{"id":2455,"date":"2025-01-16T11:50:08","date_gmt":"2025-01-16T08:50:08","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2455"},"modified":"2025-01-16T13:21:23","modified_gmt":"2025-01-16T10:21:23","slug":"solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/es\/solid-biosciences-releases-information-on-clinical-trial-for-sgt-003-gene-therapy\/","title":{"rendered":"Solid Biosciences publica informaci\u00f3n sobre el ensayo cl\u00ednico de la terapia g\u00e9nica SGT-003"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Solid Biosciences comparti\u00f3 que se administr\u00f3 la dosis a cuatro pacientes en el ensayo cl\u00ednico de terapia g\u00e9nica SGT-003; fue bien tolerado en todos los pacientes y no se observaron efectos secundarios; y los datos de los primeros tres pacientes podr\u00edan estar disponibles en el primer trimestre de 2025.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">Terapia g\u00e9nica SGT-003 para la distrofia muscular de Duchenne (DMD)<\/h2>\n\n\n\n<ul class=\"wp-block-list\">\n<li>El SGT-003 contin\u00faa siendo bien tolerado en los primeros cuatro pacientes tratados en el ensayo cl\u00ednico INSPIRE DUCHENNE en curso.<\/li>\n\n\n\n<li>La inscripci\u00f3n y la dosificaci\u00f3n de pacientes bajo el protocolo ampliado INSPIRE DUCHENNE est\u00e1 en curso.<\/li>\n\n\n\n<li>Se han activado seis centros cl\u00ednicos en Am\u00e9rica del Norte (cinco en EE. UU. y uno en Canad\u00e1).<\/li>\n\n\n\n<li>La Agencia Reguladora de Medicamentos y Productos Sanitarios del Reino Unido (MHRA) aprob\u00f3 la solicitud de ensayo cl\u00ednico (CTA) de INSPIRE DUCHENNE y se espera que la activaci\u00f3n inicial del sitio tenga lugar en el segundo semestre de 2025.<\/li>\n\n\n\n<li>Solid espera informar datos de los primeros tres pacientes dosificados en el primer trimestre de 2025.<\/li>\n<\/ul>\n\n\n\n<p class=\"wp-block-paragraph\"><strong>M\u00e1s informaci\u00f3n:<\/strong> <a href=\"https:\/\/dmdwarrior.com\/es\/new-gene-therapies-for-duchenne-muscular-dystrophy\/\">Posibles nuevas terapias gen\u00e9ticas para la distrofia muscular de Duchenne<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Solid Biosciences shared that four patients have been dosed in the SGT-003 gene therapy clinical trial; it was well tolerated in all patients with no side effects observed; and data from the first three patients could be available in Q1 2025. SGT-003 Gene Therapy for Duchenne Muscular Dystrophy (DMD) Learn More: Potential Upcoming New Gene [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2458,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[171,72,61,110,170,109,79],"class_list":["post-2455","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-canada","tag-gene-editing","tag-gene-therapy","tag-sgt-003","tag-sgt-003-gene-therapy","tag-solid-biosciences","tag-usa"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2455","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/comments?post=2455"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2455\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media\/2458"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media?parent=2455"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/categories?post=2455"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/tags?post=2455"}],"curies":[{"name":"gracias","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}