{"id":2570,"date":"2025-01-24T11:20:01","date_gmt":"2025-01-24T08:20:01","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2570"},"modified":"2025-03-07T13:21:44","modified_gmt":"2025-03-07T10:21:44","slug":"will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies\/","title":{"rendered":"Le partenariat entre G\u00e9n\u00e9thon et Eukar\u00ffs permettra-t-il de r\u00e9duire le co\u00fbt des th\u00e9rapies g\u00e9niques ?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">La th\u00e9rapie g\u00e9nique FDA, la seule approuv\u00e9e pour la dystrophie musculaire de Duchenne, co\u00fbte beaucoup trop cher pour les familles. Les familles ne peuvent tout simplement pas se permettre ce prix prohibitif. Les fabricants devraient reconsid\u00e9rer le prix des th\u00e9rapies g\u00e9niques contre la DMD. Selon une annonce de G\u00e9n\u00e9thon du 23 janvier, la collaboration avec Eukar\u00ffs pourrait ramener le prix des th\u00e9rapies g\u00e9niques contre la DMD \u00e0 un niveau raisonnable.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Eukar\u00ffs, une soci\u00e9t\u00e9 de biotechnologie qui a cr\u00e9\u00e9 une technologie r\u00e9volutionnaire qui augmente consid\u00e9rablement les rendements de la bioproduction, et Genethon, pionnier et leader dans la recherche et le d\u00e9veloppement de traitements g\u00e9niques pour les maladies rares, ont annonc\u00e9 aujourd&#039;hui la conclusion d&#039;un accord strat\u00e9gique. Cette collaboration utilise la technologie C3P3 unique d&#039;Eukar\u00ffs, une nouvelle m\u00e9thode d&#039;expression de l&#039;ARN messager (ARNm) dans les cellules de mammif\u00e8res, pour r\u00e9duire le co\u00fbt de production des m\u00e9dicaments de th\u00e9rapie g\u00e9nique.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Apprendre encore plus:<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/fr\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Nouvelles th\u00e9rapies g\u00e9niques potentielles \u00e0 venir pour la dystrophie musculaire de Duchenne<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>En savoir plus:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/fr\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\">Questions fr\u00e9quemment pos\u00e9es sur Elevidys<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA-approved only gene therapy for Duchenne muscular dystrophy is costing far too much for families to afford. Families simply cannot afford this prohibitive price. Manufacturers should reconsider the price of DMD gene therapies. According to an announcement by Genethon on January 23, the collaboration with Eukar\u00ffs could bring the price of DMD gene therapies [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2572,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[201,66,200,72,61,105,202],"class_list":["post-2570","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-c3p3-technology","tag-duchenne-muscular-dystrophy","tag-eukarys","tag-gene-editing","tag-gene-therapy","tag-genethon","tag-mrna"],"subtitle":"Le prix de 2,9 millions de dollars de la th\u00e9rapie g\u00e9nique ELEVIDYS, d\u00e9velopp\u00e9e pour la myopathie de Duchenne et approuv\u00e9e par l'FDA, inqui\u00e8te les familles. Selon l'annonce faite par G\u00e9n\u00e9thon, leur partenariat avec Eukar\u00ffs permettra de r\u00e9duire le co\u00fbt des th\u00e9rapies g\u00e9niques.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2570","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=2570"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2570\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/2572"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=2570"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=2570"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=2570"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}