{"id":6203,"date":"2026-02-11T17:08:53","date_gmt":"2026-02-11T14:08:53","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6203"},"modified":"2026-02-11T17:08:55","modified_gmt":"2026-02-11T14:08:55","slug":"precision-biosciences-pbgene-dmd-function-dmd-phase-1-2-clinical-study","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/precision-biosciences-pbgene-dmd-function-dmd-phase-1-2-clinical-study\/","title":{"rendered":"\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u092a\u094d\u0930\u0925\u092e \u0936\u094d\u0930\u0947\u0923\u0940 \u0915\u0940 \u0926\u0935\u093e PBGENE-DMD \u0915\u0947 \u0932\u093f\u090f \u091c\u093e\u0902\u091a\u093e\u0927\u0940\u0928 \u0928\u0908 \u0926\u0935\u093e \u0906\u0935\u0947\u0926\u0928 \u0915\u0947 \u0932\u093f\u090f Precision BioSciences \u0915\u094b \u0905\u092e\u0947\u0930\u093f\u0915\u093e \u0938\u0947 \u092e\u0902\u091c\u0942\u0930\u0940 \u092e\u093f\u0932 \u0917\u0908 \u0939\u0948\u0964"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Precision BioSciences \u0928\u0947 \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0915\u093f \u0915\u0902\u092a\u0928\u0940 \u0915\u094b \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0916\u093e\u0926\u094d\u092f \u090f\u0935\u0902 \u0914\u0937\u0927\u093f \u092a\u094d\u0930\u0936\u093e\u0938\u0928 (FDA) \u0938\u0947 \u0905\u0927\u094d\u092f\u092f\u0928 \u0906\u0917\u0947 \u092c\u0922\u093c\u093e\u0928\u0947 \u0915\u0940 \u0905\u0927\u093f\u0938\u0942\u091a\u0928\u093e \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u0941\u0908 \u0939\u0948\u0964. <strong>\u0907\u0938\u0938\u0947 Precision BioSciences \u0915\u094b \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (DMD) \u0915\u0947 \u092e\u0930\u0940\u091c\u094b\u0902 \u0915\u0947 \u0907\u0932\u093e\u091c \u0915\u0947 \u0932\u093f\u090f PBGENE-DMD \u0915\u0947 FUNCTION-DMD \u091a\u0930\u0923 1\/2 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0932\u093f\u090f IRB \u0917\u0924\u093f\u0935\u093f\u0927\u093f\u092f\u094b\u0902 \u0914\u0930 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u094d\u0925\u0932 \u0938\u0915\u094d\u0930\u093f\u092f\u0923 \u0915\u094b \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0905\u0928\u0941\u092e\u0924\u093f \u092e\u093f\u0932\u0924\u0940 \u0939\u0948, \u091c\u094b \u0915\u093f \u0905\u0924\u094d\u092f\u0927\u093f\u0915 \u0935\u093f\u0936\u093f\u0937\u094d\u091f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u094d\u0925\u0932\u094b\u0902 \u092a\u0930 \u0915\u093f\u092f\u093e \u091c\u093e\u090f\u0917\u093e\u0964.<\/strong> \u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0938\u0941\u0930\u0915\u094d\u0937\u093e, \u0938\u0939\u0928\u0936\u0940\u0932\u0924\u093e \u0914\u0930 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u093e \u0939\u0948, \u091c\u093f\u0938\u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0914\u0930 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u092a\u0930\u093f\u0923\u093e\u092e \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u2013 \u092f\u0942\u090f\u0938 FDA \u0905\u0927\u094d\u092f\u092f\u0928 \u0906\u0917\u0947 \u092c\u0922\u093c \u0938\u0915\u0924\u093e \u0939\u0948 \u0905\u0927\u093f\u0938\u0942\u091a\u0928\u093e \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0915\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 FUNCTION-DMD \u091a\u0930\u0923 1\/2 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0932\u093f\u090f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u094d\u0925\u0932 \u0938\u0915\u094d\u0930\u093f\u092f\u0923 \u0915\u0940 \u0936\u0941\u0930\u0941\u0906\u0924 \u0915\u094b \u0938\u0915\u094d\u0937\u092e \u092c\u0928\u093e\u0924\u0940 \u0939\u0948 \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u2013 \u0935\u093f\u0936\u094d\u0935 \u0938\u094d\u0924\u0930\u0940\u092f \u0921\u0940\u090f\u092e\u0921\u0940 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u0938\u094d\u0925\u0932\u094b\u0902 \u092a\u0930 \u0938\u0902\u0938\u094d\u0925\u093e\u0917\u0924 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u092c\u094b\u0930\u094d\u0921 (\u0906\u0908\u0906\u0930\u092c\u0940) \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u091a\u0932 \u0930\u0939\u0940 \u0939\u0948 \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u2013 PBGENE-DMD \u090f\u0915 \u0907\u0928 \u0935\u093f\u0935\u094b \u091c\u0940\u0928 \u090f\u0921\u093f\u091f\u093f\u0902\u0917 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0909\u0924\u094d\u092a\u093e\u0926 \u0939\u0948 \u091c\u093f\u0938\u0947 \u090f\u0915 \u0928\u0935\u0940\u0928 \u090f\u0915\u092e\u0941\u0936\u094d\u0924 \u091c\u0940\u0928 \u090f\u0921\u093f\u091f\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 DMD \u0915\u0947 \u0905\u0902\u0924\u0930\u094d\u0928\u093f\u0939\u093f\u0924 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u0915\u093e\u0930\u0923 \u0915\u094b \u0920\u0940\u0915 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u2013 \u0915\u0902\u092a\u0928\u0940 \u0928\u0947 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0938\u094b\u0938\u093f\u090f\u0936\u0928 \u0938\u092e\u094d\u092e\u0947\u0932\u0928 \u0915\u0947 \u092c\u093e\u0926 \u092e\u093e\u0930\u094d\u091a \u092e\u0947\u0902 \u090f\u0915 \u0935\u0930\u094d\u091a\u0941\u0905\u0932 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0906\u092f\u094b\u091c\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u092c\u0928\u093e\u0908 \u0939\u0948, \u091c\u093f\u0938\u092e\u0947\u0902 PBGENE-DMD \u0914\u0930 FUNCTION-DMD \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0930 \u091a\u0930\u094d\u091a\u093e \u0915\u0940 \u091c\u093e\u090f\u0917\u0940 \u0914\u0930 \u0907\u0938\u092e\u0947\u0902 \u0930\u094b\u0917\u0940 \u0905\u0927\u093f\u0935\u0915\u094d\u0924\u093e\u0913\u0902 \u0938\u0939\u093f\u0924 \u092a\u094d\u0930\u092e\u0941\u0916 \u0930\u093e\u092f \u0926\u0947\u0928\u0947 \u0935\u093e\u0932\u0947 \u0928\u0947\u0924\u093e\u0913\u0902 \u0915\u0940 \u092d\u093e\u0917\u0940\u0926\u093e\u0930\u0940 \u0939\u094b\u0917\u0940\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">PBGENE-DMD \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">PBGENE-DMD, \u092a\u094d\u0930\u0947\u0938\u093f\u091c\u0928 \u0915\u093e \u092a\u0942\u0930\u094d\u0923 \u0938\u094d\u0935\u093e\u092e\u093f\u0924\u094d\u0935 \u0935\u093e\u0932\u093e, \u0905\u092a\u0928\u0940 \u0924\u0930\u0939 \u0915\u093e \u092a\u0939\u0932\u093e \u0907\u0928 \u0935\u093f\u0935\u094b \u091c\u0940\u0928 \u0938\u0902\u092a\u093e\u0926\u0928 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0939\u0948 \u091c\u094b \u091c\u0940\u0928 \u0928\u093f\u0937\u094d\u0915\u093e\u0938\u0928 \u0926\u0943\u0937\u094d\u091f\u093f\u0915\u094b\u0923 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0924\u093e \u0939\u0948, \u091c\u093f\u0938\u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u090f\u0915\u094d\u0938\u0949\u0928 45 \u0914\u0930 55 \u0915\u0947 \u092c\u0940\u091a \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0935\u093e\u0932\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u094b \u0938\u094d\u0925\u093e\u092f\u0940 \u0930\u0942\u092a \u0938\u0947 \u0920\u0940\u0915 \u0915\u0930\u0928\u093e \u0939\u0948, \u091c\u093f\u0938\u0947 &quot;\u0939\u0949\u091f-\u0938\u094d\u092a\u0949\u091f&quot; \u0915\u094d\u0937\u0947\u0924\u094d\u0930 \u0915\u0939\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u091c\u094b \u0932\u0917\u092d\u0917 60% \u092a\u0930 DMD \u0935\u093e\u0932\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0938\u092c\u0938\u0947 \u092c\u0921\u093c\u0947 \u0906\u0923\u0935\u093f\u0915 \u0909\u092a\u0938\u092e\u0942\u0939 \u0915\u0947 \u0932\u093f\u090f \u091c\u093f\u092e\u094d\u092e\u0947\u0926\u093e\u0930 \u0939\u0948\u0964. <strong>\u0907\u0938 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u0940\u092f \u0932\u0915\u094d\u0937\u094d\u092f \u0915\u093e \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u0940 \u0932\u0917\u092d\u0917 \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0947 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u0947 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u0915\u094b \u092c\u0939\u093e\u0932 \u0915\u0930\u0928\u093e \u0939\u0948\u0964 \u092f\u0939 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0947 80% \u092d\u093e\u0917 \u0915\u094b \u092c\u0930\u0915\u0930\u093e\u0930 \u0930\u0916\u0924\u093e \u0939\u0948, \u091c\u094b \u0906\u091c \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u092f\u093e \u0935\u093f\u0915\u093e\u0938 \u0915\u0947 \u0905\u0927\u0940\u0928 \u0938\u093f\u0902\u0925\u0947\u091f\u093f\u0915 \u092e\u093e\u0907\u0915\u094d\u0930\u094b-\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0938\u0902\u0930\u091a\u0928\u093e\u0913\u0902 (\u091c\u094b \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0947 \u0906\u0915\u093e\u0930 \u0915\u0947 \u0932\u0917\u092d\u0917 34% \u0939\u0948\u0902) \u0938\u0947 \u0915\u093e\u092b\u0940 \u092c\u0921\u093c\u093e \u0939\u0948\u0964.<\/strong><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0935\u0930\u094d\u0937 2026 \u0915\u0940 \u092a\u0939\u0932\u0940 \u091b\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u092a\u0939\u0932\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0915\u0947\u0902\u0926\u094d\u0930 \u0915\u094b \u0938\u0915\u094d\u0930\u093f\u092f \u0915\u0930\u0928\u0947 \u0915\u093e \u0932\u0915\u094d\u0937\u094d\u092f \u0939\u0948\u0964<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u201cFDA \u0926\u094d\u0935\u093e\u0930\u093e PBGENE-DMD \u0915\u0947 \u0932\u093f\u090f \u0905\u0927\u094d\u092f\u092f\u0928 \u0906\u0917\u0947 \u092c\u0922\u093c\u093e\u0928\u0947 \u0915\u0940 \u0905\u0927\u093f\u0938\u0942\u091a\u0928\u093e Precision BioSciences \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u0914\u0930 \u0928\u093f\u092f\u093e\u092e\u0915 \u0909\u092a\u0932\u092c\u094d\u0927\u093f \u0939\u0948, \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0939\u092e \u0905\u092a\u0928\u0947 \u0926\u0942\u0938\u0930\u0947 \u092a\u0942\u0930\u094d\u0923 \u0938\u094d\u0935\u093e\u092e\u093f\u0924\u094d\u0935 \u0935\u093e\u0932\u0947 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0915\u094b \u0915\u094d\u0932\u093f\u0928\u093f\u0915 \u0915\u0940 \u0913\u0930 \u0906\u0917\u0947 \u092c\u0922\u093c\u093e \u0930\u0939\u0947 \u0939\u0948\u0902\u0964 \u0906\u091c \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926, DMD \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u0921\u093c\u0915\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0910\u0938\u0947 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u0940 \u0915\u092e\u0940 \u0939\u0948 \u091c\u093f\u0928\u0938\u0947 \u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0925 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0938\u0941\u0927\u093e\u0930 \u0939\u094b \u0938\u0915\u0947\u0902\u0964 \u0939\u092e DMD \u0915\u0947 \u0932\u093f\u090f \u0907\u0938 \u0928\u0935\u0940\u0928 \u091c\u0940\u0928 \u0928\u093f\u0937\u094d\u0915\u093e\u0938\u0928 \u092a\u0926\u094d\u0927\u0924\u093f \u0915\u094b \u0915\u094d\u0932\u093f\u0928\u093f\u0915 \u092e\u0947\u0902 \u0932\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0909\u0924\u094d\u0938\u093e\u0939\u093f\u0924 \u0939\u0948\u0902, \u091c\u093f\u0938\u0915\u093e \u0932\u0915\u094d\u0937\u094d\u092f 2026 \u0915\u0940 \u092a\u0939\u0932\u0940 \u091b\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0905\u092e\u0947\u0930\u093f\u0915\u093e \u092e\u0947\u0902 \u092a\u0939\u0932\u093e \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0915\u0947\u0902\u0926\u094d\u0930 \u0938\u0915\u094d\u0930\u093f\u092f \u0915\u0930\u0928\u093e \u0939\u0948\u0964 \u092e\u0941\u091d\u0947 \u0905\u092a\u0928\u0940 \u091f\u0940\u092e \u092a\u0930 \u0917\u0930\u094d\u0935 \u0939\u0948 \u0915\u093f \u0939\u092e\u0928\u0947 \u0935\u0930\u094d\u0937 \u0915\u0947 \u0905\u0902\u0924 \u0924\u0915 IND \u0926\u093e\u0916\u093f\u0932 \u0915\u0930\u0928\u0947 \u0915\u093e \u0905\u092a\u0928\u093e \u0932\u0915\u094d\u0937\u094d\u092f \u092a\u0942\u0930\u093e \u0915\u093f\u092f\u093e \u0914\u0930 \u092a\u0939\u0932\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 FDA \u0905\u0927\u094d\u092f\u092f\u0928 \u0906\u0917\u0947 \u092c\u0922\u093c\u093e\u0928\u0947 \u0915\u0940 \u0905\u0927\u093f\u0938\u0942\u091a\u0928\u093e \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0940\u0964 \u0915\u0902\u092a\u0928\u0940 \u0915\u0908 IRB \u0914\u0930 FDA \u0915\u0947 \u0938\u093e\u0925 \u092e\u093f\u0932\u0915\u0930 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0915\u0947\u0902\u0926\u094d\u0930\u094b\u0902 \u0915\u094b \u0938\u0915\u094d\u0930\u093f\u092f \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0915\u093e\u092e \u0915\u0930\u0928\u093e \u091c\u093e\u0930\u0940 \u0930\u0916\u0947\u0917\u0940,\u201d Precision BioSciences \u0915\u0947 \u092e\u0941\u0916\u094d\u092f \u0915\u093e\u0930\u094d\u092f\u0915\u093e\u0930\u0940 \u0905\u0927\u093f\u0915\u093e\u0930\u0940 \u092e\u093e\u0907\u0915\u0932 \u0905\u092e\u094b\u0930\u094b\u0938\u094b \u0928\u0947 \u0915\u0939\u093e\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Precision BioSciences announced that the Company received a Study May Proceed notification from the U.S. Food and Drug Administration (FDA). This allows Precision BioSciences to initiate IRB activities and clinical trial site activation for the FUNCTION-DMD Phase 1\/2 clinical trial for PBGENE-DMD for the treatment of ambulatory Duchenne muscular dystrophy (DMD) patients at highly specialized [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6205,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[359,479,72,314,313],"class_list":["post-6203","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-full-length-dystrophin","tag-function-dmd","tag-gene-editing","tag-pbgene-dmd","tag-precision-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/6203","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=6203"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/6203\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/6205"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=6203"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=6203"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=6203"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}