{"id":3823,"date":"2025-05-07T15:43:13","date_gmt":"2025-05-07T12:43:13","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3823"},"modified":"2025-05-07T15:43:14","modified_gmt":"2025-05-07T12:43:14","slug":"sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells\/","title":{"rendered":"La m\u00e9thode d&#039;administration par ultrasons SonoThera peut d\u00e9livrer la dystrophine compl\u00e8te aux cellules"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Les r\u00e9sultats de l&#039;\u00e9tude, actuellement en cours de d\u00e9veloppement pour le traitement de la dystrophie musculaire de Duchenne (DMD) du SonoThera, d\u00e9montrent la capacit\u00e9 de la technologie d&#039;administration par ultrasons \u00e0 administrer des m\u00e9dicaments g\u00e9n\u00e9tiques. <strong>Cette technologie permet l\u2019expression compl\u00e8te de la prot\u00e9ine dystrophine dans les muscles squelettiques, cardiaques et diaphragmatiques dans les mod\u00e8les de souris et de primates non humains (NHP).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">SonoThera, une soci\u00e9t\u00e9 de biotechnologie d\u00e9di\u00e9e au traitement de la cause profonde des maladies humaines en d\u00e9veloppant la prochaine g\u00e9n\u00e9ration de m\u00e9dicaments g\u00e9n\u00e9tiques, a annonc\u00e9 aujourd&#039;hui qu&#039;elle pr\u00e9senterait de nouvelles donn\u00e9es lors de la 28e r\u00e9union annuelle de l&#039;American Society of Gene and Cell Therapy (ASGCT) qui se tiendra du 13 au 17 mai \u00e0 la Nouvelle-Orl\u00e9ans, en Louisiane.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u00ab Nous sommes heureux de pr\u00e9senter de nouvelles donn\u00e9es \u00e0 l&#039;ASGCT soulignant le potentiel de l&#039;administration par ultrasons pour r\u00e9soudre les principaux d\u00e9fis de la m\u00e9decine g\u00e9n\u00e9tique \u00bb, a d\u00e9clar\u00e9 Kenneth Greenberg, PhD, PDG de SonoThera. <strong>\u00ab Ces donn\u00e9es continuent de d\u00e9montrer nos capacit\u00e9s uniques, notamment l&#039;expression cibl\u00e9e de la dystrophine humaine sur toute sa longueur dans le muscle et la fourniture de charges g\u00e9n\u00e9tiques surdimensionn\u00e9es de mani\u00e8re durable, s\u00fbre, redosable et non invasive.<\/strong> Nous sommes impatients de partager nos derni\u00e8res donn\u00e9es lors de la r\u00e9union annuelle de cette ann\u00e9e. \u00bb<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Apprendre encore plus: <a href=\"https:\/\/dmdwarrior.com\/fr\/sonothera-presents-new-data-of-genetic-medicine-using-targeted-ultrasound-mediated-delivery-umd-in-treating-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Transmission par ultrasons (AUM)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The findings of the study, which are currently being developed for SonoThera&#8217;s Duchenne Muscular Dystrophy (DMD) treatment, demonstrate the capability of Ultrasound-Mediated Delivery technology to deliver genetic drugs. This technology enables full-length dystrophin protein expression in skeletal, cardiac, and diaphragm muscles in mouse and non-human primate (NHP) models. SonoThera, a biotechnology company dedicated to treating [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3824,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[366,359,367,285,286],"class_list":["post-3823","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-asgct-2025","tag-full-length-dystrophin","tag-kenneth-greenberg","tag-sonothera","tag-ultrasound-mediated-delivery"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/3823","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=3823"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/3823\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/3824"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=3823"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=3823"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=3823"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}