{"id":3823,"date":"2025-05-07T15:43:13","date_gmt":"2025-05-07T12:43:13","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3823"},"modified":"2025-05-07T15:43:14","modified_gmt":"2025-05-07T12:43:14","slug":"sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/es\/sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells\/","title":{"rendered":"El m\u00e9todo de administraci\u00f3n por ultrasonido SonoThera puede administrar distrofina de longitud completa a las c\u00e9lulas"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Los resultados del estudio, que actualmente se est\u00e1n desarrollando para el tratamiento de la distrofia muscular de Duchenne (DMD) de SonoThera, demuestran la capacidad de la tecnolog\u00eda de administraci\u00f3n mediada por ultrasonido para administrar medicamentos gen\u00e9ticos. <strong>Esta tecnolog\u00eda permite la expresi\u00f3n de la prote\u00edna distrofina de longitud completa en los m\u00fasculos esquel\u00e9ticos, card\u00edacos y del diafragma en modelos de ratones y primates no humanos (NHP).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">SonoThera, una compa\u00f1\u00eda de biotecnolog\u00eda dedicada a tratar la causa ra\u00edz de las enfermedades humanas a trav\u00e9s del desarrollo de la pr\u00f3xima generaci\u00f3n de medicamentos gen\u00e9ticos, anunci\u00f3 hoy que presentar\u00e1 nuevos datos en la 28\u00aa reuni\u00f3n anual de la Sociedad Americana de Terapia G\u00e9nica y Celular (ASGCT) que se llevar\u00e1 a cabo del 13 al 17 de mayo en Nueva Orleans, Luisiana.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">&quot;Nos complace presentar nuevos datos en ASGCT que resaltan el potencial de la administraci\u00f3n mediada por ultrasonido para resolver los desaf\u00edos clave en la medicina gen\u00e9tica&quot;, afirm\u00f3 Kenneth Greenberg, PhD, director ejecutivo de SonoThera. <strong>\u201cEstos datos contin\u00faan demostrando nuestras capacidades \u00fanicas, incluida la expresi\u00f3n dirigida de distrofina humana de longitud completa en el m\u00fasculo y la administraci\u00f3n de cargas gen\u00e9ticas de gran tama\u00f1o de una manera duradera, segura, redosificable y no invasiva.<\/strong> \u201cEsperamos compartir nuestros \u00faltimos datos en la reuni\u00f3n anual de este a\u00f1o\u201d.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">M\u00e1s informaci\u00f3n: <a href=\"https:\/\/dmdwarrior.com\/es\/sonothera-presents-new-data-of-genetic-medicine-using-targeted-ultrasound-mediated-delivery-umd-in-treating-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Transmisi\u00f3n mediada por ultrasonido (UMD)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The findings of the study, which are currently being developed for SonoThera&#8217;s Duchenne Muscular Dystrophy (DMD) treatment, demonstrate the capability of Ultrasound-Mediated Delivery technology to deliver genetic drugs. This technology enables full-length dystrophin protein expression in skeletal, cardiac, and diaphragm muscles in mouse and non-human primate (NHP) models. SonoThera, a biotechnology company dedicated to treating [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3824,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[366,359,367,285,286],"class_list":["post-3823","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-asgct-2025","tag-full-length-dystrophin","tag-kenneth-greenberg","tag-sonothera","tag-ultrasound-mediated-delivery"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/3823","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/comments?post=3823"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/3823\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media\/3824"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media?parent=3823"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/categories?post=3823"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/tags?post=3823"}],"curies":[{"name":"gracias","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}