{"id":3173,"date":"2025-03-10T17:19:24","date_gmt":"2025-03-10T14:19:24","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3173"},"modified":"2025-05-07T10:15:23","modified_gmt":"2025-05-07T07:15:23","slug":"sonothera-presents-new-data-of-genetic-medicine-using-targeted-ultrasound-mediated-delivery-umd-in-treating-duchenne-muscular-dystrophy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/sonothera-presents-new-data-of-genetic-medicine-using-targeted-ultrasound-mediated-delivery-umd-in-treating-duchenne-muscular-dystrophy\/","title":{"rendered":"SonoThera pr\u00e9sentera de nouvelles donn\u00e9es sur la m\u00e9decine g\u00e9n\u00e9tique utilisant l&#039;administration cibl\u00e9e par ultrasons (UMD) dans le traitement de la dystrophie musculaire de Duchenne"},"content":{"rendered":"<p class=\"wp-block-paragraph\">SonoThera pr\u00e9sentera de nouvelles donn\u00e9es lors de la conf\u00e9rence MDA 2025 d\u00e9montrant le potentiel de la m\u00e9decine g\u00e9n\u00e9tique utilisant l&#039;administration cibl\u00e9e par ultrasons (UMD) dans le traitement de la dystrophie musculaire de Duchenne.<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>De nouvelles donn\u00e9es pr\u00e9cliniques d\u00e9montrent la capacit\u00e9 de la nouvelle technologie UMD non virale de SonoThera \u00e0 d\u00e9livrer des m\u00e9dicaments g\u00e9n\u00e9tiques, permettant l&#039;expression compl\u00e8te de la prot\u00e9ine dystrophine dans les muscles squelettiques, cardiaques et du diaphragme.<\/li>\n\n\n\n<li>L&#039;approche non invasive de SonoThera est en cours de d\u00e9veloppement pour permettre une biodistribution large et hautement cibl\u00e9e de divers m\u00e9dicaments g\u00e9n\u00e9tiques sans restriction de taille, de mani\u00e8re s\u00fbre et redosable.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\">SonoThera, une soci\u00e9t\u00e9 de biotechnologie d\u00e9di\u00e9e au traitement de la cause profonde des maladies humaines en d\u00e9veloppant la prochaine g\u00e9n\u00e9ration de m\u00e9dicaments g\u00e9n\u00e9tiques, a annonc\u00e9 aujourd&#039;hui qu&#039;elle pr\u00e9senterait de nouvelles donn\u00e9es lors de la conf\u00e9rence clinique et scientifique annuelle de la Muscular Dystrophy Association (MDA), qui se tiendra du 16 au 19 mars \u00e0 Dallas, au Texas.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Transmission par ultrasons (AUM)<\/h2>\n\n\n\n<p class=\"wp-block-paragraph\">SonoThera d\u00e9veloppe la premi\u00e8re plateforme de transfert de g\u00e8nes non virale par ultrasons au monde, con\u00e7ue pour surmonter les limites des autres approches de th\u00e9rapie g\u00e9nique.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Les donn\u00e9es pr\u00e9cliniques mettent en \u00e9vidence la capacit\u00e9 de l&#039;administration par ultrasons (UMD) \u00e0 exprimer des constructions g\u00e9n\u00e9tiques non virales de mani\u00e8re redosable et durable, permettant l&#039;expression compl\u00e8te de la dystrophine dans les muscles squelettiques, cardiaques et diaphragmatiques dans des mod\u00e8les murins. SonoThera d\u00e9veloppe une approche exclusive, non virale et non invasive utilisant l&#039;administration par ultrasons, qui permet une biodistribution large et hautement cibl\u00e9e de divers m\u00e9dicaments g\u00e9n\u00e9tiques sans restriction de taille de mani\u00e8re redosable, con\u00e7ue pour \u00eatre s\u00fbre, bien tol\u00e9r\u00e9e et rentable.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u00ab Nous nous concentrons sur les d\u00e9fis importants qui restent \u00e0 relever pour le traitement de la DMD, notamment l\u2019incapacit\u00e9 \u00e0 administrer la dystrophine compl\u00e8te, l\u2019immunog\u00e9nicit\u00e9 du vecteur viral, l\u2019incapacit\u00e9 \u00e0 am\u00e9liorer la fonction motrice, l\u2019incapacit\u00e9 \u00e0 redoser, les probl\u00e8mes de s\u00e9curit\u00e9 et, bien s\u00fbr, le co\u00fbt \u00e9lev\u00e9 du traitement \u00bb, a d\u00e9clar\u00e9 Kenneth Greenberg, PhD, PDG de SonoThera. \u00ab Nous pensons que l\u2019UMD peut r\u00e9soudre ces probl\u00e8mes et le faire de mani\u00e8re non virale et non invasive. Nous sommes impatients de partager nos derni\u00e8res donn\u00e9es lors de la prochaine conf\u00e9rence de la MDA. \u00bb<\/p>","protected":false},"excerpt":{"rendered":"<p>SonoThera will present new data at the 2025 MDA Conference demonstrating the potential of genetic medicine using targeted, Ultrasound-Mediated Delivery (UMD) in treating Duchenne Muscular Dystrophy. SonoThera, a biotechnology company dedicated to treating the root cause of human diseases through developing the next generation of genetic medicines, today announced it will present new data at [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3174,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[359,285,286],"class_list":["post-3173","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-full-length-dystrophin","tag-sonothera","tag-ultrasound-mediated-delivery"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/3173","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=3173"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/3173\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/3174"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=3173"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=3173"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=3173"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}