{"id":4065,"date":"2025-07-10T11:42:12","date_gmt":"2025-07-10T08:42:12","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=4065"},"modified":"2025-07-10T11:43:34","modified_gmt":"2025-07-10T08:43:34","slug":"jcr-pharmaceuticals-proprietary-just-aav-capsids-may-be-used-in-the-development-of-duchenne-cures","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/jcr-pharmaceuticals-proprietary-just-aav-capsids-may-be-used-in-the-development-of-duchenne-cures\/","title":{"rendered":"JCR Pharmaceuticals \u0938\u094d\u0935\u093e\u092e\u093f\u0924\u094d\u0935 \u0935\u093e\u0932\u0947 JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0935\u093f\u0915\u093e\u0938 \u092e\u0947\u0902 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0939\u0948"},"content":{"rendered":"<p class=\"wp-block-paragraph\">AstraZeneca \u0915\u0940 \u0926\u0941\u0930\u094d\u0932\u092d \u0930\u094b\u0917 \u0938\u0939\u093e\u092f\u0915 \u0915\u0902\u092a\u0928\u0940 Alexion, \u091c\u093e\u092a\u093e\u0928\u0940 \u092b\u0930\u094d\u092e JCR Pharmaceuticals \u0938\u0947 \u0935\u093f\u0936\u0947\u0937 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0935\u093e\u0939\u0928\u094b\u0902 \u0915\u093e \u0932\u093e\u0907\u0938\u0947\u0902\u0938 \u0932\u0947 \u0930\u0939\u0940 \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>8 \u091c\u0942\u0928 2025 \u0915\u094b \u0918\u094b\u0937\u093f\u0924 \u0907\u0938 \u0938\u094c\u0926\u0947 \u0938\u0947 Alexion \u0915\u094b JCR \u0915\u0947 JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0924\u0915 \u092a\u0939\u0941\u0902\u091a \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0939\u094b\u0917\u0940, \u091c\u093f\u0938\u0915\u093e \u0909\u092a\u092f\u094b\u0917 Alexion \u0915\u0947 \u092a\u093e\u0902\u091a \u091c\u0940\u0928\u094b\u092e\u093f\u0915 \u0914\u0937\u0927\u093f \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e\u094b\u0902 \u092e\u0947\u0902 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0947\u0917\u093e\u0964<\/strong> \u092c\u0926\u0932\u0947 \u092e\u0947\u0902, Alexion, JCR \u0915\u094b \u090f\u0915 \u0905\u091c\u094d\u091e\u093e\u0924 \u0905\u0917\u094d\u0930\u093f\u092e \u0936\u0941\u0932\u094d\u0915 \u0915\u0947 \u0938\u093e\u0925-\u0938\u093e\u0925 \u0905\u0928\u0941\u0938\u0902\u0927\u093e\u0928 \u090f\u0935\u0902 \u0935\u093f\u0915\u093e\u0938 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 225 \u092e\u093f\u0932\u093f\u092f\u0928 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0924\u0915 \u0915\u0947 \u092e\u093e\u0907\u0932\u0938\u094d\u091f\u094b\u0928 \u092d\u0941\u0917\u0924\u093e\u0928, \u0914\u0930 \u092c\u093f\u0915\u094d\u0930\u0940 \u092e\u093e\u0907\u0932\u0938\u094d\u091f\u094b\u0928 \u0915\u0947 \u0932\u093f\u090f \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 600 \u092e\u093f\u0932\u093f\u092f\u0928 \u0905\u092e\u0947\u0930\u093f\u0915\u0940 \u0921\u0949\u0932\u0930 \u0915\u093e \u092d\u0941\u0917\u0924\u093e\u0928 \u0915\u0930\u0947\u0917\u093e\u0964 JCR \u0915\u094b \u092c\u093f\u0915\u094d\u0930\u0940 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0938\u094d\u0924\u0930\u0940\u092f \u0930\u0949\u092f\u0932\u094d\u091f\u0940 \u092d\u0940 \u092e\u093f\u0932\u0947\u0917\u0940, \u0939\u093e\u0932\u093e\u0901\u0915\u093f \u0915\u094b\u0908 \u0935\u093f\u0936\u093f\u0937\u094d\u091f \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u0928\u0939\u0940\u0902 \u0926\u0940 \u0917\u0908\u0964<\/p>\n\n\n\n<div class=\"wp-block-rank-math-toc-block\" id=\"rank-math-toc\"><h2>\u0935\u093f\u0937\u092f\u0938\u0942\u091a\u0940<\/h2><nav><ul><li><a href=\"#whar-is-just-aav-capsids\">JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921\u094d\u0938 \u0915\u094d\u092f\u093e \u0939\u0948?<\/a><\/li><li><a href=\"#just-aav-capsids-may-be-used-for-duchenne-cures\">JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u0915\u0947 \u0907\u0932\u093e\u091c \u0915\u0947 \u0932\u093f\u090f \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0939\u0948<\/a><\/li><li><a href=\"#pre-clinical-trials-of-just-aav-capsids\">JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u0947 \u092a\u0942\u0930\u094d\u0935 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/a><\/li><\/ul><\/nav><\/div>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"whar-is-just-aav-capsids\">JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921\u094d\u0938 \u0915\u094d\u092f\u093e \u0939\u0948?<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>JUST-AAV \u090f\u0915 \u0938\u094d\u0935\u093e\u092e\u093f\u0924\u094d\u0935 \u092a\u094d\u0932\u0947\u091f\u092b\u093c\u0949\u0930\u094d\u092e \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u0940 \u0939\u0948 \u091c\u094b \u0938\u0902\u0936\u094b\u0927\u093f\u0924 \u090f\u0921\u0947\u0928\u094b-\u090f\u0938\u094b\u0938\u093f\u090f\u091f\u0947\u0921 \u0935\u093e\u092f\u0930\u0938 (AAV) \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u0930\u0924\u0940 \u0939\u0948\u0964<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938 \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u0940 \u092e\u0947\u0902 \u091a\u092f\u0928\u093f\u0924 \u090a\u0924\u0915\u094b\u0902, \u0905\u0902\u0917\u094b\u0902 \u092f\u093e \u0930\u0915\u094d\u0924-\u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915 \u0905\u0935\u0930\u094b\u0927 \u092a\u0930 \u0938\u094d\u0925\u093f\u0924 \u0930\u093f\u0938\u0947\u092a\u094d\u091f\u0930\u094d\u0938 \u0915\u0947 \u0935\u093f\u0930\u0941\u0926\u094d\u0927 \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0938\u0924\u0939 \u092a\u0930 \u0932\u0918\u0941 \u090f\u0902\u091f\u0940\u092c\u0949\u0921\u0940\u091c \u0915\u094b \u092a\u094d\u0930\u0935\u093f\u0937\u094d\u091f \u0915\u093f\u092f\u093e \u091c\u093e\u0924\u093e \u0939\u0948, \u091c\u093f\u0938\u0938\u0947 \u0909\u0928 \u090a\u0924\u0915\u094b\u0902 \u0914\u0930 \u0905\u0902\u0917\u094b\u0902 \u0924\u0915 \u0932\u0915\u094d\u0937\u093f\u0924 \u0935\u093f\u0924\u0930\u0923 \u092e\u0947\u0902 \u0935\u0943\u0926\u094d\u0927\u093f \u0939\u094b\u0924\u0940 \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u092e\u0947\u0902 \u0914\u0930 \u092d\u0940 \u0938\u0902\u0936\u094b\u0927\u0928, \u0932\u0915\u094d\u0937\u094d\u092f \u0938\u0947 \u092c\u093e\u0939\u0930 \u0915\u0947 \u092a\u094d\u0930\u092d\u093e\u0935\u094b\u0902 \u0915\u094b \u0915\u092e \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u0914\u0930 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092e\u0947\u0902 \u0938\u0941\u0927\u093e\u0930 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964 \u0907\u0938\u0915\u093e \u0928\u093e\u092e &quot;\u091c\u0947\u0938\u0940\u0906\u0930&quot; &quot;\u0905\u0902\u0917 \u0915\u093e \u0905\u0902\u0924\u093f\u092e \u0917\u0902\u0924\u0935\u094d\u092f&quot;, &quot;\u0932\u0915\u094d\u0937\u094d\u092f \u0938\u0947 \u092c\u093e\u0939\u0930 \u0915\u0940 \u0921\u093f\u0932\u0940\u0935\u0930\u0940 \u0938\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e&quot; \u0914\u0930 &quot;\u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928\u0915\u093e\u0930\u0940 \u0924\u0915\u0928\u0940\u0915&quot; \u0938\u0947 \u0932\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948, \u091c\u094b \u0935\u093f\u092d\u093f\u0928\u094d\u0928 \u0930\u094b\u0917\u094b\u0902 \u092e\u0947\u0902 \u0907\u0938\u0915\u0947 \u0935\u094d\u092f\u093e\u092a\u0915 \u0905\u0928\u0941\u092a\u094d\u0930\u092f\u094b\u0917 \u0915\u0940 \u0915\u094d\u0937\u092e\u0924\u093e \u0915\u094b \u0926\u0930\u094d\u0936\u093e\u0924\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"just-aav-capsids-may-be-used-for-duchenne-cures\">JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u0915\u0947 \u0907\u0932\u093e\u091c \u0915\u0947 \u0932\u093f\u090f \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0924\u093e \u0939\u0948<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Alexion \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0915\u093f\u0928 \u0938\u0902\u0915\u0947\u0924\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0915\u0930\u0947\u0917\u093e, \u092f\u0939 \u092d\u0940 \u0928\u093f\u0930\u094d\u0926\u093f\u0937\u094d\u091f \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0925\u093e\u0964 AstraZeneca \u0915\u0940 \u0926\u0941\u0930\u094d\u0932\u092d \u0930\u094b\u0917 \u092a\u093e\u0907\u092a\u0932\u093e\u0907\u0928 \u092e\u093e\u092f\u0938\u094d\u0925\u0947\u0928\u093f\u092f\u093e \u0917\u094d\u0930\u0947\u0935\u093f\u0938 \u0914\u0930 \u0932\u094d\u092f\u0942\u092a\u0938 \u0928\u0947\u092b\u094d\u0930\u093e\u0907\u091f\u093f\u0938 \u091c\u0948\u0938\u0940 \u092c\u0940\u092e\u093e\u0930\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u092e\u0927\u094d\u092f \u0938\u0947 \u0932\u0947\u0915\u0930 \u0905\u0902\u0924\u093f\u092e \u091a\u0930\u0923 \u0915\u0940 \u092a\u0930\u093f\u0938\u0902\u092a\u0924\u094d\u0924\u093f\u092f\u094b\u0902 \u0938\u0947 \u092d\u0930\u0940 \u0939\u0941\u0908 \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u091c\u0947\u0938\u0940\u0906\u0930 \u0915\u093e \u0926\u093e\u0935\u093e \u0939\u0948 \u0915\u093f \u0909\u0938\u0915\u0947 \u0938\u094d\u0935\u093e\u092e\u093f\u0924\u094d\u0935 \u0935\u093e\u0932\u0947 JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u0908 \u0915\u093f\u0938\u094d\u092e\u094b\u0902 \u092e\u0947\u0902 \u0906\u0924\u0947 \u0939\u0948\u0902, \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 &quot;\u092f\u0915\u0943\u0924-\u092c\u091a\u0924&quot;, \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940-\u0932\u0915\u094d\u0937\u094d\u092f\u0940\u0915\u0930\u0923 \u0914\u0930 \u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915-\u0932\u0915\u094d\u0937\u094d\u092f\u0940\u0915\u0930\u0923 \u092a\u094d\u0930\u0915\u093e\u0930\u094b\u0902 \u092a\u0930 \u092a\u094d\u0930\u0915\u093e\u0936 \u0921\u093e\u0932\u0924\u0947 \u0939\u0948\u0902\u0964<\/strong> \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0938\u0947 \u0932\u0940\u0935\u0930 \u0915\u094b \u0939\u094b\u0928\u0947 \u0935\u093e\u0932\u0940 \u0915\u094d\u0937\u0924\u093f \u092a\u0930 \u0939\u093e\u0932 \u0939\u0940 \u092e\u0947\u0902 \u0917\u0939\u0928 \u091c\u093e\u0902\u091a \u0915\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948, \u0915\u094d\u092f\u094b\u0902\u0915\u093f \u0907\u0938 \u0935\u0930\u094d\u0937 \u0915\u0947 \u0936\u0941\u0930\u0942 \u092e\u0947\u0902 \u0921\u094d\u092f\u0942\u0936\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940, Elevidys \u0915\u0947 \u0932\u093f\u090f \u0938\u0930\u0947\u092a\u094d\u091f\u093e \u0915\u0940 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u092c\u093e\u0926 \u0932\u0940\u0935\u0930 \u0915\u0940 \u0915\u094d\u0937\u0924\u093f \u0938\u0947 \u0926\u094b \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0940 \u092e\u0943\u0924\u094d\u092f\u0941 \u0939\u094b \u0917\u0908 \u0925\u0940\u0964 - \u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/sarepta-reported-elevidys-gene-therapy-for-duchenne-muscular-dystrophy-will-not-be-used-in-non-ambulatory-patients\/\">Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u093e \u0909\u092a\u092f\u094b\u0917 \u0917\u0948\u0930-\u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0928\u0939\u0940\u0902 \u0915\u093f\u092f\u093e \u091c\u093e\u090f\u0917\u093e<\/a> \u2013<\/p>\n\n\n\n<h2 class=\"wp-block-heading\" id=\"pre-clinical-trials-of-just-aav-capsids\">JUST-AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0915\u0947 \u092a\u0942\u0930\u094d\u0935 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u092a\u0930\u0940\u0915\u094d\u0937\u0923<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">\u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0928\u0947 \u091f\u094d\u0930\u093e\u0902\u0938\u092b\u093c\u0930\u093f\u0928 \u0930\u093f\u0938\u0947\u092a\u094d\u091f\u0930 \u0938\u0947 \u091c\u0941\u0921\u093c\u0928\u0947 \u0935\u093e\u0932\u0947 \u090f\u0915 \u091b\u094b\u091f\u0947 \u090f\u0902\u091f\u0940\u092c\u0949\u0921\u0940 \u0915\u094b AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0915\u0930\u0915\u0947, \u090f\u0915 \u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915-\u0932\u0915\u094d\u0937\u094d\u092f\u093f\u0924 AAV \u0935\u0947\u0915\u094d\u091f\u0930 (\u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915-\u0932\u0915\u094d\u0937\u094d\u092f\u093f\u0924 JUST-AAV) \u0938\u092b\u0932\u0924\u093e\u092a\u0942\u0930\u094d\u0935\u0915 \u092c\u0928\u093e\u092f\u093e\u0964 \u0907\u0938\u0915\u0947 \u0905\u0932\u093e\u0935\u093e, AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u0905\u0928\u0941\u0915\u094d\u0930\u092e \u092e\u0947\u0902 \u0905\u0928\u0942\u0920\u0947 \u0938\u0902\u0936\u094b\u0927\u0928\u094b\u0902 \u0928\u0947 \u092f\u0915\u0943\u0924 \u092e\u0947\u0902 AAV \u0935\u0947\u0915\u094d\u091f\u0930 \u0915\u0947 \u0938\u0902\u091a\u092f \u0915\u094b \u0915\u093e\u092b\u093c\u0940 \u0939\u0926 \u0924\u0915 \u0915\u092e \u0915\u0930 \u0926\u093f\u092f\u093e, \u091c\u094b \u092a\u094d\u0930\u0924\u093f\u0915\u0942\u0932 \u092a\u094d\u0930\u092d\u093e\u0935\u094b\u0902 \u0915\u093e \u090f\u0915 \u091c\u094d\u091e\u093e\u0924 \u0938\u094d\u0930\u094b\u0924 \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091a\u0942\u0939\u094b\u0902 \u092a\u0930 \u0915\u093f\u090f \u0917\u090f \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u092e\u0947\u0902, JUST-AAV \u0935\u0947\u0915\u094d\u091f\u0930 \u0928\u0947 AAV9 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915 \u092e\u0947\u0902 \u0917\u094d\u0930\u0940\u0928 \u092b\u094d\u0932\u094b\u0930\u094b\u0938\u0947\u0902\u091f \u092a\u094d\u0930\u094b\u091f\u0940\u0928 (GFP) \u0915\u0940 77 \u0917\u0941\u0928\u093e \u0905\u0927\u093f\u0915 \u0905\u092d\u093f\u0935\u094d\u092f\u0915\u094d\u0924\u093f \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0915\u0940, \u091c\u092c\u0915\u093f \u092f\u0915\u0943\u0924 \u092e\u0947\u0902 \u091f\u094d\u0930\u094b\u092a\u093f\u091c\u094d\u092e \u0915\u094b 99% \u0926\u094d\u0935\u093e\u0930\u093e \u0915\u092e \u0915\u093f\u092f\u093e\u0964 \u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915 \u0932\u0915\u094d\u0937\u094d\u092f\u0940\u0915\u0930\u0923 \u0914\u0930 BBB \u092a\u093e\u0930\u0917\u092e\u094d\u092f\u0924\u093e \u0915\u094b \u0914\u0930 \u092c\u0947\u0939\u0924\u0930 \u092c\u0928\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f, \u0936\u094b\u0927\u0915\u0930\u094d\u0924\u093e\u0913\u0902 \u0928\u0947 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0905\u0923\u0941\u0913\u0902 \u0915\u094b AAV \u0915\u0948\u092a\u094d\u0938\u093f\u0921 \u092e\u0947\u0902 \u0936\u093e\u092e\u093f\u0932 \u0915\u093f\u092f\u093e \u091c\u094b \u091f\u094d\u0930\u093e\u0902\u0938\u092b\u093c\u0930\u093f\u0928 \u0930\u093f\u0938\u0947\u092a\u094d\u091f\u0930 \u0915\u0947 \u0905\u0932\u093e\u0935\u093e \u0905\u0928\u094d\u092f \u0930\u093f\u0938\u0947\u092a\u094d\u091f\u0930\u094d\u0938 \u0938\u0947 \u091c\u0941\u0921\u093c\u0924\u0947 \u0939\u0948\u0902\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092c\u0902\u0926\u0930\u094b\u0902 \u092a\u0930 \u0915\u093f\u090f \u0917\u090f \u0905\u0927\u094d\u092f\u092f\u0928\u094b\u0902 \u092e\u0947\u0902, \u0907\u0938 \u0926\u094d\u0935\u093f\u0935\u093f\u0936\u093f\u0937\u094d\u091f \u0935\u0947\u0915\u094d\u091f\u0930 \u0928\u0947 AAV9 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u092e\u0938\u094d\u0924\u093f\u0937\u094d\u0915 \u0924\u0915 \u091c\u0940\u0928 \u092a\u0939\u0941\u0902\u091a\u093e\u0928\u0947 \u0915\u0940 \u0926\u0915\u094d\u0937\u0924\u093e \u092e\u0947\u0902 \u0915\u0908 \u0917\u0941\u0928\u093e \u0938\u0941\u0927\u093e\u0930 \u0915\u093f\u092f\u093e, \u091c\u092c\u0915\u093f \u092f\u0915\u0943\u0924 \u0914\u0930 \u092a\u0943\u0937\u094d\u0920\u0940\u092f \u092e\u0942\u0932 \u0917\u0948\u0902\u0917\u094d\u0932\u093f\u092f\u093e \u091c\u0948\u0938\u0947 \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0938\u092e\u0938\u094d\u092f\u093e\u0917\u094d\u0930\u0938\u094d\u0924 \u090a\u0924\u0915\u094b\u0902 \u092e\u0947\u0902 \u0938\u0902\u0915\u094d\u0930\u092e\u0923 \u0915\u094b 90% \u0938\u0947 \u0905\u0927\u093f\u0915 \u0915\u092e \u0915\u0930 \u0926\u093f\u092f\u093e\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0928\u094d\u092f\u0942\u0930\u094b\u0928\u0932 \u0938\u0947\u0930\u0949\u0907\u0921 \u0932\u093f\u092a\u094b\u092b\u094d\u092f\u0942\u0938\u093f\u0928\u094b\u0938\u093f\u0938 \u0915\u0947 \u090f\u0915 \u092e\u093e\u0909\u0938 \u092e\u0949\u0921\u0932 \u092a\u0930 JUST-AAV \u0915\u0947 \u092a\u094d\u0930\u092f\u094b\u0917 \u0938\u0947 \u0926\u094c\u0930\u0947 \u091c\u0948\u0938\u0947 \u0932\u0915\u094d\u0937\u0923 \u0917\u093e\u092f\u092c \u0939\u094b \u0917\u090f \u0914\u0930 \u0915\u093e\u0930\u094d\u092f\u093e\u0924\u094d\u092e\u0915 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0938\u094d\u0924\u0930 \u0924\u0915 \u091c\u0940\u0935\u0928\u0915\u093e\u0932 \u092c\u0922\u093c \u0917\u092f\u093e\u0964 \u092f\u0947 \u092a\u0930\u093f\u0923\u093e\u092e \u092c\u0924\u093e\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f \u0928\u0935 \u0935\u093f\u0915\u0938\u093f\u0924 JUST-AAV \u0924\u0915\u0928\u0940\u0915 \u092a\u093e\u0930\u0902\u092a\u0930\u093f\u0915 \u091c\u0940\u0928 \u0935\u093f\u0924\u0930\u0923 \u0935\u0947\u0915\u094d\u091f\u0930\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u0905\u0927\u093f\u0915 \u0938\u0941\u0930\u0915\u094d\u0937\u093f\u0924 \u0914\u0930 \u0915\u0941\u0936\u0932 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0940 \u0938\u0902\u092d\u093e\u0935\u0928\u093e \u092a\u094d\u0930\u0926\u093e\u0928 \u0915\u0930\u0924\u0940 \u0939\u0948\u0964 - \u0914\u0930 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/jcrpharm.com\/updatedjcr-pharmaceuticals-presents-preclinical-gene-therapy-data-at-asgct-28th-annual-meeting\/\" target=\"_blank\" rel=\"noreferrer noopener\">JCR Pharmaceuticals \u092a\u094d\u0930\u0940\u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0921\u0947\u091f\u093e \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0930\u0924\u093e \u0939\u0948<\/a> \u2013<\/p>","protected":false},"excerpt":{"rendered":"<p>Alexion, AstraZeneca\u2019s rare disease subsidiary, is licensing specialized gene therapy vehicles from the Japanese firm JCR Pharmaceuticals. The deal, announced on 8th June 2025, gives Alexion access to JCR\u2019s JUST-AAV capsids to use in up to five of Alexion\u2019s genomic medicines programs. In exchange, Alexion will pay JCR an undisclosed upfront fee plus up to [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":4069,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[386,387,388,385],"class_list":["post-4065","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-alexion","tag-astrazeneca","tag-genomic-medicines","tag-jcr-pharmaceuticals"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4065","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=4065"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/4065\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/4069"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=4065"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=4065"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=4065"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}