{"id":2570,"date":"2025-01-24T11:20:01","date_gmt":"2025-01-24T08:20:01","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2570"},"modified":"2025-03-07T13:21:44","modified_gmt":"2025-03-07T10:21:44","slug":"will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/es\/will-genethon-and-eukarys-partnership-reduce-the-cost-of-gene-therapies\/","title":{"rendered":"\u00bfLa colaboraci\u00f3n entre Genethon y Eukar\u00ffs reducir\u00e1 el coste de las terapias gen\u00e9ticas?"},"content":{"rendered":"<p class=\"wp-block-paragraph\">La terapia g\u00e9nica FDA, \u00fanica en su tipo, para la distrofia muscular de Duchenne est\u00e1 costando demasiado para las familias. Las familias simplemente no pueden permitirse este precio prohibitivo. Los fabricantes deber\u00edan reconsiderar el precio de las terapias g\u00e9nicas para la distrofia muscular de Duchenne. Seg\u00fan un anuncio de Genethon del 23 de enero, la colaboraci\u00f3n con Eukar\u00ffs podr\u00eda reducir el precio de las terapias g\u00e9nicas para la distrofia muscular de Duchenne a un nivel razonable.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Hoy, Eukar\u00ffs, una empresa de biotecnolog\u00eda que crea una tecnolog\u00eda revolucionaria que aumenta dr\u00e1sticamente los rendimientos de la biofabricaci\u00f3n, y Genethon, una empresa pionera y l\u00edder en la investigaci\u00f3n y el desarrollo de tratamientos gen\u00e9ticos para enfermedades raras, anunciaron la formaci\u00f3n de un acuerdo estrat\u00e9gico. La colaboraci\u00f3n utiliza la tecnolog\u00eda C3P3 exclusiva de Eukar\u00ffs, un novedoso m\u00e9todo de expresi\u00f3n de ARN mensajero (ARNm) en c\u00e9lulas de mam\u00edferos, para reducir el costo de producci\u00f3n de medicamentos de terapia gen\u00e9tica.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>M\u00e1s informaci\u00f3n:<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/es\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Posibles nuevas terapias gen\u00e9ticas para la distrofia muscular de Duchenne<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>Leer m\u00e1s:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/es\/frequently-asked-questions-about-elevidys-used-for-duchenne-muscular-dystrophy\/\">Preguntas frecuentes sobre Elevidys<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA-approved only gene therapy for Duchenne muscular dystrophy is costing far too much for families to afford. Families simply cannot afford this prohibitive price. Manufacturers should reconsider the price of DMD gene therapies. According to an announcement by Genethon on January 23, the collaboration with Eukar\u00ffs could bring the price of DMD gene therapies [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2572,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[201,66,200,72,61,105,202],"class_list":["post-2570","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-c3p3-technology","tag-duchenne-muscular-dystrophy","tag-eukarys","tag-gene-editing","tag-gene-therapy","tag-genethon","tag-mrna"],"subtitle":"El precio de 2,9 millones de d\u00f3lares de la terapia g\u00e9nica ELEVIDYS, desarrollada para la distrofia muscular de Duchenne y aprobada por el FDA, preocupa a las familias. Seg\u00fan el anuncio de Genethon, su asociaci\u00f3n con Eukar\u00ffs permitir\u00e1 reducir el coste de las terapias g\u00e9nicas.","_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2570","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/comments?post=2570"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2570\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media\/2572"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media?parent=2570"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/categories?post=2570"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/tags?post=2570"}],"curies":[{"name":"gracias","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}