{"id":2564,"date":"2025-01-23T22:26:59","date_gmt":"2025-01-23T19:26:59","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2564"},"modified":"2025-03-07T14:53:34","modified_gmt":"2025-03-07T11:53:34","slug":"belief-biomed-announces-ind-clearance-by-fda-for-duchenne-muscular-dystrophy-gene-therapy-candidate-bbm-d101","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/es\/belief-biomed-announces-ind-clearance-by-fda-for-duchenne-muscular-dystrophy-gene-therapy-candidate-bbm-d101\/","title":{"rendered":"Belief BioMed anuncia la autorizaci\u00f3n de IND por parte de FDA para el candidato a terapia g\u00e9nica para la distrofia muscular de Duchenne, BBM-D101"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Belief BioMed informa de la autorizaci\u00f3n IND FDA para el candidato a terapia gen\u00e9tica BBM-D101 para la distrofia muscular de Duchenne.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">La Administraci\u00f3n de Alimentos y Medicamentos de los Estados Unidos (FDA) ha aprobado una solicitud de nuevo f\u00e1rmaco en investigaci\u00f3n (IND) para el candidato a terapia g\u00e9nica para la distrofia muscular de Duchenne (DMD) de Belief BioMed (BBM), BBM-D101. BBM es una empresa de biotecnolog\u00eda con visi\u00f3n de futuro que se centra en la creaci\u00f3n de terapias g\u00e9nicas innovadoras.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">El objetivo de esta investigaci\u00f3n cl\u00ednica abierta de dosis \u00fanica fue evaluar la seguridad y la eficacia de una \u00fanica infusi\u00f3n intravenosa en pacientes con DMD de entre 4 y 9 a\u00f1os. Debido a su c\u00e1pside modificada, BBM-D101 es m\u00e1s eficaz en la transducci\u00f3n de tejido muscular. Como resultado, se prev\u00e9 que BBM-D101 tenga una buena seguridad y la dosis cl\u00ednica sugerida sea inferior a la de los productos de terapia g\u00e9nica con virus adenoasociados (AAV) comparables autorizados.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>M\u00e1s informaci\u00f3n:<\/strong>\u00a0<a href=\"https:\/\/dmdwarrior.com\/es\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Posibles nuevas terapias gen\u00e9ticas para la distrofia muscular de Duchenne<\/a><\/p>\n\n\n\n<p class=\"wp-block-paragraph\"><\/p>","protected":false},"excerpt":{"rendered":"<p>Belief BioMed Reports FDA IND Clearance for Gene Therapy Candidate BBM-D101 for Duchenne Muscular Dystrophy. The U.S. Food and Drug Administration (FDA) has approved an Investigational New Drug (IND) application for Belief BioMed&#8217;s (BBM) Duchenne Muscular Dystrophy (DMD) gene therapy candidate, BBM-D101. BBM is a forward-thinking biotechnology company that focuses on creating innovative gene therapies. [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2565,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[199,197,123,66,61,198],"class_list":["post-2564","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-bbm-d101","tag-belief-biomed","tag-china","tag-duchenne-muscular-dystrophy","tag-gene-therapy","tag-shanghai"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2564","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/comments?post=2564"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2564\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media\/2565"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media?parent=2564"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/categories?post=2564"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/tags?post=2564"}],"curies":[{"name":"gracias","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}