{"id":3223,"date":"2025-03-17T10:57:18","date_gmt":"2025-03-17T07:57:18","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3223"},"modified":"2025-03-17T11:00:40","modified_gmt":"2025-03-17T08:00:40","slug":"roche-to-share-ongoing-work-on-elevidys-gene-therapy-at-muscular-dystrophy-association-mda-2025-conference","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/roche-to-share-ongoing-work-on-elevidys-gene-therapy-at-muscular-dystrophy-association-mda-2025-conference\/","title":{"rendered":"\u0930\u094b\u0936 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0938\u094b\u0938\u093f\u090f\u0936\u0928 (\u090f\u092e\u0921\u0940\u090f) 2025 \u0938\u092e\u094d\u092e\u0947\u0932\u0928 \u092e\u0947\u0902 Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u0930 \u091a\u0932 \u0930\u0939\u0947 \u0915\u093e\u092e \u0915\u094b \u0938\u093e\u091d\u093e \u0915\u0930\u0947\u0917\u093e"},"content":{"rendered":"<p class=\"wp-block-paragraph\">\u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u090f\u0938\u094b\u0938\u093f\u090f\u0936\u0928 (\u090f\u092e\u0921\u0940\u090f) 2025 \u0938\u092e\u094d\u092e\u0947\u0932\u0928 \u092e\u0947\u0902, \u0930\u094b\u0936 Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u092a\u0930 \u0905\u092a\u0928\u0947 \u091a\u0932 \u0930\u0939\u0947 \u0915\u093e\u092e \u092a\u0930 \u091a\u0930\u094d\u091a\u093e \u0915\u0930\u0947\u0902\u0917\u0947\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0932\u0947\u091f-\u092c\u094d\u0930\u0947\u0915\u093f\u0902\u0917 \u0913\u0930\u0932 \u0911\u0928 1\u091f\u0940\u092a\u094031\u091f\u0940&#039; \u090f\u092e\u094d\u092c\u093e\u0930\u094d\u0915 \u0915\u0947 \u0926\u094b-\u0935\u0930\u094d\u0937\u0940\u092f \u0921\u0947\u091f\u093e \u0914\u0930 \u0905\u0927\u094d\u092f\u092f\u0928 101, 102 \u0914\u0930 \u090f\u0902\u0921\u0947\u0935\u0930 \u0915\u0947 \u0938\u0902\u092f\u0941\u0915\u094d\u0924 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923 \u0928\u0947 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u0921\u093c\u0915\u094b\u0902 \u092e\u0947\u0902 \u092e\u094b\u091f\u0930 \u092b\u093c\u0902\u0915\u094d\u0936\u0928 \u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u0909\u092a\u093e\u092f\u094b\u0902 \u092e\u0947\u0902 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0938\u093e\u0930\u094d\u0925\u0915 \u0914\u0930 \u0938\u093e\u0902\u0916\u094d\u092f\u093f\u0915\u0940\u092f \u0930\u0942\u092a \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0938\u0941\u0927\u093e\u0930 \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u093f\u090f\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Elevidys \u091a\u0932 \u0930\u0939\u0947 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0905\u0927\u094d\u092f\u092f\u0928<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys, EMBARK&#039;ta (A\u015fama III, NCT05096221 ) 101&#039;in (A\u015fama I\/II, NCT03375164 , n=4), \u00c7al\u0131\u015fma 102&#039;nin (A\u015fama II, NCT03769116, n=26) \u0914\u0930 \u090f\u0902\u0921\u0947\u0935\u0930 \u0915\u094b\u0939\u094b\u0930\u094d\u091f 1&#039;in (\u0905\u0938\u093e\u092e\u093e \u0906\u0908\u092c\u0940, NCT04626674, n=20) \u090f\u0915 \u0935\u0930\u094d\u0937 \u0938\u0947 \u0905\u0927\u093f\u0915 \u0938\u092e\u092f \u0924\u0915 \u091a\u0932\u0928\u0947 \u0935\u093e\u0932\u093e \u090f\u0928\u093e\u0932\u093e\u0907\u091c\u093c\u094d\u0921 \u091f\u0947\u0921\u093e\u0935\u093f\u0921\u0947\u0928 \u00fc\u00e7 y\u0131l \u0938\u094b\u0928\u0930\u093e \u092e\u094b\u091f\u0930 \u092b\u093c\u094b\u0928\u0915\u094d\u0938\u093f\u092f\u094b\u0928\u0941\u0928 \u091f\u0947\u092e\u0947\u0932 \u0913\u0932\u0915\u092e\u0932\u0947\u0930\u093f\u0928\u094d\u0921\u0947 \u0907\u0938\u094d\u091f\u0948\u091f\u093f\u0938\u094d\u091f\u093f\u0915\u094d\u0938\u0947\u0932 \u0915\u0943\u092a\u092f\u093e \u0905\u092a\u0928\u093e \u0915\u094d\u0932\u093f\u0928\u093f\u0915 \u0916\u094b\u0932\u0947\u0902 \u0905\u0902\u0924\u093f\u092e \u091a\u0930\u0923 \u092e\u0947\u0902, \u0906\u092a\u0915\u0947 \u092a\u093e\u0938 \u0938\u092e\u0942\u0939 \u0928\u093f\u092f\u0902\u0924\u094d\u0930\u0923 \u0915\u0947 \u0932\u093f\u090f \u0905\u0924\u093f\u0930\u093f\u0915\u094d\u0924 \u0938\u0902\u0938\u093e\u0927\u0928 \u0939\u0948\u0902\u0964 \u091f\u0949\u092a\u0932\u0942 \u0913\u0932\u093e\u0930\u093e\u0915, \u0935\u0947\u0930\u093f\u0932\u0930 1\u091f\u0940\u092a\u094031\u091f\u0940 \u0907\u0932\u0947 \u091f\u0947\u0921\u093e\u0935\u093f\u0928\u093f\u0928, \u091f\u0947\u0921\u093e\u0935\u0940 \u0938\u093f\u0930\u093e\u0938\u093f\u0902\u0921\u093e \u0921\u0949\u0930\u094d\u091f \u0907\u0932\u093e \u0938\u0947\u0915\u093f\u091c\u093c \u092f\u093e\u0938\u0932\u093e\u0930\u093f\u0902\u0921\u093e\u0915\u093f \u092c\u093f\u0930\u0947\u0932\u0947\u0930\u094d\u0921\u0947 \u0939\u0947\u0938\u094d\u091f\u0932\u093f\u0928\u093f\u0928 \u0907\u0932\u0947\u0932\u0947\u092e\u0947\u0938\u093f\u0928\u093f\u0928 \u0909\u091c\u093c\u0941\u0928 \u0935\u0947\u0921\u0947\u0932\u0940 \u0938\u094d\u091f\u0948\u092c\u093f\u0932\u093f\u091c\u093c\u093e\u0938\u094b\u0928\u0941 \u0935\u0947\u092f\u093e \u092f\u093e\u0935\u093e\u0938\u094d\u0932\u0948\u092e\u093e\u0938\u0940 \u0907\u0932\u0947 \u0938\u094b\u0928\u0941\u0915\u094d\u0932\u093e\u0928\u094d\u0921\u093e\u0917\u093f\u0928 g\u00f6stermektedir.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u0928\u0947 EMBARK (\u091a\u0930\u0923 III, NCT05096221) \u092e\u0947\u0902 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0926\u094b \u0938\u093e\u0932 \u092c\u093e\u0926 \u0914\u0930 \u0905\u0927\u094d\u092f\u092f\u0928 101 (\u091a\u0930\u0923 I\/II, NCT03375164, n=4), \u0905\u0927\u094d\u092f\u092f\u0928 102 (\u091a\u0930\u0923 II, NCT03769116, n=26) \u0914\u0930 ENDEAVOR \u0915\u094b\u0939\u094b\u0930\u094d\u091f 1 (\u091a\u0930\u0923 Ib, NCT04626674, n=20) \u0915\u0947 \u0938\u0902\u092f\u0941\u0915\u094d\u0924 \u0935\u093f\u0936\u094d\u0932\u0947\u0937\u0923 \u092e\u0947\u0902 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0924\u0940\u0928 \u0938\u093e\u0932 \u092c\u093e\u0926 \u092e\u094b\u091f\u0930 \u092b\u093c\u0902\u0915\u094d\u0936\u0928 \u0915\u0947 \u092a\u094d\u0930\u092e\u0941\u0916 \u0909\u092a\u093e\u092f\u094b\u0902 \u092e\u0947\u0902 \u0938\u093e\u0902\u0916\u094d\u092f\u093f\u0915\u0940\u092f \u0930\u0942\u092a \u0938\u0947 \u092e\u0939\u0924\u094d\u0935\u092a\u0942\u0930\u094d\u0923 \u0914\u0930 \u0928\u0948\u0926\u093e\u0928\u093f\u0915 \u0930\u0942\u092a \u0938\u0947 \u0938\u093e\u0930\u094d\u0925\u0915 \u0938\u0941\u0927\u093e\u0930 \u0926\u093f\u0916\u093e\u090f, \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u092e\u0947\u0932 \u0916\u093e\u0928\u0947 \u0935\u093e\u0932\u0947 \u092c\u093e\u0939\u0930\u0940 \u0928\u093f\u092f\u0902\u0924\u094d\u0930\u0923 \u0938\u092e\u0942\u0939\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902\u0964 \u0938\u093e\u092e\u0942\u0939\u093f\u0915 \u0930\u0942\u092a \u0938\u0947, \u092f\u0947 \u0921\u0947\u091f\u093e \u092a\u094d\u0930\u0926\u0930\u094d\u0936\u093f\u0924 \u0915\u0930\u0924\u0947 \u0939\u0948\u0902 \u0915\u093f Elevidys \u0915\u0947 \u0938\u093e\u0925 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u092a\u0930\u093f\u0923\u093e\u092e\u0938\u094d\u0935\u0930\u0942\u092a \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0938\u092e\u092f \u091a\u093e\u0930 \u0938\u0947 \u0906\u0920 \u0935\u0930\u094d\u0937 \u0915\u0940 \u0906\u092f\u0941 \u0915\u0947 \u0935\u094d\u092f\u0915\u094d\u0924\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0926\u0940\u0930\u094d\u0918\u0915\u093e\u0932\u093f\u0915 \u0938\u094d\u0925\u093f\u0930\u0924\u093e \u092f\u093e \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u0927\u0940\u092e\u0940 \u0939\u094b \u091c\u093e\u0924\u0940 \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><a href=\"https:\/\/dmdwarrior.com\/hi\/roche-announces-new-results-from-the-embark-study-of-elevidys-in-outpatients-with-duchenne-muscular-dystrophy-dmd\/\" target=\"_blank\" data-type=\"post\" data-id=\"2612\" rel=\"noreferrer noopener\">EMBARK \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0947 \u0926\u0942\u0938\u0930\u0947 \u0935\u0930\u094d\u0937 \u0915\u0947 \u092e\u0941\u0916\u094d\u092f \u0906\u0902\u0915\u0921\u093c\u0947 \u091c\u0928\u0935\u0930\u0940 2025 \u092e\u0947\u0902 \u0918\u094b\u0937\u093f\u0924 \u0915\u093f\u090f \u091c\u093e\u090f\u0902\u0917\u0947\u0964<\/a> \u0926\u094b \u0935\u0930\u094d\u0937 \u0915\u0940 \u0905\u0935\u0927\u093f \u092e\u0947\u0902 EMBARK \u0905\u0927\u094d\u092f\u092f\u0928 \u092e\u0947\u0902 \u0915\u094b\u0908 \u0928\u092f\u093e \u0938\u0941\u0930\u0915\u094d\u0937\u093e \u0938\u0902\u0915\u0947\u0924 \u0928\u0939\u0940\u0902 \u0926\u0947\u0916\u093e \u0917\u092f\u093e\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u092a\u0930 Elevidys \u0915\u0947 \u092a\u094d\u0930\u092d\u093e\u0935 \u0915\u093e \u0914\u0930 \u0905\u0927\u093f\u0915 \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u0930\u0928\u0947 \u0915\u0947 \u0932\u093f\u090f, EMBARK \u092d\u093e\u0917 \u090f\u0915 \u092e\u0947\u0902 \u0935\u094d\u092f\u0915\u094d\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u090f\u0915 \u0909\u092a\u0938\u092e\u0942\u0939 \u092e\u0947\u0902 \u091a\u0941\u0902\u092c\u0915\u0940\u092f \u0905\u0928\u0941\u0928\u093e\u0926 \u0907\u092e\u0947\u091c\u093f\u0902\u0917 (MRI) \u0926\u094d\u0935\u093e\u0930\u093e \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0947 \u0938\u094d\u0935\u093e\u0938\u094d\u0925\u094d\u092f \u0914\u0930 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0915\u0940 \u0935\u093f\u0915\u0943\u0924\u093f \u092e\u0947\u0902 \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u0915\u093e \u092e\u0942\u0932\u094d\u092f\u093e\u0902\u0915\u0928 \u0915\u093f\u092f\u093e \u0917\u092f\u093e\u0964 \u0938\u092a\u094d\u0924\u093e\u0939 52 \u092e\u0947\u0902, \u092a\u0930\u093f\u0923\u093e\u092e\u094b\u0902 \u0928\u0947 \u092a\u094d\u0932\u0947\u0938\u092c\u094b-\u0909\u092a\u091a\u093e\u0930\u093f\u0924 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 Elevidys-\u0909\u092a\u091a\u093e\u0930\u093f\u0924 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u0930\u094b\u0917 \u0915\u0940 \u092a\u094d\u0930\u0917\u0924\u093f \u092e\u0947\u0902 \u0938\u094d\u0925\u093f\u0930\u0924\u093e \u092f\u093e \u092e\u0902\u0926\u0940 \u0926\u093f\u0916\u093e\u0908\u0964 \u0938\u092a\u094d\u0924\u093e\u0939 104 \u092e\u0947\u0902, \u092c\u0947\u0938\u0932\u093e\u0907\u0928 \u0938\u0947 MRI \u092a\u0930\u093f\u0935\u0930\u094d\u0924\u0928 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u093f\u092f\u094b\u0902 \u0914\u0930 \u092e\u093e\u0902\u0938\u092a\u0947\u0936\u0940 \u0938\u092e\u0942\u0939\u094b\u0902 \u092e\u0947\u0902 \u0938\u092a\u094d\u0924\u093e\u0939 52 \u092a\u0930 \u092a\u094d\u0932\u0947\u0938\u092c\u094b \u0915\u0940 \u0924\u0941\u0932\u0928\u093e \u092e\u0947\u0902 \u0906\u092e \u0924\u094c\u0930 \u092a\u0930 Elevidys \u0915\u0947 \u092a\u0915\u094d\u0937 \u092e\u0947\u0902 \u091c\u093e\u0930\u0940 \u0930\u0939\u093e\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u092a\u0922\u093c\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/clinical-trials-review-of-elevidys-gene-therapy-is-elevidys-cost-worthy\/\" target=\"_blank\" data-type=\"post\" data-id=\"3027\" rel=\"noreferrer noopener\">Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940: \u0915\u094d\u092f\u093e \u092f\u0939 \u0915\u0940\u092e\u0924 \u0915\u0947 \u0932\u093e\u092f\u0915 \u0939\u0948?<\/a><\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Elevidys \u0915\u0947 \u0932\u093f\u090f \u0935\u093f\u092a\u0923\u0928 \u092a\u094d\u0930\u093e\u0927\u093f\u0915\u0930\u0923<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">Elevidys \u0915\u094b \u0905\u092e\u0947\u0930\u093f\u0915\u093e, \u0938\u0902\u092f\u0941\u0915\u094d\u0924 \u0905\u0930\u092c \u0905\u092e\u0940\u0930\u093e\u0924 (\u092f\u0942\u090f\u0908), \u0915\u0924\u0930, \u0915\u0941\u0935\u0948\u0924, \u092c\u0939\u0930\u0940\u0928 \u0914\u0930 \u0913\u092e\u093e\u0928 \u092e\u0947\u0902 \u091a\u093e\u0930 \u0938\u093e\u0932 \u092f\u093e \u0909\u0938\u0938\u0947 \u0905\u0927\u093f\u0915 \u0909\u092e\u094d\u0930 \u0915\u0947 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u0938\u0947 \u092a\u0940\u0921\u093c\u093f\u0924 \u0932\u094b\u0917\u094b\u0902 \u0915\u0947 \u0932\u093f\u090f \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948, \u092d\u0932\u0947 \u0939\u0940 \u0935\u0947 \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0939\u094b\u0902 \u092f\u093e \u0928\u0939\u0940\u0902\u0964 Elevidys \u0915\u094b \u092c\u094d\u0930\u093e\u091c\u0940\u0932 \u0914\u0930 \u0907\u091c\u093c\u0930\u093e\u0907\u0932 \u092e\u0947\u0902 \u091a\u093e\u0930 \u0938\u0947 \u0938\u093e\u0924 \u0938\u093e\u0932 \u0915\u0940 \u0909\u092e\u094d\u0930 \u0915\u0947 \u091a\u0932\u0928\u0947-\u092b\u093f\u0930\u0928\u0947 \u092e\u0947\u0902 \u0938\u0915\u094d\u0937\u092e \u0935\u094d\u092f\u0915\u094d\u0924\u093f\u092f\u094b\u0902 \u0915\u0947 \u0909\u092a\u091a\u093e\u0930 \u0915\u0947 \u0932\u093f\u090f \u092d\u0940 \u0938\u094d\u0935\u0940\u0915\u0943\u0924 \u0915\u093f\u092f\u093e \u0917\u092f\u093e \u0939\u0948\u0964 \u092f\u0942\u0930\u094b\u092a\u0940\u092f \u091a\u093f\u0915\u093f\u0924\u094d\u0938\u093e \u090f\u091c\u0947\u0902\u0938\u0940 (EMA) \u0914\u0930 \u091c\u093e\u092a\u093e\u0928, \u0938\u094d\u0935\u093f\u091f\u091c\u0930\u0932\u0948\u0902\u0921, \u0938\u093f\u0902\u0917\u093e\u092a\u0941\u0930, \u0939\u093e\u0902\u0917\u0915\u093e\u0902\u0917 \u0914\u0930 \u0938\u090a\u0926\u0940 \u0905\u0930\u092c \u092e\u0947\u0902 \u0928\u093f\u092f\u093e\u092e\u0915 \u092a\u094d\u0930\u093e\u0927\u093f\u0915\u0930\u0923\u094b\u0902 \u0915\u094b \u092d\u0940 \u092b\u093e\u0907\u0932\u093f\u0902\u0917 \u092a\u094d\u0930\u0938\u094d\u0924\u0941\u0924 \u0915\u0940 \u0917\u0908 \u0939\u0948\u0964 \u0906\u091c \u0924\u0915, Elevidys \u0915\u0947 \u0938\u093e\u0925 600 \u0938\u0947 \u0905\u0927\u093f\u0915 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u093e \u0907\u0932\u093e\u091c \u0915\u093f\u092f\u093e \u091c\u093e \u091a\u0941\u0915\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902: <a href=\"https:\/\/dmdwarrior.com\/hi\/why-isnt-roche-applying-marketing-authorization-in-every-country-for-elevidys-gene-therapy\/\">\u0930\u094b\u0936 Elevidys \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0932\u093f\u090f \u0939\u0930 \u0926\u0947\u0936 \u092e\u0947\u0902 \u0935\u093f\u092a\u0923\u0928 \u092a\u094d\u0930\u093e\u0927\u093f\u0915\u0930\u0923 \u0915\u094d\u092f\u094b\u0902 \u0928\u0939\u0940\u0902 \u0932\u093e\u0917\u0942 \u0915\u0930 \u0930\u0939\u093e \u0939\u0948?<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>At the Muscular Dystrophy Association (MDA) 2025 Conference, Roche will discuss their ongoing work on Elevidys Gene Therapy. Late-breaking oral on Elevidys\u2019 Embark two-year data and pooled analysis of Study 101, 102 and Endeavor, demonstrated clinically meaningful and statistically significant improvements across key measures of motor function in boys with Duchenne muscular dystrophy (DMD) Elevidys [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3224,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[33,61,297,203],"class_list":["post-3223","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-elevidys","tag-gene-therapy","tag-muscular-dystrophy-association","tag-roche"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/3223","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=3223"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/3223\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/3224"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=3223"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=3223"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=3223"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}