\u0936\u094d\u0935\u093e\u0938 \u092e\u0947\u0902 \u092d\u093e\u0930\u0940 \u0915\u092e\u0940 \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\" id=\"conclusion\">\u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f, \u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0938\u0935\u093e\u0932 \u092f\u0939 \u0928\u0939\u0940\u0902 \u0939\u0948 \u0915\u093f \u0928\u093f\u0935\u0947\u0936\u0915 Elevidys \u092a\u0930 \u092d\u0930\u094b\u0938\u093e \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u092f\u093e \u0928\u0939\u0940\u0902\u0964 \u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0938\u0935\u093e\u0932 \u092f\u0939 \u0939\u0948 \u0915\u093f \u0915\u094d\u092f\u093e \u0935\u0930\u094d\u0924\u092e\u093e\u0928 \u092e\u0947\u0902 \u0909\u092a\u0932\u092c\u094d\u0927 \u0938\u093e\u0915\u094d\u0937\u094d\u092f \u0906\u091c \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u094b \u0909\u091a\u093f\u0924 \u0920\u0939\u0930\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092a\u0930\u094d\u092f\u093e\u092a\u094d\u0924 \u0939\u0948\u0902, \u092f\u093e \u0915\u094d\u092f\u093e \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0921\u0947\u091f\u093e \u0914\u0930 \u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940 \u0915\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0915\u093e \u0907\u0902\u0924\u091c\u093e\u0930 \u0915\u0930\u0928\u093e \u0909\u0928\u0915\u0947 \u092c\u091a\u094d\u091a\u0947 \u0915\u0947 \u0932\u093f\u090f \u092c\u0947\u0939\u0924\u0930 \u0935\u093f\u0915\u0932\u094d\u092a \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964 \u0939\u0930 \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u094b \u092a\u093e\u0930\u0926\u0930\u094d\u0936\u0940 \u091c\u093e\u0928\u0915\u093e\u0930\u0940, \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e\u0913\u0902 \u092a\u0930 \u0908\u092e\u093e\u0928\u0926\u093e\u0930 \u091a\u0930\u094d\u091a\u093e \u0914\u0930 \u0905\u092a\u0928\u0947 \u092c\u091a\u094d\u091a\u0947 \u0915\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u094b \u0906\u0915\u093e\u0930 \u0926\u0947\u0928\u0947 \u0935\u093e\u0932\u0947 \u0928\u093f\u0930\u094d\u0923\u092f \u0932\u0947\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0938\u092d\u0940 \u0909\u092a\u0932\u092c\u094d\u0927 \u0938\u093e\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a \u0915\u093e \u0905\u0927\u093f\u0915\u093e\u0930 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0905\u0902\u0924 \u092e\u0947\u0902 \u090f\u0915 \u092c\u093e\u0924: \u0905\u0917\u0930 \u0915\u094b\u0908 \u0906\u092a\u0938\u0947 \u0915\u0939\u0947, &quot;\u0938\u0940\u0915\u0947 \u0915\u093e \u0915\u094b\u0908 \u092e\u0939\u0924\u094d\u0935 \u0928\u0939\u0940\u0902 \u0939\u0948,&quot; \u0924\u094b \u092c\u093f\u0928\u093e \u0938\u092c\u0942\u0924 \u0915\u0947 \u0907\u0938 \u092c\u093e\u0924 \u0915\u094b \u0938\u094d\u0935\u0940\u0915\u093e\u0930 \u0928 \u0915\u0930\u0947\u0902\u0964 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0915 \u0910\u0938\u0940 \u092c\u0940\u092e\u093e\u0930\u0940 \u0939\u0948 \u091c\u093f\u0938\u092e\u0947\u0902 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u094b \u0932\u0917\u093e\u0924\u093e\u0930 \u0928\u0941\u0915\u0938\u093e\u0928 \u092a\u0939\u0941\u0902\u091a\u0924\u093e \u0939\u0948, \u0914\u0930 \u0938\u0940\u0915\u0947 \u0909\u0938 \u0928\u0941\u0915\u0938\u093e\u0928 \u0915\u093e \u0938\u092c\u0938\u0947 \u0938\u094d\u092a\u0937\u094d\u091f \u0938\u0902\u0915\u0947\u0924 \u0939\u0948\u0964.<\/strong> \u092f\u0926\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0915\u0947 \u0928\u093f\u0926\u093e\u0928 \u0914\u0930 \u0928\u093f\u0917\u0930\u093e\u0928\u0940 \u092e\u0947\u0902 \u0938\u0940\u0915\u0947 \u0938\u094d\u0924\u0930 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0902, \u0924\u094b Elevidys \u0915\u0947 \u092c\u093e\u0926 \u092d\u0940 \u0935\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092c\u0928\u0947 \u0930\u0939\u0924\u0947 \u0939\u0948\u0902\u0964 \u0938\u0940\u0915\u0947 \u0930\u0941\u091d\u093e\u0928\u094b\u0902 \u0915\u0947 \u0938\u0902\u092c\u0902\u0927 \u092e\u0947\u0902 \u092a\u093e\u0930\u0926\u0930\u094d\u0936\u093f\u0924\u093e \u0915\u094b \u090f\u0915 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u092e\u093e\u0928\u093e \u091c\u093e\u0928\u093e \u091a\u093e\u0939\u093f\u090f, \u0928 \u0915\u093f \u090f\u0915 \u0935\u093f\u0915\u0932\u094d\u092a\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u0940\u090f\u092e\u0921\u0940 \u0935\u093e\u0930\u093f\u092f\u0930 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902, \u0939\u092e\u0928\u0947 \u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u094b \u0909\u0928 \u0935\u093f\u0937\u092f\u094b\u0902 \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0915\u0908 \u092a\u094d\u0930\u0936\u094d\u0928 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u093f\u090f, \u091c\u093f\u0928\u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0915\u0908 \u092a\u0930\u093f\u0935\u093e\u0930 \u0905\u0915\u094d\u0938\u0930 \u092a\u0942\u091b\u0924\u0947 \u0939\u0948\u0902, \u091c\u093f\u0928\u092e\u0947\u0902 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e, \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930, \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0905\u092a\u0947\u0915\u094d\u0937\u093e\u090f\u0902 \u0914\u0930 \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0938\u0902\u092c\u0902\u0927\u0940 \u0935\u093f\u091a\u093e\u0930 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902\u0964.<\/strong> \u0939\u092e\u0947\u0902 \u0938\u0942\u091a\u093f\u0924 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e \u0915\u093f \u091c\u0935\u093e\u092c \u0926\u093f\u090f \u091c\u093e\u090f\u0902\u0917\u0947, \u0932\u0947\u0915\u093f\u0928 \u0907\u0938 \u0932\u0947\u0916 \u0915\u0947 \u092a\u094d\u0930\u0915\u093e\u0936\u0928 \u0924\u0915 \u0939\u092e\u0947\u0902 \u0909\u0928 \u0938\u0935\u093e\u0932\u094b\u0902 \u0915\u0947 \u0935\u093f\u0938\u094d\u0924\u0943\u0924 \u091c\u0935\u093e\u092c \u0928\u0939\u0940\u0902 \u092e\u093f\u0932\u0947 \u0939\u0948\u0902\u0964 \u092f\u0926\u093f \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u092d\u0940 \u092d\u0940 \u091c\u0935\u093e\u092c \u0926\u0947\u0928\u0947 \u0915\u093e \u0928\u093f\u0930\u094d\u0923\u092f \u0932\u0947\u0924\u0940 \u0939\u0948, \u0924\u094b \u0939\u092e \u0909\u0928\u0915\u0947 \u091c\u0935\u093e\u092c\u094b\u0902 \u0915\u094b \u092a\u0942\u0930\u0940 \u0924\u0930\u0939 \u0938\u0947 \u092a\u094d\u0930\u0915\u093e\u0936\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0924\u0948\u092f\u093e\u0930 \u0939\u0948\u0902 \u0924\u093e\u0915\u093f \u092e\u0930\u0940\u091c\u093c, \u0909\u0928\u0915\u0947 \u092a\u0930\u093f\u0935\u093e\u0930 \u0914\u0930 \u0938\u094d\u0935\u093e\u0938\u094d\u0925\u094d\u092f \u0938\u0947\u0935\u093e \u092a\u0947\u0936\u0947\u0935\u0930 \u0938\u0940\u0927\u0947 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0915\u0940 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0915\u0930 \u0938\u0915\u0947\u0902 \u0914\u0930 \u0905\u092a\u0928\u0947 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u0928\u093f\u0915\u093e\u0932 \u0938\u0915\u0947\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>Few Duchenne muscular dystrophy (DMD) treatments have generated as much excitement, controversy, and debate as Elevidys (delandistrogene moxeparvovec), the gene therapy developed by Sarepta Therapeutics. For many families, Elevidys represents hope. It is the first approved gene therapy designed to address the underlying genetic cause of Duchenne muscular dystrophy by delivering a micro-dystrophin gene to [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":8120,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[33,743,179,742,821],"class_list":["post-8116","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-elevidys","tag-elevidys-cost","tag-elevidys-gene-therapy","tag-elevidys-price","tag-sarepta-stock"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8116","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=8116"}],"version-history":[{"count":9,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8116\/revisions"}],"predecessor-version":[{"id":8126,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/8116\/revisions\/8126"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/8120"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=8116"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=8116"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=8116"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}