{"id":4142,"date":"2025-07-17T12:11:19","date_gmt":"2025-07-17T09:11:19","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4142"},"modified":"2025-11-03T20:21:36","modified_gmt":"2025-11-03T17:21:36","slug":"insmed-ins1201-gene-therapy-phase-1-clinical-trial-nct06817382","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/insmed-ins1201-gene-therapy-phase-1-clinical-trial-nct06817382\/","title":{"rendered":"INS1201 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0930\u0923 1 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942"},"content":{"rendered":"<p class=\"wp-block-paragraph\">ClinicalTrials.gov \u092a\u0930 \u092a\u094d\u0930\u0915\u093e\u0936\u093f\u0924 \u092a\u0943\u0937\u094d\u0920 \u092a\u0930 I.D. NCT06817382 \u0915\u0947 \u0938\u093e\u0925 Insmed \u0928\u0947 \u0918\u094b\u0937\u0923\u093e \u0915\u0940 \u0915\u093f \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0935\u093f\u0915\u0938\u093f\u0924 INS1201 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u091a\u0930\u0923 1 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0936\u0941\u0930\u0942 \u0915\u093f\u090f \u091c\u093e\u090f\u0902\u0917\u0947\u0964<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">INS1201 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0930\u0923 1 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/li><li><a href=\"#what-is-insmed-ins-1201-gene-therapy\">\u0907\u0928\u0938\u094d\u092e\u0947\u0921 INS1201 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#bbm-d-101-clinical-trial-nct-07058662\">INS1201 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u2013 NCT06817382<\/a><\/li><li><a href=\"#bbm-d-101-phase-1-2-participation-criteria\">INS1201 \u091a\u0930\u0923 1 \u092d\u093e\u0917\u0940\u0926\u093e\u0930\u0940 \u092e\u093e\u0928\u0926\u0902\u0921<\/a><\/li><li><a href=\"#how-can-i-contact-with-belief-bio-med\">\u092e\u0948\u0902 \u0907\u0928\u094d\u0938\u092e\u0947\u0921 \u0938\u0947 \u0915\u0948\u0938\u0947 \u0938\u0902\u092a\u0930\u094d\u0915 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0942\u0901?<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-gene-therapy-phase-1-2-clinical-trial\">INS1201 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u091a\u0930\u0923 1 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u093e \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u0909\u0926\u094d\u0926\u0947\u0936\u094d\u092f \u0921\u0940\u090f\u092e\u0921\u0940 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u091a\u0932-\u092b\u093f\u0930 \u0938\u0915\u0928\u0947 \u0935\u093e\u0932\u0947 \u092a\u0941\u0930\u0941\u0937 \u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0906\u0908\u091f\u0940 \u092a\u094d\u0930\u0936\u093e\u0938\u0928 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 \u0906\u0908\u090f\u0928\u090f\u09381201 \u0915\u0940 \u090f\u0915\u0932 \u0916\u0941\u0930\u093e\u0915 \u0915\u0940 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u0938\u0939\u0928\u0936\u0940\u0932\u0924\u093e \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"what-is-insmed-ins-1201-gene-therapy\">\u0907\u0928\u0938\u094d\u092e\u0947\u0921 INS1201 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">INS1201 \u0938\u0940\u0927\u0947 \u0915\u0947\u0902\u0926\u094d\u0930\u0940\u092f \u0924\u0902\u0924\u094d\u0930\u093f\u0915\u093e \u0924\u0902\u0924\u094d\u0930 \u0915\u094b \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0924\u093e \u0939\u0948 \u0914\u0930 \u0907\u0938\u0947 \u0905\u0902\u0924\u0903\u0936\u093f\u0930\u093e \u0930\u0942\u092a \u0938\u0947 \u092a\u094d\u0930\u0936\u093e\u0938\u093f\u0924 \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u091c\u092c\u0915\u093f Elevidys \u0915\u094b \u092a\u094d\u0930\u0923\u093e\u0932\u0940\u0917\u0924 \u0905\u0902\u0924\u0903\u0936\u093f\u0930\u093e \u0907\u0902\u091c\u0947\u0915\u094d\u0936\u0928 \u0915\u0940 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e \u0939\u094b\u0924\u0940 \u0939\u0948\u0964 \u092a\u094d\u0930\u0923\u093e\u0932\u0940\u0917\u0924 \u091c\u0940\u0928 \u0909\u092a\u091a\u093e\u0930\u094b\u0902 \u0915\u0947 \u0938\u093e\u0925 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u092a\u094d\u0930\u092d\u093e\u0935\u0936\u0940\u0932\u0924\u093e \u0915\u0947 \u092e\u0941\u0926\u094d\u0926\u094b\u0902 \u0915\u094b \u0907\u0938 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924 \u0935\u093f\u0924\u0930\u0923 \u0930\u0923\u0928\u0940\u0924\u093f \u0926\u094d\u0935\u093e\u0930\u093e \u0938\u0902\u092c\u094b\u0927\u093f\u0924 \u0915\u093f\u092f\u093e \u091c\u093e\u0928\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0902\u091f\u094d\u0930\u093e\u0925\u0947\u0915\u0932 \u092a\u094d\u0930\u0936\u093e\u0938\u0928 \u0928\u093e\u091f\u0915\u0940\u092f \u0930\u0942\u092a \u0938\u0947 \u0906\u0935\u0936\u094d\u092f\u0915 \u0916\u0941\u0930\u093e\u0915 \u0915\u094b \u0926\u0938 \u0938\u0947 \u092a\u091a\u093e\u0938 \u0917\u0941\u0928\u093e \u0924\u0915 \u0915\u092e \u0915\u0930 \u0926\u0947\u0924\u093e \u0939\u0948, \u091c\u093f\u0938\u0938\u0947 \u0926\u0935\u093e \u0915\u094b \u091c\u0939\u093e\u0901 \u091c\u093c\u0930\u0942\u0930\u0924 \u0939\u094b\u0924\u0940 \u0939\u0948 \u0935\u0939\u093e\u0901 \u0915\u0947\u0902\u0926\u094d\u0930\u093f\u0924 \u0915\u0930\u0915\u0947 \u092a\u094d\u0930\u0923\u093e\u0932\u0940\u0917\u0924 \u0935\u093f\u0937\u093e\u0915\u094d\u0924\u0924\u093e \u0914\u0930 \u0911\u092b-\u091f\u093e\u0930\u0917\u0947\u091f \u092a\u094d\u0930\u092d\u093e\u0935\u094b\u0902 \u0915\u094b \u0930\u094b\u0915\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0939\u0948\u0964 \u0930\u0940\u0922\u093c \u0915\u0940 \u0939\u0921\u094d\u0921\u0940 \u0915\u0940 \u091a\u094b\u091f, \u0924\u0902\u0924\u094d\u0930\u093f\u0915\u093e \u0915\u094d\u0937\u0924\u093f \u0914\u0930 \u0938\u0902\u0915\u094d\u0930\u092e\u0923 \u0915\u0947 \u091c\u094b\u0916\u093f\u092e \u091c\u0948\u0938\u0940 \u092c\u093e\u0927\u093e\u0913\u0902 \u0915\u0947 \u092c\u093e\u0935\u091c\u0942\u0926, \u092f\u0939 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u090f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0914\u0930 \u0938\u0902\u092d\u0935\u0924\u0903 \u0905\u0927\u093f\u0915 \u0938\u092b\u0932 \u0935\u093f\u0915\u0932\u094d\u092a \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948, \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u0905\u0902\u0924\u0903\u0936\u093f\u0930\u093e \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u092e\u0947\u0902 \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u090f \u091c\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092c\u0921\u093c\u0947 \u0935\u093e\u092f\u0930\u0932 \u0935\u0947\u0915\u094d\u091f\u0930 \u0916\u0941\u0930\u093e\u0915 \u0938\u0947 \u091c\u0941\u0921\u093c\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u0941\u0926\u094d\u0926\u094b\u0902 \u0915\u0947 \u092e\u0926\u094d\u0926\u0947\u0928\u091c\u0930\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-clinical-trial-nct-07058662\">INS1201 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u2013 NCT06817382<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u094d\u0930\u093e\u0930\u0902\u092d (\u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924)<\/strong>: 2025-05-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915 \u092a\u0942\u0930\u094d\u0923\u0924\u093e (\u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924)<\/strong>: 2028-01-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0905\u0927\u094d\u092f\u092f\u0928 \u092a\u0942\u0930\u094d\u0923\u0924\u093e (\u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924)<\/strong>: 2028-03-31<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u092a\u094d\u0930\u0924\u093f\u092d\u093e\u0917\u093f\u092f\u094b\u0902 \u0915\u0940 \u0938\u0902\u0916\u094d\u092f\u093e (\u0905\u0928\u0941\u092e\u093e\u0928\u093f\u0924)<\/strong>: 12 (\u092a\u0941\u0930\u0941\u0937)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0938\u094d\u0925\u093e\u0928\u094b\u0902<\/strong>: \u092f\u0942\u090f\u0938\u090f<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0932\u093f\u090f \u092f\u094b\u0917\u094d\u092f \u0906\u092f\u0941<\/strong>: 2 \u0935\u0930\u094d\u0937 \u0938\u0947 4 \u0935\u0930\u094d\u0937 (\u092c\u091a\u094d\u091a\u093e)<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"bbm-d-101-phase-1-2-participation-criteria\">INS1201 \u091a\u0930\u0923 1 \u092d\u093e\u0917\u0940\u0926\u093e\u0930\u0940 \u092e\u093e\u0928\u0926\u0902\u0921<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u093e\u0924\u094d\u0930 \u0939\u094b\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u0932\u094b\u0917\u094b\u0902 \u0915\u094b \u0938\u092e\u093e\u0935\u0947\u0936\u0928 \u0906\u0935\u0936\u094d\u092f\u0915\u0924\u093e\u0913\u0902 \u0915\u094b \u092a\u0942\u0930\u093e \u0915\u0930\u0928\u093e \u0939\u094b\u0917\u093e\u0964 \u092f\u0926\u093f \u0915\u093f\u0938\u0940 \u0935\u094d\u092f\u0915\u094d\u0924\u093f \u0915\u094b \u0915\u094b\u0908 \u0905\u0928\u094d\u092f \u092c\u0940\u092e\u093e\u0930\u0940 \u0939\u0948 \u092f\u093e \u0935\u0939 \u0910\u0938\u0947 \u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u0917\u0941\u091c\u0930 \u0930\u0939\u093e \u0939\u0948 \u091c\u094b \u0909\u0938\u0947 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0938\u0947 \u0930\u094b\u0915 \u0938\u0915\u0924\u093e \u0939\u0948, \u0924\u094b \u0935\u0939 \u092d\u093e\u0917 \u0932\u0947\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0928\u0939\u0940\u0902 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964 \u0938\u092e\u093e\u0935\u0947\u0936\u0928 \u0914\u0930 \u092c\u0939\u093f\u0937\u094d\u0915\u0930\u0923 \u092e\u093e\u0928\u0926\u0902\u0921\u094b\u0902 \u0915\u093e \u092a\u0942\u0930\u093e \u0938\u0947\u091f \u0907\u0938 \u0905\u0927\u094d\u092f\u092f\u0928 \u0932\u093f\u0902\u0915 \u092a\u0930 \u0915\u094d\u0932\u093f\u0915 \u0915\u0930\u0915\u0947 \u092a\u093e\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0939\u0948 - <a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06817382\" target=\"_blank\" rel=\"noreferrer noopener\">\u090f\u0928\u0938\u0940\u091f\u094006817382<\/a> \u2013.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"how-can-i-contact-with-belief-bio-med\">\u092e\u0948\u0902 \u0907\u0928\u094d\u0938\u092e\u0947\u0921 \u0938\u0947 \u0915\u0948\u0938\u0947 \u0938\u0902\u092a\u0930\u094d\u0915 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0942\u0901?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0928\u093e\u092e<\/strong>: \u0907\u0902\u0938\u094d\u092e\u0947\u0921 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u091c\u093e\u0928\u0915\u093e\u0930\u0940<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u092b\u093c\u094b\u0928 \u0928\u0902\u092c\u0930<\/strong>: 18444467633<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0908\u092e\u0947\u0932<\/strong>: medicalinformation@insmed.com<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u092a\u0922\u093c\u0947\u0902<\/strong>:\u00a0<a href=\"https:\/\/dmdwarrior.com\/hi\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">\u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u0915\u0947 \u0932\u093f\u090f \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 (\u0938\u092d\u0940 \u0936\u094b\u0927\u094b\u0902 \u0915\u0940 \u0938\u0942\u091a\u0940)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Insmed was announced on the page published on ClinicalTrials.gov with the ID NCT06817382 that the phase 1 trials of INS1201 gene therapy developed for Duchenne Muscular Dystrophy will be initiated. INS1201 Gene Therapy Phase 1 Clinical Trial The primary objective of this study is to evaluate the safety and tolerability of a single dose of [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4148,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[137,61,173,174,172],"class_list":["post-4142","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-clinical-trial","tag-gene-therapy","tag-ins1201","tag-ins1201-gene-therapy","tag-insmed"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4142","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=4142"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4142\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/4148"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=4142"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=4142"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=4142"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}