{"id":2455,"date":"2025-01-16T11:50:08","date_gmt":"2025-01-16T08:50:08","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2455"},"modified":"2025-01-16T13:21:23","modified_gmt":"2025-01-16T10:21:23","slug":"solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy\/","title":{"rendered":"Solid Biosciences publie des informations sur l&#039;essai clinique de la th\u00e9rapie g\u00e9nique SGT-003"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Solid Biosciences a indiqu\u00e9 que quatre patients ont \u00e9t\u00e9 trait\u00e9s dans le cadre de l&#039;essai clinique de th\u00e9rapie g\u00e9nique SGT-003 ; celui-ci a \u00e9t\u00e9 bien tol\u00e9r\u00e9 chez tous les patients sans aucun effet secondaire observ\u00e9 ; et les donn\u00e9es des trois premiers patients pourraient \u00eatre disponibles au premier trimestre 2025.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Th\u00e9rapie g\u00e9nique SGT-003 pour la dystrophie musculaire de Duchenne (DMD)<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>Le SGT-003 continue d\u2019\u00eatre bien tol\u00e9r\u00e9 chez les quatre premiers patients trait\u00e9s dans le cadre de l\u2019essai clinique INSPIRE DUCHENNE en cours.<\/li>\n\n\n\n<li>L\u2019inscription des patients et le dosage dans le cadre du protocole INSPIRE DUCHENNE \u00e9largi sont en cours.<\/li>\n\n\n\n<li>Six sites cliniques sont activ\u00e9s en Am\u00e9rique du Nord (cinq aux \u00c9tats-Unis, un au Canada).<\/li>\n\n\n\n<li>L&#039;Agence de r\u00e9glementation des m\u00e9dicaments et des produits de sant\u00e9 du Royaume-Uni (MHRA) a approuv\u00e9 la demande d&#039;essai clinique (CTA) INSPIRE DUCHENNE avec une activation initiale du site pr\u00e9vue au deuxi\u00e8me semestre 2025.<\/li>\n\n\n\n<li>Solid pr\u00e9voit de communiquer les donn\u00e9es des trois premiers patients trait\u00e9s au premier trimestre 2025.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Apprendre encore plus:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/fr\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\">Nouvelles th\u00e9rapies g\u00e9niques potentielles \u00e0 venir pour la dystrophie musculaire de Duchenne<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Solid Biosciences shared that four patients have been dosed in the SGT-003 gene therapy clinical trial; it was well tolerated in all patients with no side effects observed; and data from the first three patients could be available in Q1 2025. SGT-003 Gene Therapy for Duchenne Muscular Dystrophy (DMD) Learn More: Potential Upcoming New Gene [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2458,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[171,72,61,110,170,109,79],"class_list":["post-2455","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-canada","tag-gene-editing","tag-gene-therapy","tag-sgt-003","tag-sgt-003-gene-therapy","tag-solid-biosciences","tag-usa"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2455","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=2455"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2455\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/2458"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=2455"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=2455"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=2455"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}