{"id":4799,"date":"2025-10-14T10:10:06","date_gmt":"2025-10-14T07:10:06","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4799"},"modified":"2025-10-14T10:17:10","modified_gmt":"2025-10-14T07:17:10","slug":"brogidirsen-ns-089-ncnp-02-has-the-potential-to-slow-disease-progression-in-dmd-patients-amenable-to-exon-44-skipping","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/brogidirsen-ns-089-ncnp-02-has-the-potential-to-slow-disease-progression-in-dmd-patients-amenable-to-exon-44-skipping\/","title":{"rendered":"Brogidirsen (NS-089\/NCNP-02) \u092e\u0947\u0902 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0915\u0947 \u0932\u093f\u090f \u0909\u0924\u094d\u0924\u0930\u0926\u093e\u092f\u0940 DMD \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0915\u0930\u0928\u0947 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u0939\u0948"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Nippon Shinyaku \u0928\u0947 \u090f\u0915 \u0913\u092a\u0928-\u0932\u0947\u092c\u0932 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0906\u0927\u093e\u0930 \u092a\u0930 3.5-\u0935\u0930\u094d\u0937\u0940\u092f \u0906\u0935\u0947\u0926\u0928 \u0938\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0914\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0921\u0947\u091f\u093e \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940, \u091c\u093f\u0938\u092e\u0947\u0902 \u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u0938\u0947\u0928 (NS-089\/NCNP-02) \u0915\u0947 \u0932\u093f\u090f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0940 \u0936\u0941\u0930\u0941\u0906\u0924 \u092d\u0940 \u0936\u093e\u092e\u093f\u0932 \u0925\u0940\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0947 \u0906\u0902\u0915\u0921\u093c\u0947 \u0928\u0947\u0936\u0928\u0932 \u0938\u0947\u0902\u091f\u0930 \u0911\u092b \u0928\u094d\u092f\u0942\u0930\u094b\u0932\u0949\u091c\u0940 \u090f\u0902\u0921 \u0938\u093e\u0907\u0915\u093f\u092f\u093e\u091f\u094d\u0930\u0940 (\u090f\u0928\u0938\u0940\u090f\u0928\u092a\u0940, \u0915\u094b\u0921\u0948\u0930\u093e \u0938\u093f\u091f\u0940, \u091f\u094b\u0915\u094d\u092f\u094b; \u0905\u0927\u094d\u092f\u0915\u094d\u0937, \u0915\u093e\u091c\u0941\u092f\u0941\u0915\u0940 \u0928\u093e\u0915\u093e\u0917\u094b\u092e) \u0926\u094d\u0935\u093e\u0930\u093e 7 \u0938\u0947 11 \u0905\u0915\u094d\u091f\u0942\u092c\u0930, 2025 \u0924\u0915 \u0911\u0938\u094d\u091f\u094d\u0930\u093f\u092f\u093e \u092e\u0947\u0902 \u0906\u092f\u094b\u091c\u093f\u0924 \u0935\u0930\u094d\u0932\u094d\u0921 \u092e\u0938\u0932 \u0938\u094b\u0938\u093e\u0907\u091f\u0940 \u0915\u0940 30\u0935\u0940\u0902 \u0935\u093e\u0930\u094d\u0937\u093f\u0915 \u0905\u0902\u0924\u0930\u094d\u0930\u093e\u0937\u094d\u091f\u094d\u0930\u0940\u092f \u0915\u093e\u0902\u0917\u094d\u0930\u0947\u0938 \u092e\u0947\u0902 \u090f\u0915 \u092a\u094b\u0938\u094d\u091f\u0930 \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u093f\u090f \u0917\u090f \u0925\u0947\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u094d\u0938\u0947\u0928 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Brogidirsen \u090f\u0915 \u090f\u0902\u091f\u0940\u0938\u0947\u0928\u094d\u0938 \u0911\u0932\u093f\u0917\u094b\u0928\u094d\u092f\u0941\u0915\u094d\u0932\u093f\u092f\u094b\u091f\u093e\u0907\u0921 \u0939\u0948, \u091c\u093f\u0938\u0915\u0940 \u0916\u094b\u091c Nippon Shinyaku \u0914\u0930 NCNP \u0926\u094d\u0935\u093e\u0930\u093e \u0938\u0902\u092f\u0941\u0915\u094d\u0924 \u0930\u0942\u092a \u0938\u0947 \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964 \u092f\u0939 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0935\u093e\u0932\u0947 DMD \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915 \u091c\u093e\u0902\u091a\u093e\u0924\u094d\u092e\u0915 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0915\u0947 \u0930\u0942\u092a \u092e\u0947\u0902 \u0939\u0948, \u091c\u094b \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0915\u0947 \u0932\u093f\u090f \u0905\u0928\u0941\u0915\u0942\u0932 \u0939\u0948\u0902\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0906\u0901\u0915\u0921\u093c\u0947 \u090f\u0928\u0938\u0940\u090f\u0928\u092a\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u0915\u093f\u090f \u0917\u090f \u0905\u0928\u094d\u0935\u0947\u0937\u0915-\u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0914\u0930 1\u091f\u0940\u092a\u094045\u091f\u0940 \u0926\u094d\u0935\u093e\u0930\u093e \u0915\u093f\u090f \u0917\u090f \u0907\u0938\u0915\u0947 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0930 \u0906\u0927\u093e\u0930\u093f\u0924 \u0939\u0948\u0902\u0964 \u0907\u0928 \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u0928\u0947 \u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u0938\u0947\u0928 \u0915\u093e \u0938\u093e\u092a\u094d\u0924\u093e\u0939\u093f\u0915 \u0905\u0902\u0924\u0903\u0936\u093f\u0930\u093e \u092a\u094d\u0930\u0936\u093e\u0938\u0928 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 6 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0914\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u092a\u0922\u093c\u0947\u0902<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/hi\/upcoming-exon-44-skipping-therapies-for-dmd\/\">\u0906\u0917\u093e\u092e\u0940 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u0930\u093f\u0923\u093e\u092e<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0928\u0947 25\/26\u0935\u0947\u0902 \u0938\u092a\u094d\u0924\u093e\u0939 \u0914\u0930 99\/100\u0935\u0947\u0902 \u0938\u092a\u094d\u0924\u093e\u0939 \u092e\u0947\u0902 \u092c\u093e\u092f\u094b\u092a\u094d\u0938\u0940 \u0915\u0940 \u0917\u0908 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0909\u091a\u094d\u091a \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0926\u0915\u094d\u0937\u0924\u093e \u0914\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0938\u094d\u0924\u0930 \u0915\u0947 \u0930\u0941\u091d\u093e\u0928 \u0926\u093f\u0916\u093e\u090f\u0964 \u0907\u0938\u0915\u0947 \u0905\u0932\u093e\u0935\u093e, \u0932\u0902\u092c\u0947 \u0938\u092e\u092f \u0924\u0915 \u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u0938\u0947\u0928 \u0932\u0947\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u092d\u0940 \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0930\u0939\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0928\u0947 \u0928\u0949\u0930\u094d\u0925 \u0938\u094d\u091f\u093e\u0930 \u090f\u092e\u094d\u092c\u0941\u0932\u0947\u091f\u0930\u0940 \u0905\u0938\u0947\u0938\u092e\u0947\u0902\u091f \u0938\u0939\u093f\u0924 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u092e\u0947\u0902 \u0905\u092a\u0928\u0940 \u092e\u094b\u091f\u0930 \u0915\u093e\u0930\u094d\u092f \u0915\u094d\u0937\u092e\u0924\u093e \u092c\u0928\u093e\u090f \u0930\u0916\u0940\u0964 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u092e\u0947\u0902 \u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u0938\u0947\u0928 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0915\u094b\u0908 \u0917\u0902\u092d\u0940\u0930 \u092f\u093e \u0917\u0902\u092d\u0940\u0930 \u092a\u094d\u0930\u0924\u093f\u0915\u0942\u0932 \u0918\u091f\u0928\u093e, \u092f\u093e \u090f\u0928\u093e\u092b\u093f\u0932\u0947\u0915\u094d\u0938\u093f\u0938 \u091c\u0948\u0938\u0940 \u0907\u0928\u094d\u092b\u094d\u092f\u0942\u091c\u0928-\u0938\u0902\u092c\u0902\u0927\u0940 \u092a\u094d\u0930\u0924\u093f\u0915\u094d\u0930\u093f\u092f\u093e\u0913\u0902 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0915\u094b\u0908 \u092a\u094d\u0930\u0924\u093f\u0915\u0942\u0932 \u0918\u091f\u0928\u093e, \u092f\u093e \u092a\u094d\u0930\u0924\u093f\u0915\u0942\u0932 \u0918\u091f\u0928\u093e\u0913\u0902 \u0915\u0947 \u0915\u093e\u0930\u0923 \u0926\u0935\u093e \u092c\u0902\u0926 \u0915\u0930\u0928\u0947 \u0915\u0940 \u0915\u094b\u0908 \u0918\u091f\u0928\u093e \u0928\u0939\u0940\u0902 \u0926\u0947\u0916\u0940 \u0917\u0908\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u0924\u093e \u0939\u0948 \u0915\u093f \u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u0938\u0947\u0928 \u092e\u0947\u0902 \u0921\u0940\u090f\u092e\u0921\u0940 \u0915\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0915\u0930\u0928\u0947 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u0939\u0948, \u091c\u094b \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0915\u094b \u091b\u094b\u0921\u093c\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0909\u0924\u094d\u0924\u0930\u0926\u093e\u092f\u0940 \u0939\u0948\u0902\u0964<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092f\u0939 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0935\u093f\u0938\u094d\u0924\u093e\u0930 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u092a\u094d\u0930\u0936\u093e\u0938\u0928 \u0915\u0940 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u0914\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u0940 \u091c\u093e\u0901\u091a \u0915\u0947 \u0932\u093f\u090f \u091c\u093e\u0930\u0940 \u0939\u0948\u0964 \u0907\u0938\u0915\u0947 \u0905\u0932\u093e\u0935\u093e, Nippon Shinyaku \u0914\u0930 \u0909\u0938\u0915\u0940 \u0938\u0939\u093e\u092f\u0915 \u0915\u0902\u092a\u0928\u0940 NS Pharma, Inc. \u0926\u094d\u0935\u093e\u0930\u093e \u092c\u094d\u0930\u094b\u0917\u093f\u0921\u093f\u0930\u0938\u0947\u0928 \u0915\u093e \u090f\u0915 \u0935\u0948\u0936\u094d\u0935\u093f\u0915 \u091a\u0930\u0923 II \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/hi\/mutations-and-deletions-amenable-to-exon-44-skipping-therapies-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0914\u0930 \u0935\u093f\u0932\u094b\u092a\u0928<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Nippon Shinyaku announced efficacy and safety data from a 3.5-year application based on an open-label extension study that also included the initiation of a clinical trial for brogidirsen (NS-089\/NCNP-02). These data were presented as a poster by the National Center of Neurology and Psychiatry (NCNP, Kodaira City, Tokyo; President, Kazuyuki Nakagome) at the 30th annual [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4800,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[138,141,127,246,136,140],"class_list":["post-4799","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-brogidirsen","tag-exon-44","tag-exon-44-skipping","tag-exon-44-skipping-therapies","tag-nippon-shinyaku","tag-ns-089-ncnp-02"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4799","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=4799"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4799\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/4800"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=4799"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=4799"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=4799"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}