{"id":2543,"date":"2025-01-23T11:09:58","date_gmt":"2025-01-23T08:09:58","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2543"},"modified":"2025-01-23T11:10:00","modified_gmt":"2025-01-23T08:10:00","slug":"personalized-miniorgans-could-speed-up-treatment-of-duchenne","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/personalized-miniorgans-could-speed-up-treatment-of-duchenne\/","title":{"rendered":"Des mini-organes personnalis\u00e9s pourraient acc\u00e9l\u00e9rer le traitement de la maladie de Duchenne"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Les oligonucl\u00e9otides antisens (ASO) personnalis\u00e9s peuvent acc\u00e9l\u00e9rer les \u00e9tudes sur le traitement de la dystrophie musculaire de Duchenne (DMD).<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Chaque ann\u00e9e, des dizaines de milliers de b\u00e9b\u00e9s naissent avec des maladies myst\u00e9rieuses provoqu\u00e9es par des anomalies g\u00e9n\u00e9tiques si rares qu&#039;aucun traitement n&#039;a encore \u00e9t\u00e9 tent\u00e9. Des chercheurs ont d\u00e9couvert une m\u00e9thode permettant d&#039;acc\u00e9l\u00e9rer le travail de laboratoire n\u00e9cessaire pour tester des m\u00e9dicaments personnalis\u00e9s pour certains de ces enfants malades en utilisant de minuscules amas de tissu produit \u00e0 partir de cellules sanguines de patients.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Les oligonucl\u00e9otides antisens personnalis\u00e9s (ASO) ont montr\u00e9 des r\u00e9sultats prometteurs dans le traitement de maladies g\u00e9n\u00e9tiques rares. La capacit\u00e9 \u00e0 identifier les individus atteints de maladies rares et pr\u00e9sentant des variations g\u00e9n\u00e9tiques pathog\u00e8nes sensibles \u00e0 cette approche th\u00e9rapeutique devrait s&#039;am\u00e9liorer \u00e0 mesure que la technologie du s\u00e9quen\u00e7age clinique continue de progresser.<\/p>","protected":false},"excerpt":{"rendered":"<p>Personalized antisense oligonucleotides (ASOs) may accelerate studies on treating Duchenne muscular dystrophy (DMD). Every year, tens of thousands of babies are born with enigmatic illnesses brought on by genetic abnormalities that are so uncommon that no treatment has yet been attempted. Researchers have now discovered a method to expedite the laboratory work required to test [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2545,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[191,66,190,189],"class_list":["post-2543","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-aso","tag-duchenne-muscular-dystrophy","tag-miniorgans","tag-organoids"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2543","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=2543"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2543\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/2545"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=2543"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=2543"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=2543"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}