{"id":2438,"date":"2025-01-15T12:28:10","date_gmt":"2025-01-15T09:28:10","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2438"},"modified":"2025-01-15T12:28:12","modified_gmt":"2025-01-15T09:28:12","slug":"the-fda-designates-ips-hearts-givi-mpc-stem-cell-therapy-for-becker-muscular-dystrophy-an-orphan-drug","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/es\/the-fda-designates-ips-hearts-givi-mpc-stem-cell-therapy-for-becker-muscular-dystrophy-an-orphan-drug\/","title":{"rendered":"El FDA designa como medicamento hu\u00e9rfano la terapia con c\u00e9lulas madre GIVI-MPC de IPS HEART para la distrofia muscular de Becker"},"content":{"rendered":"<p class=\"wp-block-paragraph\">El FDA ha otorgado a IPS HEART la designaci\u00f3n de medicamento hu\u00e9rfano (ODD) para GIVI-MPC debido a su capacidad excepcional para producir m\u00fasculo nuevo con distrofina de longitud completa en pacientes con distrofia muscular de Becker (BMD).<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">IPS HEART ha demostrado que las MPC de GIVI producen nuevos m\u00fasculos humanos con distrofina humana de longitud completa en un modelo de rat\u00f3n con sarcopenia, ratones con distrofia muscular de Duchenne (DMD) j\u00f3venes y muy viejos y cerdos distr\u00f3ficos. Para demostrar el potencial excepcional de la plataforma de las MPC de GIVI para revertir enfermedades debilitantes, el FDA otorg\u00f3 previamente a las MPC de GIVI la designaci\u00f3n de medicamento hu\u00e9rfano para la DMD.<\/p>","protected":false},"excerpt":{"rendered":"<p>The FDA has granted IPS HEART Orphan Drug Designation (ODD) for GIVI-MPCs because of its exceptional capacity to produce new muscle with full length dystrophin in patients with Becker Muscular Dystrophy (BMD). It has now been demonstrated by IPS HEART that GIVI-MPCs produce new human muscle with full length human dystrophin in a mouse model [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2441,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[67,73,88,160,161],"class_list":["post-2438","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-becker-muscular-dystrophy","tag-dystrophin","tag-fda","tag-givi-mpc","tag-ips-heart"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2438","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/comments?post=2438"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/posts\/2438\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media\/2441"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/media?parent=2438"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/categories?post=2438"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/es\/wp-json\/wp\/v2\/tags?post=2438"}],"curies":[{"name":"gracias","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}