{"id":5141,"date":"2025-11-13T11:00:25","date_gmt":"2025-11-13T08:00:25","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5141"},"modified":"2025-11-13T11:10:04","modified_gmt":"2025-11-13T08:10:04","slug":"why-does-the-fda-approve-dmd-therapies-that-fail-in-clinical-trials","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/why-does-the-fda-approve-dmd-therapies-that-fail-in-clinical-trials\/","title":{"rendered":"FDA \u0909\u0928 DMD \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u094b \u0915\u094d\u092f\u094b\u0902 \u092e\u0902\u091c\u0942\u0930\u0940 \u0926\u0947\u0924\u093e \u0939\u0948 \u091c\u094b \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0935\u093f\u092b\u0932 \u0939\u094b \u091c\u093e\u0924\u0947 \u0939\u0948\u0902?"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>\u0915\u094d\u092f\u093e \u0932\u093e\u0916\u094b\u0902 \u0921\u0949\u0932\u0930 \u092e\u0947\u0902 \u092c\u0947\u091a\u0940 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0914\u0930 \u092e\u093e\u0938\u093f\u0915 \u0906\u0927\u093e\u0930 \u092a\u0930 \u0926\u0940 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0940 \u0924\u0925\u093e \u0939\u091c\u093e\u0930\u094b\u0902 \u0921\u0949\u0932\u0930 \u092e\u0947\u0902 \u092c\u0947\u091a\u0940 \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0940 \u090f\u0915\u094d\u0938\u0949\u0928-\u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u0915\u093e\u092e \u0915\u0930\u0924\u0940 \u0939\u0948\u0902?<\/strong> \u0924\u0940\u0935\u094d\u0930 \u0924\u0928\u093e\u0935 \u0915\u0947 \u092c\u0940\u091a \u0909\u092a\u091a\u093e\u0930 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0905\u092d\u093f\u092f\u093e\u0928 \u091a\u0932\u093e \u0930\u0939\u0947 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948 \u0915\u093f \u0921\u0940\u090f\u092e\u0921\u0940 \u0909\u092a\u091a\u093e\u0930 \u0909\u0928\u0915\u0947 \u092c\u091a\u094d\u091a\u094b\u0902 \u0915\u0947 \u091c\u0940\u0935\u0928 \u092a\u0930 \u0938\u0915\u093e\u0930\u093e\u0924\u094d\u092e\u0915 \u092a\u094d\u0930\u092d\u093e\u0935 \u0921\u093e\u0932\u0947\u0917\u093e, \u0932\u0947\u0915\u093f\u0928 \u0906\u0902\u0915\u0921\u093c\u0947 \u0909\u0924\u0928\u0947 \u0906\u0936\u093e\u091c\u0928\u0915 \u0928\u0939\u0940\u0902 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u092c Sarepta Therapeutics \u0928\u0947 \u0907\u0938 \u092e\u0939\u0940\u0928\u0947 \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0909\u0938\u0915\u0947 \u0926\u094d\u0935\u093e\u0930\u093e \u0935\u093f\u092a\u0923\u0928 \u0915\u0940 \u0917\u0908 \u0926\u094b \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0926\u0935\u093e\u0913\u0902 \u0915\u0947 \u0932\u093f\u090f \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0905\u092a\u0928\u0947 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0938\u092e\u093e\u092a\u0928 \u092c\u093f\u0902\u0926\u0941 \u0924\u0915 \u0928\u0939\u0940\u0902 \u092a\u0939\u0941\u0902\u091a \u092a\u093e\u092f\u093e \u0939\u0948, \u0924\u094b \u092f\u0939 \u0926\u0935\u093e\u0913\u0902 \u0915\u0947 \u0932\u093f\u090f \u0905\u0902\u0924 \u0915\u093e \u0938\u0902\u0915\u0947\u0924 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964 &gt;&gt; <a href=\"https:\/\/dmdwarrior.com\/hi\/sarepta-dmd-exon-skipping-therapies-fail-confirmatory-study-stock-price-down\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0940 \u0921\u0940\u090f\u092e\u0921\u0940 \u090f\u0915\u094d\u0938\u0949\u0928-\u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940\u091c\u093c \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0935\u093f\u092b\u0932, \u0938\u094d\u091f\u0949\u0915 \u092e\u0942\u0932\u094d\u092f \u092e\u0947\u0902 \u0917\u093f\u0930\u093e\u0935\u091f<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0939\u093e\u0932\u093e\u0901\u0915\u093f, \u0915\u0902\u092a\u0928\u0940 \u0915\u0947 \u0928\u0947\u0924\u093e \u0907\u0938 \u092d\u093e\u0935\u0928\u093e \u0915\u094b \u091b\u094b\u0921\u093c\u0928\u0947 \u0915\u094b \u0924\u0948\u092f\u093e\u0930 \u0928\u0939\u0940\u0902 \u0925\u0947\u0964 \u0936\u094b\u0927 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902, \u091c\u093f\u0928\u0915\u0940 \u0909\u092e\u094d\u0930 6 \u0938\u0947 13 \u0935\u0930\u094d\u0937 \u0915\u0947 \u092c\u0940\u091a \u0939\u0948, \u092e\u0947\u0902 \u0926\u0947\u0916\u0947 \u0917\u090f \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u0915\u0940\u092f \u0930\u0942\u092a \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928\u094b\u0902 \u0915\u0947 \u0906\u0927\u093e\u0930 \u092a\u0930, \u0935\u0947 FDA \u0938\u0947 \u092e\u093f\u0932\u0915\u0930 &quot;\u0924\u094d\u0935\u0930\u093f\u0924 \u0938\u0947 \u092a\u093e\u0930\u0902\u092a\u0930\u093f\u0915 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092e\u0947\u0902 \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928&quot; \u092a\u0930 \u091a\u0930\u094d\u091a\u093e \u0915\u0930\u0928\u0947 \u0915\u093e \u0907\u0930\u093e\u0926\u093e \u0930\u0916\u0924\u0947 \u0939\u0948\u0902\u0964\u201c<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0915 \u0905\u0938\u092b\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0939\u092e\u0947\u0936\u093e \u092e\u094c\u0924 \u0915\u0940 \u0938\u091c\u093c\u093e \u0928\u0939\u0940\u0902 \u0939\u094b\u0924\u093e, \u0914\u0930 Sarepta \u092f\u0939 \u0938\u092e\u091d\u0928\u0947 \u0935\u093e\u0932\u0940 \u092a\u0939\u0932\u0940 \u0915\u0902\u092a\u0928\u0940 \u0928\u0939\u0940\u0902 \u0939\u0948; \u0926\u0930\u0905\u0938\u0932, \u0907\u0938\u0928\u0947 \u090f\u0915 \u0926\u0935\u093e \u0915\u094b \u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u092e\u094c\u0924 \u0938\u0947 \u092c\u091a\u093e \u0932\u093f\u092f\u093e \u0939\u0948\u0964 \u0905\u0902\u0924\u093f\u092e \u091a\u0930\u0923 \u0915\u0947 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0932\u0915\u094d\u0937\u094d\u092f \u0939\u093e\u0938\u093f\u0932 \u0928 \u0915\u0930 \u092a\u093e\u0928\u0947 \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926, \u0907\u0938\u0915\u0947 DMD \u091c\u0940\u0928 \u0909\u092a\u091a\u093e\u0930, Elevidys \u0915\u094b \u092a\u0942\u0930\u0940 \u0924\u0930\u0939 \u0938\u0947 \u092e\u0902\u091c\u093c\u0942\u0930\u0940 \u092e\u093f\u0932 \u0917\u0908 \u0914\u0930 \u0932\u0947\u092c\u0932 \u0915\u093e \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u092d\u0940 \u0939\u094b \u0917\u092f\u093e\u0964 &gt;&gt; <a href=\"https:\/\/dmdwarrior.com\/hi\/why-elevidys-was-not-approved-by-the-european-medicines-agency-ema\/\" target=\"_blank\" rel=\"noreferrer noopener\">Elevidys \u0915\u094b \u092f\u0942\u0930\u094b\u092a\u0940\u092f \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u090f\u091c\u0947\u0902\u0938\u0940 (EMA) \u0926\u094d\u0935\u093e\u0930\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u094d\u092f\u094b\u0902 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0905\u0928\u0941\u0915\u0942\u0932\u0928\u0940\u092f \u0930\u0923\u0928\u0940\u0924\u093f \u0915\u0947 \u0905\u092a\u0928\u0947 \u0906\u0932\u094b\u091a\u0915 \u092d\u0940 \u0939\u0948\u0902\u0964 \u0915\u0941\u091b \u0935\u093f\u0936\u0947\u0937\u091c\u094d\u091e\u094b\u0902 \u0915\u0947 \u0905\u0928\u0941\u0938\u093e\u0930, \u091c\u092c \u0915\u094b\u0908 \u0926\u0935\u093e \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0935\u093f\u092b\u0932 \u0939\u094b \u091c\u093e\u0924\u093e \u0939\u0948, \u0924\u094b \u0915\u0902\u092a\u0928\u0940 \u0915\u094b \u0909\u0938 \u092a\u0930 \u0915\u0921\u093c\u0940 \u0930\u094b\u0915 \u0932\u0917\u093e \u0926\u0947\u0928\u0940 \u091a\u093e\u0939\u093f\u090f\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c\u092f\u0947\u0932 \u0938\u094d\u0915\u0942\u0932 \u0911\u092b \u092e\u0947\u0921\u093f\u0938\u093f\u0928 \u092e\u0947\u0902 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0914\u0930 \u091c\u0928 \u0938\u094d\u0935\u093e\u0938\u094d\u0925\u094d\u092f \u0915\u0947 \u092a\u094d\u0930\u094b\u092b\u0947\u0938\u0930 \u0921\u0949. \u091c\u094b\u0938\u0947\u092b \u0930\u0949\u0938 \u0928\u0947 \u0915\u0939\u093e, &quot;\u092e\u0947\u0930\u0947 \u092e\u0928 \u092e\u0947\u0902 \u0915\u094b\u0908 \u0917\u0941\u0902\u091c\u093e\u0907\u0936 \u0928\u0939\u0940\u0902 \u0939\u0948\u0964 \u092e\u0948\u0902 \u0938\u092e\u091d \u0928\u0939\u0940\u0902 \u092a\u093e \u0930\u0939\u093e \u0939\u0942\u0901 \u0915\u093f \u090f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923, \u091c\u094b \u092f\u0939 \u0926\u093f\u0916\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092c\u0928\u093e\u092f\u093e \u0917\u092f\u093e \u0939\u0948 \u0915\u093f \u0915\u094b\u0908 \u0926\u0935\u093e \u0915\u093e\u092e \u0915\u0930\u0924\u0940 \u0939\u0948 \u092f\u093e \u0928\u0939\u0940\u0902, \u0905\u0917\u0930 \u0935\u0939 \u0935\u093f\u092b\u0932 \u0939\u094b \u091c\u093e\u0924\u093e \u0939\u0948, \u0924\u094b \u0909\u0938\u0947 \u0907\u0938\u094d\u0924\u0947\u092e\u093e\u0932 \u0915\u0947 \u0932\u093f\u090f \u0915\u0948\u0938\u0947 \u092e\u0902\u091c\u093c\u0942\u0930\u0940 \u092e\u093f\u0932 \u0938\u0915\u0924\u0940 \u0939\u0948\u0964 \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u093e \u0915\u094d\u092f\u093e \u092e\u0924\u0932\u092c \u0925\u093e?&quot;\u201d<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u0939\u0932\u0947 \u0938\u0947 \u0939\u0940 \u0909\u0924\u094d\u092a\u093e\u0926\u094b\u0902 \u0915\u094b \u0932\u093e\u092d \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u093e \u0938\u0930\u094d\u0935\u094b\u0924\u094d\u0924\u092e \u0938\u0902\u092d\u0935 \u0905\u0935\u0938\u0930 \u0926\u0947\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0924\u0948\u092f\u093e\u0930 \u0915\u093f\u090f \u0917\u090f \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u201c\u0909\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u0915\u0939\u093e, &quot;\u0914\u0930 \u092f\u0926\u093f \u092f\u0939 \u0936\u0942\u0928\u094d\u092f \u0939\u0948 \u0924\u094b \u092f\u0939 \u0936\u0942\u0928\u094d\u092f \u0939\u0948\u0964&quot;.<\/strong><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092e\u093e\u0930\u094d\u0917<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">FDA \u0928\u0947 \u0939\u093e\u0932 \u0915\u0947 \u0935\u0930\u094d\u0937\u094b\u0902 \u092e\u0947\u0902 \u0915\u0908 \u0918\u091f\u093f\u092f\u093e \u0926\u0935\u093e\u0913\u0902 \u0915\u094b \u092e\u0902\u091c\u093c\u0942\u0930\u0940 \u0926\u0940 \u0939\u0948\u0964 \u0930\u0949\u0938 \u0915\u0947 \u0938\u0939-\u0932\u0947\u0916\u0915 \u090f\u0915 \u0936\u094b\u0927 \u0915\u0947 \u0905\u0928\u0941\u0938\u093e\u0930, 2018 \u0914\u0930 2021 \u0915\u0947 \u092c\u0940\u091a, \u0938\u092d\u0940 \u0938\u094d\u0935\u0940\u0915\u0943\u0924\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 10% \u0938\u0947 \u091c\u093c\u094d\u092f\u093e\u0926\u093e \u0910\u0938\u0940 \u0926\u0935\u093e\u090f\u0901 \u0925\u0940\u0902 \u091c\u094b \u0915\u093f\u0938\u0940 \u0928\u093f\u0930\u094d\u0923\u093e\u092f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u0915\u092e \u0938\u0947 \u0915\u092e \u090f\u0915 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0938\u092e\u093e\u092a\u0928 \u092c\u093f\u0902\u0926\u0941 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0935\u093f\u092b\u0932 \u0930\u0939\u0940\u0902\u0964 &gt;&gt; <a href=\"https:\/\/jamanetwork.com\/journals\/jamainternalmedicine\/fullarticle\/2801023\" target=\"_blank\" rel=\"noreferrer noopener\">\u0932\u0947\u0916 \u092a\u0922\u093c\u094b<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091c\u092c \u0915\u093f\u0938\u0940 \u0926\u0935\u093e \u0915\u094b \u0932\u093e\u092d \u0915\u0947 \u0938\u094d\u092a\u0937\u094d\u091f \u092a\u094d\u0930\u092e\u093e\u0923 \u0915\u0947 \u092c\u093f\u0928\u093e \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u0924\u094b \u0907\u0938\u0938\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u0932\u093e\u0917\u0924 \u0915\u0947 \u0938\u0902\u092c\u0902\u0927 \u092e\u0947\u0902 \u0915\u0908 \u091c\u094b\u0916\u093f\u092e \u0909\u0924\u094d\u092a\u0928\u094d\u0928 \u0939\u094b \u091c\u093e\u0924\u0947 \u0939\u0948\u0902\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c\u0909\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u0915\u0939\u093e, &quot;\u0907\u0928\u092e\u0947\u0902 \u0938\u0947 \u0915\u0941\u091b \u092c\u0947\u0939\u0926 \u092e\u0939\u0902\u0917\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940, \u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0914\u0930 \u0905\u0928\u094d\u092f \u0935\u093f\u0936\u093f\u0937\u094d\u091f \u0926\u0935\u093e\u090f\u0901 \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u094b \u0926\u093f\u0935\u093e\u0932\u093f\u092f\u093e \u092c\u0928\u093e \u0938\u0915\u0924\u0940 \u0939\u0948\u0902\u0964&quot; \u0906\u092e \u091c\u0928\u0924\u093e \u0915\u094b \u092d\u0940 \u091c\u093c\u094d\u092f\u093e\u0926\u093e \u092c\u0940\u092e\u093e \u092a\u094d\u0930\u0940\u092e\u093f\u092f\u092e \u0914\u0930 \u0905\u0928\u094d\u092f \u0932\u093e\u0917\u0924\u094b\u0902 \u0915\u0947 \u0915\u093e\u0930\u0923 \u0915\u0941\u091b \u0935\u093f\u0924\u094d\u0924\u0940\u092f \u092c\u094b\u091d \u0909\u0920\u093e\u0928\u093e \u092a\u0921\u093c\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0909\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u0915\u0939\u093e \u0915\u093f \u092e\u0930\u0940\u091c\u094b\u0902 \u0915\u0940 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u0947 \u0932\u093f\u090f FDA \u092e\u093e\u0928\u0915\u094b\u0902 \u0915\u094b \u0914\u0930 \u0905\u0927\u093f\u0915 \u0915\u0920\u094b\u0930 \u092c\u0928\u093e\u0928\u0947 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u0948\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c\u0930\u0949\u0938 \u0928\u0947 \u0915\u0939\u093e, &quot;\u092e\u0947\u0930\u0940 \u0938\u093e\u092e\u093e\u0928\u094d\u092f \u092d\u093e\u0935\u0928\u093e \u092f\u0939 \u0939\u0948 \u0915\u093f \u092f\u0926\u093f \u0939\u092e \u090f\u0915 \u0938\u092e\u093e\u091c \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u093e\u0926\u094b\u0902 \u0915\u094b \u0915\u092e \u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u092a\u094d\u0930\u092e\u093e\u0923\u094b\u0902 \u0915\u0947 \u0938\u093e\u0925 \u0905\u0928\u0941\u092e\u094b\u0926\u093f\u0924 \u0939\u094b\u0928\u0947 \u0915\u0940 \u0905\u0928\u0941\u092e\u0924\u093f \u0926\u0947\u0924\u0947 \u0939\u0948\u0902, \u0924\u093e\u0915\u093f \u0935\u0947 \u092e\u0930\u0940\u091c\u094b\u0902 \u0924\u0915 \u091c\u0932\u094d\u0926\u0940 \u092a\u0939\u0941\u0902\u091a \u0938\u0915\u0947\u0902, \u0924\u094b \u0939\u092e\u0947\u0902 \u092f\u0939 \u0938\u0941\u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092c\u0947\u0939\u0924\u0930 \u0915\u093e\u092e \u0915\u0930\u0928\u0947 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u0948 \u0915\u093f \u0915\u0902\u092a\u0928\u093f\u092f\u093e\u0902 \u0909\u091a\u093f\u0924 \u0938\u092e\u092f \u0915\u0947 \u092d\u0940\u0924\u0930 \u092c\u093e\u091c\u093e\u0930 \u092e\u0947\u0902 \u0906\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0915\u0940 \u0905\u0935\u0927\u093f \u092e\u0947\u0902 \u092a\u0941\u0937\u094d\u091f\u093f\u0915\u0930\u0923 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092a\u0942\u0930\u093e \u0915\u0930 \u0932\u0947\u0902, \u0924\u093e\u0915\u093f \u0939\u092e\u0947\u0902 \u092a\u0924\u093e \u091a\u0932\u0947 \u0915\u093f \u0935\u0947 \u0915\u093e\u092e \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u092e\u0930\u0940\u091c \u0905\u092a\u0928\u093e \u092a\u0948\u0938\u093e \u092c\u0930\u094d\u092c\u093e\u0926 \u0928\u0939\u0940\u0902 \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902\u0964&quot;.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Do gene therapies, marketed for millions of dollars, and exon-skipping therapies administered monthly and sold for thousands of dollars, actually work well? Families campaigning under intense stress to access the therapies hope that DMD therapies will positively impact their children&#8217;s lives, but the data is less promising. It might have been the end of the [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":5142,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[137,33,178,88,61,65],"class_list":["post-5141","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-clinical-trial","tag-elevidys","tag-exon-skipping-therapies","tag-fda","tag-gene-therapy","tag-sarepta"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/5141","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=5141"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/5141\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/5142"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=5141"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=5141"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=5141"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}