{"id":3823,"date":"2025-05-07T15:43:13","date_gmt":"2025-05-07T12:43:13","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=3823"},"modified":"2025-05-07T15:43:14","modified_gmt":"2025-05-07T12:43:14","slug":"sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/de\/sonothera-ultrasound-mediated-delivery-method-can-deliver-full-length-dystrophin-to-cells\/","title":{"rendered":"Die ultraschallvermittelte Verabreichungsmethode SonoThera kann Dystrophin in voller L\u00e4nge an Zellen abgeben"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Die Ergebnisse der Studie, die derzeit f\u00fcr die Behandlung der Duchenne-Muskeldystrophie (DMD) durch SonoThera entwickelt werden, zeigen die Leistungsf\u00e4higkeit der Ultraschall-vermittelten Verabreichungstechnologie zur Verabreichung genetischer Medikamente. <strong>Diese Technologie erm\u00f6glicht die Expression des Dystrophin-Proteins in voller L\u00e4nge in Skelett-, Herz- und Zwerchfellmuskeln in Maus- und nichtmenschlichen Primatenmodellen (NHP).<\/strong><\/p>\n\n\n\n<p class=\"wp-block-paragraph\">SonoThera, ein Biotechnologieunternehmen, das sich der Behandlung der Grundursachen menschlicher Krankheiten durch die Entwicklung der n\u00e4chsten Generation genetischer Medikamente widmet, gab heute bekannt, dass es auf der 28. Jahrestagung der American Society of Gene and Cell Therapy (ASGCT), die vom 13. bis 17. Mai in New Orleans, Louisiana, stattfindet, neue Daten vorstellen wird.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">\u201eWir freuen uns, auf der ASGCT neue Daten pr\u00e4sentieren zu k\u00f6nnen, die das Potenzial der ultraschallvermittelten Verabreichung bei der L\u00f6sung der wichtigsten Herausforderungen in der genetischen Medizin hervorheben\u201c, sagte Kenneth Greenberg, PhD, CEO von SonoThera. <strong>\u201eDiese Daten demonstrieren weiterhin unsere einzigartigen F\u00e4higkeiten, einschlie\u00dflich der gezielten Expression von menschlichem Dystrophin in voller L\u00e4nge im Muskel und der Bereitstellung \u00fcbergro\u00dfer genetischer Nutzlasten auf dauerhafte, sichere, wiederdosierbare und nichtinvasive Weise.<\/strong> Wir freuen uns darauf, unsere neuesten Daten auf der diesj\u00e4hrigen Jahrestagung vorzustellen.\u201c<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Mehr erfahren: <a href=\"https:\/\/dmdwarrior.com\/de\/sonothera-presents-new-data-of-genetic-medicine-using-targeted-ultrasound-mediated-delivery-umd-in-treating-duchenne-muscular-dystrophy\/\" target=\"_blank\" rel=\"noreferrer noopener\">Ultraschall-vermittelte \u00dcbertragung (UMD)<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>The findings of the study, which are currently being developed for SonoThera&#8217;s Duchenne Muscular Dystrophy (DMD) treatment, demonstrate the capability of Ultrasound-Mediated Delivery technology to deliver genetic drugs. This technology enables full-length dystrophin protein expression in skeletal, cardiac, and diaphragm muscles in mouse and non-human primate (NHP) models. SonoThera, a biotechnology company dedicated to treating [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":3824,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[281],"tags":[366,359,367,285,286],"class_list":["post-3823","post","type-post","status-publish","format-standard","has-post-thumbnail","category-press-releases","tag-asgct-2025","tag-full-length-dystrophin","tag-kenneth-greenberg","tag-sonothera","tag-ultrasound-mediated-delivery"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/posts\/3823","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/comments?post=3823"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/posts\/3823\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/media\/3824"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/media?parent=3823"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/categories?post=3823"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/tags?post=3823"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}