{"id":5101,"date":"2025-11-04T16:49:31","date_gmt":"2025-11-04T13:49:31","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=5101"},"modified":"2025-11-04T17:01:51","modified_gmt":"2025-11-04T14:01:51","slug":"solid-biosciences-provides-update-on-inspire-duchenne-clinical-trial-progress-and-planned-regulatory-discussions","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/solid-biosciences-provides-update-on-inspire-duchenne-clinical-trial-progress-and-planned-regulatory-discussions\/","title":{"rendered":"Solid Biosciences INSPIRE DUCHENNE \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0914\u0930 \u0928\u093f\u092f\u094b\u091c\u093f\u0924 \u0928\u093f\u092f\u093e\u092e\u0915 \u091a\u0930\u094d\u091a\u093e\u0913\u0902 \u092a\u0930 \u0905\u0926\u094d\u092f\u0924\u0928 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u093e \u0939\u0948"},"content":{"rendered":"<p class=\"wp-block-paragraph\"><strong>Solid Biosciences \u0928\u0947 \u091a\u0930\u0923 1\/2 INSPIRE DUCHENNE \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u0947 \u0938\u0915\u093e\u0930\u093e\u0924\u094d\u092e\u0915 \u0928\u090f \u0905\u0902\u0924\u0930\u093f\u092e \u0921\u0947\u091f\u093e \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940\u0964.<\/strong> \u0915\u0902\u092a\u0928\u0940 \u0928\u0947 \u090f\u0938\u091c\u0940\u091f\u0940-003 \u0915\u0947 \u0932\u093f\u090f \u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092e\u093e\u0930\u094d\u0917\u094b\u0902 \u0938\u0939\u093f\u0924 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092a\u0902\u091c\u0940\u0915\u0930\u0923 \u092e\u093e\u0930\u094d\u0917\u094b\u0902 \u092a\u0930 \u091a\u0930\u094d\u091a\u093e \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0916\u093e\u0926\u094d\u092f \u090f\u0935\u0902 \u0914\u0937\u0927\u093f \u092a\u094d\u0930\u0936\u093e\u0938\u0928 (1\u091f\u0940\u092a\u0940135\u091f\u0940) \u0915\u0947 \u0938\u093e\u0925 \u0905\u092a\u0928\u0940 \u092c\u0948\u0920\u0915 \u0915\u0947 \u0928\u093f\u092f\u094b\u091c\u093f\u0924 \u0938\u092e\u092f \u0915\u0947 \u092c\u093e\u0930\u0947 \u092e\u0947\u0902 \u092d\u0940 \u0905\u0926\u094d\u092f\u0924\u0928 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0940\u0964.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Solid Biosciences \u0915\u0947 \u0905\u0927\u094d\u092f\u0915\u094d\u0937 \u0914\u0930 \u0938\u0940\u0908\u0913 \u092c\u094b \u0915\u0941\u092e\u094d\u092c\u094b \u0928\u0947 \u091f\u093f\u092a\u094d\u092a\u0923\u0940 \u0915\u0940, &quot;\u0906\u091c \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 INSPIRE DUCHENNE \u0915\u0947 \u0905\u0902\u0924\u0930\u093f\u092e \u0906\u0901\u0915\u0921\u093c\u0947 SGT-003 \u0915\u0940 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u0940\u092f \u0915\u094d\u0937\u092e\u0924\u093e \u092e\u0947\u0902 \u0939\u092e\u093e\u0930\u0947 \u0935\u093f\u0936\u094d\u0935\u093e\u0938 \u0915\u094b \u092e\u091c\u093c\u092c\u0942\u0924 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964 SGT-003 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0938\u094d\u0924\u0930\u094b\u0902 \u0915\u0947 \u092e\u091c\u093c\u092c\u0942\u0924 \u0926\u0947\u0916\u0947 \u0917\u090f \u091c\u0948\u0935\u093f\u0915 \u0938\u0939\u0938\u0902\u092c\u0902\u0927\u094b\u0902 \u0938\u0947 \u0932\u0947\u0915\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928-\u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u0949\u092e\u094d\u092a\u094d\u0932\u0947\u0915\u094d\u0938 \u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u0918\u091f\u0915\u094b\u0902 \u0915\u0940 \u0909\u091a\u093f\u0924 \u0938\u094d\u0925\u093e\u0928\u0940\u092f\u0915\u0943\u0924 \u092a\u0941\u0928\u0930\u094d\u0938\u094d\u0925\u093e\u092a\u0928\u093e \u0914\u0930 \u0939\u0943\u0926\u092f \u0915\u094d\u0930\u093f\u092f\u093e \u0938\u093e\u092e\u093e\u0928\u094d\u092f\u0940\u0915\u0930\u0923 \u0915\u0947 \u0936\u0941\u0930\u0941\u0906\u0924\u0940 \u092a\u094d\u0930\u092e\u093e\u0923\u094b\u0902 \u0924\u0915, \u0939\u092e \u092e\u093e\u0928\u0935 \u0936\u0930\u0940\u0930 \u092e\u0947\u0902 \u090f\u0915 \u0938\u094d\u092a\u0937\u094d\u091f \u0914\u0930 \u0935\u094d\u092f\u093e\u092a\u0915 \u092a\u094d\u0930\u092d\u093e\u0935 \u0926\u0947\u0916 \u0930\u0939\u0947 \u0939\u0948\u0902, \u091c\u094b \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092a\u094d\u0930\u0924\u093f \u090f\u0915 \u0938\u092e\u0928\u094d\u0935\u093f\u0924, \u092a\u094d\u0930\u0923\u093e\u0932\u0940\u0917\u0924 \u092a\u094d\u0930\u0924\u093f\u0915\u094d\u0930\u093f\u092f\u093e \u0915\u093e \u0938\u0902\u0915\u0947\u0924 \u0926\u0947\u0924\u093e \u0939\u0948\u0964 \u0939\u092e\u093e\u0930\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u092f\u0947 \u0905\u0902\u0924\u0930\u093f\u092e \u0906\u0901\u0915\u0921\u093c\u0947 \u0906\u091c \u0924\u0915 \u0915\u093f\u0938\u0940 \u092d\u0940 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0938\u092c\u0938\u0947 \u0917\u0939\u0928 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0939\u0948\u0902\u0964 \u0907\u0928 \u0905\u0902\u0924\u0930\u093f\u092e \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937\u094b\u0902 \u0915\u0940 \u0917\u0941\u0923\u0935\u0924\u094d\u0924\u093e \u0914\u0930 \u0938\u0941\u0938\u0902\u0917\u0924\u0924\u093e, \u0906\u0923\u0935\u093f\u0915 \u092a\u094d\u0930\u092d\u093e\u0935 \u0915\u094b \u0938\u093e\u0930\u094d\u0925\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u092e\u0947\u0902 \u092c\u0926\u0932\u0928\u0947 \u0915\u0940 SGT-003 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u092e\u0947\u0902 \u0939\u092e\u093e\u0930\u0947 \u0935\u093f\u0936\u094d\u0935\u093e\u0938 \u0915\u094b \u092a\u0941\u0937\u094d\u091f \u0915\u0930\u0924\u0940 \u0939\u0948\u0964&quot;\u201c<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0936\u094d\u0930\u0940 \u0915\u092e\u094d\u092c\u094b \u0928\u0947 \u0906\u0917\u0947 \u0915\u0939\u093e, &quot;\u0935\u093f\u0915\u0938\u093f\u0924 \u0939\u094b\u0924\u0947 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u0930\u093f\u0926\u0943\u0936\u094d\u092f \u0914\u0930 INSPIRE DUCHENNE \u092e\u0947\u0902 \u0928\u093e\u092e\u093e\u0902\u0915\u0928 \u0915\u0940 \u0924\u0940\u0935\u094d\u0930 \u0917\u0924\u093f \u0915\u094b \u0926\u0947\u0916\u0924\u0947 \u0939\u0941\u090f, \u0939\u092e\u0928\u0947 FDA \u0915\u0947 \u0938\u093e\u0925 \u0905\u092a\u0928\u0940 \u0928\u093f\u092f\u094b\u091c\u093f\u0924 \u092c\u0948\u0920\u0915 \u0915\u094b 2026 \u0915\u0940 \u092a\u0939\u0932\u0940 \u091b\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0938\u094d\u0925\u093e\u0928\u093e\u0902\u0924\u0930\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u093e \u0938\u0915\u094d\u0930\u093f\u092f \u0928\u093f\u0930\u094d\u0923\u092f \u0932\u093f\u092f\u093e \u0939\u0948\u0964 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0938\u092e\u092f \u0939\u092e\u0947\u0902 1) FDA \u0915\u0947 \u0938\u093e\u0925 \u091a\u0930\u094d\u091a\u093e \u0915\u0947 \u0932\u093f\u090f \u0905\u0927\u093f\u0915 \u0935\u093f\u0938\u094d\u0924\u0943\u0924 \u0921\u0947\u091f\u093e \u0938\u0947\u091f \u0924\u0948\u092f\u093e\u0930 \u0915\u0930\u0928\u0947, 2) \u0909\u091a\u094d\u091a-\u0917\u0941\u0923\u0935\u0924\u094d\u0924\u093e \u0935\u093e\u0932\u0947, \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u092e\u0947\u0932 \u0916\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u093e\u0915\u0943\u0924\u093f\u0915 \u0907\u0924\u093f\u0939\u093e\u0938 \u0921\u0947\u091f\u093e \u092a\u0930 \u0906\u0927\u093e\u0930\u093f\u0924 \u090f\u0915 \u0935\u094d\u092f\u093e\u092a\u0915 \u092c\u093e\u0939\u0930\u0940 \u0924\u0941\u0932\u0928\u093f\u0924\u094d\u0930 \u0915\u0940 \u0926\u093f\u0936\u093e \u092e\u0947\u0902 \u0915\u093e\u092e \u0915\u0930\u0928\u0947, 3) \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0906\u0935\u0947\u0926\u0928 (BLA) \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0924\u0948\u092f\u093e\u0930\u0940 \u092e\u0947\u0902 \u0905\u092a\u0928\u0947 CDMO \u092d\u093e\u0917\u0940\u0926\u093e\u0930 \u0915\u0947 \u0938\u093e\u0925 \u0939\u092e\u093e\u0930\u0940 \u092a\u094d\u0930\u0915\u094d\u0930\u093f\u092f\u093e \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 \u092f\u094b\u0917\u094d\u092f\u0924\u093e (PPQ) \u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0930\u0928 \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947, \u0914\u0930 4) IMPACT DUCHENNE \u092e\u0947\u0902 \u0916\u0941\u0930\u093e\u0915 \u0936\u0941\u0930\u0942 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0915\u0930\u0947\u0917\u093e, \u091c\u094b \u0939\u092e\u093e\u0930\u093e \u091a\u0930\u0923 3 \u092f\u093e\u0926\u0943\u091a\u094d\u091b\u093f\u0915, \u0921\u092c\u0932-\u092c\u094d\u0932\u093e\u0907\u0902\u0921, \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0939\u0948.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201c&quot;\u0905\u092c \u0939\u092e\u093e\u0930\u0940 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915\u0924\u093e SGT-003 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0924\u094d\u0935\u0930\u093f\u0924 \u0928\u093f\u092f\u093e\u092e\u0915 \u092e\u093e\u0930\u094d\u0917 \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0928\u0947 \u0939\u0947\u0924\u0941 \u090f\u0915 \u092e\u091c\u093c\u092c\u0942\u0924 \u0921\u0947\u091f\u093e \u0938\u0947\u091f \u0915\u093e \u0924\u0947\u091c\u093c\u0940 \u0938\u0947 \u0928\u093f\u0930\u094d\u092e\u093e\u0923 \u0915\u0930\u0928\u093e \u0939\u0948, \u0914\u0930 \u0939\u092e SGT-003 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u0915\u094b \u092f\u0925\u093e\u0936\u0940\u0918\u094d\u0930 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0924\u0924\u094d\u092a\u0930\u0924\u093e \u0938\u0947 \u0915\u093e\u0930\u094d\u092f \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092a\u094d\u0930\u0924\u093f\u092c\u0926\u094d\u0927 \u0939\u0948\u0902\u0964 SGT-003 \u0915\u0947 \u092c\u093e\u0926, \u0939\u092e\u093e\u0930\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u092a\u093e\u0907\u092a\u0932\u093e\u0907\u0928 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0928\u093f\u0930\u0902\u0924\u0930 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902\u0964&quot; \u0936\u094d\u0930\u0940 \u0915\u092e\u094d\u092c\u094b \u0928\u0947 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u0928\u093f\u0915\u093e\u0932\u093e\u0964.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">SGT-003 \u2013 INSPIRE DUCHENNE \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>31 \u0905\u0915\u094d\u091f\u0942\u092c\u0930, 2025 \u0924\u0915 INSPIRE DUCHENNE \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 23 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0916\u0941\u0930\u093e\u0915 \u0926\u0940 \u0917\u0908 \u0939\u0948; \u0938\u0949\u0932\u093f\u0921 \u0915\u094b \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948 \u0915\u093f 2026 \u0915\u0940 \u0936\u0941\u0930\u0941\u0906\u0924 \u0924\u0915 \u0915\u0941\u0932 30 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0916\u0941\u0930\u093e\u0915 \u0926\u0940 \u091c\u093e\u090f\u0917\u0940, \u092b\u093f\u0930 H1 2026 \u092e\u0947\u0902 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092a\u0902\u091c\u0940\u0915\u0930\u0923 \u092e\u093e\u0930\u094d\u0917\u094b\u0902 \u092a\u0930 \u091a\u0930\u094d\u091a\u093e \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f FDA \u0915\u0947 \u0938\u093e\u0925 \u092c\u0948\u0920\u0915 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u0939\u0948 -<\/li>\n\n\n\n<li>\u090f\u0938\u091c\u0940\u091f\u0940-003 \u0915\u094b \u0906\u092e \u0924\u094c\u0930 \u092a\u0930 \u0938\u094d\u091f\u0947\u0930\u0949\u092f\u0921-\u0915\u0947\u0935\u0932 \u0930\u094b\u0917\u0928\u093f\u0930\u094b\u0927\u0940 \u0907\u092e\u094d\u092f\u0942\u0928\u094b\u092e\u0949\u0921\u094d\u092f\u0941\u0932\u0947\u0936\u0928 \u0935\u094d\u092f\u0935\u0938\u094d\u0925\u093e \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0915\u0947 \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u0938\u0939\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948; \u0939\u0943\u0926\u092f \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0928\u093f\u0917\u0930\u093e\u0928\u0940 \u0928\u0947 \u0939\u0943\u0926\u092f \u0915\u0940 \u091a\u094b\u091f \u092e\u0947\u0902 \u0915\u092e\u0940 \u0914\u0930 \u0939\u0943\u0926\u092f \u0915\u093e\u0930\u094d\u092f \u0938\u093e\u092e\u093e\u0928\u094d\u092f\u0940\u0915\u0930\u0923 \u0915\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0938\u0902\u0915\u0947\u0924\u094b\u0902 \u0915\u094b \u0926\u093f\u0916\u093e\u0928\u093e \u091c\u093e\u0930\u0940 \u0930\u0916\u093e \u0939\u0948 -<\/li>\n\n\n\n<li>10 \u0909\u092a\u091a\u093e\u0930\u093f\u0924 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 (5-10 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0906\u092f\u0941) \u0915\u0947 90\u0935\u0947\u0902 \u0926\u093f\u0928 \u0915\u0947 \u092c\u093e\u092f\u094b\u092a\u094d\u0938\u0940 \u0921\u0947\u091f\u093e \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u093e \u0915\u093f \u0938\u092d\u0940 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0928\u0947 \u0935\u0947\u0938\u094d\u091f\u0930\u094d\u0928 \u092c\u094d\u0932\u0949\u091f \u0926\u094d\u0935\u093e\u0930\u093e 58% \u0915\u0947 \u0914\u0938\u0924 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f, \u092e\u093e\u0938 \u0938\u094d\u092a\u0947\u0915\u094d\u091f\u094d\u0930\u094b\u092e\u0947\u091f\u094d\u0930\u0940 \u0926\u094d\u0935\u093e\u0930\u093e 58%, \u0907\u092e\u094d\u092f\u0942\u0928\u094b\u092b\u094d\u0932\u094b\u0930\u0947\u0938\u0947\u0902\u0938 \u0926\u094d\u0935\u093e\u0930\u093e 51% \u0915\u0947 \u0914\u0938\u0924 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u0949\u091c\u093f\u091f\u093f\u0935 \u092b\u093e\u0907\u092c\u0930 \u0914\u0930 \u0907\u092e\u094d\u092f\u0942\u0928\u094b\u092b\u094d\u0932\u094b\u0930\u0947\u0938\u0947\u0902\u0938 \u0926\u094d\u0935\u093e\u0930\u093e 50% \u0915\u0947 \u0914\u0938\u0924 \u092c\u0940\u091f\u093e-\u0938\u093e\u0930\u094d\u0915\u094b\u0917\u094d\u0932\u093e\u0907\u0915\u0928 \u092a\u0949\u091c\u093f\u091f\u093f\u0935 \u092b\u093e\u0907\u092c\u0930 \u0915\u0947 \u0938\u093e\u0925 \u0909\u092a\u091a\u093e\u0930 \u092a\u0930 \u092a\u094d\u0930\u0924\u093f\u0915\u094d\u0930\u093f\u092f\u093e \u0926\u0940\u0964<\/li>\n\n\n\n<li>\u0926\u093f\u0928 90 \u092e\u093e\u0907\u0915\u094d\u0930\u094b\u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0915\u0947 \u0938\u094d\u0924\u0930 \u0914\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928-\u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u0949\u092e\u094d\u092a\u094d\u0932\u0947\u0915\u094d\u0938 (\u0921\u0940\u090f\u092a\u0940\u0938\u0940) \u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u0918\u091f\u0915\u094b\u0902, \u092c\u0940\u091f\u093e-\u0938\u093e\u0930\u094d\u0915\u094b\u0917\u094d\u0932\u093e\u0907\u0915\u0928 (\u0906\u0930 = 0.95) \u0914\u0930 \u090f\u0928\u090f\u0928\u0913\u090f\u0938 (\u0906\u0930 = 0.95) \u0915\u0947 \u092c\u0940\u091a \u092e\u091c\u092c\u0942\u0924 \u0938\u093e\u0902\u0916\u094d\u092f\u093f\u0915\u0940\u092f \u0938\u0939\u0938\u0902\u092c\u0902\u0927\u094b\u0902 \u0928\u0947 \u090f\u0938\u091c\u0940\u091f\u0940-003-\u092e\u0927\u094d\u092f\u0938\u094d\u0925 \u0921\u0940\u090f\u092a\u0940\u0938\u0940 \u092c\u0939\u093e\u0932\u0940 \u0914\u0930 \u0938\u0940\u0915\u0947 \u0938\u094d\u0924\u0930\u094b\u0902 \u092e\u0947\u0902 \u0915\u092e\u0940 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u0947 \u0938\u0941\u0938\u0902\u0917\u0924 \u0938\u0902\u0915\u0947\u0924\u094b\u0902 \u0915\u0947 \u0938\u092c\u0942\u0924 \u0915\u093e \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 \u0915\u093f\u092f\u093e (\u0906\u0930 = -0.78) -<\/li>\n\n\n\n<li>\u0938\u0949\u0932\u093f\u0921 \u0928\u0947 \u092a\u0939\u0932\u093e \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u094d\u0925\u0932 \u0938\u0915\u094d\u0930\u093f\u092f \u0915\u0930 \u0926\u093f\u092f\u093e \u0939\u0948 \u0914\u0930 \u0935\u0930\u094d\u0924\u092e\u093e\u0928 \u092e\u0947\u0902 \u0907\u092e\u094d\u092a\u0948\u0915\u094d\u091f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u0940 \u0938\u094d\u0915\u094d\u0930\u0940\u0928\u093f\u0902\u0917 \u0915\u0930 \u0930\u0939\u093e \u0939\u0948, \u091c\u094b \u0915\u093f SGT-003 \u0915\u093e \u090f\u0915 \u091a\u0930\u0923 3 \u092f\u093e\u0926\u0943\u091a\u094d\u091b\u093f\u0915, \u0921\u092c\u0932-\u092c\u094d\u0932\u093e\u0907\u0902\u0921, \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u092a\u0942\u0930\u094d\u0935-\u092f\u0942\u090f\u0938 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0939\u0948 -<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">\u0926\u093f\u0928 90 \u0914\u0930 \u0926\u093f\u0928 360 \u0926\u094b\u0928\u094b\u0902 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u091a\u094b\u091f \u0914\u0930 \u091f\u0942\u091f\u0928\u0947 \u0915\u0947 \u0935\u093f\u092d\u093f\u0928\u094d\u0928 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930\u094b\u0902 \u092e\u0947\u0902 \u0905\u0928\u0941\u0915\u0942\u0932 \u0915\u092e\u0940 \u0926\u0947\u0916\u0940 \u0917\u0908:<\/p>\n\n\n\n<figure class=\"wp-block-table\"><table class=\"has-fixed-layout\"><tbody><tr><td><strong>\u0938\u0940\u0930\u092e \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930<\/strong><\/td><td class=\"has-text-align-center\" data-align=\"center\"><strong>\u0926\u093f\u0928 90 \u0914\u0938\u0924 \u0915\u091f\u094c\u0924\u0940<\/strong><br><strong>(N=14 \u091c\u092c \u0924\u0915 \u0909\u0932\u094d\u0932\u0947\u0916 \u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u094b)<\/strong><\/td><td class=\"has-text-align-center\" data-align=\"center\"><strong>\u0926\u093f\u0928 360 \u0914\u0938\u0924 \u0915\u091f\u094c\u0924\u0940<\/strong><br><strong>(N=3 \u091c\u092c \u0924\u0915 \u0909\u0932\u094d\u0932\u0947\u0916 \u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u094b)<\/strong><\/td><\/tr><tr><td>\u0938\u0940\u0930\u092e \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c (CK)<\/td><td class=\"has-text-align-center\" data-align=\"center\">34%<\/td><td class=\"has-text-align-center\" data-align=\"center\">42%<\/td><\/tr><tr><td>\u0938\u0940\u0930\u092e \u090f\u0932\u093e\u0928\u093f\u0928 \u091f\u094d\u0930\u093e\u0902\u0938\u090f\u092e\u093f\u0928\u0947\u0938 (ALT)<\/td><td class=\"has-text-align-center\" data-align=\"center\">41%<\/td><td class=\"has-text-align-center\" data-align=\"center\">29%<\/td><\/tr><tr><td>\u0938\u0940\u0930\u092e \u090f\u0938\u094d\u092a\u093e\u0930\u094d\u091f\u0947\u091f \u090f\u092e\u093f\u0928\u094b\u091f\u094d\u0930\u093e\u0902\u0938\u094d\u092b\u0930\u0947\u091c\u093c (AST)<\/td><td class=\"has-text-align-center\" data-align=\"center\">25%<\/td><td class=\"has-text-align-center\" data-align=\"center\">40%<\/td><\/tr><tr><td>\u0938\u0940\u0930\u092e \u0932\u0948\u0915\u094d\u091f\u0947\u091f \u0921\u093f\u0939\u093e\u0907\u0921\u094d\u0930\u094b\u091c\u0928\u0947\u091c (LDH)*<\/td><td class=\"has-text-align-center\" data-align=\"center\">42%<\/td><td class=\"has-text-align-center\" data-align=\"center\">46%<\/td><\/tr><tr><td>\u0938\u0940\u0930\u092e \u091f\u093f\u091f\u093f\u0928**<\/td><td class=\"has-text-align-center\" data-align=\"center\">22%<\/td><td class=\"has-text-align-center\" data-align=\"center\">25%<\/td><\/tr><tr><td colspan=\"3\"><em>*\u090f\u0932\u0921\u0940\u090f\u091a \u0915\u0947 \u0932\u093f\u090f \u0926\u093f\u0928 90 \u092a\u0930 \u0909\u092a\u0932\u092c\u094d\u0927 \u090f\u0928 = 12 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940 \u0928\u092e\u0942\u0928\u0947 (\u0926\u094b \u0928\u092e\u0942\u0928\u0947 \u0939\u0947\u092e\u094b\u0932\u093e\u0907\u091c\u094d\u0921); **\u0926\u093f\u0928 90 \u092a\u0930 \u0909\u092a\u0932\u092c\u094d\u0927 \u090f\u0928 = 11 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u0940 \u0928\u092e\u0942\u0928\u0947 \u0914\u0930 \u091f\u093f\u091f\u093f\u0928 \u0915\u0947 \u0932\u093f\u090f \u0926\u093f\u0928 360 \u092a\u0930 \u0909\u092a\u0932\u092c\u094d\u0927 \u090f\u0928 = 2 \u0928\u092e\u0942\u0928\u0947, \u091c\u093f\u0938\u0915\u093e \u092a\u0939\u0932\u0947 \u0915\u0940 \u0915\u091f\u0911\u092b \u0924\u093f\u0925\u093f \u092a\u0930 \u092c\u0948\u091a-\u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e\u0964.<\/em><\/td><\/tr><\/tbody><\/table><\/figure>\n\n\n\n<h2 class=\"wp-block-heading\">\u0907\u092e\u094d\u092a\u0948\u0915\u094d\u091f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u091a\u0930\u0923 3<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0905\u0915\u094d\u091f\u0942\u092c\u0930 2025 \u092e\u0947\u0902, \u0938\u0949\u0932\u093f\u0921 \u0928\u0947 \u092a\u0939\u0932\u093e \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u094d\u0925\u0932 \u0938\u0915\u094d\u0930\u093f\u092f \u0915\u093f\u092f\u093e \u0914\u0930 \u0907\u092e\u094d\u092a\u0948\u0915\u094d\u091f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u0940 \u0938\u094d\u0915\u094d\u0930\u0940\u0928\u093f\u0902\u0917 \u0936\u0941\u0930\u0942 \u0915\u0940, \u091c\u094b \u090f\u0915 \u091a\u0930\u0923 3 \u092f\u093e\u0926\u0943\u091a\u094d\u091b\u093f\u0915, \u0921\u092c\u0932-\u092c\u094d\u0932\u093e\u0907\u0902\u0921, \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0939\u0948 \u091c\u094b SGT-003 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0924\u093e \u0939\u0948\u0964 \u0907\u092e\u094d\u092a\u0948\u0915\u094d\u091f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u093e \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0938\u0902\u092f\u0941\u0915\u094d\u0924 \u0930\u093e\u091c\u094d\u092f \u0905\u092e\u0947\u0930\u093f\u0915\u093e (\u092f\u0942\u090f\u0938) \u0915\u0947 \u092c\u093e\u0939\u0930 \u092c\u093e\u0932 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u092a\u0930 \u0915\u093f\u092f\u093e \u091c\u093e\u090f\u0917\u093e \u0914\u0930 \u0907\u0938\u0947 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u092a\u0942\u0930\u094d\u0935-\u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u094d\u0930\u093e\u0927\u093f\u0915\u0930\u0923\u094b\u0902 \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e\u0964 \u0939\u092e\u0947\u0902 \u0915\u0928\u093e\u0921\u093e \u0914\u0930 \u0911\u0938\u094d\u091f\u094d\u0930\u0947\u0932\u093f\u092f\u093e \u0926\u094b\u0928\u094b\u0902 \u092e\u0947\u0902 \u0907\u092e\u094d\u092a\u0948\u0915\u094d\u091f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0938\u0902\u091a\u093e\u0932\u0928 \u0915\u0947 \u0932\u093f\u090f \u0928\u093f\u092f\u093e\u092e\u0915 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b \u0917\u090f \u0939\u0948\u0902, \u0914\u0930 \u0939\u092e \u0928\u093f\u092f\u093e\u092e\u0915 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b\u0928\u0947 \u0915\u0947 \u0905\u0927\u0940\u0928, \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u094b \u0905\u0928\u094d\u092f \u0926\u0947\u0936\u094b\u0902 \u092e\u0947\u0902 \u0935\u093f\u0938\u094d\u0924\u093e\u0930\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0940 \u092f\u094b\u091c\u0928\u093e \u092c\u0928\u093e \u0930\u0939\u0947 \u0939\u0948\u0902\u0964. <a href=\"https:\/\/dmdwarrior.com\/hi\/solid-biosciences-sgt-003-gene-therapy-phase-3-clinical-trial-nct07160634\/\" target=\"_blank\" rel=\"noreferrer noopener\">(IMPACT DUCHENNE)<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0907\u0938 \u092a\u0947\u091c \u0915\u094b \u092b\u093c\u0949\u0932\u094b \u0915\u0930\u0947\u0902<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0938\u092d\u0940 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Solid Biosciences announced positive new interim data from the Phase 1\/2 INSPIRE DUCHENNE clinical trial. The Company also provided an update to the planned timing of its meeting with the U.S. Food and Drug Administration (FDA) to discuss potential registrational pathways, including accelerated approval pathways, for SGT-003. Bo Cumbo, President and CEO of Solid Biosciences [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":5102,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[61,110,170,109],"class_list":["post-5101","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-gene-therapy","tag-sgt-003","tag-sgt-003-gene-therapy","tag-solid-biosciences"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/5101","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=5101"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/5101\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/5102"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=5101"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=5101"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=5101"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}