{"id":2543,"date":"2025-01-23T11:09:58","date_gmt":"2025-01-23T08:09:58","guid":{"rendered":"https:\/\/dmdwarrior.com\/?p=2543"},"modified":"2025-01-23T11:10:00","modified_gmt":"2025-01-23T08:10:00","slug":"personalized-miniorgans-could-speed-up-treatment-of-duchenne","status":"publish","type":"post","link":"https:\/\/dmdwarrior.com\/de\/personalized-miniorgans-could-speed-up-treatment-of-duchenne\/","title":{"rendered":"Personalisierte Miniorgane k\u00f6nnten die Behandlung von Duchenne beschleunigen"},"content":{"rendered":"<p class=\"wp-block-paragraph\">Personalisierte Antisense-Oligonukleotide (ASOs) k\u00f6nnen Studien zur Behandlung der Duchenne-Muskeldystrophie (DMD) beschleunigen.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Jedes Jahr werden Zehntausende Babys mit r\u00e4tselhaften Krankheiten geboren, die durch genetische Anomalien verursacht werden, die so selten sind, dass bisher keine Behandlung versucht wurde. Forscher haben nun eine Methode entdeckt, um die Laborarbeit zu beschleunigen, die erforderlich ist, um ma\u00dfgeschneiderte Medikamente f\u00fcr einige dieser kranken Kinder zu testen. Dazu verwenden sie winzige Gewebeproben, die aus Blutzellen der Patienten hergestellt wurden.<\/p>\n\n\n\n<p class=\"wp-block-paragraph\">Bei der Behandlung seltener genetischer Krankheiten haben personalisierte Antisense-Oligonukleotide (ASOs) vielversprechende Ergebnisse gezeigt. Die F\u00e4higkeit, Personen mit seltenen Krankheiten zu identifizieren, die pathogene genetische Variationen aufweisen und f\u00fcr diesen therapeutischen Ansatz empf\u00e4nglich sind, d\u00fcrfte sich mit der Weiterentwicklung der klinischen Sequenzierungstechnologie verbessern.<\/p>","protected":false},"excerpt":{"rendered":"<p>Personalized antisense oligonucleotides (ASOs) may accelerate studies on treating Duchenne muscular dystrophy (DMD). Every year, tens of thousands of babies are born with enigmatic illnesses brought on by genetic abnormalities that are so uncommon that no treatment has yet been attempted. Researchers have now discovered a method to expedite the laboratory work required to test [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":2545,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[27],"tags":[191,66,190,189],"class_list":["post-2543","post","type-post","status-publish","format-standard","has-post-thumbnail","category-research","tag-aso","tag-duchenne-muscular-dystrophy","tag-miniorgans","tag-organoids"],"_links":{"self":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/posts\/2543","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/comments?post=2543"}],"version-history":[{"count":0,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/posts\/2543\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/media\/2545"}],"wp:attachment":[{"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/media?parent=2543"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/categories?post=2543"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/dmdwarrior.com\/de\/wp-json\/wp\/v2\/tags?post=2543"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}