{"id":2438,"date":"2025-01-15T12:28:10","date_gmt":"2025-01-15T09:28:10","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2438"},"modified":"2025-01-15T12:28:12","modified_gmt":"2025-01-15T09:28:12","slug":"the-fda-designates-ips-hearts-givi-mpc-stem-cell-therapy-for-becker-muscular-dystrophy-an-orphan-drug","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/fr\/the-fda-designates-ips-hearts-givi-mpc-stem-cell-therapy-for-becker-muscular-dystrophy-an-orphan-drug\/","title":{"rendered":"Le FDA d\u00e9signe la th\u00e9rapie par cellules souches GIVI-MPC d&#039;IPS HEART pour la dystrophie musculaire de Becker comme m\u00e9dicament orphelin"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Le FDA a accord\u00e9 la d\u00e9signation de m\u00e9dicament orphelin (ODD) d&#039;IPS HEART pour les GIVI-MPC en raison de sa capacit\u00e9 exceptionnelle \u00e0 produire de nouveaux muscles avec de la dystrophine pleine longueur chez les patients atteints de dystrophie musculaire de Becker (BMD).<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">IPS HEART a d\u00e9montr\u00e9 que les GIVI-MPC produisent de nouveaux muscles humains avec de la dystrophine humaine compl\u00e8te dans un mod\u00e8le murin de sarcop\u00e9nie, de souris atteintes de dystrophie musculaire de Duchenne (DMD) juv\u00e9niles et tr\u00e8s \u00e2g\u00e9es et de porcs dystrophiques. Afin de d\u00e9montrer le potentiel exceptionnel de la plateforme GIVI-MPC pour inverser les maladies invalidantes, le FDA a pr\u00e9c\u00e9demment accord\u00e9 aux GIVI-MPC la d\u00e9signation de m\u00e9dicament orphelin pour la DMD.<\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA has granted IPS HEART Orphan Drug Designation (ODD) for GIVI-MPCs because of its exceptional capacity to produce new muscle with full length dystrophin in patients with Becker Muscular Dystrophy (BMD). It has now been demonstrated by IPS HEART that GIVI-MPCs produce new human muscle with full length human dystrophin in a mouse model [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2441,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[67,73,88,160,161],"class_list":["post-2438","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-becker-muscular-dystrophy","tag-dystrophin","tag-fda","tag-givi-mpc","tag-ips-heart"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2438","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/comments?post=2438"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/posts\/2438\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media\/2441"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/media?parent=2438"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/categories?post=2438"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/fr\/wp-json\/wp\/v2\/tags?post=2438"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}