{"id":7875,"date":"2026-05-08T10:37:41","date_gmt":"2026-05-08T07:37:41","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=7875"},"modified":"2026-05-08T10:37:43","modified_gmt":"2026-05-08T07:37:43","slug":"bmn-351-exon-51-skipping-therapy-phase-2-clinical-trial-nct07573631","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/bmn-351-exon-51-skipping-therapy-phase-2-clinical-trial-nct07573631\/","title":{"rendered":"BioMarin \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f BMN 351 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u091a\u0930\u0923 2 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u093e \u0936\u0941\u092d\u093e\u0930\u0902\u092d \u0915\u093f\u092f\u093e\u0964"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>BioMarin Pharmaceutical \u0928\u0947 \u0906\u0927\u093f\u0915\u093e\u0930\u093f\u0915 \u0924\u094c\u0930 \u092a\u0930 \u090f\u0915 \u0928\u090f \u091a\u0930\u0923 2 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0905\u0927\u094d\u092f\u092f\u0928 (NCT07573631) \u0915\u0940 \u0936\u0941\u0930\u0941\u0906\u0924 \u0915\u0940 \u0939\u0948, \u091c\u093f\u0938\u092e\u0947\u0902 BMN 351 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948, \u091c\u094b \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (DMD) \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u0940 \u0917\u0908 \u090f\u0915 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0939\u0948\u0964.<\/strong> \u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0909\u0928 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e, \u0938\u0939\u0928\u0936\u0940\u0932\u0924\u093e \u0914\u0930 \u0936\u093e\u0930\u0940\u0930\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0937\u092e\u0924\u093e \u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u092a\u0930 \u0927\u094d\u092f\u093e\u0928 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924 \u0915\u093f\u092f\u093e \u091c\u093e\u090f\u0917\u093e \u091c\u093f\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u092a\u0939\u0932\u0947 351-201 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u0942\u0930\u093e \u0915\u0930 \u0932\u093f\u092f\u093e \u0925\u093e\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u092c\u0940\u090f\u092e\u090f\u0928 351 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u092b\u0947\u091c 2 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u092c\u0940\u090f\u092e\u090f\u0928 351 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u091a\u0930\u0923 2 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0909\u0928 \u0935\u094d\u092f\u0915\u094d\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u092c\u0939\u0941-\u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924, \u0913\u092a\u0928-\u0932\u0947\u092c\u0932 \u090f\u0915\u094d\u0938\u091f\u0947\u0902\u0936\u0928 \u0905\u0927\u094d\u092f\u092f\u0928 \u0939\u0948 \u091c\u094b \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0915\u0947 \u0932\u093f\u090f \u0909\u092a\u092f\u0941\u0915\u094d\u0924 \u0939\u0948\u0902\u0964.<\/strong> \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e \u0907\u0938 \u092c\u093e\u0924 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0947\u0902\u0917\u0947 \u0915\u093f \u0932\u0902\u092c\u0940 \u0909\u092a\u091a\u093e\u0930 \u0905\u0935\u0927\u093f \u092e\u0947\u0902 \u0938\u093e\u092a\u094d\u0924\u093e\u0939\u093f\u0915 \u0905\u0902\u0924\u0903\u0936\u093f\u0930\u093e \u092c\u0940\u090f\u092e\u090f\u0928 351 \u091c\u0932\u0938\u0947\u0915 \u0915\u093f\u0924\u0928\u093e \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0914\u0930 \u092a\u094d\u0930\u092d\u093e\u0935\u0940 \u0930\u0939\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 4 \u0938\u0947 23 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0906\u092f\u0941 \u0915\u0947 \u0905\u0927\u093f\u0915\u0924\u092e 18 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0936\u093e\u092e\u093f\u0932 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u0939\u0948, \u091c\u093f\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u092a\u0939\u0932\u0947 \u091a\u0930\u0923 1\/2 \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0942\u0930\u093e \u0915\u0930 \u0932\u093f\u092f\u093e \u0939\u0948, \u091c\u093f\u0938\u0947 351-201 \u0915\u0947 \u0928\u093e\u092e \u0938\u0947 \u091c\u093e\u0928\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0914\u0930 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0915\u094b \u0938\u092e\u091d\u0928\u093e<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0915 \u0926\u0941\u0930\u094d\u0932\u092d \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0930\u094b\u0917 \u0939\u0948 \u091c\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0932\u0917\u093e\u0924\u093e\u0930 \u0915\u092e\u091c\u094b\u0930\u0940 \u0914\u0930 \u0915\u094d\u0937\u092f \u0915\u093e \u0915\u093e\u0930\u0923 \u092c\u0928\u0924\u093e \u0939\u0948\u0964 \u092f\u0939 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u0947 \u0915\u093e\u0930\u0923 \u0939\u094b\u0924\u093e \u0939\u0948, \u091c\u094b \u0938\u094d\u0935\u0938\u094d\u0925 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u0915\u094b \u092c\u0928\u093e\u090f \u0930\u0916\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a \u0915\u094d\u092f\u094b\u0902 \u0939\u094b\u0924\u093e \u0939\u0948?<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0936\u0930\u0940\u0930 \u0915\u094b \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u090f\u0915 \u091b\u094b\u091f\u093e \u0932\u0947\u0915\u093f\u0928 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0938\u0902\u0938\u094d\u0915\u0930\u0923 \u092c\u0928\u093e\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0928\u093e \u0939\u0948\u0964 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u0909\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0924\u0940 \u0939\u0948 \u091c\u093f\u0928\u0915\u0947 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0915\u094b \u091b\u094b\u0921\u093c\u0928\u0947 \u0938\u0947 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u0932\u093e\u092d\u093e\u0928\u094d\u0935\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092c\u0940\u090f\u092e\u090f\u0928 351 \u0915\u094b \u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940 \u0915\u0940 \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u091c\u093e\u0902\u091a\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948 \u091c\u094b \u092f\u094b\u0917\u094d\u092f \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"847\" height=\"1024\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-847x1024.jpg\" alt=\"\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0914\u0930 \u0935\u093f\u0932\u094b\u092a\u0928\" class=\"wp-image-4526\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-847x1024.jpg 847w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-248x300.jpg 248w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-768x929.jpg 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1270x1536.jpg 1270w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1693x2048.jpg 1693w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-10x12.jpg 10w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-347x420.jpg 347w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-150x181.jpg 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-300x363.jpg 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-696x842.jpg 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1068x1292.jpg 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping-1920x2323.jpg 1920w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2025\/03\/amenable-to-exon-51-skipping.jpg 1984w\" sizes=\"(max-width: 847px) 100vw, 847px\" \/><\/figure>\n\n\n\n<h2 class=\"wp-block-heading\">\u092b\u0947\u091c 2 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u092e\u0941\u0916\u094d\u092f \u0935\u093f\u0935\u0930\u0923<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\">\u092a\u0922\u093c\u093e\u0908 \u0915\u0940 \u0938\u0930\u0902\u091a\u0928\u093e<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u092e\u0941\u0915\u0926\u092e\u093e \u0907\u0938 \u092a\u094d\u0930\u0915\u093e\u0930 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092e\u0932\u094d\u091f\u0940 \u0915\u0947\u0902\u0926\u094d\u0930<\/li>\n\n\n\n<li>\u0916\u0941\u0932\u093e \u0932\u0947\u092c\u0932<\/li>\n\n\n\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0905\u0927\u094d\u092f\u092f\u0928<\/li>\n\n\n\n<li>\u0938\u093e\u092a\u094d\u0924\u093e\u0939\u093f\u0915 \u0905\u0902\u0924\u0903\u0936\u093f\u0930\u093e \u0916\u0941\u0930\u093e\u0915 \u092a\u0930 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u092a\u0939\u0932\u0940 \u092f\u093e\u0924\u094d\u0930\u093e, \u092a\u0939\u0932\u0947 \u0915\u0947 351-201 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0940 \u0905\u0902\u0924\u093f\u092e \u092f\u093e\u0924\u094d\u0930\u093e \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u092d\u0940 \u0915\u093e\u092e \u0915\u0930\u0947\u0917\u0940\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924 \u0938\u092e\u092f\u0938\u0940\u092e\u093e<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u094d\u0930\u093e\u0930\u0902\u092d: \u0905\u092a\u094d\u0930\u0948\u0932 2026<\/li>\n\n\n\n<li>\u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u092a\u0942\u0930\u094d\u0923\u0924\u093e \u0924\u093f\u0925\u093f: \u0926\u093f\u0938\u0902\u092c\u0930 2031<\/li>\n\n\n\n<li>\u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092a\u0942\u0930\u093e \u0939\u094b\u0928\u0947 \u0915\u093e \u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924 \u0938\u092e\u092f: \u0926\u093f\u0938\u0902\u092c\u0930 2031<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\">\u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u092d\u093e\u0917 \u0932\u0947\u0928\u0947 \u0935\u093e\u0932\u0947 \u0926\u0947\u0936<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0938\u094d\u0925\u093e\u0928\u094b\u0902 \u092a\u0930 \u0915\u093f\u090f \u0917\u090f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0907\u091f\u0932\u0940<\/li>\n\n\n\n<li>\u0928\u0940\u0926\u0930\u0932\u0948\u0902\u0921<\/li>\n\n\n\n<li>\u0938\u094d\u092a\u0947\u0928<\/li>\n\n\n\n<li>\u0924\u0941\u0930\u094d\u0915\u0940<\/li>\n\n\n\n<li>\u092f\u0942\u0928\u093e\u0907\u091f\u0947\u0921 \u0915\u093f\u0902\u0917\u0921\u092e<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\">\u0915\u094c\u0928 \u092d\u093e\u0917 \u0932\u0947 \u0938\u0915\u0924\u093e \u0939\u0948?<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\">\u092e\u0941\u0916\u094d\u092f \u0938\u092e\u093e\u0935\u0947\u0936\u0928 \u092e\u093e\u0928\u0926\u0902\u0921<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u0930\u0928\u093e \u0939\u094b\u0917\u093e:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>351-201 \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0942\u0930\u093e \u0915\u0930 \u0932\u093f\u092f\u093e \u0939\u0948<\/li>\n\n\n\n<li>\u0938\u094d\u0925\u093f\u0930 \u0915\u0949\u0930\u094d\u091f\u093f\u0915\u094b\u0938\u094d\u091f\u0947\u0930\u0949\u0907\u0921 \u0909\u092a\u091a\u093e\u0930 \u091c\u093e\u0930\u0940 \u0930\u0916\u0947\u0902<\/li>\n\n\n\n<li>\u0905\u0927\u094d\u092f\u092f\u0928 \u092f\u093e\u0924\u094d\u0930\u093e \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e\u0913\u0902 \u0915\u093e \u092a\u093e\u0932\u0928 \u0915\u0930\u0947\u0902<\/li>\n\n\n\n<li>\u091c\u0939\u093e\u0902 \u0932\u093e\u0917\u0942 \u0939\u094b, \u0935\u0939\u093e\u0902 \u0938\u0942\u091a\u093f\u0924 \u0938\u0939\u092e\u0924\u093f \u092f\u093e \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0947\u0902\u0964<\/li>\n\n\n\n<li>\u092a\u094d\u0930\u094b\u091f\u094b\u0915\u0949\u0932 \u0926\u093f\u0936\u093e\u0928\u093f\u0930\u094d\u0926\u0947\u0936\u094b\u0902 \u0915\u0947 \u0905\u0928\u0941\u0938\u093e\u0930 \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u094b\u0928\u0947 \u092a\u0930 \u0917\u0930\u094d\u092d\u0928\u093f\u0930\u094b\u0927\u0915 \u0915\u093e \u092a\u094d\u0930\u092f\u094b\u0917 \u0915\u0930\u0947\u0902\u0964<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\">\u092e\u0941\u0916\u094d\u092f \u0905\u092a\u0935\u0930\u094d\u091c\u0928 \u092e\u093e\u0928\u0926\u0902\u0921<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0938\u094d\u0925\u093f\u0924\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0928\u0939\u0940\u0902 \u0939\u094b \u0938\u0915\u0924\u0947:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0930\u0915\u094d\u0924 \u0915\u0947 \u0925\u0915\u094d\u0915\u0947 \u091c\u092e\u0928\u0947 \u0938\u0902\u092c\u0902\u0927\u0940 \u0935\u093f\u0915\u093e\u0930 \u091c\u094d\u091e\u093e\u0924 \u0939\u0948\u0902<\/li>\n\n\n\n<li>\u0928\u093f\u0937\u093f\u0926\u094d\u0927 \u0926\u0935\u093e\u0913\u0902 \u0915\u093e \u092a\u094d\u0930\u092f\u094b\u0917 \u0915\u0930\u0947\u0902<\/li>\n\n\n\n<li>\u092c\u0947\u0938\u0932\u093e\u0907\u0928 \u0938\u0947 12 \u0938\u092a\u094d\u0924\u093e\u0939 \u092a\u0939\u0932\u0947 \u090f\u0915 \u0914\u0930 \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0940\u0964<\/li>\n\n\n\n<li>\u0907\u0938\u0938\u0947 \u092a\u0939\u0932\u0947 DMD \u0915\u0947 \u0932\u093f\u090f \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0940 \u0925\u0940\u0964<\/li>\n\n\n\n<li>\u090f\u0902\u091f\u0940-\u0915\u094b\u090f\u0917\u0941\u0932\u0947\u0902\u091f \u092f\u093e \u0907\u092e\u094d\u092f\u0942\u0928\u094b\u0938\u092a\u094d\u0930\u0947\u0938\u0947\u0902\u091f \u0915\u093e \u092a\u094d\u0930\u092f\u094b\u0917 \u0915\u0930\u0947\u0902<\/li>\n<\/ul>\n\n\n\n<h2 class=\"wp-block-heading\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u092f\u0939 \u092e\u0941\u0915\u0926\u092e\u093e \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u092c\u0940\u090f\u092e\u090f\u0928 351 \u090f\u0915\u094d\u0938\u0949\u0928 51 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u091a\u0930\u0923 2 \u0915\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u093e \u0936\u0941\u092d\u093e\u0930\u0902\u092d \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0932\u0915\u094d\u0937\u093f\u0924 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u0947 \u0935\u093f\u0915\u093e\u0938 \u092e\u0947\u0902 \u090f\u0915 \u0914\u0930 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0915\u0926\u092e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0905\u0927\u094d\u092f\u092f\u0928 \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0902 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0935\u0947 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0915\u094b \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u092c\u093e\u0924\u094b\u0902 \u0915\u094b \u0938\u092e\u091d\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0915\u094d\u092f\u093e \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093e\u092d \u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0925 \u092c\u0930\u0915\u0930\u093e\u0930 \u0930\u0939 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902?<\/li>\n\n\n\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093e\u0907\u0932<\/li>\n\n\n\n<li>\u0926\u0948\u0928\u093f\u0915 \u0936\u093e\u0930\u0940\u0930\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u094b\u0902 \u092a\u0930 \u092a\u094d\u0930\u092d\u093e\u0935<\/li>\n\n\n\n<li>\u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u092a\u0930 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092a\u094d\u0930\u092d\u093e\u0935<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917 \u0938\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f, \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u092e\u0947\u0902 \u0928\u093f\u0930\u0902\u0924\u0930 \u092a\u094d\u0930\u0917\u0924\u093f \u092d\u0935\u093f\u0937\u094d\u092f \u092e\u0947\u0902 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0935\u093f\u0915\u0932\u094d\u092a\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0928\u0908 \u0909\u092e\u094d\u092e\u0940\u0926\u0947\u0902 \u091c\u0917\u093e\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>BioMarin Pharmaceutical has officially launched a new Phase 2 extension study (NCT07573631) evaluating BMN 351, an investigational exon 51 skipping therapy designed for people living with Duchenne muscular dystrophy (DMD). The study will focus on long-term safety, tolerability, and physical function outcomes in participants who previously completed the earlier 351-201 clinical trial. 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