{"id":7683,"date":"2026-04-21T17:37:11","date_gmt":"2026-04-21T14:37:11","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=7683"},"modified":"2026-04-21T17:37:12","modified_gmt":"2026-04-21T14:37:12","slug":"elevidys-phase-4-enhance-clinical-trial-nct07542314","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/elevidys-phase-4-enhance-clinical-trial-nct07542314\/","title":{"rendered":"ELEVIDYS ENHANCE \u0905\u0927\u094d\u092f\u092f\u0928: \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u091a\u0930\u0923 4 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0939\u0941\u0906"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>ENHANCE \u0905\u0927\u094d\u092f\u092f\u0928 \u090f\u0915 \u091a\u0930\u0923 4 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0939\u0948 \u091c\u093f\u0938\u0947 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 ELEVIDYS \u0915\u0940 \u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915 \u0926\u0941\u0928\u093f\u092f\u093e \u092e\u0947\u0902 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0905\u0927\u094d\u092f\u092f\u0928 \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092f\u0939 \u0909\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092a\u0930 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924 \u0939\u0948 \u091c\u093f\u0928\u0915\u093e \u0907\u0932\u093e\u091c \u092a\u094b\u0938\u094d\u091f-\u092e\u093e\u0930\u094d\u0915\u0947\u091f\u093f\u0902\u0917 \u0938\u0947\u091f\u093f\u0902\u0917 \u092e\u0947\u0902 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u092f\u093e\u0928\u0940 \u0915\u093f \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094b \u092a\u0939\u0932\u0947 \u0939\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091a\u0941\u0915\u0940 \u0939\u0948 \u0914\u0930 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0905\u092d\u094d\u092f\u093e\u0938 \u092e\u0947\u0902 \u0907\u0938\u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 Sarepta Therapeutics \u0926\u094d\u0935\u093e\u0930\u093e \u092a\u094d\u0930\u093e\u092f\u094b\u091c\u093f\u0924 \u0939\u0948 \u0914\u0930 \u0907\u0938\u0915\u093e \u0905\u0927\u094d\u092f\u092f\u0928 \u0906\u0908\u0921\u0940 SRP-9001-402 \u0939\u0948\u0964.<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#primary-goal-understanding-liver-safety-risks\">\u092e\u0941\u0916\u094d\u092f \u0932\u0915\u094d\u0937\u094d\u092f: \u092f\u0915\u0943\u0924 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u091c\u094b\u0916\u093f\u092e\u094b\u0902 \u0915\u094b \u0938\u092e\u091d\u0928\u093e<\/a><\/li><li><a href=\"#study-design-and-key-details\">\u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0940 \u0930\u0942\u092a\u0930\u0947\u0916\u093e \u0914\u0930 \u092e\u0941\u0916\u094d\u092f \u0935\u093f\u0935\u0930\u0923<\/a><\/li><li><a href=\"#who-can-participate\">\u0915\u094c\u0928 \u092d\u093e\u0917 \u0932\u0947 \u0938\u0915\u0924\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#who-cannot-participate\">\u0915\u094c\u0928 \u092d\u093e\u0917 \u0928\u0939\u0940\u0902 \u0932\u0947 \u0938\u0915\u0924\u093e?<\/a><\/li><li><a href=\"#why-this-study-is-important-for-the-dmd-community\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u092f\u0939 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/a><\/li><li><a href=\"#contact-information\">\u0938\u0902\u092a\u0930\u094d\u0915 \u091c\u093e\u0928\u0915\u093e\u0930\u0940<\/a><\/li><li><a href=\"#clinical-trial-locations-not-yet-announced\">\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0938\u094d\u0925\u093e\u0928\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0905\u092d\u0940 \u0924\u0915 \u0928\u0939\u0940\u0902 \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"primary-goal-understanding-liver-safety-risks\">\u092e\u0941\u0916\u094d\u092f \u0932\u0915\u094d\u0937\u094d\u092f: \u092f\u0915\u0943\u0924 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u091c\u094b\u0916\u093f\u092e\u094b\u0902 \u0915\u094b \u0938\u092e\u091d\u0928\u093e<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"why-liver-safety-matters\">\u0932\u093f\u0935\u0930 \u0915\u0940 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">ELEVIDYS \u091c\u0948\u0938\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0938\u0947 \u091c\u0941\u0921\u093c\u0940 \u092e\u0941\u0916\u094d\u092f \u091a\u093f\u0902\u0924\u093e\u0913\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0924\u0940\u0935\u094d\u0930 \u092f\u0915\u0943\u0924 \u0915\u094d\u0937\u0924\u093f (ALI) \u0915\u093e \u0916\u0924\u0930\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"role-of-sirolimus\">\u0938\u093f\u0930\u094b\u0932\u093f\u092e\u0938 \u0915\u0940 \u092d\u0942\u092e\u093f\u0915\u093e<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u092f\u0939 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948 \u0915\u093f \u0915\u094d\u092f\u093e \u0938\u093f\u0930\u094b\u0932\u093f\u092e\u0938 \u0915\u094b \u0928\u093f\u0935\u093e\u0930\u0915 (\u092a\u094d\u0930\u094b\u092b\u093f\u0932\u0948\u0915\u094d\u091f\u093f\u0915) \u092a\u094d\u0930\u0924\u093f\u0930\u0915\u094d\u0937\u093e\u0926\u092e\u0928\u0915\u093e\u0930\u0940 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092f\u0915\u0943\u0924 \u0938\u0902\u092c\u0902\u0927\u0940 \u091c\u091f\u093f\u0932\u0924\u093e\u0913\u0902 \u0915\u094b \u0915\u092e \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u093e\u092e\u093e\u0928\u094d\u092f \u0936\u0930\u094d\u0924\u094b\u0902 \u092e\u0947\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>ELEVIDYS \u090f\u0915 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u094b \u092a\u0939\u0941\u0902\u091a\u093e\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/li>\n\n\n\n<li>\u0938\u093f\u0930\u094b\u0932\u093f\u092e\u0938, \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092a\u094d\u0930\u0924\u093f \u092a\u094d\u0930\u0924\u093f\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u0923\u093e\u0932\u0940 \u0915\u0940 \u092a\u094d\u0930\u0924\u093f\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u094b \u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/li>\n\n\n\n<li>\u0907\u0938\u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0909\u092a\u091a\u093e\u0930 \u0915\u0940 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u094b \u0915\u092e \u0915\u093f\u090f \u092c\u093f\u0928\u093e \u0909\u0938\u0947 \u0905\u0927\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u092c\u0928\u093e\u0928\u093e \u0939\u0948\u0964.<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"study-design-and-key-details\">\u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0940 \u0930\u0942\u092a\u0930\u0947\u0916\u093e \u0914\u0930 \u092e\u0941\u0916\u094d\u092f \u0935\u093f\u0935\u0930\u0923<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"trial-overview\">\u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u093e \u0905\u0935\u0932\u094b\u0915\u0928<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u091f\u093e\u0907\u092a \u0915\u0930\u0928\u093e \u0938\u0940\u0916\u094b:<\/strong> \u0905\u0928\u094d\u0924\u0903\u0915\u094d\u0937\u0947\u092a\u0940<\/li>\n\n\n\n<li><strong>\u091a\u0930\u0923:<\/strong> \u091a\u0930\u0923 4<\/li>\n\n\n\n<li><strong>\u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924 \u0928\u093e\u092e\u093e\u0902\u0915\u0928:<\/strong> 20 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940<\/li>\n\n\n\n<li><strong>\u0906\u0930\u0902\u092d \u0915\u0930\u0928\u0947 \u0915\u0940 \u0924\u093f\u0925\u093f:<\/strong> 30 \u0905\u092a\u094d\u0930\u0948\u0932, 2026<\/li>\n\n\n\n<li><strong>\u092a\u0942\u0930\u093e \u0915\u0930\u0928\u0947 \u0915\u0940 \u0924\u093f\u0925\u093f:<\/strong> 31 \u092e\u093e\u0930\u094d\u091a, 2027<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"study-groups-cohorts\">\u0905\u0927\u094d\u092f\u092f\u0928 \u0938\u092e\u0942\u0939 (\u0938\u0939\u092f\u094b\u0917)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u0926\u094b \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940 \u0938\u092e\u0942\u0939 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902:<\/p>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"cohort-1\">\u0938\u092e\u0942\u0939 1:<\/h4>\n\n\n\n<ul class=\"wp-block-list\">\n<li>4 \u0935\u0930\u094d\u0937 \u0914\u0930 \u0909\u0938\u0938\u0947 \u0905\u0927\u093f\u0915 \u0906\u092f\u0941 \u0915\u0947 \u0932\u0921\u093c\u0915\u0947<\/li>\n\n\n\n<li>\u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u094b\u0928\u093e \u091a\u093e\u0939\u093f\u090f (\u091a\u0932\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u094b\u0928\u093e \u091a\u093e\u0939\u093f\u090f)<\/li>\n\n\n\n<li>\u0935\u093e\u0923\u093f\u091c\u094d\u092f\u093f\u0915 ELEVIDYS \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u092a\u093e\u0924\u094d\u0930<\/li>\n<\/ul>\n\n\n\n<h4 class=\"wp-block-heading\" id=\"cohort-2\">\u0938\u092e\u0942\u0939 2:<\/h4>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092a\u0939\u0932\u0947 \u090f\u0932\u0940\u0935\u093f\u0921\u093f\u0938 \u0938\u0947 \u0907\u0932\u093e\u091c \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e<\/li>\n\n\n\n<li>\u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0939\u0940 \u0938\u093f\u0930\u094b\u0932\u093f\u092e\u0938 \u0914\u0930 \u0915\u0949\u0930\u094d\u091f\u093f\u0915\u094b\u0938\u094d\u091f\u0947\u0930\u0949\u0907\u0921\u094d\u0938 \u0926\u093f\u090f \u091c\u093e \u091a\u0941\u0915\u0947 \u0925\u0947\u0964<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"who-can-participate\">\u0915\u094c\u0928 \u092d\u093e\u0917 \u0932\u0947 \u0938\u0915\u0924\u093e \u0939\u0948?<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-inclusion-criteria\">\u092e\u0941\u0916\u094d\u092f \u0938\u092e\u093e\u0935\u0947\u0936\u0928 \u092e\u093e\u0928\u0926\u0902\u0921<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u0930\u0928\u093e \u0939\u094b\u0917\u093e:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u091c\u0928\u094d\u092e \u0915\u0947 \u0938\u092e\u092f \u092a\u0941\u0930\u0941\u0937 \u0939\u094b\u0928\u093e \u091a\u093e\u0939\u093f\u090f<\/li>\n\n\n\n<li>\u0906\u092f\u0941 \u0914\u0930 \u0909\u092a\u091a\u093e\u0930 \u092a\u093e\u0924\u094d\u0930\u0924\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e\u0913\u0902 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u0930\u0947\u0902<\/li>\n\n\n\n<li>\u0926\u0947\u0916\u092d\u093e\u0932\u0915\u0930\u094d\u0924\u093e \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b\u0902 \u092f\u093e \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e\u0913\u0902 \u0915\u093e \u092a\u093e\u0932\u0928 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u094b\u0902\u0964<\/li>\n\n\n\n<li>\u0938\u0942\u091a\u093f\u0924 \u0938\u0939\u092e\u0924\u093f \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0947\u0902 (\u092f\u093e \u0915\u093f\u0938\u0940 \u0915\u093e\u0928\u0942\u0928\u0940 \u0905\u092d\u093f\u092d\u093e\u0935\u0915 \u0938\u0947 \u0910\u0938\u093e \u0915\u0930\u0935\u093e\u090f\u0902)<\/li>\n\n\n\n<li>\u092f\u0926\u093f \u0906\u092a \u092f\u094c\u0928 \u0930\u0942\u092a \u0938\u0947 \u0938\u0915\u094d\u0930\u093f\u092f \u0939\u0948\u0902 \u0924\u094b \u0909\u091a\u093f\u0924 \u0917\u0930\u094d\u092d\u0928\u093f\u0930\u094b\u0927\u0915 \u0915\u093e \u092a\u094d\u0930\u092f\u094b\u0917 \u0915\u0930\u0947\u0902\u0964<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"who-cannot-participate\">\u0915\u094c\u0928 \u092d\u093e\u0917 \u0928\u0939\u0940\u0902 \u0932\u0947 \u0938\u0915\u0924\u093e?<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-exclusion-criteria\">\u092e\u0941\u0916\u094d\u092f \u0905\u092a\u0935\u0930\u094d\u091c\u0928 \u092e\u093e\u0928\u0926\u0902\u0921<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0938\u094d\u0925\u093f\u0924\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0928\u0939\u0940\u0902 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>ELEVIDYS \u0915\u094b \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u0917\u094d\u0930\u0939\u0923 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e<\/li>\n\n\n\n<li>\u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u092a\u094d\u0930\u0915\u093e\u0930 \u0915\u0947 \u0938\u0902\u0915\u094d\u0930\u092e\u0923 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902:\n<ul class=\"wp-block-list\">\n<li>HIV<\/li>\n\n\n\n<li>\u0939\u0947\u092a\u0947\u091f\u093e\u0907\u091f\u093f\u0938 \u092c\u0940 \u092f\u093e \u0938\u0940<\/li>\n<\/ul>\n<\/li>\n\n\n\n<li>\u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u0938\u0902\u0915\u094d\u0930\u092e\u0923 \u0939\u0941\u0906 \u0939\u094b \u092f\u093e \u091f\u0940\u0915\u093e\u0915\u0930\u0923 \u0939\u0941\u0906 \u0939\u094b<\/li>\n\n\n\n<li>\u0910\u0938\u0940 \u0938\u094d\u0925\u093f\u0924\u093f\u092f\u093e\u0901 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948\u0902 \u091c\u094b \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092f\u093e \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u094b \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0915\u0930 \u0938\u0915\u0924\u0940 \u0939\u0948\u0902\u0964<\/li>\n\n\n\n<li>\u0938\u093f\u0930\u094b\u0932\u093f\u092e\u0938 \u0938\u0939\u0928 \u0928\u0939\u0940\u0902 \u0915\u0930 \u0938\u0915\u0924\u093e<\/li>\n\n\n\n<li>\u0910\u0938\u0947 \u0918\u093e\u0935 \u092f\u093e \u091a\u094b\u091f\u0947\u0902 \u0939\u094b\u0928\u093e \u091c\u094b \u092a\u094d\u0930\u0924\u093f\u0930\u0915\u094d\u0937\u093e \u0926\u092e\u0928 \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u092e\u0947\u0902 \u0920\u0940\u0915 \u0938\u0947 \u0920\u0940\u0915 \u0928 \u0939\u094b \u0938\u0915\u0947\u0902<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"why-this-study-is-important-for-the-dmd-community\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u092f\u0939 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"real-world-evidence\">\u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915 \u0926\u0941\u0928\u093f\u092f\u093e \u0915\u0947 \u0938\u093e\u0915\u094d\u0937\u094d\u092f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0939\u0932\u0947 \u0915\u0947 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0915\u0947 \u0935\u093f\u092a\u0930\u0940\u0924, \u092f\u0939 \u0905\u0927\u094d\u092f\u092f\u0928 \u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915 \u091c\u0940\u0935\u0928 \u0915\u0940 \u0909\u092a\u091a\u093e\u0930 \u0938\u094d\u0925\u093f\u0924\u093f\u092f\u094b\u0902 \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0924\u093e \u0939\u0948, \u091c\u093f\u0938\u0938\u0947 \u0921\u0949\u0915\u094d\u091f\u0930\u094b\u0902 \u0915\u094b \u0938\u092e\u091d\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u092e\u093f\u0932\u0924\u0940 \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u0935\u093e\u0924\u093e\u0935\u0930\u0923 \u0915\u0947 \u092c\u093e\u0939\u0930 ELEVIDYS \u0915\u093f\u0924\u0928\u093e \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0939\u0948?<\/li>\n\n\n\n<li>\u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0925 \u092e\u0930\u0940\u091c\u094b\u0902 \u0915\u0940 \u092a\u094d\u0930\u0924\u093f\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u0948\u0938\u0940 \u0930\u0939\u0924\u0940 \u0939\u0948<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"improving-treatment-safety\">\u0909\u092a\u091a\u093e\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f \u092f\u0939 \u0905\u0927\u094d\u092f\u092f\u0928 \u0938\u092b\u0932 \u0939\u094b\u0924\u093e \u0939\u0948, \u0924\u094b \u0907\u0938\u0938\u0947 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u092a\u0930\u093f\u0923\u093e\u092e \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0932\u093f\u0935\u0930 \u0938\u0902\u092c\u0902\u0927\u0940 \u091c\u094b\u0916\u093f\u092e\u094b\u0902 \u0915\u094b \u0915\u092e \u0915\u0930\u0947\u0902<\/li>\n\n\n\n<li>\u0909\u092a\u091a\u093e\u0930 \u092a\u094d\u0930\u094b\u091f\u094b\u0915\u0949\u0932 \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0915\u0930\u0947\u0902<\/li>\n\n\n\n<li>\u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0909\u092a\u092f\u094b\u0917 \u092e\u0947\u0902 \u0935\u093f\u0936\u094d\u0935\u093e\u0938 \u092c\u0922\u093c\u093e\u0928\u093e<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"contact-information\">\u0938\u0902\u092a\u0930\u094d\u0915 \u091c\u093e\u0928\u0915\u093e\u0930\u0940<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0915\u0947 \u0932\u093f\u090f:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0938\u0902\u0917\u0920\u0928:<\/strong> \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0925\u0947\u0930\u0947\u092a\u094d\u092f\u0941\u091f\u093f\u0915\u094d\u0938<\/li>\n\n\n\n<li><strong>\u092b\u093c\u094b\u0928:<\/strong> 1-888-\u0938\u0930\u0947\u092a\u094d\u091f\u093e (1-888-727-3782)<\/li>\n\n\n\n<li><strong>\u0908\u092e\u0947\u0932:<\/strong> <a>SareptAlly@sarepta.com<\/a><\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"clinical-trial-locations-not-yet-announced\">\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0938\u094d\u0925\u093e\u0928\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0905\u092d\u0940 \u0924\u0915 \u0928\u0939\u0940\u0902 \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">ENHANCE \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u0915\u0947 \u0938\u094d\u0925\u093e\u0928\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0905\u092d\u0940 \u0924\u0915 \u0938\u093e\u0930\u094d\u0935\u091c\u0928\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0928\u0939\u0940\u0902 \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u092a\u094d\u0930\u093e\u092f\u094b\u091c\u0915, Sarepta Therapeutics \u0926\u094d\u0935\u093e\u0930\u093e \u092d\u093e\u0917 \u0932\u0947\u0928\u0947 \u0935\u093e\u0932\u0947 \u0938\u094d\u0925\u093e\u0928\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u092c\u093e\u0926 \u092e\u0947\u0902 \u0915\u093f\u090f \u091c\u093e\u0928\u0947 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948\u0964 \u092e\u0930\u0940\u091c\u094b\u0902, \u0926\u0947\u0916\u092d\u093e\u0932\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0914\u0930 \u0938\u094d\u0935\u093e\u0938\u094d\u0925\u094d\u092f \u092a\u0947\u0936\u0947\u0935\u0930\u094b\u0902 \u0915\u094b \u0938\u0932\u093e\u0939 \u0926\u0940 \u091c\u093e\u0924\u0940 \u0939\u0948 \u0915\u093f \u091c\u0948\u0938\u0947 \u0939\u0940 \u0938\u094d\u0925\u093e\u0928\u094b\u0902 \u0915\u0940 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b, \u0906\u0927\u093f\u0915\u093e\u0930\u093f\u0915 \u0905\u092a\u0921\u0947\u091f \u092a\u0930 \u0928\u091c\u093c\u0930 \u0930\u0916\u0947\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The ENHANCE study is a Phase 4 clinical trial designed to evaluate the real-world safety and effectiveness of ELEVIDYS in patients with Duchenne muscular dystrophy (DMD). This study is particularly important because it focuses on patients treated in a post-marketing setting, meaning after the therapy has already been approved and is being used in clinical [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":7684,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,33,179,702,61,65,703],"class_list":["post-7683","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-elevidys","tag-elevidys-gene-therapy","tag-enhance","tag-gene-therapy","tag-sarepta","tag-sirolimus"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/7683","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=7683"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/7683\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/7684"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=7683"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=7683"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=7683"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}