{"id":3953,"date":"2025-06-20T18:39:58","date_gmt":"2025-06-20T15:39:58","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3953"},"modified":"2025-06-20T18:43:44","modified_gmt":"2025-06-20T15:43:44","slug":"capricor-therapeutics-announces-positive-4-year-data-of-deramiocel-cap-1002-in-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/capricor-therapeutics-announces-positive-4-year-data-of-deramiocel-cap-1002-in-duchenne-muscular-dystrophy\/","title":{"rendered":"Capricor Therapeutics \u0928\u0947 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u092e\u0947\u0902 Deramiocel (CAP-1002) \u0915\u0947 \u0938\u0915\u093e\u0930\u093e\u0924\u094d\u092e\u0915 4-\u0935\u0930\u094d\u0937\u0940\u092f \u0921\u0947\u091f\u093e \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Capricor Therapeutics, \u090f\u0915 \u091c\u0948\u0935 \u092a\u094d\u0930\u094c\u0926\u094d\u092f\u094b\u0917\u093f\u0915\u0940 \u0915\u0902\u092a\u0928\u0940 \u091c\u094b \u0926\u0941\u0930\u094d\u0932\u092d \u0930\u094b\u0917\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928\u0915\u093e\u0930\u0940 \u0915\u094b\u0936\u093f\u0915\u093e \u0914\u0930 \u090f\u0915\u094d\u0938\u094b\u0938\u094b\u092e-\u0906\u0927\u093e\u0930\u093f\u0924 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u0935\u093f\u0915\u0938\u093f\u0924 \u0915\u0930 \u0930\u0939\u0940 \u0939\u0948, \u0928\u0947 \u0906\u091c Deramiocel \u0915\u0947 \u0905\u092a\u0928\u0947 \u091a\u0932 \u0930\u0939\u0947 HOPE-2 \u0913\u092a\u0928-\u0932\u0947\u092c\u0932 \u090f\u0915\u094d\u0938\u091f\u0947\u0902\u0936\u0928 (OLE) \u0905\u0927\u094d\u092f\u092f\u0928 \u0938\u0947 \u0938\u0915\u093e\u0930\u093e\u0924\u094d\u092e\u0915 \u091a\u093e\u0930 \u0938\u093e\u0932 \u0915\u0947 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0914\u0930 \u092a\u094d\u0930\u092d\u093e\u0935\u0915\u093e\u0930\u093f\u0924\u093e \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940, \u091c\u094b \u0915\u0902\u092a\u0928\u0940 \u0915\u093e \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (DMD) \u0915\u0947 \u0932\u093f\u090f \u092a\u094d\u0930\u092e\u0941\u0916 \u0938\u0947\u0932 \u0925\u0947\u0930\u0947\u092a\u0940 \u0909\u092e\u094d\u092e\u0940\u0926\u0935\u093e\u0930 \u0939\u0948\u0964 - \u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/what-is-deramiocel\/\">Deramiocel \u0915\u094d\u092f\u093e \u0939\u0948? CAP-1002 \u0915\u094d\u092f\u093e \u0915\u0930\u0924\u093e \u0939\u0948?<\/a> \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u091a\u093e\u0930 \u0938\u093e\u0932 \u0915\u0947 \u0932\u0917\u093e\u0924\u093e\u0930 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092c\u093e\u0926, Deramiocel-\u0909\u092a\u091a\u093e\u0930\u093f\u0924 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u092c\u0947\u0938\u0932\u093e\u0907\u0928 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 -0.5 \u0905\u0902\u0915\u094b\u0902 \u0915\u093e \u0914\u0938\u0924 \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0926\u093f\u0916\u093e\u0964 \u0907\u0938\u0915\u0947 \u0905\u0932\u093e\u0935\u093e, \u092c\u0947\u0938\u0932\u093e\u0907\u0928 LVEF &gt;45% \u0935\u093e\u0932\u0947 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0947 \u0909\u092a\u0938\u092e\u0942\u0939 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923 \u0928\u0947 \u0914\u0930 \u092d\u0940 \u0905\u0927\u093f\u0915 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0932\u093e\u092d \u0926\u093f\u0916\u093e\u092f\u093e, \u091c\u094b \u0939\u0943\u0926\u092f \u0938\u092e\u093e\u0930\u094b\u0939 \u0915\u094b \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0930\u0942\u092a \u0938\u0947 \u0938\u0902\u0930\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f Deramiocel \u0915\u0947 \u0938\u093e\u0925 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0939\u0938\u094d\u0924\u0915\u094d\u0937\u0947\u092a \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0924\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0907\u0938\u0915\u0947 \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924, \u0909\u092a\u091a\u093e\u0930 \u0938\u0947 \u0915\u0902\u0915\u093e\u0932 \u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0927\u0940\u092e\u0940 \u0939\u094b\u0924\u0940 \u0930\u0939\u0940, \u091c\u0948\u0938\u093e \u0915\u093f \u090a\u092a\u0930\u0940 \u0905\u0902\u0917 \u0915\u0947 \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u0928 (PUL v2.0) \u0926\u094d\u0935\u093e\u0930\u093e \u092e\u093e\u092a\u093e \u0917\u092f\u093e, \u091c\u093f\u0938\u092e\u0947\u0902 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0928\u0947 \u092a\u0939\u0932\u0947 \u0935\u0930\u094d\u0937 (1.8 \u0905\u0902\u0915) \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u091a\u094c\u0925\u0947 \u0935\u0930\u094d\u0937 (0.6 \u0905\u0902\u0915) \u092e\u0947\u0902 \u0915\u092e \u0914\u0938\u0924 \u0917\u093f\u0930\u093e\u0935\u091f \u0915\u093e \u0905\u0928\u0941\u092d\u0935 \u0915\u093f\u092f\u093e\u0964 <strong>\u0915\u0941\u0932 \u092e\u093f\u0932\u093e\u0915\u0930, \u092f\u0947 \u0928\u093f\u0937\u094d\u0915\u0930\u094d\u0937 \u092c\u0924\u093e\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f Deramiocel \u0915\u0947 \u0938\u093e\u0925 \u0935\u093f\u0938\u094d\u0924\u093e\u0930\u093f\u0924 \u0909\u092a\u091a\u093e\u0930 \u0938\u092e\u092f \u0915\u0947 \u0938\u093e\u0925 \u0921\u0940\u090f\u092e\u0921\u0940 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u094b \u0915\u092e \u0915\u0930\u0928\u0947 \u092e\u0947\u0902 \u092e\u0926\u0926 \u0915\u0930 \u0938\u0915\u0924\u093e \u0939\u0948\u0964<\/strong> Deramiocel \u0928\u0947 \u092a\u0942\u0930\u0947 \u0905\u0927\u094d\u092f\u092f\u0928 \u0915\u0947 \u0926\u094c\u0930\u093e\u0928 \u0905\u0928\u0941\u0915\u0942\u0932 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932 \u092c\u0928\u093e\u090f \u0930\u0916\u0940 \u0939\u0948\u0964 \u2013 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/capricor-therapeutics-deramiocel-mid-cycle-review-meeting-with-fda\/\">Capricor Therapeutics \u0928\u0947 Deramiocel \u092a\u0930 FDA \u0915\u0947 \u0938\u093e\u0925 \u092e\u0927\u094d\u092f-\u091a\u0915\u094d\u0930 \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u092c\u0948\u0920\u0915 \u0915\u0947 \u0938\u092e\u093e\u092a\u0928 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940<\/a> \u2013<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u092a\u0940\u092a\u0940\u090f\u092e\u0921\u0940 \u0915\u0947 \u0938\u0902\u0938\u094d\u0925\u093e\u092a\u0915 \u0905\u0927\u094d\u092f\u0915\u094d\u0937 \u0914\u0930 \u0938\u0940\u0908\u0913 \u092a\u0948\u091f \u092b\u0930\u0932\u094b\u0902\u0917 \u0928\u0947 \u0915\u0939\u093e, &quot;\u0915\u093e\u0930\u094d\u0921\u093f\u092f\u094b\u092e\u093e\u092f\u094b\u092a\u0948\u0925\u0940 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0947\u0902 \u092e\u0943\u0924\u094d\u092f\u0941 \u0926\u0930 \u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u0915\u093e\u0930\u0923\u094b\u0902 \u092e\u0947\u0902 \u0938\u0947 \u090f\u0915 \u0939\u0948 \u0914\u0930 \u092c\u0940\u092e\u093e\u0930\u0940 \u0915\u0947 \u0907\u0938 \u092a\u0939\u0932\u0942 \u0915\u094b \u0938\u0902\u092c\u094b\u0927\u093f\u0924 \u0915\u0930\u0928\u093e \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0915\u094b \u092c\u0947\u0939\u0924\u0930 \u092c\u0928\u093e\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0939\u0948\u0964&quot; &quot;HOPE-2 OLE \u0905\u0927\u094d\u092f\u092f\u0928 \u0938\u0947 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0921\u0947\u091f\u093e \u0909\u0924\u094d\u0938\u093e\u0939\u091c\u0928\u0915 \u0939\u0948\u0902, \u0935\u093f\u0936\u0947\u0937 \u0930\u0942\u092a \u0938\u0947 \u091a\u093e\u0930 \u0935\u0930\u094d\u0937\u094b\u0902 \u092e\u0947\u0902 \u0939\u0943\u0926\u092f \u0938\u094d\u0925\u093f\u0930\u0940\u0915\u0930\u0923 \u0915\u094b \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u0930\u0928\u0947 \u092e\u0947\u0902\u0964 Deramiocel \u090f\u0915 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u0940\u092f \u0926\u0943\u0937\u094d\u091f\u093f\u0915\u094b\u0923 \u0915\u093e \u092a\u094d\u0930\u0924\u093f\u0928\u093f\u0927\u093f\u0924\u094d\u0935 \u0915\u0930\u0924\u093e \u0939\u0948 \u0914\u0930 \u0939\u092e \u0935\u093f\u0928\u093f\u092f\u093e\u092e\u0915 \u092e\u093e\u0930\u094d\u0917 \u0915\u0947 \u092e\u093e\u0927\u094d\u092f\u092e \u0938\u0947 \u0928\u093f\u0930\u0902\u0924\u0930 \u092a\u094d\u0930\u0917\u0924\u093f \u0915\u093e \u0938\u092e\u0930\u094d\u0925\u0928 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u0924\u093e\u0915\u093f \u092f\u0939 \u0938\u0941\u0928\u093f\u0936\u094d\u091a\u093f\u0924 \u0915\u093f\u092f\u093e \u091c\u093e \u0938\u0915\u0947 \u0915\u093f \u0939\u0943\u0926\u092f \u0914\u0930 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f \u0926\u094b\u0928\u094b\u0902 \u0915\u094b \u0932\u0915\u094d\u0937\u093f\u0924 \u0915\u0930\u0928\u0947 \u0935\u093e\u0932\u0947 \u0909\u092a\u091a\u093e\u0930 \u0939\u092e\u093e\u0930\u0947 \u0938\u092e\u0941\u0926\u093e\u092f \u0915\u0947 \u0932\u093f\u090f \u091c\u093f\u0924\u0928\u0940 \u091c\u0932\u094d\u0926\u0940 \u0939\u094b \u0938\u0915\u0947 \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b\u0902\u0964&quot;<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Capricor Therapeutics \u0915\u0940 \u0938\u0940\u0908\u0913 \u0932\u093f\u0902\u0921\u093e \u092e\u093e\u0930\u094d\u092c\u0928, \u092a\u0940\u090f\u091a\u0921\u0940 \u0928\u0947 \u0915\u0939\u093e, &quot;\u092f\u0947 \u091a\u093e\u0930 \u0938\u093e\u0932 \u0915\u0947 \u0921\u0947\u091f\u093e Deramiocel \u0915\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0932\u093e\u092d \u0914\u0930 \u0939\u0943\u0926\u092f \u0924\u0925\u093e \u0915\u0902\u0915\u093e\u0932 \u0915\u0940 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0915\u093e\u0930\u094d\u092f \u092e\u0947\u0902 \u0905\u0928\u0941\u0915\u0942\u0932 \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u092a\u094d\u0930\u094b\u092b\u093c\u093e\u0907\u0932 \u0915\u0940 \u0924\u093e\u0915\u0924 \u0914\u0930 \u0938\u094d\u0925\u093e\u092f\u093f\u0924\u094d\u0935 \u0915\u094b \u092a\u0941\u0937\u094d\u091f \u0915\u0930\u0924\u0947 \u0939\u0948\u0902\u0964&quot; &quot;\u0939\u092e\u093e\u0930\u0947 BLA \u0915\u0940 \u092a\u094d\u0930\u093e\u0925\u092e\u093f\u0915\u0924\u093e \u0938\u092e\u0940\u0915\u094d\u0937\u093e \u0915\u0940 \u091c\u093e \u0930\u0939\u0940 \u0939\u0948 \u0914\u0930 \u0915\u0908 \u092a\u094d\u0930\u092e\u0941\u0916 \u0935\u093f\u0928\u093f\u092f\u093e\u092e\u0915 \u0915\u0926\u092e \u0905\u092c \u092a\u0942\u0930\u0947 \u0939\u094b \u091a\u0941\u0915\u0947 \u0939\u0948\u0902, \u0939\u092e \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0905\u0928\u0941\u092e\u094b\u0926\u0928 \u0915\u0940 \u0913\u0930 \u092c\u0922\u093c\u0924\u0947 \u0939\u0941\u090f \u0927\u094d\u092f\u093e\u0928 \u0914\u0930 \u0924\u0924\u094d\u092a\u0930\u0924\u093e \u0915\u0947 \u0938\u093e\u0925 \u0915\u093e\u092e \u0915\u0930 \u0930\u0939\u0947 \u0939\u0948\u0902\u0964 FDA \u0915\u0947 \u0938\u093e\u0925 \u0939\u092e\u093e\u0930\u0940 \u0928\u093f\u0930\u0902\u0924\u0930 \u092c\u093e\u0924\u091a\u0940\u0924 \u0915\u093f\u0938\u0940 \u092d\u0940 \u0926\u0947\u0930\u0940 \u0915\u0947 \u0938\u092c\u0942\u0924 \u0915\u0947 \u092c\u093f\u0928\u093e \u092a\u091f\u0930\u0940 \u092a\u0930 \u092c\u0928\u0940 \u0939\u0941\u0908 \u0939\u0948\u0964 \u0939\u092e \u0909\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902, \u092a\u0930\u093f\u0935\u093e\u0930\u094b\u0902 \u0914\u0930 \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u0915\u094b\u0902 \u0915\u094b \u0927\u0928\u094d\u092f\u0935\u093e\u0926 \u0926\u0947\u0924\u0947 \u0939\u0948\u0902 \u091c\u093f\u0928\u094d\u0939\u094b\u0902\u0928\u0947 \u0907\u0938 \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0915\u094b \u0906\u0917\u0947 \u092c\u0922\u093c\u093e\u0928\u0947 \u092e\u0947\u0902 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u092d\u0942\u092e\u093f\u0915\u093e \u0928\u093f\u092d\u093e\u0908 \u0939\u0948\u0964&quot;<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/capricor-therapeutics-announces-bmd-orphan-drug-designation-and-dmd-program-regulatory-development-for-deramiocel-cap-1002\/\">Capricor Therapeutics \u0928\u0947 Deramiocel (CAP-1002) \u0915\u0947 \u0932\u093f\u090f BMD \u0905\u0928\u093e\u0925 \u0914\u0937\u0927\u093f \u092a\u0926\u0928\u093e\u092e \u0914\u0930 DMD \u0915\u093e\u0930\u094d\u092f\u0915\u094d\u0930\u092e \u0935\u093f\u0928\u093f\u092f\u093e\u092e\u0915 \u0935\u093f\u0915\u093e\u0938 \u0915\u0940 \u0918\u094b\u0937\u0923\u093e \u0915\u0940<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Capricor Therapeutics, a biotechnology company developing transformative cell and exosome-based therapeutics for rare diseases, today announced positive four-year safety and efficacy results from its ongoing HOPE-2 Open-Label Extension (OLE) study of Deramiocel, the Company\u2019s lead cell therapy candidate for Duchenne Muscular Dystrophy (DMD). &#8211; Read More: What is Deramiocel? What Does CAP-1002 Do? &#8211; After [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3954,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[90,86,87,89,85,362,301],"class_list":["post-3953","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-cap-1002","tag-capricor","tag-capricor-therapeutics","tag-cardiomyopathy","tag-deramiocel","tag-dmd-cardiomyopathy","tag-hope-2"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/3953","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=3953"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/3953\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/3954"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=3953"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=3953"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=3953"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}