{"id":2455,"date":"2025-01-16T11:50:08","date_gmt":"2025-01-16T08:50:08","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2455"},"modified":"2025-01-16T13:21:23","modified_gmt":"2025-01-16T10:21:23","slug":"solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/hi\/solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy\/","title":{"rendered":"Solid Biosciences \u0928\u0947 SGT-003 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u0947 \u0932\u093f\u090f \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u0915\u0940 \u091c\u093e\u0928\u0915\u093e\u0930\u0940 \u091c\u093e\u0930\u0940 \u0915\u0940"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Solid Biosciences \u0928\u0947 \u092c\u0924\u093e\u092f\u093e \u0915\u093f SGT-003 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u091a\u093e\u0930 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0915\u094b \u0916\u0941\u0930\u093e\u0915 \u0926\u0940 \u0917\u0908 \u0939\u0948; \u0938\u092d\u0940 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 \u092f\u0939 \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u0938\u0939\u0928 \u0915\u0940 \u0917\u0908 \u0924\u0925\u093e \u0915\u094b\u0908 \u0926\u0941\u0937\u094d\u092a\u094d\u0930\u092d\u093e\u0935 \u0928\u0939\u0940\u0902 \u0926\u0947\u0916\u093e \u0917\u092f\u093e; \u0924\u0925\u093e \u092a\u0939\u0932\u0947 \u0924\u0940\u0928 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u0938\u0947 \u092a\u094d\u0930\u093e\u092a\u094d\u0924 \u0921\u0947\u091f\u093e \u0935\u0930\u094d\u0937 2025 \u0915\u0940 \u092a\u0939\u0932\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0909\u092a\u0932\u092c\u094d\u0927 \u0939\u094b \u0938\u0915\u0924\u093e \u0939\u0948\u0964<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">\u090f\u0938\u091c\u0940\u091f\u0940-003 \u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 (\u0921\u0940\u090f\u092e\u0921\u0940) \u0915\u0947 \u0932\u093f\u090f \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>\u091a\u0932 \u0930\u0939\u0947 INSPIRE DUCHENNE \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u092a\u0930\u0940\u0915\u094d\u0937\u0923 \u092e\u0947\u0902 \u092a\u0939\u0932\u0947 \u091a\u093e\u0930 \u0930\u094b\u0917\u093f\u092f\u094b\u0902 \u092e\u0947\u0902 SGT-003 \u0915\u094b \u0905\u091a\u094d\u091b\u0940 \u0924\u0930\u0939 \u0938\u0947 \u0938\u0939\u0928 \u0915\u093f\u092f\u093e \u091c\u093e \u0930\u0939\u093e \u0939\u0948\u0964<\/li>\n\n\n\n<li>\u0935\u093f\u0938\u094d\u0924\u093e\u0930\u093f\u0924 INSPIRE DUCHENNE \u092a\u094d\u0930\u094b\u091f\u094b\u0915\u0949\u0932 \u0915\u0947 \u0905\u0902\u0924\u0930\u094d\u0917\u0924 \u0930\u094b\u0917\u0940 \u0928\u093e\u092e\u093e\u0902\u0915\u0928 \u0914\u0930 \u0916\u0941\u0930\u093e\u0915 \u0915\u093e \u0915\u093e\u0930\u094d\u092f \u091c\u093e\u0930\u0940 \u0939\u0948\u0964<\/li>\n\n\n\n<li>\u0909\u0924\u094d\u0924\u0930\u0940 \u0905\u092e\u0947\u0930\u093f\u0915\u093e \u092e\u0947\u0902 \u091b\u0939 \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u0938\u094d\u0925\u0932 \u0938\u0915\u094d\u0930\u093f\u092f \u0939\u0948\u0902 (\u092a\u093e\u0902\u091a \u0905\u092e\u0947\u0930\u093f\u0915\u093e \u092e\u0947\u0902, \u090f\u0915 \u0915\u0928\u093e\u0921\u093e \u092e\u0947\u0902)\u0964<\/li>\n\n\n\n<li>\u092f\u0942\u0915\u0947 \u092e\u0947\u0921\u093f\u0938\u093f\u0928\u094d\u0938 \u090f\u0902\u0921 \u0939\u0947\u0932\u094d\u0925\u0915\u0947\u092f\u0930 \u092a\u094d\u0930\u094b\u0921\u0915\u094d\u091f\u094d\u0938 \u0930\u0947\u0917\u0941\u0932\u0947\u091f\u0930\u0940 \u090f\u091c\u0947\u0902\u0938\u0940 (MHRA) \u0928\u0947 INSPIRE DUCHENNE \u0915\u094d\u0932\u093f\u0928\u093f\u0915\u0932 \u091f\u094d\u0930\u093e\u092f\u0932 \u090f\u092a\u094d\u0932\u0940\u0915\u0947\u0936\u0928 (CTA) \u0915\u094b \u092e\u0902\u091c\u0942\u0930\u0940 \u0926\u0947 \u0926\u0940 \u0939\u0948, \u091c\u093f\u0938\u0915\u0947 \u092a\u094d\u0930\u093e\u0930\u0902\u092d\u093f\u0915 \u0938\u093e\u0907\u091f \u0938\u0915\u094d\u0930\u093f\u092f\u0923 \u0915\u0940 \u0909\u092e\u094d\u092e\u0940\u0926 2025 \u0915\u0940 \u0926\u0942\u0938\u0930\u0940 \u091b\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0939\u0948\u0964<\/li>\n\n\n\n<li>\u0938\u0949\u0932\u093f\u0921 \u0915\u094b \u0909\u092e\u094d\u092e\u0940\u0926 \u0939\u0948 \u0915\u093f \u0935\u0939 2025 \u0915\u0940 \u092a\u0939\u0932\u0940 \u0924\u093f\u092e\u093e\u0939\u0940 \u092e\u0947\u0902 \u0916\u0941\u0930\u093e\u0915 \u0926\u093f\u090f \u0917\u090f \u092a\u0939\u0932\u0947 \u0924\u0940\u0928 \u092e\u0930\u0940\u091c\u094b\u0902 \u0938\u0947 \u0938\u0902\u092c\u0902\u0927\u093f\u0924 \u0921\u0947\u091f\u093e \u0915\u0940 \u0930\u093f\u092a\u094b\u0930\u094d\u091f \u0915\u0930\u0947\u0917\u093e\u0964<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>\u0914\u0930 \u0905\u0927\u093f\u0915 \u091c\u093e\u0928\u0947\u0902:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/hi\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\">\u0921\u094d\u092f\u0942\u091a\u0947\u0928 \u092e\u0938\u094d\u0915\u0941\u0932\u0930 \u0921\u093f\u0938\u094d\u091f\u094d\u0930\u0949\u092b\u0940 \u0915\u0947 \u0932\u093f\u090f \u0938\u0902\u092d\u093e\u0935\u093f\u0924 \u0906\u0917\u093e\u092e\u0940 \u0928\u0908 \u091c\u0940\u0928 \u0925\u0947\u0930\u0947\u092a\u0940<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Solid Biosciences shared that four patients have been dosed in the SGT-003 gene therapy clinical trial; it was well tolerated in all patients with no side effects observed; and data from the first three patients could be available in Q1 2025. SGT-003 Gene Therapy for Duchenne Muscular Dystrophy (DMD) Learn More: Potential Upcoming New Gene [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2458,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[171,72,61,110,170,109,79],"class_list":["post-2455","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-canada","tag-gene-editing","tag-gene-therapy","tag-sgt-003","tag-sgt-003-gene-therapy","tag-solid-biosciences","tag-usa"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/2455","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/comments?post=2455"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/posts\/2455\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media\/2458"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/media?parent=2455"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/categories?post=2455"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/hi\/wp-json\/wp\/v2\/tags?post=2455"}],"curies":[{"name":"\u0921\u092c\u094d\u0932\u094d\u092f\u0942\u092a\u0940","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}