{"id":4500,"date":"2025-09-18T14:58:30","date_gmt":"2025-09-18T11:58:30","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4500"},"modified":"2025-09-18T14:58:31","modified_gmt":"2025-09-18T11:58:31","slug":"del-zota-dmd-rna-therapy-from-avidity-biosciences-reverses-the-progression-of-disease","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/del-zota-dmd-rna-therapy-from-avidity-biosciences-reverses-the-progression-of-disease\/","title":{"rendered":"Avidity Biosciences \u0938\u0947 Del-Zota DMD RNA \u0925\u0947\u0930\u0947\u092a\u0940 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0909\u0932\u091f \u0926\u0947\u0924\u0940 \u0939\u0948"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Sarepta Therapeutics \u0938\u0947 \u0935\u093f\u0915\u0938\u093f\u0924 DMD \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940, Elevidys \u0915\u0947 \u0907\u0938\u094d\u0924\u0947\u092e\u093e\u0932 \u0915\u0947 \u092c\u093e\u0926 \u0926\u094b \u092e\u0930\u0940\u091c\u093c\u094b\u0902 \u0915\u0940 \u092e\u094c\u0924 \u0915\u0947 \u0915\u093e\u0930\u0923, DMD \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u092f\u0939 \u0938\u093e\u0932 \u092e\u0941\u0936\u094d\u0915\u093f\u0932\u094b\u0902 \u092d\u0930\u093e \u0930\u0939\u093e\u0964 \u092a\u0930\u093f\u0935\u093e\u0930, \u0915\u093e\u0930\u094d\u092f\u0915\u0930\u094d\u0924\u093e \u0914\u0930 \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e, \u0938\u092d\u0940 \u0907\u0938 \u0915\u094d\u0937\u0924\u093f \u0938\u0947 \u0938\u094d\u0924\u092c\u094d\u0927 \u0925\u0947, \u091c\u093f\u0938\u0928\u0947 \u092a\u094d\u0930\u093e\u092f\u094b\u0917\u093f\u0915 \u0906\u0928\u0941\u0935\u0902\u0936\u093f\u0915 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0915\u0947 \u0916\u0924\u0930\u094b\u0902 \u0914\u0930 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0932\u093e\u092d\u094b\u0902 \u0915\u0940 \u090f\u0915 \u0917\u0902\u092d\u0940\u0930 \u092f\u093e\u0926 \u0926\u093f\u0932\u093e \u0926\u0940\u0964 <strong>\u0932\u0947\u0915\u093f\u0928 \u0907\u0938 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0936\u0941\u0930\u0941\u0906\u0924 \u092e\u0947\u0902, \u0909\u0926\u093e\u0938\u0940 \u0914\u0930 \u0905\u0928\u093f\u0936\u094d\u091a\u093f\u0924\u0924\u093e \u0915\u0947 \u092c\u0940\u091a \u0906\u0936\u093e \u0915\u0940 \u090f\u0915 \u0915\u093f\u0930\u0923 \u0926\u093f\u0916\u093e\u0908 \u0926\u0940: Del-Zota, \u091c\u094b Avidity Biosciences \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u090f\u0915 \u0906\u0930\u090f\u0928\u090f \u0925\u0947\u0930\u0947\u092a\u0940 \u0939\u0948\u0964<\/strong> \u090f\u0935\u093f\u0921\u093f\u091f\u0940 \u0928\u0947 \u0935\u0938\u0902\u0924 \u090b\u0924\u0941 \u092e\u0947\u0902 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u092f\u093e\u0902\u0924\u094d\u0930\u093f\u0915 \u0938\u092b\u0932\u0924\u093e \u0915\u0940 \u0938\u0942\u091a\u0928\u093e \u0926\u0940, \u091c\u093f\u0938\u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u092e\u0947\u0902 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0915\u094b \u092c\u093e\u092f\u092a\u093e\u0938 \u0915\u0930\u0915\u0947, \u0932\u0915\u094d\u0937\u0923\u0939\u0940\u0928 \u0930\u094b\u0917 \u0938\u0947 \u091c\u0941\u0921\u093c\u0947 \u0938\u094d\u0924\u0930\u094b\u0902 \u092a\u0930 \u0932\u0917\u092d\u0917 \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u094b\u091f\u0940\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u092c\u0939\u093e\u0932 \u0915\u093f\u092f\u093e \u0917\u092f\u093e\u0964 \u0909\u0938 \u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0915\u094d\u0937\u094d\u092f\u094b\u0902 \u0938\u0947 \u092a\u0924\u093e \u091a\u0932\u093e \u0915\u093f \u0907\u0938 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0906\u0923\u0935\u093f\u0915 \u092a\u094d\u0930\u092d\u093e\u0935 \u0939\u094b \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964 \u090f\u0935\u093f\u0921\u093f\u091f\u0940 \u0915\u0947 EXPLORE44 \u0936\u094b\u0927 \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0928\u0935\u0940\u0928\u0924\u092e \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0930\u0940\u0921\u0906\u0909\u091f\u094d\u0938 \u0915\u0947 \u0905\u0928\u0941\u0938\u093e\u0930, del-zota \u0928 \u0915\u0947\u0935\u0932 DMD \u0915\u0947 \u0928\u093f\u0930\u0902\u0924\u0930 \u092c\u0922\u093c\u0928\u0947 \u092e\u0947\u0902 \u0926\u0947\u0930\u0940 \u0915\u0930\u0924\u093e \u0939\u0948; \u092c\u0932\u094d\u0915\u093f \u0907\u0938\u0947 \u0909\u0932\u091f \u092d\u0940 \u0926\u0947\u0924\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#what-is-del-zota\">\u0921\u0947\u0932-\u091c\u093c\u094b\u091f\u093e \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#reverses-the-progression-of-disease\">\u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0909\u0932\u091f \u0926\u0947\u0924\u093e \u0939\u0948<\/a><\/li><li><a href=\"#full-length-dystrophin-is-not-a-dream\">\u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0940 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u094b\u0908 \u0938\u092a\u0928\u093e \u0928\u0939\u0940\u0902 \u0939\u0948<\/a><\/li><li><a href=\"#growing-and-building-muscle\">\u0932\u0921\u093c\u0915\u094b\u0902 \u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u093e \u0935\u093f\u0915\u093e\u0938 \u0914\u0930 \u0928\u093f\u0930\u094d\u092e\u093e\u0923<\/a><\/li><li><a href=\"#a-patient-or-family-friendly-dosing-regimen\">\u0930\u094b\u0917\u0940 \u092f\u093e \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0916\u0941\u0930\u093e\u0915 \u0935\u094d\u092f\u0935\u0938\u094d\u0925\u093e<\/a><\/li><li><a href=\"#biologics-license-application-bla\">\u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0906\u0935\u0947\u0926\u0928 (\u092c\u0940\u090f\u0932\u090f)<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-del-zota\">\u0921\u0947\u0932-\u091c\u093c\u094b\u091f\u093e \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0921\u0947\u0932-\u091c\u093c\u094b\u091f\u093e \u0915\u094b \u092b\u0949\u0938\u094d\u092b\u094b\u0930\u094b\u0921\u093e\u092f\u092e\u093f\u0921\u0947\u091f \u092e\u0949\u0930\u094d\u092b\u094b\u0932\u093f\u0928\u094b \u0911\u0932\u093f\u0917\u094b\u092e\u0930\u094d\u0938 (\u092a\u0940\u090f\u092e\u0913) \u0915\u094b \u0915\u0902\u0915\u093e\u0932 \u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0914\u0930 \u0939\u0943\u0926\u092f \u0915\u0947 \u090a\u0924\u0915\u094b\u0902 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0921\u093f\u091c\u093c\u093e\u0907\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948, \u0924\u093e\u0915\u093f \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u091c\u0940\u0928 \u0915\u0947 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0915\u094b \u091b\u094b\u0921\u093c \u0926\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0947, \u091c\u093f\u0938\u0938\u0947 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 (\u0921\u0940\u090f\u092e\u0921\u094044) \u0915\u0947 \u0932\u093f\u090f \u0905\u0928\u0941\u0915\u0942\u0932 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u0947 \u0938\u093e\u0925 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u092e\u0947\u0902 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u094b \u0938\u0915\u094d\u0937\u092e \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0947\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/hi\/mutations-and-deletions-amenable-to-exon-44-skipping-therapies-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0914\u0930 \u0935\u093f\u0932\u094b\u092a\u0928<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"reverses-the-progression-of-disease\">\u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0909\u0932\u091f \u0926\u0947\u0924\u093e \u0939\u0948<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0935\u093f\u0921\u093f\u091f\u0940 \u0915\u0947 \u092e\u0941\u0916\u094d\u092f \u0935\u0948\u091c\u094d\u091e\u093e\u0928\u093f\u0915 \u0905\u0927\u093f\u0915\u093e\u0930\u0940 \u0921\u092c\u094d\u0932\u094d\u092f\u0942. \u092e\u093e\u0907\u0915\u0932 \u092b\u094d\u0932\u0948\u0928\u0917\u0928, \u092a\u0940\u090f\u091a\u0921\u0940 \u0928\u0947 \u0915\u0939\u093e, &#039;\u0939\u092e\u0928\u0947 \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u092c\u0940\u092e\u093e\u0930\u0940 \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0926\u0947\u0916\u093e \u0939\u0948\u0964&#039;<strong>\u092f\u0939 \u0938\u093f\u0930\u094d\u092b\u093c \u092c\u0940\u092e\u093e\u0930\u0940 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0927\u0940\u092e\u093e \u0928\u0939\u0940\u0902 \u0915\u0930 \u0930\u0939\u093e \u0939\u0948\u0964 \u092f\u0939 \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u092c\u0940\u092e\u093e\u0930\u0940 \u0915\u094b \u0909\u0932\u091f \u0930\u0939\u093e \u0939\u0948\u0964 \u0914\u0930 \u0910\u0938\u093e \u092a\u0939\u0932\u0940 \u092c\u093e\u0930 \u0939\u0941\u0906 \u0939\u0948\u0964<\/strong>\u2018&#039;\u2018<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092b\u0949\u0938\u094d\u092b\u094b\u0928\u094b\u0921\u093e\u092f\u092e\u093f\u0921\u093e\u0907\u091f \u092e\u0949\u0930\u094d\u092b\u094b\u0932\u093f\u0928\u094b \u0913\u0932\u093f\u0917\u094b\u092e\u0930 (PMO), \u090f\u0915 \u0910\u0938\u093e \u0930\u0938\u093e\u092f\u0928 \u091c\u094b \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u092e\u0947\u0902 \u092a\u094d\u0930\u092d\u093e\u0935\u0940 \u0938\u093e\u092c\u093f\u0924 \u0939\u0941\u0906 \u0939\u0948, \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u090f\u0935\u093f\u0921\u093f\u091f\u0940 \u0915\u093e \u092a\u0938\u0902\u0926\u0940\u0926\u093e RNA \u092a\u0947\u0932\u094b\u0921 \u0939\u0948\u0964 PMO, \u090f\u0915\u094d\u0938\u0949\u0928 44-\u0905\u0928\u0941\u0915\u0942\u0932 DMD \u092e\u0947\u0902 \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u090f\u0915\u094d\u0938\u0949\u0928 \u0915\u094b \u092c\u093e\u092f\u092a\u093e\u0938 \u0915\u0930\u0924\u093e \u0939\u0948, \u0930\u0940\u0921\u093f\u0902\u0917 \u092b\u094d\u0930\u0947\u092e \u0915\u094b \u092a\u0941\u0928\u0930\u094d\u0938\u094d\u0925\u093e\u092a\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948, \u0914\u0930 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u093e \u0909\u0924\u094d\u092a\u093e\u0926\u0928 \u0915\u0930\u0924\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"full-length-dystrophin-is-not-a-dream\">\u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u0940 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u094b\u0908 \u0938\u092a\u0928\u093e \u0928\u0939\u0940\u0902 \u0939\u0948<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">&quot;\u092f\u0939 \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902 \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u090f\u0915\u094d\u0938\u0949\u0928 \u0938\u0947 \u091b\u0941\u091f\u0915\u093e\u0930\u093e \u092a\u093e\u0928\u0947 \u0914\u0930 \u0909\u091a\u094d\u091a \u0917\u0941\u0923\u0935\u0924\u094d\u0924\u093e \u0935\u093e\u0932\u093e, \u0932\u0917\u092d\u0917 \u092a\u0942\u0930\u094d\u0923 \u0932\u0902\u092c\u093e\u0908 \u0935\u093e\u0932\u093e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0928\u0947 \u0915\u093e \u090f\u0915 \u0924\u0930\u0940\u0915\u093e \u0939\u0948, \u0914\u0930 \u0939\u092e\u093e\u0930\u0940 \u0924\u0915\u0928\u0940\u0915 \u092f\u0939\u0940 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u0948,&quot; \u092b\u094d\u0932\u0948\u0928\u0917\u0928 \u0928\u0947 \u0915\u0939\u093e\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0915\u094d\u0938\u0949\u0928 44 \u092e\u0947\u0902 \u0909\u0924\u094d\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0935\u093e\u0932\u0947 26 \u0932\u0921\u093c\u0915\u094b\u0902 \u0914\u0930 \u092f\u0941\u0935\u093e \u092a\u0941\u0930\u0941\u0937\u094b\u0902 \u0915\u094b \u091a\u0930\u0923 I\/II EXPLORE44 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u0915\u0947 \u0932\u093f\u090f \u092d\u0930\u094d\u0924\u0940 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e, \u091c\u094b \u092f\u093e\u0926\u0943\u091a\u094d\u091b\u093f\u0915, \u092a\u094d\u0932\u0947\u0938\u0940\u092c\u094b-\u0928\u093f\u092f\u0902\u0924\u094d\u0930\u093f\u0924 \u0914\u0930 \u0921\u092c\u0932-\u092c\u094d\u0932\u093e\u0907\u0902\u0921 \u0925\u093e\u0964 <strong>\u092a\u094d\u0930\u0925\u092e \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u0909\u0924\u094d\u0938\u093e\u0939\u0935\u0930\u094d\u0927\u0915 \u0925\u0947: \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0915\u094b \u091b\u094b\u0921\u093c\u0928\u0947 \u0938\u0947 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c (\u0938\u0940.\u0915\u0947.) \u092e\u0947\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0915\u092e\u0940 \u0906\u0908, \u091c\u094b \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u091a\u094b\u091f \u0915\u093e \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930 \u0939\u0948, \u0924\u0925\u093e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u0915\u0940 \u092e\u091c\u092c\u0942\u0924 \u092e\u0930\u092e\u094d\u092e\u0924 \u0939\u0941\u0908\u0964<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902<\/strong>: <a href=\"https:\/\/dmdwarrior.com\/hi\/avidity-biosciences-del-zota-increase-dystrophin-phase-1-2-clinical-trial\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u0947\u0932-\u091c\u093c\u094b\u091f\u093e (\u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940) \u0928\u0947 \u091a\u0930\u0923 1\/2 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u092a\u094d\u0930\u092e\u0941\u0916 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0905\u0902\u0924 \u092c\u093f\u0902\u0926\u0941\u0913\u0902 \u092a\u0930 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0909\u0932\u091f\u0928\u0947 \u0915\u093e \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 \u0915\u093f\u092f\u093e<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">&quot;\u091c\u093f\u0928 \u092e\u093e\u092e\u0932\u094b\u0902 \u092e\u0947\u0902 \u090f\u0915 \u0915\u094d\u0937\u0924\u093f\u0917\u094d\u0930\u0938\u094d\u0924 \u090f\u0932\u0940\u0932 \u0939\u094b\u0924\u093e \u0939\u0948, \u0909\u0928\u092e\u0947\u0902 \u0932\u0917\u092d\u0917 50% \u0909\u0924\u094d\u092a\u0928\u094d\u0928 \u0939\u094b\u0928\u0947 \u0915\u0940 \u0938\u0902\u092d\u093e\u0935\u0928\u093e \u0939\u094b\u0924\u0940 \u0939\u0948 \u0914\u0930 \u0935\u0947 \u0932\u0915\u094d\u0937\u0923\u0939\u0940\u0928 \u0930\u0939\u0924\u0947 \u0939\u0948\u0902,&quot; \u092b\u093c\u094d\u0932\u0948\u0928\u093e\u0917\u0928 \u0928\u0947 \u0915\u0939\u093e\u0964 &quot;\u0939\u092e \u0910\u0938\u0947 \u0938\u094d\u0924\u0930\u094b\u0902 \u0924\u0915 \u092a\u0939\u0941\u0901\u091a \u0930\u0939\u0947 \u0939\u0948\u0902 \u091c\u094b \u0938\u093e\u092e\u093e\u0928\u094d\u092f \u0938\u094d\u0924\u0930 \u0915\u0947 \u0915\u0930\u0940\u092c \u0939\u0948\u0902 \u092f\u093e \u0915\u092e \u0938\u0947 \u0915\u092e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928 \u0915\u0947 \u0932\u0915\u094d\u0937\u0923\u0939\u0940\u0928 \u0938\u094d\u0924\u0930 \u092a\u0930 \u0939\u0948\u0902\u0964 \u092f\u0947 \u092a\u0930\u093f\u0923\u093e\u092e \u0926\u0930\u094d\u0936\u093e\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u0938\u0940\u0915\u0947 \u0928\u093e\u091f\u0915\u0940\u092f \u0930\u0942\u092a \u0938\u0947 \u0932\u0917\u092d\u0917 \u0938\u093e\u092e\u093e\u0928\u094d\u092f \u0938\u094d\u0924\u0930 \u0924\u0915 \u0917\u093f\u0930 \u091c\u093e\u0924\u093e \u0939\u0948\u0964 \u092e\u0941\u091d\u0947 \u0928\u0939\u0940\u0902 \u0932\u0917\u0924\u093e \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0947\u0902 \u0915\u093f\u0938\u0940 \u0905\u0928\u094d\u092f \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0928\u0947 \u0938\u0940\u0915\u0947 \u0915\u0947 \u0938\u094d\u0924\u0930 \u0915\u093e \u0932\u0917\u092d\u0917 \u0938\u093e\u092e\u093e\u0928\u094d\u092f\u0940\u0915\u0930\u0923 \u0915\u092d\u0940 \u0926\u093f\u0916\u093e\u092f\u093e \u0939\u0948\u0964 \u0914\u0930 \u0939\u092e \u0926\u0947\u0916\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f del-zota \u0938\u0947 \u0909\u092a\u091a\u093e\u0930\u093f\u0924 \u0932\u0917\u092d\u0917 50% \u0932\u094b\u0917 \u0938\u093e\u092e\u093e\u0928\u094d\u092f \u0936\u094d\u0930\u0947\u0923\u0940 \u092e\u0947\u0902 \u0939\u0948\u0902\u0964 \u092c\u093e\u0915\u0940 \u0938\u092d\u0940 \u0938\u093e\u092e\u093e\u0928\u094d\u092f \u0936\u094d\u0930\u0947\u0923\u0940 \u0938\u0947 \u0925\u094b\u0921\u093c\u093e \u090a\u092a\u0930 \u0939\u0948\u0902\u0964&quot; <a href=\"https:\/\/dmdwarrior.com\/hi\/what-is-creatine-kinase-ck\/\" data-type=\"post\" data-id=\"2167\" target=\"_blank\" rel=\"noreferrer noopener\">\u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c \u0915\u094d\u092f\u093e \u0939\u0948?<\/a> \u2013<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"growing-and-building-muscle\">\u0932\u0921\u093c\u0915\u094b\u0902 \u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u093e \u0935\u093f\u0915\u093e\u0938 \u0914\u0930 \u0928\u093f\u0930\u094d\u092e\u093e\u0923<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0932\u0921\u093c\u0915\u094b\u0902 \u092e\u0947\u0902 \u092f\u0947 \u092c\u0926\u0932\u093e\u0935 \u0938\u093e\u092b\u093c \u0926\u093f\u0916\u093e\u0908 \u0926\u0947 \u0930\u0939\u0947 \u0939\u0948\u0902: \u0905\u092c \u0935\u0947 \u0906\u0938\u093e\u0928\u0940 \u0938\u0947 \u0938\u0940\u0922\u093c\u093f\u092f\u093e\u0901 \u091a\u0922\u093c \u0930\u0939\u0947 \u0939\u0948\u0902, \u091c\u093c\u092e\u0940\u0928 \u0938\u0947 \u0924\u0947\u091c\u093c\u0940 \u0938\u0947 \u0916\u0921\u093c\u0947 \u0939\u094b \u0930\u0939\u0947 \u0939\u0948\u0902, \u092f\u093e\u2014\u091c\u094b \u092e\u0930\u0940\u091c\u093c \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0905\u0938\u092e\u0930\u094d\u0925 \u0939\u0948\u0902\u2014\u0916\u093e\u0928\u0947 \u0915\u0940 \u092e\u0947\u091c\u093c \u092a\u0930 \u091c\u093c\u094d\u092f\u093e\u0926\u093e \u0926\u0942\u0930 \u0924\u0915 \u092a\u0939\u0941\u0901\u091a \u0930\u0939\u0947 \u0939\u0948\u0902\u0964 \u092b\u093c\u094d\u0932\u0948\u0928\u093e\u0917\u0928 \u0928\u0947 \u0915\u0939\u093e, &quot;\u0939\u092e\u0928\u0947 \u091c\u094b \u0926\u0947\u0916\u093e \u0939\u0948 \u0935\u0939 \u0905\u092d\u0942\u0924\u092a\u0942\u0930\u094d\u0935 \u0939\u0948\u0964 \u0910\u0938\u093e \u0924\u092c \u0939\u094b\u0924\u093e \u0939\u0948 \u091c\u092c \u0906\u092a \u0909\u091a\u094d\u091a-\u0917\u0941\u0923\u0935\u0924\u094d\u0924\u093e \u0935\u093e\u0932\u093e \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928 \u092c\u0928\u093e\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u094b \u0915\u094d\u0937\u0924\u093f \u0938\u0947 \u092c\u091a\u093e\u0924\u0947 \u0939\u0948\u0902\u0964 \u0914\u0930 \u0932\u0921\u093c\u0915\u0947 \u092c\u0922\u093c \u0930\u0939\u0947 \u0939\u0948\u0902 \u0914\u0930 \u0909\u0928\u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u093e\u0901 \u092c\u0928 \u0930\u0939\u0940 \u0939\u0948\u0902, \u0914\u0930 \u0906\u092a \u0915\u0908 \u0905\u0932\u0917-\u0905\u0932\u0917 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0905\u0902\u0924\u092c\u093f\u0902\u0926\u0941\u0913\u0902 \u092a\u0930 \u092c\u0940\u092e\u093e\u0930\u0940 \u0915\u093e \u092f\u0939 \u0909\u0932\u091f\u093e\u0935 \u0926\u0947\u0916\u0947\u0902\u0917\u0947\u0964 \u092f\u0939 \u092c\u0921\u093c\u0940 \u0916\u092c\u0930 \u0939\u0948! \u092f\u0939\u0940 \u0924\u094b \u0932\u094b\u0917\u094b\u0902 \u0915\u0940 \u091a\u093f\u0902\u0924\u093e \u0915\u093e \u0935\u093f\u0937\u092f \u0939\u0948\u0964&quot;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"a-patient-or-family-friendly-dosing-regimen\">\u0930\u094b\u0917\u0940 \u092f\u093e \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0916\u0941\u0930\u093e\u0915 \u0935\u094d\u092f\u0935\u0938\u094d\u0925\u093e<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0921\u0947\u0932-\u091c\u093c\u094b\u091f\u093e \u0915\u0940 \u0916\u0941\u0930\u093e\u0915 \u0939\u0930 \u091b\u0939 \u0938\u092a\u094d\u0924\u093e\u0939 \u092e\u0947\u0902 \u0926\u0940 \u091c\u093e\u0924\u0940 \u0939\u0948, \u091c\u093f\u0938\u0947 \u092b\u093c\u094d\u0932\u0948\u0928\u093e\u0917\u0928 &quot;\u0930\u094b\u0917\u0940 \u092f\u093e \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u0947 \u0905\u0928\u0941\u0915\u0942\u0932 \u0916\u0941\u0930\u093e\u0915 \u0935\u094d\u092f\u0935\u0938\u094d\u0925\u093e&quot; \u0915\u0939\u0924\u0947 \u0939\u0948\u0902, \u091c\u092c\u0915\u093f \u092c\u093e\u091c\u093c\u093e\u0930 \u092e\u0947\u0902 \u0909\u092a\u0932\u092c\u094d\u0927 \u0915\u0941\u091b \u092a\u0940\u090f\u092e\u0913 \u092e\u0947\u0902 \u0938\u093e\u092a\u094d\u0924\u093e\u0939\u093f\u0915 \u0916\u0941\u0930\u093e\u0915 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u094b\u0924\u0940 \u0939\u0948\u0964<\/strong> &quot;\u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u092f\u093e\u0924\u094d\u0930\u093e \u0915\u0930\u0928\u093e \u0914\u0930 \u0910\u0938\u0940 \u0917\u0924\u093f\u0935\u093f\u0927\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0939\u094b\u0928\u093e \u092c\u0947\u0939\u0926 \u092e\u0941\u0936\u094d\u0915\u093f\u0932 \u0939\u0948, \u092f\u093e \u092b\u093f\u0930 \u0918\u0930 \u092a\u0930 \u0939\u0940 \u0926\u0935\u093e \u0926\u0947\u0928\u0940 \u092a\u0921\u093c\u0924\u0940 \u0939\u0948,&quot; \u092b\u093c\u094d\u0932\u0948\u0928\u093e\u0917\u0928 \u0928\u0947 \u0915\u0939\u093e\u0964 &quot;\u092f\u0939 \u0935\u093e\u0915\u0908 \u092a\u0930\u093f\u0935\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u092c\u0947\u0939\u0926 \u092b\u093e\u092f\u0926\u0947\u092e\u0902\u0926 \u0939\u0948\u0964 \u0906\u092a \u091b\u0941\u091f\u094d\u091f\u093f\u092f\u094b\u0902 \u092a\u0930 \u091c\u093e \u0938\u0915\u0924\u0947 \u0939\u0948\u0902\u0964 \u0906\u092a \u0915\u094d\u0930\u0942\u091c\u093c \u092a\u0930 \u091c\u093e \u0938\u0915\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u0939\u0930 \u092c\u093e\u0930 \u0907\u0928 \u0917\u0924\u093f\u0935\u093f\u0927\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0939\u093f\u0938\u094d\u0938\u093e \u0932\u0947 \u0938\u0915\u0924\u0947 \u0939\u0948\u0902, \u0914\u0930 \u0939\u0930 \u091b\u0939 \u0939\u092b\u093c\u094d\u0924\u0947 \u092e\u0947\u0902 \u0926\u0935\u093e \u0926\u0940 \u091c\u093e\u0924\u0940 \u0939\u0948\u0964 \u0939\u092e\u093e\u0930\u093e \u092e\u093e\u0928\u0928\u093e \u0939\u0948 \u0915\u093f \u092f\u0939 \u0928 \u0915\u0947\u0935\u0932 \u092c\u0940\u092e\u093e\u0930\u0940 \u0915\u094b \u0905\u092d\u0942\u0924\u092a\u0942\u0930\u094d\u0935 \u0930\u0942\u092a \u0938\u0947 \u0909\u0932\u091f \u0926\u0947\u0924\u093e \u0939\u0948, \u092c\u0932\u094d\u0915\u093f \u0907\u0938\u092e\u0947\u0902 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0915\u0947 \u092d\u0940 \u0905\u091a\u094d\u091b\u0947 \u092a\u0939\u0932\u0942 \u0939\u0948\u0902 \u0914\u0930 \u092f\u0939 \u092e\u0930\u0940\u091c\u093c\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u092c\u0947\u0939\u0926 \u0938\u0941\u0935\u093f\u0927\u093e\u091c\u0928\u0915 \u0939\u0948\u0964&quot; <strong>\u0914\u0930 \u092a\u0922\u093c\u0947\u0902<\/strong>: <a href=\"https:\/\/filecache.investorroom.com\/mr5ir_aviditybiosciences\/270\/Sep_10_2025_Del-zota_Fxnl_Data_Webcast_FINAL_09-09-25.pdf\" target=\"_blank\" rel=\"noopener\">\u0921\u0947\u0932-\u091c\u093c\u094b\u091f\u093e EXPLORE44-OLE \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0921\u0947\u091f\u093e<\/a> \u2013<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"biologics-license-application-bla\">\u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0906\u0935\u0947\u0926\u0928 (\u092c\u0940\u090f\u0932\u090f)<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u090f\u0935\u093f\u0921\u093f\u091f\u0940 \u0915\u094b \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948 \u0915\u093f \u0935\u0939 \u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0915\u0947 \u0924\u0939\u0924 \u0938\u093e\u0932 \u0915\u0947 \u0905\u0902\u0924 \u0924\u0915 \u0905\u092a\u0928\u093e \u092a\u0939\u0932\u093e \u092c\u093e\u092f\u094b\u0932\u0949\u091c\u093f\u0915\u094d\u0938 \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0906\u0935\u0947\u0926\u0928 (\u092c\u0940\u090f\u0932\u090f) \u091c\u092e\u093e \u0915\u0930 \u0926\u0947\u0917\u0940\u0964 \u092b\u093c\u094d\u0932\u0948\u0928\u093e\u0917\u0928 \u0928\u0947 \u0915\u0939\u093e, &quot;\u0939\u092e \u0905\u092d\u0940 \u0907\u0938 \u092a\u0930 \u0915\u0921\u093c\u0940 \u092e\u0947\u0939\u0928\u0924 \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902 \u0914\u0930 \u0907\u0938\u092e\u0947\u0902 \u0932\u0947\u0916\u0928 \u0914\u0930 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0905\u0928\u0941\u092d\u093e\u0917 \u0936\u093e\u092e\u093f\u0932 \u0939\u0948\u0902\u0964&quot; &quot;\u092f\u0939 \u090f\u0915 \u0924\u094d\u0935\u0930\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0939\u094b\u0917\u093e\u0964 \u0907\u0938\u0932\u093f\u090f \u0939\u092e\u093e\u0930\u0947 \u092a\u093e\u0938 \u0938\u092d\u0940 \u0906\u0935\u0936\u094d\u092f\u0915 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928 \u092e\u094c\u091c\u0942\u0926 \u0939\u0948\u0902\u0964 \u0935\u093e\u0938\u094d\u0924\u0935 \u092e\u0947\u0902, \u0939\u092e\u0928\u0947 \u092a\u093f\u091b\u0932\u0947 \u0938\u093e\u0932 \u0915\u0947 \u0905\u0902\u0924 \u092e\u0947\u0902 \u0905\u092a\u0928\u093e \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0921\u0947\u091f\u093e\u092c\u0947\u0938 \u0924\u0948\u092f\u093e\u0930 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092e\u0930\u0940\u091c\u093c\u094b\u0902 \u0915\u094b \u091c\u094b\u0921\u093c\u093e \u0925\u093e, \u0932\u0947\u0915\u093f\u0928 \u0939\u092e\u0947\u0902 \u092c\u093e\u092f\u094b\u092a\u094d\u0938\u0940 \u0915\u0947 \u0932\u093f\u090f \u0915\u093f\u0938\u0940 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u092e\u0930\u0940\u091c\u093c \u0915\u0940 \u091c\u093c\u0930\u0942\u0930\u0924 \u0928\u0939\u0940\u0902 \u092a\u0921\u093c\u0940\u0964 \u0907\u0938\u0932\u093f\u090f \u092f\u0939 \u092e\u0930\u0940\u091c\u093c\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u092c\u0939\u0941\u0924 \u0939\u0940 \u0905\u0928\u0941\u0915\u0942\u0932 \u0925\u093e \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0939\u092e\u093e\u0930\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928 \u092e\u0947\u0902 \u0907\u0924\u0928\u093e \u0905\u0902\u0924\u0930 \u0925\u093e \u0915\u093f \u090f\u091c\u0947\u0902\u0938\u0940 \u0915\u094b \u092f\u0915\u0940\u0928 \u0939\u094b \u0917\u092f\u093e \u0915\u093f \u0939\u092e\u093e\u0930\u0947 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093c\u093f\u0928 \u0915\u093e \u0938\u094d\u0924\u0930 \u0905\u092d\u0942\u0924\u092a\u0942\u0930\u094d\u0935 \u0925\u093e\u0964&quot; \u0938\u092b\u0932\u0924\u093e \u0915\u0940 \u0917\u093e\u0930\u0902\u091f\u0940 \u092e\u093f\u0932\u0928\u0947 \u0915\u0947 \u0938\u093e\u0925, \u092b\u093c\u094d\u0932\u0948\u0928\u093e\u0917\u0928 \u0915\u094b FDA \u0915\u0940 \u0924\u0947\u091c\u093c \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0914\u0930 2026 \u092f\u093e 2027 \u092e\u0947\u0902 \u0907\u0938\u0915\u0947 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0932\u0949\u0928\u094d\u091a \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u092a\u0922\u093c\u0947\u0902<\/strong>:&nbsp;<a href=\"https:\/\/dmdwarrior.com\/hi\/upcoming-exon-44-skipping-therapies-for-dmd\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u0906\u0917\u093e\u092e\u0940 \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Due to the deaths of two patients following the use of Elevidys, a DMD gene therapy from Sarepta Therapeutics, the DMD community has had a difficult year. Families, activists, and researchers were all shaken by the loss, which served as a sobering reminder of the dangers and potential benefits of experimental genetic therapy. But earlier [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4508,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[282],"tags":[126,298,397,141,127,246,299],"class_list":["post-4500","post","type-post","status-publish","format-standard","has-post-thumbnail","category-editorials","tag-avidity-biosciences","tag-del-zota","tag-delpacibart-zotadirsen","tag-exon-44","tag-exon-44-skipping","tag-exon-44-skipping-therapies","tag-explore44"],"subtitle":"Del-Zota \u090f\u0915\u094d\u0938\u0949\u0928 44 \u0938\u094d\u0915\u093f\u092a\u093f\u0902\u0917 \u0925\u0947\u0930\u0947\u092a\u0940 \u0938\u0947 \u0915\u094d\u0930\u093f\u090f\u091f\u093f\u0928 \u0915\u093e\u0907\u0928\u0947\u091c (CK) \u0914\u0930 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0915\u094d\u0937\u0924\u093f \u092e\u0947\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0915\u092e\u0940 \u0906\u0908, \u091c\u094b \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (DMD) \u0915\u093e \u090f\u0915 \u092c\u093e\u092f\u094b\u092e\u093e\u0930\u094d\u0915\u0930 \u0939\u0948, \u0914\u0930 \u092e\u091c\u092c\u0942\u0924 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u094b\u092b\u093f\u0928 \u092e\u0930\u092e\u094d\u092e\u0924 \u0939\u0941\u0908\u0964","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4500","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=4500"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4500\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/4508"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=4500"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=4500"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=4500"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}