{"id":6340,"date":"2026-04-11T11:19:28","date_gmt":"2026-04-11T08:19:28","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6340"},"modified":"2026-04-11T11:19:30","modified_gmt":"2026-04-11T08:19:30","slug":"investigational-new-drug-ind-clearance-for-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/investigational-new-drug-ind-clearance-for-duchenne-muscular-dystrophy\/","title":{"rendered":"\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u091c\u093e\u0902\u091a\u093e\u0927\u0940\u0928 \u0928\u0908 \u0926\u0935\u093e (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940: \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e, \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0914\u0930 \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u0909\u092a\u091a\u093e\u0930 \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u093e \u092e\u093e\u0930\u094d\u0917 \u0906\u0927\u0941\u0928\u093f\u0915 \u0926\u0935\u093e \u0935\u093f\u0915\u093e\u0938 \u092e\u0947\u0902 \u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0928\u093f\u092f\u093e\u092e\u0915 \u092e\u0940\u0932 \u0915\u0947 \u092a\u0924\u094d\u0925\u0930\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0939\u0948\u0964.<\/strong> \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0938\u0947 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0909\u092a\u091a\u093e\u0930\u094b\u0902\u2014\u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0938\u0947 \u0932\u0947\u0915\u0930 \u090f\u0915\u094d\u0938\u0949\u0928-\u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0926\u0935\u093e\u0913\u0902 \u0924\u0915\u2014\u0915\u094b \u092a\u094d\u0930\u092f\u094b\u0917\u0936\u093e\u0932\u093e \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u0938\u0947 \u092e\u093e\u0928\u0935 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0906\u0917\u0947 \u092c\u0922\u093c\u0928\u0947 \u0915\u0940 \u0905\u0928\u0941\u092e\u0924\u093f \u092e\u093f\u0932\u0924\u0940 \u0939\u0948\u0964 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0915\u0947 \u0938\u0902\u0926\u0930\u094d\u092d \u092e\u0947\u0902, \u091c\u0939\u093e\u0902 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u091c\u0930\u0942\u0930\u0924\u094b\u0902 \u0915\u0940 \u092a\u0942\u0930\u094d\u0924\u093f \u0928\u0939\u0940\u0902 \u0939\u094b \u092a\u093e \u0930\u0939\u0940 \u0939\u0948, \u0906\u0908\u090f\u0928\u0921\u0940 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e\u090f\u0902, \u0906\u0908\u090f\u0928\u0921\u0940 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924\u093f\u092f\u093e\u0902 \u0914\u0930 \u0928\u093f\u092f\u093e\u092e\u0915 \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f\u092f\u093e\u0902 \u0909\u092a\u091a\u093e\u0930 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a \u0914\u0930 \u0928\u0935\u093e\u091a\u093e\u0930 \u0915\u0947 \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u094b \u0906\u0915\u093e\u0930 \u0926\u0947 \u0930\u0939\u0940 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0915 \u0917\u0902\u092d\u0940\u0930 \u090f\u0915\u094d\u0938-\u0932\u093f\u0902\u0915\u094d\u0921 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0935\u093f\u0915\u093e\u0930 \u0939\u0948, \u091c\u093f\u0938\u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u0905\u0928\u0941\u092a\u0938\u094d\u0925\u093f\u0924\u093f \u0915\u0947 \u0915\u093e\u0930\u0923 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u093e \u0927\u0940\u0930\u0947-\u0927\u0940\u0930\u0947 \u0915\u094d\u0937\u092f \u0939\u094b\u0924\u093e \u0939\u0948\u0964 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0914\u0930 \u090f\u0915\u094d\u0938\u0949\u0928-\u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0926\u0935\u093e\u0913\u0902 \u091c\u0948\u0938\u0940 \u0939\u093e\u0932\u093f\u092f\u093e \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926, \u0905\u092d\u0940 \u0924\u0915 \u0907\u0938\u0915\u093e \u0915\u094b\u0908 \u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u0907\u0932\u093e\u091c \u0928\u0939\u0940\u0902 \u0939\u0948\u0964. <strong>\u0907\u0938\u0932\u093f\u090f, \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940 \u0915\u0940 \u0909\u0928 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0915\u093e \u092a\u094d\u0930\u0935\u0947\u0936 \u0926\u094d\u0935\u093e\u0930 \u092c\u0928\u0940 \u0939\u0941\u0908 \u0939\u0948 \u091c\u093f\u0928\u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0915\u0930\u0928\u093e, \u0930\u094b\u0915\u0928\u093e \u092f\u093e \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u0909\u0932\u091f\u0928\u093e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#what-is-an-investigational-new-drug-ind\">\u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#why-ind-clearance-matters-in-duchenne-muscular-dystrophy\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/a><ul><\/ul><\/li><li><a href=\"#the-ind-application-process-for-dmd-therapies\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u0906\u0935\u0947\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e<\/a><ul><\/ul><\/li><li><a href=\"#types-of-ind-applications-relevant-to-dmd\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0906\u0908\u090f\u0928\u0921\u0940 \u0906\u0935\u0947\u0926\u0928\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0915\u093e\u0930<\/a><\/li><li><a href=\"#clinical-trial-phases-after-ind-clearance\">\u0906\u0908\u090f\u0928\u0921\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947 \u092c\u093e\u0926 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u091a\u0930\u0923<\/a><ul><\/ul><\/li><li><a href=\"#recent-ind-clearances-in-duchenne-muscular-dystrophy\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 \u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u0906\u0908\u090f\u0928\u0921\u0940<\/a><ul><\/ul><\/li><li><a href=\"#types-of-therapies-advancing-through-ind-in-dmd\">\u092e\u0927\u0941\u092e\u0947\u0939 \u0930\u094b\u0917 \u092e\u0947\u0902 \u0914\u0926\u094d\u092f\u094b\u0917\u093f\u0915 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u0930 \u0930\u0939\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0915\u093e\u0930<\/a><ul><\/ul><\/li><li><a href=\"#regulatory-designations-supporting-ind-programs\">IND \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e\u094b\u0902 \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u0926\u0928\u093e\u092e<\/a><\/li><li><a href=\"#challenges-in-ind-clearance-for-duchenne-muscular-dystrophy\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092e\u0947\u0902 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0901<\/a><ul><\/ul><\/li><li><a href=\"#ethical-considerations-in-ind-trials-for-dmd\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0928\u0948\u0924\u093f\u0915 \u0935\u093f\u091a\u093e\u0930<\/a><\/li><li><a href=\"#future-outlook-ind-and-the-next-generation-of-dmd-therapies\">\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u0938\u0902\u092d\u093e\u0935\u0928\u093e\u090f\u0902: \u0906\u0908\u090f\u0928\u0921\u0940 \u0914\u0930 \u0921\u0940\u090f\u092e\u0921\u0940 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u0940 \u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940<\/a><\/li><li><a href=\"#frequently-asked-questions-faq\">\u0905\u0915\u094d\u0938\u0930 \u092a\u0942\u091b\u0947 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u0936\u094d\u0928 (FAQ)<\/a><ul><li><a href=\"#faq-question-1775727500437\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#faq-question-1775727515941\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/a><\/li><li><a href=\"#faq-question-1775727522877\">IND \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932\u0928\u0947 \u092e\u0947\u0902 \u0915\u093f\u0924\u0928\u093e \u0938\u092e\u092f \u0932\u0917\u0924\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#faq-question-1775727558323\">IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092e\u093f\u0932\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0915\u094d\u092f\u093e \u0939\u094b\u0924\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#faq-question-1775727593040\">\u0915\u094d\u092f\u093e \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947 \u092c\u093e\u0926 \u092e\u0947\u0930\u093e \u092c\u091a\u094d\u091a\u093e \u0909\u092a\u091a\u093e\u0930 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#faq-question-1775727649350\">\u0915\u094d\u092f\u093e \u0906\u0908\u090f\u0928\u0921\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0909\u092a\u091a\u093e\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0939\u0948\u0902?<\/a><\/li><li><a href=\"#faq-question-1775727682964\">\u0921\u0940\u090f\u092e\u0921\u0940 \u092e\u0947\u0902 \u0915\u093f\u0938 \u092a\u094d\u0930\u0915\u093e\u0930 \u0915\u0940 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094b \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0948?<\/a><\/li><li><a href=\"#faq-question-1775727719710\">\u092a\u0930\u093f\u0935\u093e\u0930 DMD \u0915\u0947 \u0932\u093f\u090f IND \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u0915\u0948\u0938\u0947 \u0916\u094b\u091c \u0938\u0915\u0924\u0947 \u0939\u0948\u0902?<\/a><\/li><li><a href=\"#faq-question-1775727755790\">\u0915\u094d\u092f\u093e \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u093e \u092e\u0924\u0932\u092c \u092f\u0939 \u0939\u0948 \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u0915\u094b \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u090f\u0917\u0940?<\/a><\/li><li><a href=\"#faq-question-1775727770304\">IND \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0928\u0947 \u0915\u0947 \u0915\u094d\u092f\u093e \u091c\u094b\u0916\u093f\u092e \u0939\u0948\u0902?<\/a><\/li><\/ul><\/li><li><a href=\"#final-thoughts\">\u0905\u0902\u0924\u093f\u092e \u0935\u093f\u091a\u093e\u0930<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-an-investigational-new-drug-ind\">\u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u090f\u0915 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u094d\u0930\u093e\u0927\u093f\u0915\u0930\u0923 \u0939\u0948 \u091c\u094b \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0916\u093e\u0926\u094d\u092f \u090f\u0935\u0902 \u0914\u0937\u0927\u093f \u092a\u094d\u0930\u0936\u093e\u0938\u0928 (FDA) \u0926\u094d\u0935\u093e\u0930\u093e \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u091c\u094b \u0915\u093f\u0938\u0940 \u092b\u093e\u0930\u094d\u092e\u093e\u0938\u094d\u092f\u0941\u091f\u093f\u0915\u0932 \u092f\u093e \u092c\u093e\u092f\u094b\u091f\u0947\u0915\u094d\u0928\u094b\u0932\u0949\u091c\u0940 \u0915\u0902\u092a\u0928\u0940 \u0915\u094b \u092e\u0928\u0941\u0937\u094d\u092f\u094b\u0902 \u092e\u0947\u0902 \u090f\u0915 \u0928\u0908 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0905\u0928\u0941\u092e\u0924\u093f \u0926\u0947\u0924\u093e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u093f\u0938\u0940 \u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0936\u0941\u0930\u0942 \u0939\u094b\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947, \u092a\u094d\u0930\u093e\u092f\u094b\u091c\u0915\u094b\u0902 \u0915\u094b \u090f\u0915 IND \u0906\u0935\u0947\u0926\u0928 \u091c\u092e\u093e \u0915\u0930\u0928\u093e \u0939\u094b\u0917\u093e \u091c\u093f\u0938\u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0921\u0947\u091f\u093e (\u092a\u0936\u0941 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u0914\u0937\u0927 \u0935\u093f\u091c\u094d\u091e\u093e\u0928)<\/li>\n\n\n\n<li>\u0935\u093f\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0935\u093f\u0935\u0930\u0923<\/li>\n\n\n\n<li>\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u094d\u0930\u094b\u091f\u094b\u0915\u0949\u0932<\/li>\n\n\n\n<li>\u091c\u093e\u0902\u091a\u0915\u0930\u094d\u0924\u093e \u0915\u0940 \u092f\u094b\u0917\u094d\u092f\u0924\u093e\u090f\u0901<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">FDA 30 \u0926\u093f\u0928\u094b\u0902 \u0915\u0947 \u092d\u0940\u0924\u0930 IND \u0915\u0940 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0915\u0930\u0924\u093e \u0939\u0948\u0964 \u092f\u0926\u093f \u0915\u094b\u0908 \u0906\u092a\u0924\u094d\u0924\u093f \u0928\u0939\u0940\u0902 \u0909\u0920\u093e\u0908 \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b \u092e\u0941\u0915\u0926\u092e\u093e \u0906\u0917\u0947 \u092c\u0922\u093c \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u092f\u0939 \u0938\u0941\u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u0948 \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u094b \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0926\u093f\u090f \u091c\u093e\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0928\u094d\u092f\u0942\u0928\u0924\u092e \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u093e\u0928\u0915\u094b\u0902 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u093f\u092f\u093e \u091c\u093e\u090f\u0964.<\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"409\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-1024x409.png\" alt=\"\u091c\u093e\u0902\u091a\u093e\u0927\u0940\u0928 \u0928\u0908 \u0926\u0935\u093e (IND) \u0906\u0935\u0947\u0926\u0928\" class=\"wp-image-7481\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-1024x409.png 1024w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-300x120.png 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-768x307.png 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-1536x613.png 1536w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-2048x818.png 2048w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-18x7.png 18w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-1052x420.png 1052w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-150x60.png 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-696x278.png 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-1068x426.png 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-1-1-1920x767.png 1920w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"why-ind-clearance-matters-in-duchenne-muscular-dystrophy\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u0947 \u092e\u0939\u0924\u094d\u0935 \u0915\u094b \u0915\u092e \u0915\u0930\u0915\u0947 \u0928\u0939\u0940\u0902 \u0906\u0902\u0915\u093e \u091c\u093e \u0938\u0915\u0924\u093e\u0964.<\/strong> \u0921\u0940\u090f\u092e\u0921\u0940 \u090f\u0915 \u0924\u0947\u091c\u0940 \u0938\u0947 \u092c\u0922\u093c\u0928\u0947 \u0935\u093e\u0932\u0940 \u092c\u0940\u092e\u093e\u0930\u0940 \u0939\u0948, \u0914\u0930 \u0936\u0941\u0930\u0941\u0906\u0924\u0940 \u0939\u0938\u094d\u0924\u0915\u094d\u0937\u0947\u092a \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"key-reasons-ind-clearance-is-vital\">IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948, \u0907\u0938\u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u0915\u093e\u0930\u0923:<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u092e\u093e\u0928\u0935 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0915\u094b \u0938\u0902\u092d\u0935 \u092c\u0928\u093e\u0924\u093e \u0939\u0948<\/strong><\/li>\n\n\n\n<li><strong>\u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u0915\u094b \u092e\u093e\u0928\u094d\u092f \u0915\u0930\u0924\u093e \u0939\u0948<\/strong><\/li>\n\n\n\n<li><strong>\u0926\u0941\u0930\u094d\u0932\u092d \u092c\u0940\u092e\u093e\u0930\u093f\u092f\u094b\u0902 \u0915\u0947 \u0915\u094d\u0937\u0947\u0924\u094d\u0930 \u092e\u0947\u0902 \u0928\u0935\u093e\u091a\u093e\u0930 \u0915\u094b \u0917\u0924\u093f \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u093e \u0939\u0948<\/strong><\/li>\n\n\n\n<li><strong>\u091c\u0940\u0935\u0928 \u092e\u0947\u0902 \u092c\u0926\u0932\u093e\u0935 \u0932\u093e\u0928\u0947 \u0935\u093e\u0932\u0940 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0924\u0915 \u0936\u0940\u0918\u094d\u0930 \u092a\u0939\u0941\u0902\u091a \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u093e \u0939\u0948<\/strong><\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093f\u092f\u093e \u0906\u0902\u0915\u0921\u093c\u094b\u0902 \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u0924\u093e \u0939\u0948 \u0915\u093f \u0935\u093f\u0936\u094d\u0935 \u0938\u094d\u0924\u0930 \u092a\u0930 \u0939\u091c\u093e\u0930\u094b\u0902 \u092c\u091a\u094d\u091a\u0947 \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u0939\u0948\u0902, \u0914\u0930 \u092f\u0941\u0935\u093e\u0935\u0938\u094d\u0925\u093e \u0924\u0915 \u092a\u0939\u0941\u0902\u091a\u0924\u0947-\u092a\u0939\u0941\u0902\u091a\u0924\u0947 \u0909\u0928\u092e\u0947\u0902 \u0915\u093e\u092b\u0940 \u0930\u0941\u0917\u094d\u0923\u0924\u093e \u0914\u0930 \u092e\u0943\u0924\u094d\u092f\u0941 \u0926\u0930 \u0926\u0947\u0916\u0940 \u091c\u093e\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"the-ind-application-process-for-dmd-therapies\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u0906\u0935\u0947\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"preclinical-phase\">\u092a\u0942\u0930\u094d\u0935-\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u091a\u0930\u0923<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947, \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0915\u094b \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u093e\u0930\u094d\u092f \u092a\u0942\u0930\u0947 \u0915\u0930\u0928\u0947 \u0939\u094b\u0902\u0917\u0947:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0935\u093f\u0937 \u0935\u093f\u091c\u094d\u091e\u093e\u0928 \u0905\u0927\u094d\u092f\u092f\u0928<\/li>\n\n\n\n<li>\u092b\u093e\u0930\u094d\u092e\u093e\u0915\u094b\u0915\u093e\u0907\u0928\u0947\u091f\u093f\u0915 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923<\/li>\n\n\n\n<li>\u092a\u0936\u0941 \u092e\u0949\u0921\u0932\u094b\u0902 \u092e\u0947\u0902 \u0905\u0935\u0927\u093e\u0930\u0923\u093e-\u092a\u094d\u0930\u092e\u093e\u0923 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"ind-submission\">IND \u0938\u092c\u092e\u093f\u0936\u0928<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">IND \u0921\u094b\u091c\u093f\u092f\u0930 \u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0930\u0938\u093e\u092f\u0928 \u0935\u093f\u091c\u094d\u091e\u093e\u0928, \u0935\u093f\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0914\u0930 \u0928\u093f\u092f\u0902\u0924\u094d\u0930\u0923 (\u0938\u0940\u090f\u092e\u0938\u0940)<\/li>\n\n\n\n<li>\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u094d\u0930\u094b\u091f\u094b\u0915\u0949\u0932 (\u091a\u0930\u0923 1 \u0921\u093f\u091c\u093e\u0907\u0928)<\/li>\n\n\n\n<li>\u091c\u093e\u0902\u091a\u0915\u0930\u094d\u0924\u093e \u092c\u094d\u0930\u094b\u0936\u0930<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"fda-review\">FDA \u0938\u092e\u0940\u0915\u094d\u0937\u093e<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">FDA \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0924\u093e \u0939\u0948:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u091c\u094b\u0916\u093f\u092e \u092c\u0928\u093e\u092e \u0932\u093e\u092d<\/li>\n\n\n\n<li>\u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0921\u093f\u091c\u093e\u0907\u0928 \u0938\u0941\u0930\u0915\u094d\u0937\u093e<\/li>\n\n\n\n<li>\u0928\u0948\u0924\u093f\u0915 \u0935\u093f\u091a\u093e\u0930<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0926\u093f \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b \u092f\u0939 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u092a\u094d\u0930\u0935\u0947\u0936 \u0915\u0930\u0947\u0917\u0940\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"types-of-ind-applications-relevant-to-dmd\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0906\u0908\u090f\u0928\u0921\u0940 \u0906\u0935\u0947\u0926\u0928\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0915\u093e\u0930<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0938\u0902\u0926\u0930\u094d\u092d \u0915\u0947 \u0906\u0927\u093e\u0930 \u092a\u0930 \u0935\u093f\u092d\u093f\u0928\u094d\u0928 IND \u092e\u093e\u0930\u094d\u0917 \u092e\u094c\u091c\u0942\u0926 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u0935\u093e\u0923\u093f\u091c\u094d\u092f\u093f\u0915 \u0906\u0908\u090f\u0928\u0921\u0940<\/strong> \u2013 \u0926\u0935\u093e \u0935\u093f\u0915\u093e\u0938 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e\u0913\u0902 \u0915\u0947 \u0932\u093f\u090f<\/li>\n\n\n\n<li><strong>\u0905\u0928\u094d\u0935\u0947\u0937\u0915 \u0906\u0908\u090f\u0928\u0921\u0940<\/strong> \u2013 \u0905\u0915\u093e\u0926\u092e\u093f\u0915 \u0928\u0947\u0924\u0943\u0924\u094d\u0935 \u0935\u093e\u0932\u093e \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928<\/li>\n\n\n\n<li><strong>\u0935\u093f\u0938\u094d\u0924\u093e\u0930\u093f\u0924 \u092a\u0939\u0941\u0902\u091a \u0906\u0908\u090f\u0928\u0921\u0940<\/strong> \u2013 \u0917\u0902\u092d\u0940\u0930 \u092e\u093e\u092e\u0932\u094b\u0902 \u092e\u0947\u0902 \u0926\u092f\u093e\u0932\u0941\u0924\u093e\u092a\u0942\u0930\u094d\u0923 \u0909\u092a\u092f\u094b\u0917<\/li>\n\n\n\n<li><strong>\u0909\u092a\u091a\u093e\u0930 \u0906\u0908\u090f\u0928\u0921\u0940<\/strong> \u2013 \u092a\u0942\u0930\u094d\u0923 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0938\u0947 \u092a\u0939\u0932\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u092a\u0939\u0941\u0902\u091a<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0940 \u091c\u0940\u0935\u0928-\u0918\u093e\u0924\u0915 \u092a\u094d\u0930\u0915\u0943\u0924\u093f \u0915\u0947 \u0915\u093e\u0930\u0923 \u092f\u0947 \u092e\u093e\u0930\u094d\u0917 \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u092a\u094d\u0930\u093e\u0938\u0902\u0917\u093f\u0915 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"clinical-trial-phases-after-ind-clearance\">\u0906\u0908\u090f\u0928\u0921\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947 \u092c\u093e\u0926 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u091a\u0930\u0923<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926, \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u091a\u0930\u0923\u094b\u0902 \u092e\u0947\u0902 \u0906\u0917\u0947 \u092c\u0922\u093c\u0924\u0947 \u0939\u0948\u0902:<\/strong><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"phase-1-safety\">\u091a\u0930\u0923 1: \u0938\u0941\u0930\u0915\u094d\u0937\u093e<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u091b\u094b\u091f\u0947 \u0930\u094b\u0917\u0940 \u0938\u092e\u0942\u0939<\/li>\n\n\n\n<li>\u0938\u0939\u0928\u0936\u0940\u0932\u0924\u093e \u092a\u0930 \u0927\u094d\u092f\u093e\u0928 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924 \u0915\u0930\u0947\u0902<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"phase-2-efficacy-and-dosing\">\u091a\u0930\u0923 2: \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0914\u0930 \u0916\u0941\u0930\u093e\u0915<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092c\u0921\u093c\u0947 \u0938\u092e\u0942\u0939<\/li>\n\n\n\n<li>\u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0938\u0902\u0915\u0947\u0924<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"phase-3-confirmation\">\u091a\u0930\u0923 3: \u092a\u0941\u0937\u094d\u091f\u093f<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092c\u0921\u093c\u0947 \u092a\u0948\u092e\u093e\u0928\u0947 \u092a\u0930 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/li>\n\n\n\n<li>\u092e\u093e\u0928\u0915 \u0926\u0947\u0916\u092d\u093e\u0932 \u0915\u0947 \u0938\u093e\u0925 \u0924\u0941\u0932\u0928\u093e<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"phase-4-post-marketing\">\u091a\u0930\u0923 4: \u0935\u093f\u092a\u0923\u0928\u094b\u0924\u094d\u0924\u0930<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0928\u093f\u0917\u0930\u093e\u0928\u0940<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0924\u094d\u092f\u0947\u0915 \u091a\u0930\u0923 \u092a\u0942\u0930\u094d\u0923 \u0928\u093f\u092f\u093e\u092e\u0915 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0915\u0947 \u0932\u093f\u090f \u0906\u0935\u0936\u094d\u092f\u0915 \u0938\u093e\u0915\u094d\u0937\u094d\u092f \u091c\u0941\u091f\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/drug-development-phases\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0914\u0937\u0927\u093f \u0935\u093f\u0915\u093e\u0938 \u0915\u0947 5 \u091a\u0930\u0923\u094b\u0902 \u0915\u093e \u0905\u0928\u094d\u0935\u0947\u0937\u0923 \u0915\u0930\u0947\u0902<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"recent-ind-clearances-in-duchenne-muscular-dystrophy\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 \u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u0906\u0908\u090f\u0928\u0921\u0940<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u093e \u092a\u0930\u093f\u0926\u0943\u0936\u094d\u092f \u0924\u0947\u091c\u0940 \u0938\u0947 \u092c\u0926\u0932 \u0930\u0939\u093e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"example-ryoncil-remestemcel-l\">\u0909\u0926\u093e\u0939\u0930\u0923: Ryoncil (\u0930\u0947\u092e\u0947\u0938\u094d\u091f\u0947\u092e\u0938\u0947\u0932-\u090f\u0932)<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092a\u0902\u091c\u0940\u0915\u0930\u0923 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0932\u093f\u090f IND \u092e\u0902\u091c\u0942\u0930\u0940 \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0940 \u0917\u0908<\/li>\n\n\n\n<li>\u092e\u0927\u0941\u092e\u0947\u0939 \u0930\u094b\u0917 \u092e\u0947\u0902 \u0938\u0942\u091c\u0928 \u0915\u094b \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948<\/li>\n\n\n\n<li>\u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f \u0915\u094b \u0938\u0902\u0930\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0928\u0947 \u092a\u0930 \u0927\u094d\u092f\u093e\u0928 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924 \u0915\u0930\u0947\u0902<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f \u092e\u0947\u0938\u0947\u0928\u0915\u093e\u0907\u092e\u0932 \u0938\u094d\u091f\u094d\u0930\u094b\u092e\u0932 \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u092a\u0930 \u0906\u0927\u093e\u0930\u093f\u0924 \u0939\u0948 \u0914\u0930 \u0907\u0938\u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u090a\u0924\u0915\u094b\u0902 \u092e\u0947\u0902 \u0938\u0942\u091c\u0928 \u0938\u0902\u092c\u0902\u0927\u0940 \u0915\u094d\u0937\u0924\u093f \u0915\u094b \u0915\u092e \u0915\u0930\u0928\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"example-pbgene-dmd-gene-editing-therapy\">\u0909\u0926\u093e\u0939\u0930\u0923: PBGENE-DMD \u091c\u0940\u0928 \u090f\u0921\u093f\u091f\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0914\u0930 \u092b\u093e\u0938\u094d\u091f \u091f\u094d\u0930\u0948\u0915 \u092a\u0926\u0928\u093e\u092e \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0941\u0906\u0964<\/li>\n\n\n\n<li>\u091c\u0940\u0928\u094b\u092e \u0938\u0902\u092a\u093e\u0926\u0928 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0915\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u094b \u092c\u0939\u093e\u0932 \u0915\u0930\u0924\u093e \u0939\u0948<\/li>\n\n\n\n<li>\u0921\u0940\u090f\u092e\u0921\u0940 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 601\u091f\u0940\u092a\u0940163\u091f\u0940 \u0924\u0915 \u0915\u0947 \u0932\u0915\u094d\u0937\u094d\u092f<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"ongoing-clinical-trials\">\u091a\u0932 \u0930\u0939\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0908 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0909\u092a\u091a\u093e\u0930 \u0906\u0908\u090f\u0928\u0921\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947 \u0924\u0939\u0924 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>ENTR-601-44 (\u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917)<\/li>\n\n\n\n<li>INS1201 (\u0928\u0935\u0940\u0928 \u0935\u093f\u0924\u0930\u0923 \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901)<\/li>\n\n\n\n<li>\u090f\u0938\u091c\u0940\u091f\u0940-003 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940<\/li>\n<\/ul>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"types-of-therapies-advancing-through-ind-in-dmd\">\u092e\u0927\u0941\u092e\u0947\u0939 \u0930\u094b\u0917 \u092e\u0947\u0902 \u0914\u0926\u094d\u092f\u094b\u0917\u093f\u0915 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u0930 \u0930\u0939\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0915\u093e\u0930<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"1-gene-therapy\">1. \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u094b \u0936\u0930\u0940\u0930 \u092e\u0947\u0902 \u092a\u0939\u0941\u0902\u091a\u093e\u0928\u093e \u0939\u0948\u0964.<br>\u0909\u0926\u093e\u0939\u0930\u0923: \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u0939\u0932\u0947 \u0938\u0947 \u0939\u0940 \u0906\u0936\u093e\u091c\u0928\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0926\u093f\u0916\u093e \u0930\u0939\u0940 \u0939\u0948\u0902, \u0932\u0947\u0915\u093f\u0928 \u0905\u092d\u0940 \u092d\u0940 \u0909\u0928\u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"2-exon-skipping\">2. \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0930\u0940\u0921\u093f\u0902\u0917 \u092b\u094d\u0930\u0947\u092e \u0915\u094b \u092c\u0939\u093e\u0932 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0935\u093f\u0936\u093f\u0937\u094d\u091f \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928\u094b\u0902 \u0915\u094b \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"3-gene-editing-crispr-like\">3. \u091c\u0940\u0928 \u0938\u0902\u092a\u093e\u0926\u0928 (\u0915\u094d\u0930\u093f\u0938\u092a\u0940\u0906\u0930-\u091c\u0948\u0938\u0947)<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0926\u094b\u0937\u094b\u0902 \u0915\u093e \u0938\u094d\u0925\u093e\u092f\u0940 \u0909\u092a\u091a\u093e\u0930\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"4-cell-therapy\">4. \u0938\u0947\u0932 \u0925\u0947\u0930\u0947\u092a\u0940<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u090a\u0924\u0915\u094b\u0902 \u0915\u094b \u092a\u0941\u0928\u0930\u094d\u091c\u0940\u0935\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0938\u094d\u091f\u0947\u092e \u0915\u094b\u0936\u093f\u0915\u093e\u0913\u0902 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"5-anti-inflammatory-approaches\">5. \u0938\u0942\u091c\u0928\u0930\u094b\u0927\u0940 \u0909\u092a\u093e\u092f<\/h3>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0938\u0942\u091c\u0928 \u091c\u0948\u0938\u0940 \u0926\u094d\u0935\u093f\u0924\u0940\u092f\u0915 \u0930\u094b\u0917 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e\u0913\u0902 \u0915\u094b \u0938\u0902\u092c\u094b\u0927\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"regulatory-designations-supporting-ind-programs\">IND \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e\u094b\u0902 \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u0926\u0928\u093e\u092e<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092e\u0947\u0902 \u0924\u0947\u091c\u0940 \u0932\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f, FDA \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0938\u0941\u0935\u093f\u0927\u093e\u090f\u0901 \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u093e \u0939\u0948:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092b\u093e\u0938\u094d\u091f \u091f\u094d\u0930\u0948\u0915 \u092a\u0926\u0928\u093e\u092e<\/li>\n\n\n\n<li>\u0905\u0928\u093e\u0925 \u0914\u0937\u0927\u093f \u092a\u0926\u0928\u093e\u092e<\/li>\n\n\n\n<li>\u092c\u094d\u0930\u0947\u0915\u0925\u094d\u0930\u0942 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u0926\u0928\u093e\u092e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0947 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0935\u093f\u0915\u093e\u0938 \u0915\u0940 \u0938\u092e\u092f\u0938\u0940\u092e\u093e \u0915\u094b \u0915\u092e \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u0928\u093f\u092f\u093e\u092e\u0915\u0940\u092f \u092c\u093e\u0924\u091a\u0940\u0924 \u0915\u094b \u0938\u0941\u0917\u092e \u092c\u0928\u093e\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"challenges-in-ind-clearance-for-duchenne-muscular-dystrophy\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092e\u0947\u0902 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0901<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0917\u0924\u093f \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926, \u0915\u0908 \u092c\u093e\u0927\u093e\u090f\u0902 \u0905\u092d\u0940 \u092d\u0940 \u092c\u0928\u0940 \u0939\u0941\u0908 \u0939\u0948\u0902:<\/p>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"scientific-challenges\">\u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0901<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0935\u093f\u0937\u092e\u0924\u093e<\/li>\n\n\n\n<li>\u092a\u0936\u0941 \u092e\u0949\u0921\u0932 \u0915\u0940 \u092a\u0942\u0930\u094d\u0935\u093e\u0928\u0941\u092e\u093e\u0928 \u0915\u094d\u0937\u092e\u0924\u093e \u0938\u0940\u092e\u093f\u0924 \u0939\u0948<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"regulatory-challenges\">\u0928\u093f\u092f\u093e\u092e\u0915 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0901<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0909\u091a\u094d\u091a \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u093e\u0928\u0915<\/li>\n\n\n\n<li>\u091c\u091f\u093f\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u0930\u093f\u0923\u093e\u092e<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\" id=\"economic-challenges\">\u0906\u0930\u094d\u0925\u093f\u0915 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0901<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u0935\u093f\u0915\u093e\u0938 \u0915\u0940 \u0932\u093e\u0917\u0924 \u092c\u0947\u0939\u0926 \u0905\u0927\u093f\u0915 \u0939\u0948<\/li>\n\n\n\n<li>\u0938\u0940\u092e\u093f\u0924 \u0930\u094b\u0917\u0940 \u0906\u092c\u093e\u0926\u0940<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939\u093e\u0902 \u0924\u0915 \u0915\u093f \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u0909\u092a\u091a\u093e\u0930 \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0915\u094b \u092d\u0940 \u0905\u0915\u094d\u0938\u0930 \u092a\u0939\u0941\u0902\u091a \u0914\u0930 \u092a\u094d\u0930\u0924\u093f\u092a\u0942\u0930\u094d\u0924\u093f \u0938\u0902\u092c\u0902\u0927\u0940 \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u094b\u0902 \u0915\u093e \u0938\u093e\u092e\u0928\u093e \u0915\u0930\u0928\u093e \u092a\u0921\u093c\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"ethical-considerations-in-ind-trials-for-dmd\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0928\u0948\u0924\u093f\u0915 \u0935\u093f\u091a\u093e\u0930<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u0947\u0902 \u0928\u0948\u0924\u093f\u0915\u0924\u093e \u090f\u0915 \u0915\u0947\u0902\u0926\u094d\u0930\u0940\u092f \u092d\u0942\u092e\u093f\u0915\u093e \u0928\u093f\u092d\u093e\u0924\u0940 \u0939\u0948:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u092c\u093e\u0932 \u0930\u094b\u0917\u0940 \u0915\u0940 \u092d\u093e\u0917\u0940\u0926\u093e\u0930\u0940<\/li>\n\n\n\n<li>\u0938\u0942\u091a\u093f\u0924 \u0938\u0939\u092e\u0924\u093f \u0915\u0940 \u091c\u091f\u093f\u0932\u0924\u093e\u090f\u0901<\/li>\n\n\n\n<li>\u091c\u094b\u0916\u093f\u092e-\u0932\u093e\u092d \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u091a\u0930\u0923 \u0915\u0947 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u092d\u093e\u0917 \u0932\u0947\u0928\u0947 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0905\u0915\u094d\u0938\u0930 \u0915\u0920\u093f\u0928 \u0928\u093f\u0930\u094d\u0923\u092f\u094b\u0902 \u0915\u093e \u0938\u093e\u092e\u0928\u093e \u0915\u0930\u0928\u093e \u092a\u0921\u093c\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"future-outlook-ind-and-the-next-generation-of-dmd-therapies\">\u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u0938\u0902\u092d\u093e\u0935\u0928\u093e\u090f\u0902: \u0906\u0908\u090f\u0928\u0921\u0940 \u0914\u0930 \u0921\u0940\u090f\u092e\u0921\u0940 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u0940 \u0905\u0917\u0932\u0940 \u092a\u0940\u0922\u093c\u0940<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u093e \u092d\u0935\u093f\u0937\u094d\u092f \u0909\u092d\u0930\u0924\u0940 \u0939\u0941\u0908 \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u093f\u092f\u094b\u0902 \u0938\u0947 \u0928\u093f\u0915\u091f\u0924\u093e \u0938\u0947 \u091c\u0941\u0921\u093c\u093e \u0939\u0941\u0906 \u0939\u0948:<\/strong><\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>CRISPR-\u0906\u0927\u093e\u0930\u093f\u0924 \u091c\u0940\u0928 \u0938\u0902\u092a\u093e\u0926\u0928<\/li>\n\n\n\n<li>\u0906\u0930\u090f\u0928\u090f-\u0906\u0927\u093e\u0930\u093f\u0924 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901<\/li>\n\n\n\n<li>\u0938\u0902\u092f\u094b\u091c\u0928 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e\u090f\u0901<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u0948\u0938\u0947-\u091c\u0948\u0938\u0947 \u0928\u093f\u092f\u093e\u092e\u0915 \u0922\u093e\u0902\u091a\u0947 \u0935\u093f\u0915\u0938\u093f\u0924 \u0939\u094b\u0924\u0947 \u0939\u0948\u0902, \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0940 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0924\u0947\u091c \u0914\u0930 \u0905\u0927\u093f\u0915 \u0905\u0928\u0941\u0915\u0942\u0932 \u0939\u094b \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n\n\n<figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"683\" height=\"1024\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-683x1024.png\" alt=\"\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u091c\u093e\u0902\u091a\u093e\u0927\u0940\u0928 \u0928\u0908 \u0926\u0935\u093e (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940: \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e, \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0914\u0930 \u092d\u0935\u093f\u0937\u094d\u092f \u0915\u0940 \u0909\u092a\u091a\u093e\u0930 \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901\" class=\"wp-image-7463\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-683x1024.png 683w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-200x300.png 200w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-768x1152.png 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-8x12.png 8w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-280x420.png 280w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-150x225.png 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-300x450.png 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance-696x1044.png 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/04\/Investigational-New-Drug-IND-Clearance.png 1024w\" sizes=\"auto, (max-width: 683px) 100vw, 683px\" \/><\/figure>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"frequently-asked-questions-faq\">\u0905\u0915\u094d\u0938\u0930 \u092a\u0942\u091b\u0947 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u0936\u094d\u0928 (FAQ)<\/h2>\n\n\n<div id=\"rank-math-faq\" class=\"rank-math-block\">\n<div class=\"rank-math-list\">\n<div id=\"faq-question-1775727500437\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 FDA \u092a\u094d\u0930\u093e\u0927\u093f\u0915\u0930\u0923 \u0939\u0948, \u091c\u094b \u090f\u0915 \u0928\u0908 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0915\u094b \u092e\u093e\u0928\u0935 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0905\u0928\u0941\u092e\u0924\u093f \u0926\u0947\u0924\u093e \u0939\u0948\u0964 \u092f\u0939 \u092a\u0941\u0937\u094d\u091f\u093f \u0915\u0930\u0924\u093e \u0939\u0948 \u0915\u093f \u092a\u094d\u0930\u0940\u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0921\u0947\u091f\u093e (\u092a\u094d\u0930\u092f\u094b\u0917\u0936\u093e\u0932\u093e \u0914\u0930 \u092a\u0936\u0941 \u0905\u0927\u094d\u092f\u092f\u0928) \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092a\u0930\u094d\u092f\u093e\u092a\u094d\u0924 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0926\u0930\u094d\u0936\u093e\u0924\u0947 \u0939\u0948\u0902\u0964 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092f\u093e \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u091c\u0948\u0938\u0940 \u0915\u093f\u0938\u0940 \u092d\u0940 \u0928\u0908 DMD \u0909\u092a\u091a\u093e\u0930 \u092a\u0926\u094d\u0927\u0924\u093f \u0915\u093e \u092c\u091a\u094d\u091a\u094b\u0902 \u092e\u0947\u0902 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u092f\u0939 \u091a\u0930\u0923 \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727515941\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u094d\u092f\u094b\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092c\u0947\u0939\u0926 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0907\u0938\u0938\u0947 \u0909\u0928 \u0928\u0908 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u094b\u0902 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a \u0916\u0941\u0932\u0924\u0940 \u0939\u0948 \u091c\u093f\u0928\u094d\u0939\u0947\u0902 \u0905\u092d\u0940 \u0924\u0915 \u092e\u0902\u091c\u0942\u0930\u0940 \u0928\u0939\u0940\u0902 \u092e\u093f\u0932\u0940 \u0939\u0948\u0964 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u093f\u0924 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f, \u092f\u0939 \u0905\u0924\u094d\u092f\u093e\u0927\u0941\u0928\u093f\u0915 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0938\u0947 \u0932\u093e\u092d \u0909\u0920\u093e\u0928\u0947 \u0915\u093e \u092a\u0939\u0932\u093e \u0935\u093e\u0938\u094d\u0924\u0935\u093f\u0915 \u0905\u0935\u0938\u0930 \u0939\u0948 \u091c\u094b \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902 \u092f\u093e \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964 \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947 \u092c\u093f\u0928\u093e, \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u093e\u0928\u0942\u0928\u0940 \u0930\u0942\u092a \u0938\u0947 \u0936\u0941\u0930\u0942 \u0928\u0939\u0940\u0902 \u0939\u094b \u0938\u0915\u0924\u0947\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727522877\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">IND \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932\u0928\u0947 \u092e\u0947\u0902 \u0915\u093f\u0924\u0928\u093e \u0938\u092e\u092f \u0932\u0917\u0924\u093e \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>FDA \u0906\u092e\u0924\u094c\u0930 \u092a\u0930 30 \u0926\u093f\u0928\u094b\u0902 \u0915\u0947 \u092d\u0940\u0924\u0930 IND \u0906\u0935\u0947\u0926\u0928 \u0915\u0940 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0915\u0930\u0924\u093e \u0939\u0948\u0964 \u092f\u0926\u093f \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u0915\u094b\u0908 \u091a\u093f\u0902\u0924\u093e \u0928\u0939\u0940\u0902 \u092a\u093e\u0908 \u091c\u093e\u0924\u0940 \u0939\u0948, \u0924\u094b \u0905\u0927\u094d\u092f\u092f\u0928 \u0906\u0917\u0947 \u092c\u0922\u093c \u0938\u0915\u0924\u093e \u0939\u0948\u0964 \u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u0924\u0948\u092f\u093e\u0930\u0940 \u0915\u093e \u091a\u0930\u0923\u2014\u092a\u094d\u0930\u0940\u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0905\u0927\u094d\u092f\u092f\u0928, \u0935\u093f\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0914\u0930 \u0926\u0938\u094d\u0924\u093e\u0935\u0947\u091c\u093c\u0940\u0915\u0930\u0923\u2014\u0906\u0935\u0947\u0926\u0928 \u091c\u092e\u093e \u0915\u0930\u0928\u0947 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0915\u0908 \u0938\u093e\u0932 \u0932\u0917 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727558323\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">IND \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092e\u093f\u0932\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0915\u094d\u092f\u093e \u0939\u094b\u0924\u093e \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926, \u092f\u0939 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u092e\u0947\u0902 \u092a\u094d\u0930\u0935\u0947\u0936 \u0915\u0930\u0924\u0940 \u0939\u0948\u0964 \u092f\u0947 \u091f\u094d\u0930\u093e\u092f\u0932 \u0935\u093f\u092d\u093f\u0928\u094d\u0928 \u091a\u0930\u0923\u094b\u0902 \u0938\u0947 \u0917\u0941\u091c\u0930\u0924\u0947 \u0939\u0948\u0902:<\/p>\n<p>\u2022 \u091a\u0930\u0923 1: \u0938\u0941\u0930\u0915\u094d\u0937\u093e<br \/>\u2022 \u091a\u0930\u0923 2: \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0914\u0930 \u0916\u0941\u0930\u093e\u0915<br \/>\u2022 \u091a\u0930\u0923 3: \u092c\u0921\u093c\u0947 \u092a\u0948\u092e\u093e\u0928\u0947 \u092a\u0930 \u0938\u0924\u094d\u092f\u093e\u092a\u0928<\/p>\n<p>\u092a\u094d\u0930\u0924\u094d\u092f\u0947\u0915 \u091a\u0930\u0923 \u092e\u0947\u0902 \u092a\u0942\u0930\u094d\u0923 \u0928\u093f\u092f\u093e\u092e\u0915 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0915\u0947 \u0932\u093f\u090f \u0906\u0935\u0936\u094d\u092f\u0915 \u0921\u0947\u091f\u093e \u090f\u0915\u0924\u094d\u0930 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727593040\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0915\u094d\u092f\u093e \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947 \u092c\u093e\u0926 \u092e\u0947\u0930\u093e \u092c\u091a\u094d\u091a\u093e \u0909\u092a\u091a\u093e\u0930 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u092f\u0939 \u0938\u094d\u0935\u0924\u0903 \u0928\u0939\u0940\u0902 \u0939\u094b\u0924\u093e\u0964 IND \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932\u0928\u0947 \u092a\u0930 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0915\u093f\u090f \u091c\u093e \u0938\u0915\u0924\u0947 \u0939\u0948\u0902, \u0932\u0947\u0915\u093f\u0928 \u092d\u093e\u0917\u0940\u0926\u093e\u0930\u0940 \u092a\u093e\u0924\u094d\u0930\u0924\u093e \u092e\u093e\u0928\u0926\u0902\u0921\u094b\u0902 \u092a\u0930 \u0928\u093f\u0930\u094d\u092d\u0930 \u0915\u0930\u0924\u0940 \u0939\u0948, \u091c\u0948\u0938\u0947 \u0915\u093f \u0906\u092f\u0941, \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u093e \u092a\u094d\u0930\u0915\u093e\u0930 \u0914\u0930 \u0930\u094b\u0917 \u0915\u0940 \u0905\u0935\u0938\u094d\u0925\u093e\u0964 \u0915\u0941\u091b \u092e\u093e\u092e\u0932\u094b\u0902 \u092e\u0947\u0902, \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u092a\u093e\u0924\u094d\u0930 \u0928 \u0939\u094b\u0928\u0947 \u0935\u093e\u0932\u0947 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0935\u093f\u0938\u094d\u0924\u093e\u0930\u093f\u0924 \u092a\u0939\u0941\u0902\u091a \u092f\u093e \u0926\u092f\u093e\u0932\u0941 \u0909\u092a\u092f\u094b\u0917 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727649350\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0915\u094d\u092f\u093e \u0906\u0908\u090f\u0928\u0921\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0909\u092a\u091a\u093e\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0939\u0948\u0902?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u093e \u092e\u0924\u0932\u092c \u0939\u0948 \u0915\u093f \u0925\u0947\u0930\u0947\u092a\u0940 \u0928\u0947 \u092a\u094d\u0930\u0940\u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u092e\u0947\u0902 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u091c\u093e\u0902\u091a \u092a\u093e\u0938 \u0915\u0930 \u0932\u0940 \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 \u092f\u0939 \u092a\u0942\u0930\u094d\u0923 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092f\u093e \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u0940 \u0917\u093e\u0930\u0902\u091f\u0940 \u0928\u0939\u0940\u0902 \u0926\u0947\u0924\u093e \u0939\u0948\u0964 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u091c\u094b\u0916\u093f\u092e\u094b\u0902 \u0914\u0930 \u0932\u093e\u092d\u094b\u0902 \u0915\u0940 \u092a\u0939\u091a\u093e\u0928 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u090f \u0917\u090f \u0939\u0948\u0902\u0964 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u094d\u0930\u094b\u091f\u094b\u0915\u0949\u0932 \u0915\u0940 \u0938\u093e\u0935\u0927\u093e\u0928\u0940\u092a\u0942\u0930\u094d\u0935\u0915 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0915\u0930\u0928\u0940 \u091a\u093e\u0939\u093f\u090f \u0914\u0930 \u0928\u093e\u092e\u093e\u0902\u0915\u0928 \u0938\u0947 \u092a\u0939\u0932\u0947 \u0935\u093f\u0936\u0947\u0937\u091c\u094d\u091e\u094b\u0902 \u0938\u0947 \u092a\u0930\u093e\u092e\u0930\u094d\u0936 \u0915\u0930\u0928\u093e \u091a\u093e\u0939\u093f\u090f\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727682964\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0921\u0940\u090f\u092e\u0921\u0940 \u092e\u0947\u0902 \u0915\u093f\u0938 \u092a\u094d\u0930\u0915\u093e\u0930 \u0915\u0940 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094b \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0948?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u091c\u093f\u0928 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u094b \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0941\u0906 \u0939\u0948, \u0909\u0928\u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902:<\/p>\n<p>\u2022 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 (\u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0921\u093f\u0932\u0940\u0935\u0930\u0940)<br \/>\u2022 \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0921\u094d\u0930\u0917\u094d\u0938<br \/>\u2022 \u091c\u0940\u0928 \u0938\u0902\u092a\u093e\u0926\u0928 \u0935\u093f\u0927\u093f\u092f\u093e\u0901 (\u0915\u094d\u0930\u093f\u0938\u092a\u0940\u0906\u0930-\u0906\u0927\u093e\u0930\u093f\u0924)<br \/>\u2022 \u0938\u0947\u0932 \u0925\u0947\u0930\u0947\u092a\u0940<br \/>\u2022 \u0938\u0942\u091c\u0928\u0930\u094b\u0927\u0940 \u0909\u092a\u091a\u093e\u0930<\/p>\n<p>\u092a\u094d\u0930\u0924\u094d\u092f\u0947\u0915 \u0909\u092a\u091a\u093e\u0930 \u0930\u094b\u0917 \u0915\u0947 \u0935\u093f\u092d\u093f\u0928\u094d\u0928 \u092a\u0939\u0932\u0941\u0913\u0902 \u0915\u094b \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727719710\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u092a\u0930\u093f\u0935\u093e\u0930 DMD \u0915\u0947 \u0932\u093f\u090f IND \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u0915\u0948\u0938\u0947 \u0916\u094b\u091c \u0938\u0915\u0924\u0947 \u0939\u0948\u0902?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u092a\u0930\u093f\u0935\u093e\u0930 \u0938\u0915\u094d\u0930\u093f\u092f \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0915\u0940 \u0916\u094b\u091c \u0928\u093f\u092e\u094d\u0928 \u092e\u093e\u0927\u094d\u092f\u092e\u094b\u0902 \u0938\u0947 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902:<\/p>\n<p>\u2022 1\u091f\u0940\u092a\u094042\u091f\u0940<br \/>\u2022 \u0928\u094d\u092f\u0942\u0930\u094b\u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0915\u094d\u0932\u0940\u0928\u093f\u0915<br \/>\u2022 \u0930\u094b\u0917\u0940 \u0935\u0915\u093e\u0932\u0924 \u0938\u0902\u0917\u0920\u0928<\/p>\n<p>&quot;\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 IND \u091f\u094d\u0930\u093e\u092f\u0932&quot; \u091c\u0948\u0938\u0947 \u0915\u0940\u0935\u0930\u094d\u0921 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0928\u0947 \u0938\u0947 \u092a\u094d\u0930\u093e\u0938\u0902\u0917\u093f\u0915 \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u0914\u0930 \u092d\u0930\u094d\u0924\u0940 \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u0915\u0940 \u092a\u0939\u091a\u093e\u0928 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727755790\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">\u0915\u094d\u092f\u093e \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u094d\u0932\u0940\u092f\u0930\u0947\u0902\u0938 \u0915\u093e \u092e\u0924\u0932\u092c \u092f\u0939 \u0939\u0948 \u0915\u093f \u0909\u092a\u091a\u093e\u0930 \u0915\u094b \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u091c\u093e\u090f\u0917\u0940?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p><strong>\u0928\u0939\u0940\u0902\u0964 IND \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0915\u0947\u0935\u0932 \u092a\u0939\u0932\u093e \u0928\u093f\u092f\u093e\u092e\u0915 \u091a\u0930\u0923 \u0939\u0948\u0964.<\/strong> \u0915\u0908 \u0909\u092a\u091a\u093e\u0930 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u0940 \u0915\u092e\u0940 \u092f\u093e \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u092c\u0902\u0927\u0940 \u091a\u093f\u0902\u0924\u093e\u0913\u0902 \u0915\u0947 \u0915\u093e\u0930\u0923 \u0935\u093f\u092b\u0932 \u0939\u094b \u091c\u093e\u0924\u0947 \u0939\u0948\u0902\u0964 \u0915\u0947\u0935\u0932 \u0935\u0947 \u0909\u092a\u091a\u093e\u0930 \u091c\u094b \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0938\u092d\u0940 \u091a\u0930\u0923\u094b\u0902 \u0915\u094b \u0938\u092b\u0932\u0924\u093e\u092a\u0942\u0930\u094d\u0935\u0915 \u092a\u0942\u0930\u093e \u0915\u0930\u0924\u0947 \u0939\u0948\u0902, \u092a\u0942\u0930\u094d\u0923 FDA \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0915\u0947 \u0932\u093f\u090f \u0906\u0935\u0947\u0926\u0928 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n<\/div>\n<\/div>\n<div id=\"faq-question-1775727770304\" class=\"rank-math-list-item\">\n<h3 class=\"rank-math-question\">IND \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0928\u0947 \u0915\u0947 \u0915\u094d\u092f\u093e \u091c\u094b\u0916\u093f\u092e \u0939\u0948\u0902?<\/h3>\n<div class=\"rank-math-answer\">\n\n<p>\u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e\u090f\u0902 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0924\u0940 \u0939\u0948\u0902\u0964 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u091c\u094b\u0916\u093f\u092e\u094b\u0902 \u092e\u0947\u0902 \u0928\u093f\u092e\u094d\u0928\u0932\u093f\u0916\u093f\u0924 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902:<\/p>\n<p>\u2022 \u0905\u091c\u094d\u091e\u093e\u0924 \u0926\u0941\u0937\u094d\u092a\u094d\u0930\u092d\u093e\u0935<br \/>\u2022 \u0938\u0940\u092e\u093f\u0924 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e<br \/>\u2022 \u092c\u093e\u0930-\u092c\u093e\u0930 \u0905\u0938\u094d\u092a\u0924\u093e\u0932 \u091c\u093e\u0928\u093e \u0914\u0930 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0930\u0935\u093e\u0928\u093e<\/p>\n<p>\u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0906\u0936\u093e\u091c\u0928\u0915 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0924\u0915 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u092a\u0939\u0941\u0902\u091a \u092d\u0940 \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u0938\u092d\u0940 \u0921\u0940\u090f\u092e\u0921\u0940 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u0915\u094b \u0906\u0917\u0947 \u092c\u0922\u093c\u093e\u0928\u0947 \u092e\u0947\u0902 \u092f\u094b\u0917\u0926\u093e\u0928 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n<\/div>\n<\/div>\n<\/div>\n<\/div>\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/www.fda.gov\/drugs\/types-applications\/investigational-new-drug-ind-application\" target=\"_blank\" rel=\"noreferrer noopener\">FDA IND<\/a><\/p>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"final-thoughts\">\u0905\u0902\u0924\u093f\u092e \u0935\u093f\u091a\u093e\u0930<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0907\u0928\u094d\u0935\u0947\u0938\u094d\u091f\u093f\u0917\u0947\u0936\u0928\u0932 \u0928\u094d\u092f\u0942 \u0921\u094d\u0930\u0917 (IND) \u0915\u0940 \u092e\u0902\u091c\u0942\u0930\u0940 \u0928\u0935\u093e\u091a\u093e\u0930 \u0915\u093e \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0926\u094d\u0935\u093e\u0930 \u092c\u0928\u0940 \u0939\u0941\u0908 \u0939\u0948\u0964.<\/strong> \u092f\u0939 \u0928\u093f\u0930\u094d\u0927\u093e\u0930\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948 \u0915\u093f \u0915\u094c\u0928 \u0938\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u0926\u094d\u0927\u0924\u093f\u092f\u093e\u0901 \u092e\u093e\u0928\u0935 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0906\u0917\u0947 \u092c\u0922\u093c\u0947\u0902\u0917\u0940 \u0914\u0930 \u0915\u093f\u0924\u0928\u0940 \u091c\u0932\u094d\u0926\u0940 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0924\u0915 \u092a\u0939\u0941\u0901\u091a\u0947\u0902\u0917\u0940\u0964 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f, \u0907\u0938 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u094b \u0938\u092e\u091d\u0928\u093e \u0938\u0942\u091a\u093f\u0924 \u0928\u093f\u0930\u094d\u0923\u092f \u0932\u0947\u0928\u0947 \u092e\u0947\u0902 \u0938\u0939\u093e\u092f\u0915 \u0939\u094b\u0924\u093e \u0939\u0948\u0964. <strong>\u0939\u093e\u0932\u093e\u0902\u0915\u093f \u091a\u0941\u0928\u094c\u0924\u093f\u092f\u093e\u0902 \u0905\u092d\u0940 \u092d\u0940 \u092c\u0928\u0940 \u0939\u0941\u0908 \u0939\u0948\u0902, \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0914\u0930 \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u092e\u0947\u0902 \u092a\u094d\u0930\u0917\u0924\u093f \u0924\u0947\u091c\u0940 \u0938\u0947 \u0939\u094b \u0930\u0939\u0940 \u0939\u0948\u0964.<\/strong> \u0926\u0941\u0930\u094d\u0932\u092d \u092c\u0940\u092e\u093e\u0930\u093f\u092f\u094b\u0902 \u0915\u0947 \u0938\u092e\u0930\u094d\u0925\u0928 \u092e\u0947\u0902 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e\u090f\u0902 \u092d\u0940 \u0935\u093f\u0915\u0938\u093f\u0924 \u0939\u094b \u0930\u0939\u0940 \u0939\u0948\u0902\u0964 \u092a\u094d\u0930\u0924\u094d\u092f\u0947\u0915 \u0906\u0908\u090f\u0928\u0921\u0940 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u0928\u0908 \u0909\u092e\u094d\u092e\u0940\u0926 \u0932\u0947\u0915\u0930 \u0906\u0924\u093e \u0939\u0948\u0964 \u0939\u093e\u0932\u093e\u0902\u0915\u093f, \u092a\u0939\u0941\u0902\u091a \u0914\u0930 \u0935\u0939\u0928\u0940\u092f\u0924\u093e \u092a\u0930 \u0905\u092d\u0940 \u092d\u0940 \u0927\u094d\u092f\u093e\u0928 \u0926\u0947\u0928\u0947 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u0948\u0964. <strong>\u0928\u093f\u092f\u093e\u092e\u0915 \u0928\u093f\u0915\u093e\u092f\u094b\u0902, \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0914\u0930 \u0905\u0927\u093f\u0935\u0915\u094d\u0924\u093e\u0913\u0902 \u0915\u0947 \u092c\u0940\u091a \u0938\u0939\u092f\u094b\u0917 \u0906\u0935\u0936\u094d\u092f\u0915 \u0939\u0948\u0964.<\/strong> \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0930\u0916\u0928\u093e \u0935\u093f\u0915\u0932\u094d\u092a\u094b\u0902 \u0915\u094b \u0938\u092e\u091d\u0928\u0947 \u0915\u0940 \u0915\u0941\u0902\u091c\u0940 \u0939\u0948\u0964 \u0921\u0940\u090f\u092e\u0921\u0940 \u0909\u092a\u091a\u093e\u0930 \u0915\u093e \u092d\u0935\u093f\u0937\u094d\u092f \u0906\u0908\u090f\u0928\u0921\u0940 \u0915\u0940 \u0928\u093f\u0930\u0902\u0924\u0930 \u092a\u094d\u0930\u0917\u0924\u093f \u092a\u0930 \u0928\u093f\u0930\u094d\u092d\u0930 \u0915\u0930\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/biologics-license-application-bla\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0906\u0935\u0947\u0926\u0928 (\u092c\u0940\u090f\u0932\u090f): 1\u091f\u0940\u092a\u0940135\u091f\u0940 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u0938\u0902\u092a\u0942\u0930\u094d\u0923 \u092e\u093e\u0930\u094d\u0917\u0926\u0930\u094d\u0936\u093f\u0915\u093e<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The pathway to Investigational New Drug (IND) clearance for Duchenne muscular dystrophy is one of the most critical regulatory milestones in modern drug development. IND clearance allows experimental therapies\u2014ranging from gene therapies to exon-skipping drugs\u2014to move from laboratory research into human clinical trials. In the context of Duchenne muscular dystrophy (DMD), where unmet medical need [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":7467,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[413,652,654,653,651],"class_list":["post-6340","post","type-post","status-publish","format-standard","has-post-thumbnail","category-dmd","tag-dmd-clinical-trials","tag-fda-drug-approval","tag-fda-regulations","tag-ind-application-process","tag-ind-clearance"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/6340","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=6340"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/6340\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/7467"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=6340"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=6340"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=6340"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}