{"id":6701,"date":"2026-03-09T18:17:40","date_gmt":"2026-03-09T15:17:40","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=6701"},"modified":"2026-03-09T18:34:31","modified_gmt":"2026-03-09T15:34:31","slug":"vamorolone-agamree-in-dmd-real-world-experience","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/es\/vamorolone-agamree-in-dmd-real-world-experience\/","title":{"rendered":"Vamorolone (Agamree) en DMD: Experiencia en el mundo real"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Santhera Pharmaceuticals anunci\u00f3 la presentaci\u00f3n de los resultados completos de los an\u00e1lisis comparativos a largo plazo en condiciones reales, incluyendo los datos de referencia del estudio GUARDIAN en curso de AGAMREE (vamorolona), en la Conferencia Cl\u00ednica y Cient\u00edfica de la Asociaci\u00f3n de Distrofia Muscular (MDA) de 2026 en Orlando, Florida. M\u00e1s informaci\u00f3n: <a href=\"https:\/\/dmdwarrior.com\/es\/what-is-agamree-vamorolone-what-is-agamree-used-for\/\" data-type=\"post\" data-id=\"2333\">\u00bfQu\u00e9 es Agamree (Vamorolone)?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">El conjunto de datos incluye hasta ocho a\u00f1os de exposici\u00f3n a AGAMREE (mediana de aproximadamente cinco a\u00f1os) en ni\u00f1os con distrofia muscular de Duchenne (DMD). Los an\u00e1lisis incorporan datos de participantes en estudios cl\u00ednicos que continuaron el tratamiento a trav\u00e9s de diversos programas de acceso, as\u00ed como del estudio GUARDIAN de fase 4 (NCT06713135). Los datos a largo plazo, incluidos los resultados iniciales de GUARDIAN, se compararon con una cohorte de control hist\u00f3rica emparejada por propensi\u00f3n tratada con deflazacort o prednisona.<a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06713135\" target=\"_blank\" rel=\"noreferrer noopener\">NCT06713135<\/a>)<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">En conjunto, los datos demuestran que la vamorolona mantiene una eficacia a largo plazo comparable a la de los corticosteroides tradicionales, a la vez que mejora la tolerabilidad y reduce significativamente los principales efectos secundarios asociados a los esteroides, que a menudo conducen a reducciones o suspensiones de la dosis, lo que afecta los resultados a largo plazo del paciente. Leer m\u00e1s: <a href=\"https:\/\/dmdwarrior.com\/es\/pros-and-cons-of-steroids-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" data-type=\"post\" data-id=\"6244\" rel=\"noreferrer noopener\">\u00bfCu\u00e1les son las ventajas y desventajas de los esteroides (cortisona) para la distrofia muscular de Duchenne?<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Sigue esta p\u00e1gina<\/strong>&nbsp;&gt;&gt;&gt;&nbsp;<a href=\"https:\/\/dmdwarrior.com\/es\/dmd-therapies\/\" target=\"_blank\" rel=\"noreferrer noopener\">Todos los ensayos cl\u00ednicos para la distrofia muscular de Duchenne<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Santhera Pharmaceuticals announced that full results from long-term real-world comparative analyses, including baseline data from the ongoing GUARDIAN study of AGAMREE (vamorolone), were presented at the Muscular Dystrophy Association (MDA) Clinical &amp; Scientific Conference 2026 in Orlando, Florida. Learn More: What is Agamree (Vamorolone)? The dataset includes up to eight years of AGAMREE exposure (median [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":6703,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[42,41,43],"class_list":["post-6701","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-agamree","tag-santhera","tag-vamorolone"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/6701","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/comments?post=6701"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/6701\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media\/6703"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media?parent=6701"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/categories?post=6701"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/tags?post=6701"}],"curies":[{"name":"gracias","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}