{"id":7866,"date":"2026-05-07T14:46:47","date_gmt":"2026-05-07T11:46:47","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=7866"},"modified":"2026-05-07T16:36:59","modified_gmt":"2026-05-07T13:36:59","slug":"entrada-therapeutics-phase-1-2-results-for-entr-601-44-in-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/entrada-therapeutics-phase-1-2-results-for-entr-601-44-in-duchenne-muscular-dystrophy\/","title":{"rendered":"Entrada Therapeutics \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 ENTR-601-44 \u0915\u0947 \u091a\u0930\u0923 1\/2 \u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e \u0918\u094b\u0937\u093f\u0924 \u0915\u093f\u090f\u0964"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Entrada Therapeutics \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (DMD) \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0909\u092a\u091a\u093e\u0930, ENTR-601-44 \u0915\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0939\u0948\u0964 \u092f\u0939 \u0925\u0947\u0930\u0947\u092a\u0940 \u0909\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u0940 \u0917\u0908 \u0939\u0948 \u091c\u094b &quot;\u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917&quot; \u0938\u0947 \u0932\u093e\u092d\u093e\u0928\u094d\u0935\u093f\u0924 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902, \u091c\u094b \u090f\u0915 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0926\u0943\u0937\u094d\u091f\u093f\u0915\u094b\u0923 \u0939\u0948 \u091c\u093f\u0938\u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0936\u0930\u0940\u0930 \u0915\u094b \u0905\u0927\u093f\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0928\u093e \u0939\u0948\u0964 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/mutations-and-deletions-amenable-to-exon-44-skipping-therapies-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0914\u0930 \u0935\u093f\u0932\u094b\u092a\u0928<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0939\u093e\u0932\u093e\u0902\u0915\u093f, Entrada Therapeutics \u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940 \u0915\u0940 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0928\u0947 \u0928\u093f\u0930\u093e\u0936\u093e\u091c\u0928\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0926\u093f\u090f\u0964.<\/strong> \u0906\u0902\u0915\u0921\u093c\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0947 \u092c\u093e\u0926, \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0935\u093f\u0915\u0938\u093f\u0924 \u0915\u0940 \u091c\u093e \u0930\u0939\u0940 \u0926\u0935\u093e \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0914\u0930 \u092e\u0927\u094d\u092f \u091a\u0930\u0923 \u0915\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0915\u094b\u0902 \u0915\u0940 \u0905\u092a\u0947\u0915\u094d\u0937\u093e\u0913\u0902 \u0938\u0947 \u0915\u093e\u092b\u0940 \u0915\u092e \u0930\u0939\u0940, \u091c\u093f\u0938\u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e\u0938\u094d\u0935\u0930\u0942\u092a \u0917\u0941\u0930\u0941\u0935\u093e\u0930 \u0915\u094b \u092a\u094d\u0930\u0940\u092e\u093e\u0930\u094d\u0915\u0947\u091f \u091f\u094d\u0930\u0947\u0921\u093f\u0902\u0917 \u092e\u0947\u0902 \u0915\u0902\u092a\u0928\u0940 \u0915\u0947 \u0936\u0947\u092f\u0930 501 \u091f\u094d\u0930\u093f\u0932\u093f\u092f\u0928 \u0938\u0947 \u0905\u0927\u093f\u0915 \u0917\u093f\u0930 \u0917\u090f\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0939\u0948 \u091c\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u094b \u092e\u091c\u092c\u0942\u0924 \u0930\u0916\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0924\u093e \u0939\u0948\u0964 DMD \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u093e \u0938\u094d\u0924\u0930 \u092c\u0939\u0941\u0924 \u0915\u092e \u092f\u093e \u0905\u0928\u0941\u092a\u0938\u094d\u0925\u093f\u0924 \u0939\u094b\u0924\u093e \u0939\u0948, \u091c\u093f\u0938\u0938\u0947 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0927\u0940\u0930\u0947-\u0927\u0940\u0930\u0947 \u0915\u092e\u091c\u094b\u0930\u0940 \u0906\u0924\u0940 \u091c\u093e\u0924\u0940 \u0939\u0948\u0964 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/dystrophin-gene\/\" target=\"_blank\" data-type=\"post\" data-id=\"3785\" rel=\"noreferrer noopener\">\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\">\u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0915\u094d\u092f\u093e \u0939\u0941\u0906?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092b\u0947\u091c 1\/2 ELEVATE-44-201 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 4 \u0938\u0947 20 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0906\u092f\u0941 \u0915\u0947 \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0932\u0921\u093c\u0915\u0947 \u0914\u0930 \u092f\u0941\u0935\u093e \u092a\u0941\u0930\u0941\u0937 \u0936\u093e\u092e\u093f\u0932 \u0925\u0947\u0964 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u092f\u093e \u0924\u094b ENTR-601-44 \u092f\u093e \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b \u0926\u093f\u092f\u093e \u0917\u092f\u093e\u0964 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0928\u0947 \u092e\u0941\u0916\u094d\u092f \u0930\u0942\u092a \u0938\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e, \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0914\u0930 \u0936\u093e\u0930\u0940\u0930\u093f\u0915 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0937\u092e\u0924\u093e \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">\u092e\u0941\u0915\u094d\u092f \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0928\u0947 \u092c\u0924\u093e\u092f\u093e \u0915\u093f:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>Entrada Therapeutics \u0928\u0947 6 \u0938\u0947 17 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0906\u092f\u0941 \u0915\u0947 \u0909\u0928 \u0932\u0921\u093c\u0915\u094b\u0902 \u092e\u0947\u0902 ENTR-601-44 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e \u091c\u094b \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0925\u0947 \u0914\u0930 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0915\u0947 \u0932\u093f\u090f \u0909\u092a\u092f\u0941\u0915\u094d\u0924 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u0947 \u0915\u093e\u0930\u0923 \u091a\u0932-\u092b\u093f\u0930 \u0938\u0915\u0924\u0947 \u0925\u0947\u0964.<\/li>\n\n\n\n<li><strong>\u092c\u094b\u0938\u094d\u091f\u0928 \u0938\u094d\u0925\u093f\u0924 \u092c\u093e\u092f\u094b\u091f\u0947\u0915 \u0915\u0902\u092a\u0928\u0940 \u0928\u0947 \u092c\u0924\u093e\u092f\u093e \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u092e\u0947\u0902 4% \u0915\u0947 \u0906\u0927\u093e\u0930\u092d\u0942\u0924 \u0938\u094d\u0924\u0930 \u0938\u0947 2.36 \u092a\u094d\u0930\u0924\u093f\u0936\u0924 \u0905\u0902\u0915 \u0915\u0940 \u0935\u0943\u0926\u094d\u0927\u093f \u0939\u0941\u0908, \u091c\u093f\u0938\u0938\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0905\u0928\u0941\u092a\u0938\u094d\u0925\u093f\u0924 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u090f\u0915 \u0939\u093f\u0938\u094d\u0938\u093e \u092c\u0939\u093e\u0932 \u0939\u094b \u0917\u092f\u093e\u0964.<\/strong><\/li>\n\n\n\n<li>\u0905\u092a\u094d\u0930\u0948\u0932 \u092e\u0947\u0902 \u092a\u094d\u0930\u0915\u093e\u0936\u093f\u0924 \u090f\u0915 \u0936\u094b\u0927 \u0928\u094b\u091f \u092e\u0947\u0902, \u0935\u093f\u0932\u093f\u092f\u092e \u092c\u094d\u0932\u0947\u092f\u0930 \u0915\u0947 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0915 \u092e\u093e\u0907\u0932\u094d\u0938 \u092e\u093f\u0902\u091f\u0930 \u0928\u0947 \u0915\u0939\u093e \u0915\u093f \u0915\u092e \u0938\u0947 \u0915\u092e 10% \u0915\u0940 \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0938\u092e\u093e\u092f\u094b\u091c\u093f\u0924 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0935\u0943\u0926\u094d\u0927\u093f \u0907\u0938 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0932\u093f\u090f \u0905\u092a\u0947\u0915\u094d\u0937\u093f\u0924 \u0906\u0927\u093e\u0930\u092d\u0942\u0924 \u092a\u0930\u093f\u0926\u0943\u0936\u094d\u092f \u0915\u093e \u092a\u094d\u0930\u0924\u093f\u0928\u093f\u0927\u093f\u0924\u094d\u0935 \u0915\u0930\u0924\u0940 \u0939\u0948, \u091c\u092c\u0915\u093f \u092b\u0930\u094d\u092e \u0915\u0947 \u0906\u0902\u0924\u0930\u093f\u0915 \u0905\u0928\u0941\u092e\u093e\u0928\u094b\u0902 \u0928\u0947 \u0932\u0917\u092d\u0917 11% \u0915\u093e \u0905\u0928\u0941\u092e\u093e\u0928 \u0932\u0917\u093e\u092f\u093e \u0939\u0948\u0964.<\/li>\n\n\n\n<li><strong>\u0907\u0928 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e del-zota \u0938\u0947 \u092d\u0940 \u092a\u094d\u0930\u0924\u093f\u0915\u0942\u0932 \u0930\u0942\u092a \u0938\u0947 \u0915\u0940 \u0917\u0908, \u091c\u094b Avidity Biosciences \u0915\u093e \u092a\u094d\u0930\u0924\u093f\u0938\u094d\u092a\u0930\u094d\u0927\u0940 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0909\u092e\u094d\u092e\u0940\u0926\u0935\u093e\u0930 \u0939\u0948, \u091c\u093f\u0938\u0928\u0947 \u092a\u0939\u0932\u0947 \u090f\u0915 \u092e\u0927\u094d\u092f-\u091a\u0930\u0923 \u0915\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0938\u092e\u093e\u092f\u094b\u091c\u093f\u0924 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0932\u093e\u092d \u0932\u0917\u092d\u0917 25% \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u093f\u092f\u093e \u0925\u093e - \u090f\u0915 \u0910\u0938\u093e \u0938\u094d\u0924\u0930 \u091c\u093f\u0938\u0947 \u0913\u092a\u0947\u0928\u0939\u093e\u0907\u092e\u0930 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0915\u094b\u0902 \u0928\u0947 Entrada \u0915\u0947 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0915\u0947 \u0932\u093f\u090f \u0938\u092b\u0932\u0924\u093e \u0915\u093e \u092c\u0947\u0902\u091a\u092e\u093e\u0930\u094d\u0915 \u092c\u0924\u093e\u092f\u093e \u0925\u093e\u0964.<\/strong><\/li>\n\n\n\n<li>\u0921\u0947\u091f\u093e \u091c\u093e\u0930\u0940 \u0939\u094b\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947, \u092e\u093f\u0902\u091f\u0930 \u0928\u0947 ENTR-601-44 \u0915\u0947 \u0932\u093f\u090f \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0926\u0935\u093e \u092a\u0939\u0941\u0902\u091a\u093e\u0928\u0947 \u0915\u0940 \u0926\u0915\u094d\u0937\u0924\u093e \u0915\u094b \u092e\u0941\u0916\u094d\u092f \u091a\u093f\u0902\u0924\u093e \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u092a\u0939\u091a\u093e\u0928\u093e, \u0914\u0930 Entrada \u0928\u0947 \u092c\u093e\u0926 \u092e\u0947\u0902 \u0916\u0941\u0932\u093e\u0938\u093e \u0915\u093f\u092f\u093e \u0915\u093f \u092c\u093e\u0932 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0926\u0935\u093e \u0915\u093e \u092a\u094d\u0930\u0923\u093e\u0932\u0940\u0917\u0924 \u092a\u094d\u0930\u092d\u093e\u0935 \u0935\u092f\u0938\u094d\u0915 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u0905\u092a\u0947\u0915\u094d\u0937\u093e \u0938\u0947 \u0915\u092e \u0925\u093e\u0964.<\/li>\n\n\n\n<li><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0915 \u0926\u0941\u0930\u094d\u0932\u092d \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0928\u094d\u092f\u0942\u0930\u094b\u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u092c\u0940\u092e\u093e\u0930\u0940 \u0939\u0948 \u091c\u094b \u092e\u0941\u0916\u094d\u092f \u0930\u0942\u092a \u0938\u0947 \u0932\u0921\u093c\u0915\u094b\u0902 \u0915\u094b \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0915\u0930\u0924\u0940 \u0939\u0948 \u0914\u0930 \u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0925 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0917\u0924\u093f\u0936\u0940\u0932 \u0915\u094d\u0937\u0930\u0923 \u0915\u093e \u0915\u093e\u0930\u0923 \u092c\u0928\u0924\u0940 \u0939\u0948\u0964.<\/strong><\/li>\n\n\n\n<li>\u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u092f\u0939 \u092d\u0940 \u0926\u093f\u0916\u093e\u092f\u093e \u0917\u092f\u093e \u0915\u093f \u0909\u092a\u091a\u093e\u0930\u093f\u0924 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u092b\u0930\u094d\u0936 \u0938\u0947 \u0916\u0921\u093c\u0947 \u0939\u094b\u0928\u0947 \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u092e\u0947\u0902 \u0906\u0928\u0947 \u092e\u0947\u0902 \u0932\u0917\u0928\u0947 \u0935\u093e\u0932\u0947 \u0938\u092e\u092f \u092e\u0947\u0902 \u0938\u093e\u0902\u0916\u094d\u092f\u093f\u0915\u0940\u092f \u0930\u0942\u092a \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0938\u0941\u0927\u093e\u0930 \u0939\u0941\u0906 \u0939\u0948, \u091c\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0924\u093e\u0915\u0924 \u0915\u0940 \u0928\u093f\u0917\u0930\u093e\u0928\u0940 \u0915\u0930\u0928\u0947 \u0914\u0930 \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u092e\u0947\u0902 \u0915\u092e\u0940 \u0915\u093e \u0905\u0928\u0941\u092e\u093e\u0928 \u0932\u0917\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0906\u092e\u0924\u094c\u0930 \u092a\u0930 \u0907\u0938\u094d\u0924\u0947\u092e\u093e\u0932 \u0915\u093f\u092f\u093e \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u093e \u090f\u0915 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0939\u0948\u0964.<\/li>\n\n\n\n<li><strong>Entrada \u0928\u0947 \u092f\u0939 \u092d\u0940 \u092a\u0941\u0937\u094d\u091f\u093f \u0915\u0940 \u0939\u0948 \u0915\u093f \u0926\u0942\u0938\u0930\u0947 \u0930\u094b\u0917\u0940 \u0938\u092e\u0942\u0939 \u092e\u0947\u0902 \u0916\u0941\u0930\u093e\u0915 \u0926\u0947\u0928\u093e \u0936\u0941\u0930\u0942 \u0939\u094b \u0917\u092f\u093e \u0939\u0948, \u091c\u093f\u0928\u094d\u0939\u0947\u0902 \u092e\u0942\u0932 \u0916\u0941\u0930\u093e\u0915 \u0938\u0947 \u0926\u094b\u0917\u0941\u0928\u0940 \u0916\u0941\u0930\u093e\u0915 \u0926\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948, \u0914\u0930 2026 \u0915\u0947 \u0905\u0902\u0924 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0906\u0928\u0947 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948\u0964.<\/strong><\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\">\u0907\u0938 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094b \u0915\u094d\u092f\u093e \u091a\u0940\u091c\u093c \u0905\u0932\u0917 \u092c\u0928\u093e\u0924\u0940 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Entrada \u0915\u0947 \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915\u094b\u0902 \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u0909\u0928\u0915\u0940 \u0921\u093f\u0932\u0940\u0935\u0930\u0940 \u0924\u0915\u0928\u0940\u0915 \u0938\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0938\u094d\u091f\u0947\u092e \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u0924\u0915 \u092a\u0939\u0941\u0901\u091a\u093e\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948, \u091c\u093f\u0928\u094d\u0939\u0947\u0902 \u0938\u0948\u091f\u0947\u0932\u093e\u0907\u091f \u0915\u094b\u0936\u093f\u0915\u093e\u090f\u0901 \u0915\u0939\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964 \u092f\u0947 \u0915\u094b\u0936\u093f\u0915\u093e\u090f\u0901 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0902 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092f\u0947 \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u092e\u0930\u092e\u094d\u092e\u0924 \u0914\u0930 \u0928\u090f \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u0924\u0902\u0924\u0941\u0913\u0902 \u0915\u0947 \u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u092e\u0947\u0902 \u0938\u0939\u093e\u092f\u0915 \u0939\u094b\u0924\u0940 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u0907\u0938\u0938\u0947 \u092f\u0939 \u0938\u094d\u092a\u0937\u094d\u091f \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948 \u0915\u093f \u0915\u0941\u091b \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u092e\u093e\u0924\u094d\u0930\u093e \u092e\u0947\u0902 \u0905\u092a\u0947\u0915\u094d\u0937\u093e\u0915\u0943\u0924 \u092e\u093e\u092e\u0942\u0932\u0940 \u0935\u0943\u0926\u094d\u0927\u093f \u0939\u094b\u0928\u0947 \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926 \u0936\u0941\u0930\u0941\u0906\u0924\u0940 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0938\u0941\u0927\u093e\u0930 \u0915\u094d\u092f\u094b\u0902 \u0926\u0947\u0916\u0928\u0947 \u0915\u094b \u092e\u093f\u0932\u0947\u0964. <\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\">\u0906\u0917\u0947 \u0915\u094d\u092f\u093e \u0939\u094b\u0924\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0939\u0932\u0947 \u0938\u092e\u0942\u0939 \u0915\u0947 \u0938\u092d\u0940 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940 \u0905\u092c \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0913\u092a\u0928-\u0932\u0947\u092c\u0932 \u0939\u093f\u0938\u094d\u0938\u0947 \u092e\u0947\u0902 \u091a\u0932\u0947 \u0917\u090f \u0939\u0948\u0902, \u091c\u0939\u093e\u0902 \u0938\u092d\u0940 \u0915\u094b \u0925\u0947\u0930\u0947\u092a\u0940 \u0926\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948\u0964 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0930\u094b\u0917\u0940 \u0938\u092e\u0942\u0939\u094b\u0902 \u092e\u0947\u0902 \u0909\u091a\u094d\u091a \u0916\u0941\u0930\u093e\u0915 \u0915\u093e \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092d\u0940 \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Entrada \u0915\u094b 2026 \u0915\u0947 \u0905\u0902\u0924 \u092e\u0947\u0902 \u0914\u0930 \u0905\u0927\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u092e\u093f\u0932\u0928\u0947 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Entrada Therapeutics announced early clinical trial results for ENTR-601-44, an experimental treatment for people with Duchenne Muscular Dystrophy (DMD). The therapy is designed for patients who can benefit from \u201cexon 44 skipping,\u201d a genetic approach aimed at helping the body produce more dystrophin protein. Learn More: Mutations and Deletions Amenable to Exon 44 Skipping Therapies [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":7867,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[137,265,233,234,141,127,246],"class_list":["post-7866","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-clinical-trial","tag-entr-601-44","tag-entrada","tag-entrada-therapeutics","tag-exon-44","tag-exon-44-skipping","tag-exon-44-skipping-therapies"],"subtitle":"Entrada Therapeutics \u0928\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 ENTR-601-44 \u0915\u0947 \u0932\u093f\u090f \u091a\u0930\u0923 1\/2 \u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e \u0918\u094b\u0937\u093f\u0924 \u0915\u093f\u090f, \u0932\u0947\u0915\u093f\u0928 \u0921\u0947\u091f\u093e DEL-ZOTA, \u090f\u0915 \u0905\u0928\u094d\u092f \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u092a\u0939\u0932\u0947 \u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0915\u093f\u090f \u0917\u090f \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u0947 \u0915\u0930\u0940\u092c \u092d\u0940 \u0928\u0939\u0940\u0902 \u092a\u0939\u0941\u0902\u091a \u092a\u093e\u092f\u093e, \u091c\u093f\u0938\u0938\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0938\u092e\u0941\u0926\u093e\u092f \u0914\u0930 \u0928\u093f\u0935\u0947\u0936\u0915 \u091c\u0917\u0924 \u092e\u0947\u0902 \u0928\u093f\u0930\u093e\u0936\u093e \u092b\u0948\u0932 \u0917\u0908\u0964.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/7866","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=7866"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/7866\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/7867"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=7866"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=7866"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=7866"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}