{"id":5673,"date":"2026-02-05T04:47:49","date_gmt":"2026-02-05T01:47:49","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5673"},"modified":"2026-02-07T09:41:46","modified_gmt":"2026-02-07T06:41:46","slug":"elevidys-gene-therapy-efficacy-in-dmd","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/elevidys-gene-therapy-efficacy-in-dmd\/","title":{"rendered":"\u0932\u093e\u0916\u094b\u0902 \u0921\u0949\u0932\u0930 \u0915\u0947 \u0907\u0938 \u0916\u0930\u094d\u091a\u0947 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902, Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0940 \u0938\u094d\u0925\u093f\u0924\u093f \u092e\u0947\u0902 \u0915\u093f\u0924\u0928\u093e \u0938\u0941\u0927\u093e\u0930 \u0932\u093e\u0924\u0940 \u0939\u0948?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0915\u0947 \u0932\u093f\u090f 1\u091f\u0940\u092a\u0940150\u091f\u0940 \u0915\u0947 \u092c\u093e\u0926 \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u090f\u0915\u092e\u093e\u0924\u094d\u0930 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 1\u091f\u0940\u092a\u0940104\u091f\u0940 \u0928\u0947 \u092e\u0930\u0940\u091c\u094b\u0902 \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0924\u0940\u0928 \u0938\u093e\u0932 \u0915\u0947 \u0906\u0902\u0915\u0921\u093c\u094b\u0902 \u0915\u0947 \u091c\u093e\u0930\u0940 \u0939\u094b\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u092e\u0941\u0926\u093e\u092f \u0914\u0930 \u0928\u093f\u0935\u0947\u0936\u0915\u094b\u0902 \u0915\u094b \u0928\u093f\u0930\u093e\u0936 \u0915\u093f\u092f\u093e \u0939\u0948\u0964 29 \u0932\u093e\u0916 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0915\u0940 \u0915\u0940\u092e\u0924 \u092a\u0930 \u0935\u093f\u092a\u0923\u0928 \u0915\u093f\u090f \u091c\u093e \u0930\u0939\u0947 \u0907\u0938 \u0909\u0924\u094d\u092a\u093e\u0926 \u0928\u0947 \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0915\u0908 \u0938\u0935\u093e\u0932 \u0916\u0921\u093c\u0947 \u0915\u0930 \u0926\u093f\u090f \u0939\u0948\u0902: &#039;1\u091f\u0940\u092a\u0940104\u091f\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093f\u0924\u0928\u0940 \u092a\u094d\u0930\u092d\u093e\u0935\u0940 \u0939\u0948, \u092f\u0939 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0940 \u091c\u0940\u0935\u0928 \u0905\u0935\u0927\u093f \u0915\u094b \u0915\u093f\u0924\u0928\u093e \u092c\u0922\u093c\u093e\u0924\u0940 \u0939\u0948, \u0914\u0930 \u0915\u094d\u092f\u093e \u0915\u093f\u0938\u0940 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0940 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u093e \u0906\u0915\u0932\u0928 \u0915\u0947\u0935\u0932 \u090f\u0928\u090f\u0938\u090f\u090f \u0938\u094d\u0915\u094b\u0930 \u0915\u0947 \u0906\u0927\u093e\u0930 \u092a\u0930 \u0915\u0930\u0928\u093e \u0938\u091f\u0940\u0915 \u0939\u0948?&#039; <strong>\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/hi\/north-star-ambulatory-assessment-nsaa-in-duchenne-dmd\/\" data-type=\"post\" data-id=\"4959\" target=\"_blank\" rel=\"noreferrer noopener\">\u090f\u0928\u090f\u0938\u090f\u090f \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#sarepta-really-needs-something-to-freshen-up-the-story\">\u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0940 \u0915\u0939\u093e\u0928\u0940 \u0915\u094b \u0915\u0941\u091b \u0928\u092f\u093e\u092a\u0928 \u0926\u0947\u0928\u0947 \u0915\u0940 \u0935\u093e\u0915\u0908 \u091c\u0930\u0942\u0930\u0924 \u0939\u0948\u0964<\/a><\/li><li><a href=\"#i-dont-know-if-elevidys-works\">\u0915\u094d\u092f\u093e Elevidys \u0915\u093e\u092e \u0915\u0930\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902?<\/a><\/li><li><a href=\"#questions-from-families-organizing-the-campaign\">\u0927\u0928 \u091c\u0941\u091f\u093e\u0928\u0947 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e\u094b\u0902 \u0915\u093e \u0906\u092f\u094b\u091c\u0928 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0936\u094d\u0928<\/a><\/li><li><a href=\"#which-dmd-gene-therapy-should-you-choose\">\u0906\u092a\u0915\u094b \u0915\u094c\u0928 \u0938\u0940 \u0921\u0940\u090f\u092e\u0921\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0941\u0928\u0928\u0940 \u091a\u093e\u0939\u093f\u090f?<\/a><\/li><li><a href=\"#sareptas-1-year-share-price\">\u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930 \u0915\u093e 1 \u0938\u093e\u0932 \u0915\u093e \u092e\u0942\u0932\u094d\u092f<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"sarepta-really-needs-something-to-freshen-up-the-story\">\u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0940 \u0915\u0939\u093e\u0928\u0940 \u0915\u094b \u0915\u0941\u091b \u0928\u092f\u093e\u092a\u0928 \u0926\u0947\u0928\u0947 \u0915\u0940 \u0935\u093e\u0915\u0908 \u091c\u0930\u0942\u0930\u0924 \u0939\u0948\u0964<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0928\u0947 \u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u0910\u0938\u0947 \u0906\u0902\u0915\u0921\u093c\u0947 \u092a\u094d\u0930\u0915\u093e\u0936\u093f\u0924 \u0915\u093f\u090f \u091c\u093f\u0928\u092e\u0947\u0902 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c \u0938\u094d\u0924\u0930 \u0936\u093e\u092e\u093f\u0932 \u0928\u0939\u0940\u0902 \u0925\u093e, \u091c\u094b \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0938\u092c\u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0939\u0948\u0964 Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a \u0915\u0947 \u0932\u093f\u090f \u0905\u092d\u093f\u092f\u093e\u0928 \u091a\u0932\u093e \u0930\u0939\u0947 \u092a\u0930\u093f\u0935\u093e\u0930 \u0907\u0938 \u092c\u093e\u0924 \u0938\u0947 \u0928\u093e\u0930\u093e\u091c \u0939\u0948\u0902 \u0915\u093f \u092f\u0939 \u0924\u0915\u0928\u0940\u0915\u0940 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0938\u093e\u091d\u093e \u0928\u0939\u0940\u0902 \u0915\u0940 \u0917\u0908\u0964 \u0925\u0947\u0930\u0947\u092a\u0940 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a \u0915\u0947 \u0932\u093f\u090f \u0905\u0925\u0915 \u092a\u094d\u0930\u092f\u093e\u0938 \u0915\u0930\u0915\u0947 \u0927\u0928 \u091c\u0941\u091f\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u0905\u0927\u093f\u0915\u093e\u0902\u0936 \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u0939\u0924\u0947 \u0939\u0948\u0902, \u201c\u0939\u092e \u0906\u092a\u0915\u094b \u0932\u093e\u0916\u094b\u0902 \u0921\u0949\u0932\u0930 \u0926\u0947 \u0930\u0939\u0947 \u0939\u0948\u0902, \u0932\u0947\u0915\u093f\u0928 \u0906\u092a \u092c\u0926\u0932\u0947 \u092e\u0947\u0902 \u0939\u092e\u0947\u0902 \u0915\u0941\u091b \u0928\u0939\u0940\u0902 \u0926\u0947 \u0930\u0939\u0947 \u0939\u0948\u0902; \u0924\u0925\u094d\u092f, \u0906\u0902\u0915\u0921\u093c\u0947 \u0914\u0930 \u0935\u093f\u091c\u094d\u091e\u093e\u0928\u0964 \u0906\u092a \u0938\u093f\u0930\u094d\u092b \u0939\u092e\u093e\u0930\u093e \u092a\u0948\u0938\u093e \u0932\u0947 \u0930\u0939\u0947 \u0939\u0948\u0902\u0964\u201d <strong>\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/hi\/sarepta-3-year-topline-data-of-elevidys-gene-therapy\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0928\u0947 \u090f\u0932\u0947\u0935\u093f\u0921\u093f\u0938 \u0915\u0947 3-\u0935\u0930\u094d\u0937\u0940\u092f \u0936\u0940\u0930\u094d\u0937-\u0938\u094d\u0924\u0930\u0940\u092f \u0906\u0902\u0915\u0921\u093c\u0947 \u091c\u093e\u0930\u0940 \u0915\u093f\u090f\u0964<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">2025 \u0915\u0940 \u0935\u0938\u0902\u0924 \u090b\u0924\u0941 \u092e\u0947\u0902 \u091c\u092c Elevidys \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0926\u094b \u092e\u094c\u0924\u0947\u0902 \u0939\u0941\u0908\u0902, \u0924\u094b \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930\u094b\u0902 \u092e\u0947\u0902 \u0917\u093f\u0930\u093e\u0935\u091f \u0936\u0941\u0930\u0942 \u0939\u094b \u0917\u0908\u0964 \u0917\u0930\u094d\u092e\u093f\u092f\u094b\u0902 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928, \u090f\u0915 \u0924\u0940\u0938\u0930\u0940 \u092e\u094c\u0924 \u0915\u0940 \u0916\u092c\u0930 \u0938\u093e\u092e\u0928\u0947 \u0906\u0908, \u091c\u094b \u0932\u093f\u092e\u094d\u092c-\u0917\u0930\u094d\u0921\u0932 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u091c\u0940\u0928 \u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u091c\u0941\u0921\u093c\u0940 \u0925\u0940, \u091c\u093f\u0938\u092e\u0947\u0902 Elevidys \u0915\u0947 \u0938\u092e\u093e\u0928 \u0939\u0940 AAV \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964 \u0915\u0941\u0932 \u092e\u093f\u0932\u093e\u0915\u0930, \u0915\u0902\u092a\u0928\u0940 \u0915\u0947 \u0936\u0947\u092f\u0930 \u0915\u0940 \u0915\u0940\u092e\u0924 \u0938\u093e\u0932 \u0915\u0940 \u0936\u0941\u0930\u0941\u0906\u0924 \u0938\u0947 80% \u0917\u093f\u0930\u0915\u0930 \u0932\u0917\u092d\u0917 \u0926\u0938 \u0935\u0930\u094d\u0937\u094b\u0902 \u092e\u0947\u0902 \u0905\u092a\u0928\u0947 \u0938\u092c\u0938\u0947 \u0928\u093f\u091a\u0932\u0947 \u0938\u094d\u0924\u0930 \u092a\u0930 \u092a\u0939\u0941\u0902\u091a \u0917\u0908\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"i-dont-know-if-elevidys-works\">\u0915\u094d\u092f\u093e Elevidys \u0915\u093e\u092e \u0915\u0930\u0924\u093e \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0902\u092a\u0928\u0940 \u092a\u094d\u0930\u092c\u0902\u0927\u0928 \u0915\u094b \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948 \u0915\u093f \u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u091c\u093e\u0930\u0940 \u0915\u093f\u090f \u0917\u090f 2025 \u0915\u0947 \u0935\u093f\u0924\u094d\u0924\u0940\u092f \u0935\u093f\u0935\u0930\u0923 \u0914\u0930 Elevidys \u092a\u0930 \u0905\u0926\u094d\u092f\u0924\u0928 \u0924\u0940\u0928-\u0935\u0930\u094d\u0937\u0940\u092f \u0906\u0901\u0915\u0921\u093c\u0947 \u0938\u094d\u0925\u093f\u0924\u093f \u0915\u094b \u092c\u0947\u0939\u0924\u0930 \u092c\u0928\u093e \u0926\u0947\u0902\u0917\u0947, \u0932\u0947\u0915\u093f\u0928 \u0909\u0928\u094d\u0939\u0947\u0902 \u0928\u093f\u0930\u093e\u0936\u093e \u0939\u093e\u0925 \u0932\u0917 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964 \u0939\u093e\u0932\u093e\u0902\u0915\u093f \u0938\u0930\u0947\u092a\u094d\u091f\u093e NSAA \u092e\u0947\u0902 4 \u0905\u0902\u0915\u094b\u0902 \u0915\u0940 \u0935\u0943\u0926\u094d\u0927\u093f \u0915\u094b \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0932\u093e\u092d\u0915\u093e\u0930\u0940 \u0939\u094b\u0928\u0947 \u0915\u093e \u0938\u0902\u0915\u0947\u0924 \u092e\u093e\u0928\u0924\u0940 \u0939\u0948, \u0932\u0947\u0915\u093f\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0940 \u0932\u093e\u0917\u0924 \u0914\u0930 4 \u0905\u0902\u0915\u094b\u0902 \u0915\u093e NSAA \u0938\u094d\u0915\u094b\u0930 \u091a\u093f\u0902\u0924\u093e \u0915\u093e \u0935\u093f\u0937\u092f \u0939\u0948\u0964. <strong>\u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0947 \u092a\u0930\u093f\u0935\u093e\u0930 \u0907\u0928 \u0938\u0935\u093e\u0932\u094b\u0902 \u0915\u0947 \u091c\u0935\u093e\u092c \u0915\u0947 \u0932\u093f\u090f \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0938\u0947 \u092a\u094d\u0930\u0924\u0940\u0915\u094d\u0937\u093e \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902:<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0922\u0942\u0902\u0922\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/what-is-creatine-kinase-ck\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c (\u0938\u0940\u0915\u0947) \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"questions-from-families-organizing-the-campaign\">\u0927\u0928 \u091c\u0941\u091f\u093e\u0928\u0947 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e\u094b\u0902 \u0915\u093e \u0906\u092f\u094b\u091c\u0928 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u092a\u094d\u0930\u0936\u094d\u0928<\/h2>\n\n\n\n<ol class=\"wp-block-list\">\n<li>\u0915\u094d\u092f\u093e \u090f\u0928\u090f\u0938\u090f\u090f \u092e\u0947\u0902 4 \u0905\u0902\u0915\u094b\u0902 \u0915\u0940 \u0935\u0943\u0926\u094d\u0927\u093f \u0938\u0947 \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 $2.9 \u092e\u093f\u0932\u093f\u092f\u0928 \u0915\u093e \u0928\u0941\u0915\u0938\u093e\u0928 \u0939\u0941\u0906?<\/li>\n\n\n\n<li>\u0924\u0940\u0928 \u0938\u093e\u0932 \u092a\u0939\u0932\u0947, \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u090f\u0915 \u092c\u091a\u094d\u091a\u0947 \u0915\u093e \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c \u0938\u094d\u0924\u0930 \u0915\u094d\u092f\u093e \u0925\u093e, \u091c\u094b 1\u091f\u0940\u092a\u0940104\u091f\u0940 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u0909\u092e\u094d\u092e\u0940\u0926\u0935\u093e\u0930 \u0925\u093e, \u0914\u0930 1\u091f\u0940\u092a\u0940104\u091f\u0940 \u0909\u092a\u091a\u093e\u0930 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0924\u0940\u0928 \u0938\u093e\u0932 \u092c\u093e\u0926 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c \u0938\u094d\u0924\u0930 \u0915\u094d\u092f\u093e \u0925\u093e?<\/li>\n\n\n\n<li>\u092f\u0926\u093f Elevidys \u0932\u0947\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c \u0915\u093e \u0938\u094d\u0924\u0930 \u0915\u092e \u0928\u0939\u0940\u0902 \u0939\u094b\u0924\u093e \u0939\u0948, \u0924\u094b \u0915\u094d\u092f\u093e \u0907\u0938\u0915\u093e \u092e\u0924\u0932\u092c \u092f\u0939 \u0928\u0939\u0940\u0902 \u0939\u0948 \u0915\u093f \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u094b \u0928\u0941\u0915\u0938\u093e\u0928 \u0939\u094b \u0930\u0939\u093e \u0939\u0948?<\/li>\n\n\n\n<li>\u0915\u094d\u092f\u093e \u0906\u092a\u0928\u0947 Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930 \u0930\u0939\u0947 \u092c\u091a\u094d\u091a\u094b\u0902 \u092e\u0947\u0902 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c \u0915\u0947 \u0938\u094d\u0924\u0930 \u0915\u094b \u092e\u093e\u092a\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u092c\u093e\u092f\u094b\u092a\u094d\u0938\u0940 \u0928\u092e\u0942\u0928\u0947 \u0932\u093f\u090f \u0925\u0947?<\/li>\n<\/ol>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u092a\u0939\u0932\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 Elevidys, \u091c\u093f\u0938\u0947 FDA \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948 (\u0932\u0947\u0915\u093f\u0928 EMA \u0926\u094d\u0935\u093e\u0930\u093e \u0928\u0939\u0940\u0902), \u0915\u094b \u092c\u0939\u0941\u0924 \u091c\u0932\u094d\u0926 \u0928\u090f \u092a\u094d\u0930\u0924\u093f\u0938\u094d\u092a\u0930\u094d\u0927\u093f\u092f\u094b\u0902 \u0915\u093e \u0938\u093e\u092e\u0928\u093e \u0915\u0930\u0928\u093e \u092a\u0921\u093c\u0947\u0917\u093e\u0964 \u092c\u093e\u091c\u093e\u0930 \u092e\u0947\u0902 \u092a\u094d\u0930\u0935\u0947\u0936 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0938\u092c\u0938\u0947 \u0915\u0930\u0940\u092c REGENXBIO \u0939\u0948, \u091c\u093f\u0938\u0928\u0947 \u092a\u093f\u091b\u0932\u0947 \u092e\u0939\u0940\u0928\u0947 \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0925\u0940 \u0915\u093f \u0935\u0939 2026 \u0915\u0947 \u092e\u0927\u094d\u092f \u0924\u0915 \u0905\u092a\u0928\u0940 RGX-202 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0915\u0947 \u0932\u093f\u090f \u0906\u0935\u0947\u0926\u0928 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u092c\u0928\u093e \u0930\u0939\u0940 \u0939\u0948\u0964 SolidBio \u0915\u0940 SGT-003 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092d\u0940 \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u093e\u0915\u093e\u0902\u0915\u094d\u0937\u0940 \u0935\u093f\u0915\u0932\u094d\u092a \u0939\u0948, \u0914\u0930 \u092f\u0926\u093f \u092f\u0947 \u0935\u093f\u0915\u0932\u094d\u092a \u092c\u093e\u091c\u093e\u0930 \u092e\u0947\u0902 \u0906\u0924\u0947 \u0939\u0948\u0902, \u0924\u094b \u092f\u0939 \u0906\u0936\u094d\u091a\u0930\u094d\u092f\u091c\u0928\u0915 \u0928\u0939\u0940\u0902 \u0939\u094b\u0917\u093e \u092f\u0926\u093f DMD \u0930\u094b\u0917\u0940 \u0914\u0930 \u0909\u0928\u0915\u0947 \u092a\u0930\u093f\u0935\u093e\u0930 \u0907\u0932\u093e\u091c \u0915\u0947 \u0932\u093f\u090f Elevidys \u0915\u094b \u091b\u094b\u0921\u093c \u0926\u0947\u0902\u0964 <strong>\u0914\u0930 \u092a\u0922\u093c\u0947\u0902:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/hi\/creatine-kinase-ck-dystrophin-level-nsaa-score-in-elevidys-gene-therapy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092e\u0947\u0902 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c (CK), \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0938\u094d\u0924\u0930 \u0914\u0930 NSAA \u0938\u094d\u0915\u094b\u0930<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0932\u093f\u090f \u0906\u0917\u0947 \u0914\u0930 \u092d\u0940 \u0915\u0920\u093f\u0928 \u0938\u092e\u092f \u0906 \u0938\u0915\u0924\u093e \u0939\u0948 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092c\u093f\u0915\u094d\u0930\u0940 \u0918\u091f \u0930\u0939\u0940 \u0939\u0948, \u092a\u094d\u0930\u0924\u093f\u0938\u094d\u092a\u0930\u094d\u0927\u093e \u0915\u0921\u093c\u0940 \u0939\u094b\u0924\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948 \u0914\u0930 \u092a\u0930\u094d\u092f\u093e\u092a\u094d\u0924 \u0938\u094d\u092a\u0937\u094d\u091f \u0914\u0930 \u0906\u0936\u094d\u0935\u0938\u094d\u0924 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0906\u0902\u0915\u0921\u093c\u0947 \u0909\u092a\u0932\u092c\u094d\u0927 \u0928\u0939\u0940\u0902 \u0939\u0948\u0902\u0964 \u0921\u0940\u090f\u092e\u0921\u0940\u0935\u0949\u0930\u093f\u092f\u0930 \u0915\u0947 \u091c\u0930\u094d\u092e\u0928 \u092a\u094d\u0930\u0924\u093f\u0928\u093f\u0927\u093f \u0915\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u091c\u0948\u0935 \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u0940 \u0915\u0902\u092a\u0928\u0940 \u0905\u092c \u090f\u0915 \u092c\u0921\u093c\u0940 \u0926\u0935\u093e \u0915\u0902\u092a\u0928\u0940 \u0915\u0947 \u0932\u093f\u090f \u092d\u0940 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0905\u0927\u093f\u0917\u094d\u0930\u0939\u0923 \u0932\u0915\u094d\u0937\u094d\u092f \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0915\u092e \u0906\u0915\u0930\u094d\u0937\u0915 \u0939\u094b\u0924\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948, \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0907\u0938\u0915\u0940 \u091b\u0935\u093f \u0916\u0930\u093e\u092c \u0939\u094b \u091a\u0941\u0915\u0940 \u0939\u0948 \u0914\u0930 \u0907\u0938\u0915\u0947 \u092e\u0930\u0940\u091c \u0905\u0938\u0902\u0924\u0941\u0937\u094d\u091f \u0939\u0948\u0902\u0964 <strong>\u0938\u094d\u0935\u092f\u0902 \u0938\u0947 \u092f\u0947 \u092a\u094d\u0930\u0936\u094d\u0928 \u092a\u0942\u091b\u0947\u0902:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/hi\/one-time-gene-therapies-or-exon-skipping-therapies-which-may-be-better-for-duchenne-muscular-dystrophy-dmd-today\/\">\u2018&#039;\u090f\u0915 \u092c\u093e\u0930 \u0915\u0940&#039; \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092f\u093e \u090f\u0915\u094d\u0938\u0949\u0928-\u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"which-dmd-gene-therapy-should-you-choose\">\u0906\u092a\u0915\u094b \u0915\u094c\u0928 \u0938\u0940 \u0921\u0940\u090f\u092e\u0921\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0941\u0928\u0928\u0940 \u091a\u093e\u0939\u093f\u090f?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u0940\u090f\u092e\u0921\u0940 \u0915\u0947 \u092e\u0930\u0940\u091c\u094b\u0902 \u0914\u0930 \u0909\u0928\u0915\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u091c\u0932\u094d\u0926 \u0939\u0940 \u0915\u0920\u093f\u0928 \u0935\u093f\u0915\u0932\u094d\u092a \u091a\u0941\u0928\u0928\u0947 \u092a\u0921\u093c \u0938\u0915\u0924\u0947 \u0939\u0948\u0902 \u0915\u094d\u092f\u094b\u0902\u0915\u093f Elevidys \u0909\u0938\u0940 \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0924\u093e \u0939\u0948 \u091c\u0948\u0938\u093e \u0915\u093f REGENXBIO \u0915\u0947 RGX-202 \u0914\u0930 Solid Biosciences \u0915\u0947 SGT-003 \u091c\u0948\u0938\u0940 \u0928\u0908 \u0925\u0947\u0930\u0947\u092a\u0940 \u092e\u0947\u0902 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong><em>\u0905\u092d\u093f\u092f\u093e\u0928 \u091a\u0932\u093e \u0930\u0939\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u090f\u0915 \u092c\u093e\u0930 \u092b\u093f\u0930 \u092f\u093e\u0926 \u0926\u093f\u0932\u093e\u0928\u093e \u091c\u093c\u0930\u0942\u0930\u0940 \u0939\u0948: \u201c\u0906\u092a AAV \u0915\u093e \u0907\u0938\u094d\u0924\u0947\u092e\u093e\u0932 \u0938\u093f\u0930\u094d\u092b\u093c \u090f\u0915 \u092c\u093e\u0930 \u0915\u0930 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902!\u201d \u201c\u0907\u0938\u0932\u093f\u090f, \u0905\u0917\u0930 \u0906\u092a Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0941\u0928\u0924\u0947 \u0939\u0948\u0902, \u0924\u094b \u0906\u092a \u0926\u0942\u0938\u0930\u0947 \u0935\u093f\u0915\u0932\u094d\u092a\u094b\u0902 \u0938\u0947 \u0935\u0902\u091a\u093f\u0924 \u0930\u0939 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964\u201d \u0907\u0938\u0940 \u0915\u093e\u0930\u0923, \u091c\u093f\u0928 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u092a\u093e\u0938 \u0905\u092d\u0940 \u0938\u092e\u092f \u0939\u0948, \u0909\u0928\u0915\u0947 \u0932\u093f\u090f \u0905\u092a\u0928\u0947 \u0905\u092d\u093f\u092f\u093e\u0928 \u0915\u0940 \u0917\u0924\u093f \u0927\u0940\u092e\u0940 \u0915\u0930\u0928\u093e \u092f\u093e \u0915\u0941\u091b \u0938\u092e\u092f \u0915\u0947 \u0932\u093f\u090f \u0938\u094d\u0925\u0917\u093f\u0924 \u0915\u0930 \u0926\u0947\u0928\u093e \u090f\u0915 \u0905\u091a\u094d\u091b\u093e \u0935\u093f\u091a\u093e\u0930 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964.<\/em><\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u0922\u0942\u0902\u0922\u0947\u0902:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/hi\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u0905\u0915\u094d\u0938\u0930 \u092a\u0942\u091b\u0947 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u0936\u094d\u0928<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"sareptas-1-year-share-price\">\u0938\u093e\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0947 \u0936\u0947\u092f\u0930 \u0915\u093e 1 \u0938\u093e\u0932 \u0915\u093e \u092e\u0942\u0932\u094d\u092f<\/h2>\n\n\n\n<div><a href=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1024x534.jpg\" class=\"td-modal-image\"><figure class=\"wp-block-image size-large\"><img loading=\"lazy\" decoding=\"async\" width=\"1024\" height=\"534\" src=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1024x534.jpg\" alt=\"Sarepta Therapeutics 1 \u0935\u0930\u094d\u0937 \u0915\u093e \u0936\u0947\u092f\u0930 \u092e\u0942\u0932\u094d\u092f\" class=\"wp-image-6177\" title=\"\" srcset=\"https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1024x534.jpg 1024w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-300x157.jpg 300w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-768x401.jpg 768w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-18x9.jpg 18w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-805x420.jpg 805w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-150x78.jpg 150w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-696x363.jpg 696w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price-1068x557.jpg 1068w, https:\/\/dmdwarrior.com\/wp-content\/uploads\/2026\/02\/Sarepta-1-Year-Share-Price.jpg 1290w\" sizes=\"auto, (max-width: 1024px) 100vw, 1024px\" \/><\/figure><\/a><\/div>\n\n\n\n<p class=\"wp-block-paragraph\">EMBARK \u0915\u0947 \u0909\u0924\u094d\u0938\u093e\u0939\u091c\u0928\u0915 \u0905\u092a\u0921\u0947\u091f \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926, Sarepta Therapeutics \u0915\u0947 \u0936\u0947\u092f\u0930 \u092e\u0942\u0932\u094d\u092f \u0915\u093e \u0939\u093e\u0932\u093f\u092f\u093e \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 \u0915\u092e\u091c\u094b\u0930 \u0930\u0939\u093e \u0939\u0948, \u091c\u093f\u0938\u092e\u0947\u0902 7 \u0926\u093f\u0928\u094b\u0902 \u092e\u0947\u0902 8.53% \u0915\u093e \u0930\u093f\u091f\u0930\u094d\u0928 \u0914\u0930 \u0938\u093e\u0932-\u0926\u0930-\u0938\u093e\u0932 4.83% \u0915\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u0926\u0930\u094d\u091c \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964 \u0935\u0939\u0940\u0902, 1 \u0938\u093e\u0932 \u092e\u0947\u0902 \u0915\u0941\u0932 \u0936\u0947\u092f\u0930\u0927\u093e\u0930\u0915 \u0930\u093f\u091f\u0930\u094d\u0928 \u092e\u0947\u0902 82.22% \u0914\u0930 3 \u0938\u093e\u0932 \u092e\u0947\u0902 \u0915\u0941\u0932 \u0936\u0947\u092f\u0930\u0927\u093e\u0930\u0915 \u0930\u093f\u091f\u0930\u094d\u0928 \u092e\u0947\u0902 83.21% \u0915\u0940 \u0917\u093f\u0930\u093e\u0935\u091f \u092f\u0939 \u0926\u0930\u094d\u0936\u093e\u0924\u0940 \u0939\u0948 \u0915\u093f \u092c\u093e\u091c\u093e\u0930 \u0915\u093e \u0930\u0941\u091d\u093e\u0928 \u0915\u093f\u0924\u0928\u093e \u0920\u0902\u0921\u093e \u092a\u0921\u093c \u0917\u092f\u093e \u0939\u0948, \u091c\u092c\u0915\u093f 90 \u0926\u093f\u0928\u094b\u0902 \u092e\u0947\u0902 8.62% \u0915\u0947 \u0930\u093f\u091f\u0930\u094d\u0928 \u0938\u0947 \u0915\u0941\u091b \u0905\u0932\u094d\u092a\u0915\u093e\u0932\u093f\u0915 \u0917\u0924\u093f \u0915\u0947 \u092a\u0941\u0928\u0930\u094d\u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0915\u093e \u0938\u0902\u0915\u0947\u0924 \u092e\u093f\u0932\u0924\u093e \u0939\u0948\u0964.<\/p>","protected":false},"excerpt":{"rendered":"<p>Elevidys, the only gene therapy approved by the FDA for Duchenne muscular dystrophy (DMD), has disappointed DMD communities and investors following the release of three years of data from patients. Marketed at a price of $2.9 million American dollars, the product has raised several questions for families of children with DMD: &#8216;How effective is Elevidys [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6174,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[33,179,61,107,108,65,110,109],"class_list":["post-5673","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-elevidys","tag-elevidys-gene-therapy","tag-gene-therapy","tag-regenxbio","tag-rgx-202","tag-sarepta","tag-sgt-003","tag-solid-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/5673","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=5673"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/5673\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/6174"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=5673"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=5673"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=5673"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}