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What does Durability of Response mean in Duchenne (DMD)?

Durability of Response is a Duchenne (DMD) clinical trial data term, explained for patients, families, and caregivers.

Category: Clinical Trial Data, Access, and Reporting

Durability of Response

The length of time a treatment's observed biological or clinical effects persist. In DMD research, durability may refer to sustained dystrophin expression, continued functional benefit, or maintained disease control, and it requires sufficient follow-up to establish how effects change over time.

Updated November 3, 2026

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