{"id":6701,"date":"2026-03-09T18:17:40","date_gmt":"2026-03-09T15:17:40","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6701"},"modified":"2026-03-09T18:34:31","modified_gmt":"2026-03-09T15:34:31","slug":"vamorolone-agamree-in-dmd-real-world-experience","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/vamorolone-agamree-in-dmd-real-world-experience\/","title":{"rendered":"Vamorolone (Agamree) dans le DMD\u00a0: Exp\u00e9rience en situation r\u00e9elle"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Santhera Pharmaceuticals a annonc\u00e9 que les r\u00e9sultats complets des analyses comparatives \u00e0 long terme en situation r\u00e9elle, y compris les donn\u00e9es initiales de l&#039;\u00e9tude GUARDIAN en cours sur AGAMREE (vamorolone), ont \u00e9t\u00e9 pr\u00e9sent\u00e9s lors de la conf\u00e9rence clinique et scientifique 2026 de la Muscular Dystrophy Association (MDA) \u00e0 Orlando, en Floride. En savoir plus\u00a0: <a href=\"https:\/\/dmdwarrior.com\/fr\/what-is-agamree-vamorolone-what-is-agamree-used-for\/\" data-type=\"post\" data-id=\"2333\">Qu&#039;est-ce qu&#039;Agamree (Vamorolone) ?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">L&#039;ensemble de donn\u00e9es comprend jusqu&#039;\u00e0 huit ans d&#039;exposition \u00e0 AGAMREE (m\u00e9diane d&#039;environ cinq ans) chez des gar\u00e7ons atteints de dystrophie musculaire de Duchenne (DMD). Les analyses int\u00e8grent les donn\u00e9es des participants aux \u00e9tudes cliniques qui ont poursuivi leur traitement par le biais de divers programmes d&#039;acc\u00e8s, ainsi que celles de l&#039;\u00e9tude de phase 4 GUARDIAN (NCT06713135). Les donn\u00e9es \u00e0 long terme, y compris les r\u00e9sultats initiaux de GUARDIAN, ont \u00e9t\u00e9 compar\u00e9es \u00e0 une cohorte t\u00e9moin historique appari\u00e9e selon la propension et trait\u00e9e par d\u00e9flazacort ou prednisone.<a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06713135\" target=\"_blank\" rel=\"noreferrer noopener\">NCT06713135<\/a>)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Ensemble, les donn\u00e9es d\u00e9montrent que la vamorolone conserve une efficacit\u00e9 \u00e0 long terme comparable \u00e0 celle des corticost\u00e9ro\u00efdes traditionnels, tout en am\u00e9liorant la tol\u00e9rance et en r\u00e9duisant significativement les principaux effets secondaires associ\u00e9s aux st\u00e9ro\u00efdes, qui entra\u00eenent souvent des r\u00e9ductions de dose ou des arr\u00eats de traitement ayant un impact sur les r\u00e9sultats \u00e0 long terme des patients. Lire la suite\u00a0: <a href=\"https:\/\/dmdwarrior.com\/fr\/pros-and-cons-of-steroids-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" data-type=\"post\" data-id=\"6244\" rel=\"noreferrer noopener\">Quels sont les avantages et les inconv\u00e9nients des st\u00e9ro\u00efdes (cortisone) pour la dystrophie musculaire de Duchenne ?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Suivre cette page<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/fr\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">Tous les essais cliniques pour la dystrophie musculaire de Duchenne<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Santhera Pharmaceuticals announced that full results from long-term real-world comparative analyses, including baseline data from the ongoing GUARDIAN study of AGAMREE (vamorolone), were presented at the Muscular Dystrophy Association (MDA) Clinical &amp; Scientific Conference 2026 in Orlando, Florida. Learn More: What is Agamree (Vamorolone)? The dataset includes up to eight years of AGAMREE exposure (median [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6703,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[42,41,43],"class_list":["post-6701","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-agamree","tag-santhera","tag-vamorolone"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/6701","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=6701"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/6701\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/6703"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=6701"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=6701"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=6701"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}